NCT01968980

Brief Summary

This is a multicenter, randomized study in subjects with heterozygous familial hypercholesterolemia receiving highly effective statins to assess the safety, efficacy and tolerability of Bococizumab (PF-04950615; RN316) to lower LDL-C.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
370

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2013

Geographic Reach
11 countries

88 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 21, 2013

Completed
2 days until next milestone

Study Start

First participant enrolled

October 23, 2013

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 24, 2013

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 15, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 15, 2016

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 19, 2017

Completed
Last Updated

June 26, 2017

Status Verified

May 1, 2017

Enrollment Period

2.5 years

First QC Date

October 21, 2013

Results QC Date

April 7, 2017

Last Update Submit

May 31, 2017

Conditions

Keywords

High Risk of cardiovascular eventsHeterozygous familial hypercholesterolemia

Outcome Measures

Primary Outcomes (1)

  • Percent Change From Baseline in Low Density Lipoprotein Cholesterol (LDL-C) at Week 12

    Baseline, Week 12

Secondary Outcomes (28)

  • Percent Change From Baseline in Total Cholesterol (TC) at Week 12

    Baseline, Week 12

  • Percent Change From Baseline in Non High Density Lipoprotein Cholesterol (Non HDL-C) at Week 12

    Baseline, Week 12

  • Percent Change From Baseline in Apolipoprotein B (ApoB) at Week 12

    Baseline, Week 12

  • Percent Change From Baseline in Lipoprotein (a) at Week 12

    Baseline, Week 12

  • Percent Change From Baseline in High Density Lipoprotein Cholesterol (HDL-C) at Week 12

    Baseline, Week 12

  • +23 more secondary outcomes

Study Arms (2)

Bococizumab (PF-04950615;RN316)

EXPERIMENTAL

Bococizumab (PF-04950615;RN316)

Drug: Bococizumab (PF-04950615;RN316)

Placebo

PLACEBO COMPARATOR
Other: Placebo

Interventions

150 mg every 2 weeks, subcutaneous injection, 12 months

Bococizumab (PF-04950615;RN316)
PlaceboOTHER

subcutaneous injection every 2 weeks for 12 months

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Treated with a statin.
  • Fasting LDL-C \> 70 mg/dL and triglyceride \<=400 mg/dL.
  • High or very high risk of incurring a cardiovascular event.
  • Heterozygous familial hypercholesterolemia.

You may not qualify if:

  • Pregnant or breastfeeding females.
  • Cardiovascular or cerebrovascular event of procedures during the past 30 days.
  • Congestive heart failure NYHA class IV.
  • Poorly controlled hypertension.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

IMD Medical Group

Los Angeles, California, 90020, United States

Location

Hartford Hospital, JB704

Hartford, Connecticut, 06102, United States

Location

Best Quality Research, Inc.

Hialeah, Florida, 33016, United States

Location

Medical Research Center

Miami, Florida, 33144, United States

Location

Premier Research Associate, Inc

Miami, Florida, 33165, United States

Location

Columbus Clinical Services, LLC

Miami, Florida, 33174, United States

Location

NewPhase Clinical Trials, Corp.

Miami Beach, Florida, 33140, United States

Location

Om Medical

Las Vegas, Nevada, 89119, United States

Location

The University of North Carolina at Chapel Hill Center for Heart & Vascular Care

Chapel Hill, North Carolina, 27599-7075, United States

Location

The University of North Carolina Hospitals - Clinical and Translational Research Center Clinic

Chapel Hill, North Carolina, 27599-7600, United States

Location

Metabolic and Atherosclerosis Research Center

Cincinnati, Ohio, 45227, United States

Location

Oklahoma Heart Hospital Physicians

Oklahoma City, Oklahoma, 73120, United States

Location

Oklahoma Heart Hospital Research Foundation

Oklahoma City, Oklahoma, 73120, United States

Location

Oklahoma Heart Hospital

Oklahoma City, Oklahoma, 73120, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

OnSite Clinical Solutions, LLC

Gaffney, South Carolina, 29340, United States

Location

Galenos Research

Dallas, Texas, 75251, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Pioneer Research Solutions, Inc.

Houston, Texas, 77099, United States

Location

Pioneer Research Solutions, Inc.

Sugar Land, Texas, 77479, United States

Location

Focus Clinical Research, LLC

Draper, Utah, 84020, United States

Location

Burke Internal Medicine & Research

Burke, Virginia, 22015, United States

Location

SHAT in Cardiology EAD

Pleven, 5800, Bulgaria

Location

UMHAT "Sveti Georgi" EAD, Clinic of Cardiology

Plovdiv, 4002, Bulgaria

Location

Second MHAT - Sofia EAD

Sofia, 1202, Bulgaria

Location

MHAT "Sveta Anna", Clinic of Internal Diseases

Sofia, 1709, Bulgaria

Location

St. Paul's Hospital, Healthy Heart

Vancouver, British Columbia, V6Z 1Y6, Canada

Location

Discovery Clinical Services Ltd.

Victoria, British Columbia, V8T 5G4, Canada

Location

Asper Clinical Research Institute

Winnipeg, Manitoba, R2H 2A6, Canada

Location

Health Sciences Centre

St. John's, Newfoundland and Labrador, A1B 3V6, Canada

Location

University of Ottawa Heart Institute

Ottawa, Ontario, K1Y 4W7, Canada

Location

Ecogene-21

Chicoutimi, Quebec, G7H 7K9, Canada

Location

Montreal Heart Institute

Montreal, Quebec, H1T 1C8, Canada

Location

Institut de Recherches Cliniques de Montreal

Montreal, Quebec, H2W 1R7, Canada

Location

Clinique des maladies lipidiques de Quebec Inc

Québec, Quebec, G1V 4W2, Canada

Location

Helsinki Central University Hospital

Helsinki, 00014, Finland

Location

Pohjois-Karjala Projekti Saatio/Ita-Suomen

Joensuu, 80100, Finland

Location

Pohjois-Karjala Projekti Saatio

Joensuu, 80100, Finland

Location

Laakarikeskus Aava Kerava/Aava Kerava Medical Center

Kerava, 04200, Finland

Location

Oulu University Hospital

Oulu, 90220, Finland

Location

Division of Medicine Turku University Hospital

Turku, 20520, Finland

Location

Policlinico "Paolo Giaccone"

Palermo, PA, 90127, Italy

Location

Ospedale "Santa Maria della Misericordia"

Perugia, PG, 06156, Italy

Location

Ospedale di Circolo e Fondazione Macchi

Varese, VA, 21100, Italy

Location

Azienda Ospedaliero Universitaria "Federico II" di Napoli

Napoli, 80131, Italy

Location

St. Franciscus Gasthuis

Rotterdam, South Holland, 3045 PM, Netherlands

Location

Admiraal de Ruyter ziekenhuis

Goes, Zeeland, 4462 RA, Netherlands

Location

Academic Medical Center

Amsterdam, 1105 AZ, Netherlands

Location

Amphia Hospital

Breda, 4818 CK, Netherlands

Location

Deventer Ziekenhuis

Deventer, 7416 SE, Netherlands

Location

Rotterdam Research Institute

Rotterdam, 3039 BD, Netherlands

Location

Albert Schweitzer Hospital

Sliedrecht, 3361 XV, Netherlands

Location

Hagaziekenhuis

The Hague, 2545 CH, Netherlands

Location

UMC Utrecht

Utrecht, 3584 CX, Netherlands

Location

Oslo Universitetssykehus HF

Oslo, 0373, Norway

Location

Oslo Universitetssykehus HF, Ulleval

Oslo, 0450, Norway

Location

NZOZ Vitamed

Bydgoszcz, 85-079, Poland

Location

NZOZ Centrum Zdrowia i Profilaktyki Dabie Sp zo.o.

Krakow, 31-567, Poland

Location

NZOZ Przychodnia Specjalistyczna Andrzej Wittek Henryk Rudzki S.C

Ruda Śląska, 41-709, Poland

Location

IATROS International

Bloemfontein, Free State, 9301, South Africa

Location

Unitas hospital

Centurion, Gauteng, 0157, South Africa

Location

Midrand Medical Centre

Halfway House, Gauteng, 1685, South Africa

Location

Medipark Centre for Clinical Research

Pretoria, Gauteng, 0158, South Africa

Location

Jongaie Research

Pretoria, Gauteng, 0183, South Africa

Location

Synexus Watermeyer Clinical Research Centre

Pretoria, Gauteng, 0184, South Africa

Location

Roodepoort Medicross Clinical Research Centre

Roodepoort, Gauteng, 1724, South Africa

Location

Chelmsford Medical Centre 3

Durban, KwaZulu-Natal, 4001, South Africa

Location

Tiervlei Trial Centre, Karl Bremer Hospital

Bellville, Cape Town, Western Cape, 7530, South Africa

Location

TREAD Research cc.

Parow, Cape Town, Western Cape, 7500, South Africa

Location

Synexus Helderberg Clinical Research Centre

Somerset West, Western Cape, 7130, South Africa

Location

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

Location

Hospital Clinico Universitario, Santiago de Compostela

Santiago de Compostela, Galicia, 15706, Spain

Location

Hospital Universitario Sant Joan de Reus

Reus, Tarragona, 43204, Spain

Location

Hospital Clinic

Barcelona, 08036, Spain

Location

Hospital Universitario Reina Sofia

Córdoba, 14004, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28007, Spain

Location

Fundacion Jimenez Diaz; Servicio de Medicina Interna

Madrid, 28040, Spain

Location

Hospital Clinico San Carlos; U. de Lipidos; Medicina Interna III

Madrid, 28040, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Clinico Universitario Miguel Servet; Medicina Interna

Zaragoza, 50009, Spain

Location

Clinical Trials Pharmacy, 4th Floor Inpatient Pharmacy

Manchester, Greater Manchester, M13 9WL, United Kingdom

Location

Pennine Acute Hospitals NHS Trust

Oldham, Greater Manchester, OL1 2JH, United Kingdom

Location

East and North Hertfordshire NHS Trust

Stevenage, Hertfordshire, SG1 4AB, United Kingdom

Location

Burton Hospitals NHS Foundation Trust

Burton-on-Trent, Staffordshire, DE13 0RB, United Kingdom

Location

Heart of England NHS Foundation Trust

Birmingham, West Midlands, B9 5SS, United Kingdom

Location

Royal Free London NHS Foundation Trust

London, NW3 2QG, United Kingdom

Location

Central Manchester University Hospitals NHS Foundation Trust

Manchester, M13 9WL, United Kingdom

Location

Peterborough and Stamford Hospitals NHS Foundation Trust

Peterborough, PE3 9GZ, United Kingdom

Location

Related Publications (5)

  • Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

  • McCush F, Wang E, Yunis C, Schwartz P, Baltrukonis D. Anti-drug Antibody Magnitude and Clinical Relevance Using Signal to Noise (S/N): Bococizumab Case Study. AAPS J. 2023 Sep 2;25(5):85. doi: 10.1208/s12248-023-00846-x.

  • Chasman DI, Hyde CL, Giulianini F, Danning RD, Wang EQ, Hickling T, Ridker PM, Loomis AK. Genome-wide pharmacogenetics of anti-drug antibody response to bococizumab highlights key residues in HLA DRB1 and DQB1. Sci Rep. 2022 Mar 11;12(1):4266. doi: 10.1038/s41598-022-07997-5.

  • Ridker PM, Rose LM, Kastelein JJP, Santos RD, Wei C, Revkin J, Yunis C, Tardif JC, Shear CL; Studies of PCSK9 Inhibition and the Reduction of vascular Events (SPIRE) Investigators. Cardiovascular event reduction with PCSK9 inhibition among 1578 patients with familial hypercholesterolemia: Results from the SPIRE randomized trials of bococizumab. J Clin Lipidol. 2018 Jul-Aug;12(4):958-965. doi: 10.1016/j.jacl.2018.03.088. Epub 2018 Apr 3.

  • Ridker PM, Tardif JC, Amarenco P, Duggan W, Glynn RJ, Jukema JW, Kastelein JJP, Kim AM, Koenig W, Nissen S, Revkin J, Rose LM, Santos RD, Schwartz PF, Shear CL, Yunis C; SPIRE Investigators. Lipid-Reduction Variability and Antidrug-Antibody Formation with Bococizumab. N Engl J Med. 2017 Apr 20;376(16):1517-1526. doi: 10.1056/NEJMoa1614062. Epub 2017 Mar 17.

Related Links

MeSH Terms

Interventions

bococizumab

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 21, 2013

First Posted

October 24, 2013

Study Start

October 23, 2013

Primary Completion

April 15, 2016

Study Completion

April 15, 2016

Last Updated

June 26, 2017

Results First Posted

May 19, 2017

Record last verified: 2017-05

Locations