NCT02135029

Brief Summary

This study is a multicenter, double blinded, active and placebo controlled randomized clinical trial to demonstrate a superior lipid lowering effect of Bococizumab (PF-04950615; RN316) compared to placebo in subjects who are statin intolerant.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
184

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jun 2014

Geographic Reach
2 countries

40 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 7, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 9, 2014

Completed
23 days until next milestone

Study Start

First participant enrolled

June 1, 2014

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2015

Completed
2.1 years until next milestone

Results Posted

Study results publicly available

December 14, 2017

Completed
Last Updated

December 14, 2017

Status Verified

November 1, 2017

Enrollment Period

1.4 years

First QC Date

May 7, 2014

Results QC Date

October 2, 2017

Last Update Submit

November 17, 2017

Conditions

Keywords

Hyperlipidemiastatin intolerance

Outcome Measures

Primary Outcomes (1)

  • Percent Change From Baseline in Fasting Low Density Lipoprotein Cholesterol (LDL-C) at Week 12

    Baseline, Week 12

Secondary Outcomes (26)

  • Percent Change From Baseline in Fasting Total Cholesterol (TC) at Weeks 12 and 24

    Baseline, Week 12, 24

  • Percent Change From Baseline in Fasting Apolipoprotein B (ApoB) at Weeks 12 and 24

    Baseline, Week 12, 24

  • Percent Change From Baseline in Fasting Non High Density Lipoprotein Cholesterol (Non HDL-C) at Weeks 12 and 24

    Baseline, Week 12, 24

  • Percent Change From Baseline in Fasting Lipoprotein (a) (Lp[a]) at Weeks 12 and 24

    Baseline, Week 12, 24

  • Percent Change From Baseline in Fasting High Density Lipoprotein Cholesterol (HDL-C) at Weeks 12 and 24

    Baseline, Week 12, 24

  • +21 more secondary outcomes

Study Arms (3)

Bococizumab (PF-04950615;RN316)

EXPERIMENTAL

Bococizumab (PF-04950615;RN316)

Drug: Bococizumab (PF-04950615;RN316)

Atorvastatin

ACTIVE COMPARATOR
Drug: Atorvastatin

Placebo

PLACEBO COMPARATOR
Other: Placebo for Bococizumab (PF-04950615;RN316)Other: Placebo for atorvastatin

Interventions

150 mg every 2 weeks by subcutaneous injection for 24 weeks

Bococizumab (PF-04950615;RN316)

Atorvastatin PO QD

Atorvastatin

150 mg every 2 weeks by subcutaneous injection for 24 weeks

Placebo

PO QD

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Hyperlipidemia
  • Statin Intolerant
  • Fasting LDL-C \> = 70 mg/dL Fasting TG \< = 400 mg/dL

You may not qualify if:

  • Pregnant or breastfeeding females
  • Cardiovascular or cerebrovascular event or procedure within 90 days
  • Severe or life-threatening adverse events with past use of statins
  • Poorly controlled hypertension

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (40)

Creekside Endocrine Associates, PC

Denver, Colorado, 80209, United States

Location

Bridgeport Hospital

Bridgeport, Connecticut, 06610, United States

Location

Watson Clinic Center for Research, Inc. (for Drug Shipment only)

Lakeland, Florida, 33805, United States

Location

Cardiovascular Research Center Of South Florida

Miami, Florida, 33173, United States

Location

St. Johns Center for Clinical Research

Ponte Vedra, Florida, 32081, United States

Location

Progressive Medical Research

Port Orange, Florida, 32127, United States

Location

East-West Medical Research Institute

Honolulu, Hawaii, 96814, United States

Location

NorthShore University HealthSystem - Evanston Hospital

Evanston, Illinois, 60201, United States

Location

Health Care Centers of Illinois Mokena Medical Commons

Mokena, Illinois, 60448, United States

Location

Advocate Medical Group Cardiology

Normal, Illinois, 61761, United States

Location

Advocate Medical Group Midwest Heart Specialists

Park Ridge, Illinois, 60068, United States

Location

Prairie Education & Research Cooperative (Administrative)

Springfield, Illinois, 62701, United States

Location

Prairie Heart Institute

Springfield, Illinois, 62701, United States

Location

St. John's Hospital

Springfield, Illinois, 62769, United States

Location

The University of Iowa - College of Public Health - Preventive Intervention Center

Iowa City, Iowa, 52242, United States

Location

The Iowa Clinic, PC

West Des Moines, Iowa, 50266, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Crescent City Clinical Research Center

Metairie, Louisiana, 70006, United States

Location

Allina Health System, dba Abbott Northwestern Hospital

Minneapolis, Minnesota, 55407, United States

Location

Minneapolis Heart Institute Foundation

Minneapolis, Minnesota, 55407, United States

Location

PMG Research of Wilmington, LLC

Wilmington, North Carolina, 28401, United States

Location

Dayton Heart Center

Dayton, Ohio, 45414, United States

Location

Clinical and Translational Research Center, Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, 19104, United States

Location

Berks Cardiologists, Ltd.

Wyomissing, Pennsylvania, 19610, United States

Location

PMG Research of Bristol

Bristol, Tennessee, 37620, United States

Location

PMG Research of Knoxville, LLC

Knoxville, Tennessee, 37912, United States

Location

San Antonio Military Medical Center

Fort Sam Houston, Texas, 78234-6200, United States

Location

Office of Michelle Zaniewski MD., PA.

Houston, Texas, 77090, United States

Location

Utah Cardiology, P.C.

Layton, Utah, 84041, United States

Location

Aspen Clinical Research LLC

Orem, Utah, 84058, United States

Location

The Medical Arts Health Research Group

Kelowna, British Columbia, V1Y 1V6, Canada

Location

Corunna Medical Research Centre

Corunna, Ontario, N0N 1G0, Canada

Location

The Office of Dr. James Cha

Oshawa, Ontario, L1J 2K1, Canada

Location

Kawartha Cardiology Clinical Trials

Peterborough, Ontario, K9J 0B2, Canada

Location

Devonshire Clinical Research Inc.

Woodstock, Ontario, N4S 5P5, Canada

Location

Ecogene-21

Chicoutimi, Quebec, G7H 7K9, Canada

Location

Omnispec clinical research inc.

Mirabel, Quebec, J7J 2K8, Canada

Location

Clinique des maladies lipidiques de Quebec

Québec, Quebec, G1V 4W2, Canada

Location

Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, J1H 1Z1, Canada

Location

Related Publications (2)

  • Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

  • Ridker PM, Tardif JC, Amarenco P, Duggan W, Glynn RJ, Jukema JW, Kastelein JJP, Kim AM, Koenig W, Nissen S, Revkin J, Rose LM, Santos RD, Schwartz PF, Shear CL, Yunis C; SPIRE Investigators. Lipid-Reduction Variability and Antidrug-Antibody Formation with Bococizumab. N Engl J Med. 2017 Apr 20;376(16):1517-1526. doi: 10.1056/NEJMoa1614062. Epub 2017 Mar 17.

Related Links

MeSH Terms

Conditions

Hyperlipidemias

Interventions

bococizumabAtorvastatin

Condition Hierarchy (Ancestors)

DyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeptanoic AcidsFatty AcidsLipids

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 7, 2014

First Posted

May 9, 2014

Study Start

June 1, 2014

Primary Completion

November 1, 2015

Study Completion

November 1, 2015

Last Updated

December 14, 2017

Results First Posted

December 14, 2017

Record last verified: 2017-11

Locations