NCT01955161

Brief Summary

To establish efficacy of idalopirdine as adjunctive therapy to donepezil for symptomatic treatment of patients with mild-to-moderate Alzheimer's disease (AD).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
933

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2013

Typical duration for phase_3

Geographic Reach
16 countries

137 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 27, 2013

Completed
4 days until next milestone

Study Start

First participant enrolled

October 1, 2013

Completed
6 days until next milestone

First Posted

Study publicly available on registry

October 7, 2013

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2016

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

September 19, 2017

Completed
Last Updated

September 19, 2017

Status Verified

August 1, 2017

Enrollment Period

2.8 years

First QC Date

September 27, 2013

Results QC Date

July 11, 2017

Last Update Submit

August 22, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in Cognition

    Change from baseline to Week 24 in Alzheimer's Disease Assessment Scale-cognitive subscale (ADAS-cog) total score. The Alzheimer's Disease Assessment Scale - Cognitive subscale (ADAS-cog) is a 11-item neuropsychological test that assess the severity of cognitive impairment. The items determine the patient's orientation, memory, language, and praxis. Total score of the 11 items range from 0 to 70 (lower score indicates lower cognitive impairment).

    Baseline to Week 24

Secondary Outcomes (10)

  • Change in Daily Functioning

    Baseline to Week 24

  • Change in Global Impression

    Baseline to Week 24

  • Change in Behavioural Disturbance

    Baseline to Week 24

  • Change in Individual Behavioural Disturbance Items

    Baseline to Week 24

  • Change in NPI Anxiety Item Score in Patients With an NPI Anxiety Item Score of at Least 2 at Baseline

    Baseline to Week 24

  • +5 more secondary outcomes

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Placebo adjunct to 10 mg Donepezil

Drug: Placebo

Idalopirdine 30 mg

EXPERIMENTAL

Idalopirdine adjunct to 10 mg Donepezil

Drug: Idalopirdine

Idalopirdine 60 mg

EXPERIMENTAL

Idalopirdine adjunct to 10 mg Donepezil

Drug: Idalopirdine

Interventions

Once daily, matching placebo capsules, orally

Placebo

Once daily, encapsulated tablets, orally

Idalopirdine 30 mgIdalopirdine 60 mg

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • The patient has a knowledgeable and reliable caregiver.
  • The patient is an outpatient.
  • The patient has probable AD.
  • The patient has mild to moderate AD.
  • Stable treatment with donepezil.
  • The patient, if a woman, must have had her last natural menstruation ≥24 months prior to baseline, OR be surgically sterile.
  • The patient, if a man, agrees to protocol-defined use of effective contraception if his female partner is of childbearing potential, OR must have been surgically sterilised prior to the screening visit.

You may not qualify if:

  • The patient has evidence of any clinically significant neurodegenerative disease, or other serious neurological disorders other than AD.
  • The patient has a Diagnostic and Statistical Manual of Mental Disorders, 4th edition, Text Revision (DSM-IV-TR) Axis I disorder other than AD.
  • The patient has evidence of clinically significant disease.
  • The patient's donepezil therapy is likely to be interrupted or discontinued during the study.
  • The patient is currently receiving memantine or has taken memantine within 2 months prior to screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (137)

US027

Birmingham, Alabama, United States

Location

US012

Phoenix, Arizona, United States

Location

US024

Little Rock, Arkansas, United States

Location

US053

Glendale, California, United States

Location

US023

Imperial, California, United States

Location

US015

La Jolla, California, United States

Location

US045

Long Beach, California, United States

Location

US002

Los Angeles, California, United States

Location

US058

San Francisco, California, United States

Location

US018

Santa Ana, California, United States

Location

US060

Denver, Colorado, United States

Location

US042

Boca Raton, Florida, United States

Location

US021

Bradenton, Florida, United States

Location

US050

Brooksville, Florida, United States

Location

US019

Orlando, Florida, United States

Location

US038

Port Charlotte, Florida, United States

Location

US001

West Palm Beach, Florida, United States

Location

US020

Atlanta, Georgia, United States

Location

US048

Kailua, Hawaii, United States

Location

US030

Chicago, Illinois, United States

Location

US051

Joliet, Illinois, United States

Location

US040

Indianapolis, Indiana, United States

Location

US036

Freeport, Maine, United States

Location

US032

Newton, Massachusetts, United States

Location

US035

Kalamazoo, Michigan, United States

Location

US041

Flowood, Mississippi, United States

Location

US054

St Louis, Missouri, United States

Location

US046

Princeton, New Jersey, United States

Location

US028

Toms River, New Jersey, United States

Location

US044

Toms River, New Jersey, United States

Location

US049

Albany, New York, United States

Location

US010

Amherst, New York, United States

Location

US014

Manhasset, New York, United States

Location

US008

New York, New York, United States

Location

US029

New York, New York, United States

Location

US056

New York, New York, United States

Location

US037

Orangeburg, New York, United States

Location

US043

Staten Island, New York, United States

Location

US007

Centerville, Ohio, United States

Location

US006

Columbus, Ohio, United States

Location

US052

Edmond, Oklahoma, United States

Location

US026

Portland, Oregon, United States

Location

US057

Jenkintown, Pennsylvania, United States

Location

US047

Arlington, Virginia, United States

Location

US025

Madison, Wisconsin, United States

Location

US004

Milwaukee, Wisconsin, United States

Location

AR002

Buenos Aires, Argentina

Location

AR003

Buenos Aires, Argentina

Location

AR006

Buenos Aires, Argentina

Location

AR007

Buenos Aires, Argentina

Location

AR009

Córdoba, Argentina

Location

AR004

Mar del Plata, Argentina

Location

AR005

Mendoza, Argentina

Location

AR008

Mendoza, Argentina

Location

AR010

Rosario, Argentina

Location

BE003

Bruges, Belgium

Location

BE002

Brussels, Belgium

Location

BE004

Brussels, Belgium

Location

BE005

Leuven, Belgium

Location

BE001

Roeselare, Belgium

Location

BE006

Thuin, Belgium

Location

BG005

Plovdiv, Bulgaria

Location

BG001

Sofia, Bulgaria

Location

BG002

Sofia, Bulgaria

Location

BG003

Sofia, Bulgaria

Location

BG004

Sofia, Bulgaria

Location

BG006

Sofia, Bulgaria

Location

BG007

Varna, Bulgaria

Location

CA002

Gatineau, Canada

Location

CA006

London, Canada

Location

CA008

Newmarket, Canada

Location

CA001

Toronto, Canada

Location

CA004

Toronto, Canada

Location

CL004

Antofagasta, Chile

Location

CL002

Santiago, Chile

Location

CL003

Santiago, Chile

Location

CL005

Santiago, Chile

Location

CL001

Valdivia, Chile

Location

CZ006

Brno, Czechia

Location

CZ007

Kutná Hora, Czechia

Location

CZ004

Pardubice, Czechia

Location

CZ001

Prague, Czechia

Location

CZ002

Prague, Czechia

Location

CZ003

Prague, Czechia

Location

CZ005

Rychnov nad Kněžnou, Czechia

Location

DK003

Aarhus N, Denmark

Location

DK001

Copenhagen, Denmark

Location

DK002

Odense C, Denmark

Location

FR006

Besançon, France

Location

FR008

Limoges Cedex1, France

Location

FR003

Nantes, France

Location

FR001

Paris, France

Location

FR005

Paris, France

Location

FR004

Saint-Etienne, France

Location

FR002

Toulouse, France

Location

DE002

Berlin, Germany

Location

DE006

Ellwangen, Germany

Location

DE010

Günzburg, Germany

Location

DE005

Hanover, Germany

Location

DE007

Heidelberg, Germany

Location

DE009

München, Germany

Location

DE008

Ulm, Germany

Location

DE004

Unterhaching, Germany

Location

IT004

Ancona, Italy

Location

IT006

Brescia, Italy

Location

IT002

Florence, Italy

Location

IT005

Genoa, Italy

Location

IT003

Lamezia Terme, Italy

Location

IT001

Milan, Italy

Location

IT007

Palermo, Italy

Location

PL004

Gliwice, Poland

Location

PL007

Katowice, Poland

Location

PL005

Poznan, Poland

Location

PL006

Sopot, Poland

Location

PL002

Szczecin, Poland

Location

PL003

Warsaw, Poland

Location

PL008

Wroclaw, Poland

Location

RO002

Bucharest, Romania

Location

RO001

Târgu Mureş, Romania

Location

ZA003

Bloemfontein, South Africa

Location

ZA006

Cape Town, South Africa

Location

ZA007

Cape Town, South Africa

Location

ZA004

George, South Africa

Location

ZA005

Port Elizabeth, South Africa

Location

ZA001

Pretoria, South Africa

Location

ZA002

Rosebank, South Africa

Location

ES002

Alicante, Spain

Location

ES006

Barcelona, Spain

Location

ES001

Donostia / San Sebastian, Spain

Location

ES005

Manresa, Spain

Location

ES004

Salamanca, Spain

Location

ES003

Santiago de Compostela, Spain

Location

UA008

Dnipropetrovsk, Ukraine

Location

UA006

Kherson,Vil. Stepanivka, Ukraine

Location

UA005

Kyiv, Ukraine

Location

UA007

Kyiv, Ukraine

Location

UA001

Lviv, Ukraine

Location

Related Publications (3)

  • Ballard C, Atri A, Boneva N, Cummings JL, Frolich L, Molinuevo JL, Tariot PN, Raket LL. Enrichment factors for clinical trials in mild-to-moderate Alzheimer's disease. Alzheimers Dement (N Y). 2019 May 20;5:164-174. doi: 10.1016/j.trci.2019.04.001. eCollection 2019.

  • Cummings JL, Atri A, Ballard C, Boneva N, Frolich L, Molinuevo JL, Raket LL, Tariot PN. Insights into globalization: comparison of patient characteristics and disease progression among geographic regions in a multinational Alzheimer's disease clinical program. Alzheimers Res Ther. 2018 Nov 24;10(1):116. doi: 10.1186/s13195-018-0443-2.

  • Atri A, Frolich L, Ballard C, Tariot PN, Molinuevo JL, Boneva N, Windfeld K, Raket LL, Cummings JL. Effect of Idalopirdine as Adjunct to Cholinesterase Inhibitors on Change in Cognition in Patients With Alzheimer Disease: Three Randomized Clinical Trials. JAMA. 2018 Jan 9;319(2):130-142. doi: 10.1001/jama.2017.20373.

MeSH Terms

Conditions

Alzheimer Disease

Interventions

(2-(6-fluoro-1H-indol-3-yl)-ethyl)-(3-(2,2,3,3-tetrafluoropropoxy)benzyl)amine

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Results Point of Contact

Title
Email contact via
Organization
H. Lundbeck A/S

Study Officials

  • Email contact via H. Lundbeck A/S

    LundbeckClinicalTrials@lundbeck.com

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 27, 2013

First Posted

October 7, 2013

Study Start

October 1, 2013

Primary Completion

July 1, 2016

Study Completion

July 1, 2016

Last Updated

September 19, 2017

Results First Posted

September 19, 2017

Record last verified: 2017-08

Locations