NCT02006641

Brief Summary

To establish efficacy of Idalopirdine as adjunctive therapy to donepezil for symptomatic treatment of patients with mild-to-moderate Alzheimer's disease (AD).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
858

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Feb 2014

Typical duration for phase_3

Geographic Reach
19 countries

162 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 5, 2013

Completed
5 days until next milestone

First Posted

Study publicly available on registry

December 10, 2013

Completed
2 months until next milestone

Study Start

First participant enrolled

February 1, 2014

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2016

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

February 20, 2018

Completed
Last Updated

February 20, 2018

Status Verified

January 1, 2018

Enrollment Period

2.8 years

First QC Date

December 5, 2013

Results QC Date

December 19, 2017

Last Update Submit

January 23, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in Cognition

    Change from baseline to Week 24 in Alzheimer's Disease Assessment Scale-cognitive subscale (ADAS-cog) total score. The Alzheimer's Disease Assessment Scale - Cognitive subscale (ADAS-cog) is a 11-item neuropsychological test that assess the severity of cognitive impairment. The items determine the patient's orientation, memory, language, and praxis. Total score of the 11 items range from 0 to 70 (lower score indicates lower cognitive impairment).

    Baseline and Week 24

Secondary Outcomes (10)

  • Change in Daily Functioning

    Baseline and Week 24

  • Change in Global Impression

    Baseline and Week 24

  • Change in Behavioural Disturbance

    Baseline and Week 24

  • Change in Individual Behavioural Disturbance Items

    Baseline and Week 24

  • Change in NPI Anxiety Item Score in Patients With an NPI Anxiety Item Score of at Least 2 at Baseline

    Baseline and Week 24

  • +5 more secondary outcomes

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Placebo adjunct to 10 mg Donepezil

Drug: Placebo

Idalopirdine 10 mg

EXPERIMENTAL

Idalopirdine adjunct to 10 mg Donepezil

Drug: Idalopirdine

Idalopirdine 30 mg

EXPERIMENTAL

Idalopirdine adjunct to 10 mg Donepezil

Drug: Idalopirdine

Interventions

Once daily, matching placebo capsules, orally

Placebo

Once daily, encapsulated tablets, orally

Also known as: Lu AE58054
Idalopirdine 10 mgIdalopirdine 30 mg

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • The patient has a knowledgeable and reliable caregiver.
  • The patient is an outpatient.
  • The patient has probable AD.
  • The patient has mild to moderate AD.
  • Stable treatment with donepezil.
  • The patient, if a woman, must have had her last natural menstruation ≥24 months prior to baseline, OR be surgically sterile.
  • The patient, if a man, agrees to protocol-defined use of effective contraception if his female partner is of childbearing potential, OR must have been surgically sterilised prior to the screening visit.

You may not qualify if:

  • The patient has evidence of any clinically significant neurodegenerative disease, or other serious neurological disorders other than AD.
  • The patient has a Diagnostic and Statistical Manual of Mental Disorders, 4th edition, Text Revision (DSM-IV-TR) Axis I disorder other than AD.
  • The patient has evidence of clinically significant disease.
  • The patient's donepezil therapy is likely to be interrupted or discontinued during the study.
  • The patient is currently receiving memantine or has taken memantine within 2 months prior to screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (162)

US338

Phoenix, Arizona, United States

Location

US342

Fayetteville, Arkansas, United States

Location

US322

Anaheim, California, United States

Location

US305

Carson, California, United States

Location

US346

Costa Mesa, California, United States

Location

US327

Fullerton, California, United States

Location

US315

Lomita, California, United States

Location

US351

Oceanside, California, United States

Location

US307

Redlands, California, United States

Location

US301

Santa Rosa, California, United States

Location

US337

New London, Connecticut, United States

Location

US332

Stamford, Connecticut, United States

Location

US308

Delray Beach, Florida, United States

Location

US320

Hallandale, Florida, United States

Location

US347

Hialeah, Florida, United States

Location

US340

Lake Worth, Florida, United States

Location

US303

Miami, Florida, United States

Location

US313

Miami, Florida, United States

Location

US335

Naples, Florida, United States

Location

US345

Orange City, Florida, United States

Location

US309

Palm Beach Gardens, Florida, United States

Location

US302

Sunrise, Florida, United States

Location

US304

Atlanta, Georgia, United States

Location

US360

Augusta, Georgia, United States

Location

US318

Decatur, Georgia, United States

Location

US334

Lake Charles, Louisiana, United States

Location

US350

Belmont, Massachusetts, United States

Location

US344

Boston, Massachusetts, United States

Location

US310

Saint Paul, Minnesota, United States

Location

US321

Hattiesburg, Mississippi, United States

Location

US330

Creve Coeur, Missouri, United States

Location

US339

Paterson, New Jersey, United States

Location

US312

Staten Island, New York, United States

Location

US316

Charlotte, North Carolina, United States

Location

US336

Winston-Salem, North Carolina, United States

Location

US323

Cincinnati, Ohio, United States

Location

US349

Cleveland, Ohio, United States

Location

US306

Columbus, Ohio, United States

Location

US352

Lakewood, Ohio, United States

Location

US333

Oklahoma City, Oklahoma, United States

Location

US314

Allentown, Pennsylvania, United States

Location

US324

Pittsburgh, Pennsylvania, United States

Location

US341

Pittsburgh, Pennsylvania, United States

Location

US325

Reading, Pennsylvania, United States

Location

US319

Port Royal, South Carolina, United States

Location

US356

Cordova, Tennessee, United States

Location

US343

Fort Worth, Texas, United States

Location

US354

Houston, Texas, United States

Location

AR303

Banfield, Argentina

Location

AR312

Buenos Aires, Argentina

Location

AR301

Ciudad Autonoma Buenos Aires, Argentina

Location

AR304

Ciudad Autonoma Buenos Aires, Argentina

Location

AR308

Ciudad Autonoma Buenos Aires, Argentina

Location

AR311

Ciudad Autonoma Buenos Aires, Argentina

Location

AR313

Ciudad Autonoma Buenos Aires, Argentina

Location

AR314

Ciudad Autonoma Buenos Aires, Argentina

Location

AR315

Ciudad Autonoma Buenos Aires, Argentina

Location

AR307

Córdoba, Argentina

Location

AR309

Córdoba, Argentina

Location

AR305

Godoy Cruz, Argentina

Location

AR310

Mendoza, Argentina

Location

AR302

Santa Fe, Argentina

Location

AR306

Santiago del Estero, Argentina

Location

BR307

Curitiba, Brazil

Location

BR309

Curitiba, Brazil

Location

BR301

Rio de Janeiro, Brazil

Location

BR306

Rio de Janeiro, Brazil

Location

BR308

São Paulo, Brazil

Location

CA301

Halifax, Canada

Location

CA302

Kelowna, Canada

Location

CA306

Montreal, Canada

Location

CA304

Qubec, Canada

Location

CA303

Sherbrooke, Canada

Location

CA305

Toronto, Canada

Location

HR304

Zabok, Croatia

Location

HR301

Zagreb, Croatia

Location

HR302

Zagreb, Croatia

Location

HR303

Zagreb, Croatia

Location

CZ305

Brno, Czechia

Location

CZ306

Choceň, Czechia

Location

CZ309

Choceň, Czechia

Location

CZ308

Pardubice, Czechia

Location

CZ301

Prague, Czechia

Location

CZ303

Prague, Czechia

Location

CZ304

Prague, Czechia

Location

CZ307

Prague, Czechia

Location

CZ310

Praha 10 - Strasnice, Czechia

Location

CZ302

Rychnov nad Kněžnou, Czechia

Location

EE301

Tallinn, Estonia

Location

EE303

Tallinn, Estonia

Location

EE302

Tartu, Estonia

Location

FI302

Kuopio, Finland

Location

FI303

Oulu, Finland

Location

FI301

Turku, Finland

Location

FR301

Bordeaux, France

Location

FR308

Bron, France

Location

FR307

Colmar, France

Location

FR304

Dijon, France

Location

FR309

Élancourt, France

Location

FR302

Marseille, France

Location

FR303

Nice, France

Location

FR306

Reims, France

Location

FR305

Rouen, France

Location

HU304

Budapest, Hungary

Location

HU305

Budapest, Hungary

Location

HU301

Esztergom, Hungary

Location

HU303

Győr, Hungary

Location

HU302

Szeged, Hungary

Location

IE301

Cork, Ireland

Location

IL302

Haifa, Israel

Location

IL303

Holon, Israel

Location

IL304

Ramat Gan, Israel

Location

IT306

Brescia, Italy

Location

IT309

Brescia, Italy

Location

IT311

Genova, Italy

Location

IT312

Monza, Italy

Location

IT302

Naples, Italy

Location

IT313

Palermo, Italy

Location

IT307

Perugia, Italy

Location

IT301

Pisa, Italy

Location

IT305

Roma, Italy

Location

IT308

Roma, Italy

Location

IT304

Torino, Italy

Location

IT310

Torrette, Italy

Location

LT302

Kaunas, Lithuania

Location

LT303

Kaunas, Lithuania

Location

LT301

Vilnius, Lithuania

Location

LT304

Vilnius, Lithuania

Location

PL301

Bialystok, Poland

Location

PL304

Bydgoszcz, Poland

Location

PL308

Gdynia, Poland

Location

PL309

Krakow, Poland

Location

PL302

Lodz, Poland

Location

PL310

Lubin, Poland

Location

PL306

Lublin, Poland

Location

PL307

Oświęcim, Poland

Location

PL303

Poznan, Poland

Location

PT301

Amadora, Portugal

Location

PT302

Coimbra, Portugal

Location

KR303

Busan, South Korea

Location

KR301

Incheon, South Korea

Location

KR308

Seongnam-si, South Korea

Location

KR302

Seoul, South Korea

Location

KR304

Seoul, South Korea

Location

KR305

Seoul, South Korea

Location

KR306

Seoul, South Korea

Location

KR307

Seoul, South Korea

Location

KR309

Seoul, South Korea

Location

TW301

Kaohsiung City, Taiwan

Location

TW302

Kaohsiung City, Taiwan

Location

TW303

Taichung, Taiwan

Location

TW304

Taipei, Taiwan

Location

TW305

Taipei, Taiwan

Location

GB307

Amersham, United Kingdom

Location

GB301

Glasgow, United Kingdom

Location

GB303

London, United Kingdom

Location

GB308

London, United Kingdom

Location

GB306

Plymouth, United Kingdom

Location

GB305

Preston, United Kingdom

Location

GB304

Southampton, United Kingdom

Location

GB302

Swindon, United Kingdom

Location

GB309

Warrington, United Kingdom

Location

Related Publications (3)

  • Ballard C, Atri A, Boneva N, Cummings JL, Frolich L, Molinuevo JL, Tariot PN, Raket LL. Enrichment factors for clinical trials in mild-to-moderate Alzheimer's disease. Alzheimers Dement (N Y). 2019 May 20;5:164-174. doi: 10.1016/j.trci.2019.04.001. eCollection 2019.

  • Cummings JL, Atri A, Ballard C, Boneva N, Frolich L, Molinuevo JL, Raket LL, Tariot PN. Insights into globalization: comparison of patient characteristics and disease progression among geographic regions in a multinational Alzheimer's disease clinical program. Alzheimers Res Ther. 2018 Nov 24;10(1):116. doi: 10.1186/s13195-018-0443-2.

  • Atri A, Frolich L, Ballard C, Tariot PN, Molinuevo JL, Boneva N, Windfeld K, Raket LL, Cummings JL. Effect of Idalopirdine as Adjunct to Cholinesterase Inhibitors on Change in Cognition in Patients With Alzheimer Disease: Three Randomized Clinical Trials. JAMA. 2018 Jan 9;319(2):130-142. doi: 10.1001/jama.2017.20373.

MeSH Terms

Conditions

Alzheimer Disease

Interventions

(2-(6-fluoro-1H-indol-3-yl)-ethyl)-(3-(2,2,3,3-tetrafluoropropoxy)benzyl)amine

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Results Point of Contact

Title
Email contact via
Organization
H. Lundbeck A/S

Study Officials

  • Email contact via H. Lundbeck A/S

    LundbeckClinicalTrials@lundbeck.com

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 5, 2013

First Posted

December 10, 2013

Study Start

February 1, 2014

Primary Completion

December 1, 2016

Study Completion

December 1, 2016

Last Updated

February 20, 2018

Results First Posted

February 20, 2018

Record last verified: 2018-01

Locations