NCT01920867

Brief Summary

This study will evaluate the use of autologous bone marrow derived stem cells (BMSC) for the treatment of retinal and optic nerve damage or disease. http://mdstemcells.com/scots-ii/

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
300

participants targeted

Target at P75+ for not_applicable

Timeline
Completed

Started Aug 2012

Longer than P75 for not_applicable

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2012

Completed
1 year until next milestone

First Submitted

Initial submission to the registry

August 8, 2013

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 12, 2013

Completed
6.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2020

Completed
Last Updated

October 23, 2019

Status Verified

October 1, 2019

Enrollment Period

7.9 years

First QC Date

August 8, 2013

Last Update Submit

October 21, 2019

Conditions

Keywords

Stem CellsBone Marrow Derived Stem CellsBMSCBMC (Bone Marrow Cell)Mesenchymal Stem CellsMSCEye DiseaseEye Stem CellsOphthalmologyOphthalmic DiseaseRetinaRetinal DiseaseMacular DegenerationAge Related Macular DegenerationMyopic Macular DegenerationGeographic AtrophyDry Macular DegenerationWet Macular DegenerationRetinal AtrophyRetinal DystrophyHereditary Retinal DystrophyRetinitis PigmentosaStargardt DiseaseCone DystrophyCone Rod DystrophyMaculopathyOptic Nerve DiseaseOptic Nerve AtrophyOptic AtrophyIschemic Optic NeuropathyOptic Nerve DamageOptic Nerve CompressionCompressive Optic NeuropathyDevics Syndrome

Outcome Measures

Primary Outcomes (1)

  • Visual acuity

    Best corrected visual acuity will be measured with Snellen Eye Chart and the ETDRS (Early Treatment Diabetic Retinopathy Study)Eye Chart when available at each post- procedure visit. Intervals at minimum will be first post- procedure day,then 3 months, 6 months and 12 months post-procedure day. Recommended visit 1 month post -procedure day.

    1 day to 12 months

Secondary Outcomes (1)

  • Visual fields

    1 day to 12 months

Study Arms (3)

RB, ST, IV

ACTIVE COMPARATOR

Injections of BMSC retrobulbar (RB), subtenon (ST) and intravenous (IV)

Procedure: RB (Retrobulbar)Procedure: ST (Subtenon)Procedure: IV (Intravenous)

RB, ST, IV, IVIT

ACTIVE COMPARATOR

Injections of BMSC retrobulbar, subtenon, intravenous and intravitreal ( IVIT )

Procedure: RB (Retrobulbar)Procedure: ST (Subtenon)Procedure: IV (Intravenous)Procedure: IVIT (Intravitreal)

RB, ST, IV, IO

ACTIVE COMPARATOR

Injection of BMSC retrobulbar, subtenon, intravenous and intraocular (IO) with vitrectomy

Procedure: RB (Retrobulbar)Procedure: ST (Subtenon)Procedure: IV (Intravenous)Procedure: IO (Intraocular)

Interventions

Retrobulbar injection of Bone Marrow Derived Stem Cells (BMSC)

Also known as: Retrobulbar injection of stem cells
RB, ST, IVRB, ST, IV, IORB, ST, IV, IVIT
ST (Subtenon)PROCEDURE

Subtenon injection of Bone Marrow Derived Stem Cells (BMSC)

Also known as: Subtenon injection of stem cells
RB, ST, IVRB, ST, IV, IORB, ST, IV, IVIT

Intravenous injection of Bone Marrow Derived Stem Cells (BMSC)

Also known as: Intravenous injection of stem cells
RB, ST, IVRB, ST, IV, IORB, ST, IV, IVIT

Intravitreal injection of Bone Marrow Derived Stem Cells (BMSC)

Also known as: Intravitreal injection of stem cells
RB, ST, IV, IVIT

Intraocular injection of Bone Marrow Derived Stem Cells (BMSC) with vitrectomy prior to intraocular injection. For example, may include larger amount of stem cells in the intravitreal cavity, intraneuronal injections or subretinal injections of stem cells.

Also known as: Intraocular injection of stem cells with vitrectomy
RB, ST, IV, IO

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have objective, documented damage to the retina or optic nerve unlikely to improve OR
  • Have objective, documented damage to the retina or optic nerve that is progressive
  • AND have less than or equal to 20/40 best corrected central visual acuity in one or both eyes AND/OR an abnormal visual field in one or both eyes.
  • Be at least 3 months post-surgical treatment intended to treat any ophthalmologic disease and stable.
  • If under current medical therapy ( pharmacologic treatment) for a retinal or optic nerve disease be considered stable on that treatment and unlikely to have visual function improvement ( for example, glaucoma with intraocular pressure stable on topical medications but visual field damage ).
  • Have the potential for improvement with BMSC treatment and be at minimal risk of any potential harm from the procedure.
  • Be over the age of 18
  • Be medically stable and able to be medically cleared by their primary care physician or a licensed primary care practitioner for the procedure. Medical clearance means that in the estimation of the primary care practitioner, the patient can reasonably be expected to undergo the procedure without significant medical risk to health.

You may not qualify if:

  • Patients who are not capable of an adequate ophthalmologic examination or evaluation to document the pathology.
  • Patients who are not capable or not willing to undergo follow up eye exams with the principle investigator or their ophthalmologist or optometrist as outlined in the protocol.
  • Patients who are not capable of providing informed consent.
  • Patients who may be at significant risk to general health or to the eyes and visual function should they undergo the procedure.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

MD Stem Cells

Westport, Connecticut, 06880, United States

Location

Related Publications (5)

  • Weiss JN, Levy S, Malkin A. Stem Cell Ophthalmology Treatment Study (SCOTS) for retinal and optic nerve diseases: a preliminary report. Neural Regen Res. 2015 Jun;10(6):982-8. doi: 10.4103/1673-5374.158365.

  • Weiss JN, Levy S, Benes SC. Stem Cell Ophthalmology Treatment Study (SCOTS) for retinal and optic nerve diseases: a case report of improvement in relapsing auto-immune optic neuropathy. Neural Regen Res. 2015 Sep;10(9):1507-15. doi: 10.4103/1673-5374.165525.

  • Weiss JN, Benes SC, Levy S. Stem Cell Ophthalmology Treatment Study (SCOTS): improvement in serpiginous choroidopathy following autologous bone marrow derived stem cell treatment. Neural Regen Res. 2016 Sep;11(9):1512-1516. doi: 10.4103/1673-5374.191229.

  • Kasetty MA, Hedges TR 3rd, Witkin AJ. BILATERAL EPIRETINAL MEMBRANE FORMATION AFTER INTRAVITREAL INJECTIONS OF AUTOLOGOUS MESENCHYMAL STEM CELLS. Retin Cases Brief Rep. 2022 Sep 1;16(5):561-564. doi: 10.1097/ICB.0000000000001032.

  • Weiss JN, Levy S, Benes SC. Stem Cell Ophthalmology Treatment Study (SCOTS): bone marrow-derived stem cells in the treatment of Leber's hereditary optic neuropathy. Neural Regen Res. 2016 Oct;11(10):1685-1694. doi: 10.4103/1673-5374.193251.

Related Links

MeSH Terms

Conditions

Retinal DiseasesMacular DegenerationOptic Nerve DiseasesGlaucomaEye DiseasesGeographic AtrophyWet Macular DegenerationRetinal DystrophiesRetinitis PigmentosaStargardt DiseaseCone DystrophyCone-Rod DystrophiesOptic AtrophyOptic Neuropathy, IschemicOptic Nerve InjuriesNeuromyelitis Optica

Interventions

Immunoglobulins, IntravenousJupiterVitrectomy

Condition Hierarchy (Ancestors)

Retinal DegenerationCranial Nerve DiseasesNervous System DiseasesOcular HypertensionEye Diseases, HereditaryGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesVascular DiseasesCardiovascular DiseasesCranial Nerve InjuriesCraniocerebral TraumaTrauma, Nervous SystemWounds and InjuriesMyelitis, TransverseDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemOptic NeuritisDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Immunoglobulin GImmunoglobulin IsotypesAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsPlanetsSolar SystemAstronomical ObjectsAstronomical PhenomenaPhysical PhenomenaOphthalmologic Surgical ProceduresSurgical Procedures, Operative

Study Officials

  • Steven Levy, MD

    MD Stem Cells

    STUDY DIRECTOR
  • Jeffrey Weiss, MD

    MD Stem Cells

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 8, 2013

First Posted

August 12, 2013

Study Start

August 1, 2012

Primary Completion

July 1, 2020

Study Completion

July 1, 2020

Last Updated

October 23, 2019

Record last verified: 2019-10

Data Sharing

IPD Sharing
Will not share

Locations