NCT01875003

Brief Summary

This randomized, multicenter, double-blind, placebo-controlled, parallel-group study will evaluate the efficacy, safety, and tolerability of lebrikizumab in adolescent participants with asthma whose disease remains uncontrolled despite daily treatment with inhaled corticosteroids (ICS) therapy and at least one second controller medication. Participants will be randomized in a 1:1:1 ratio to receive double-blind treatment with either lebrikizumab ('High' or 'Low') or placebo, administered as subcutaneous (SC) every 4 weeks (Q4W) for 52 weeks, in addition to their standard-of-care therapy. This will be followed by an optional 52-week double-blind active-treatment extension. The anticipated time on study treatment is up to 104 weeks. Participants who complete the study to Week 104, discontinue prematurely or decide not to take part in the optional active-treatment extension will transition to the 20-week safety follow-up period.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
348

participants targeted

Target at P50-P75 for phase_3 asthma

Timeline
Completed

Started Aug 2013

Longer than P75 for phase_3 asthma

Geographic Reach
23 countries

165 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 7, 2013

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 11, 2013

Completed
3 months until next milestone

Study Start

First participant enrolled

August 31, 2013

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 28, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 28, 2016

Completed
Last Updated

May 16, 2017

Status Verified

May 1, 2017

Enrollment Period

3.3 years

First QC Date

June 7, 2013

Last Update Submit

May 15, 2017

Conditions

Outcome Measures

Primary Outcomes (3)

  • Rate of Asthma Exacerbations During the 52-Week Placebo-Controlled Period

    Baseline up to Week 52

  • Percentage of Participants With Adverse Events (AEs) or Serious AEs

    Baseline up to Week 124

  • Percentage of Participants With Anti-Therapeutic Antibodies to Lebrikizumab

    Baseline up to Week 124 (assessed at Baseline, Weeks 4, 12, 24, 36, 52, 76, 104, 112, and 124 or at early termination [up to 108 weeks])

Secondary Outcomes (7)

  • Change from Baseline in Pre-Bronchodilator Forced Expiratory Volume in 1 second (FEV1) at Week 52

    Baseline , Week 52

  • Time to First Asthma Exacerbation

    Baseline up to 52 weeks

  • Change From Baseline in Fractional Exhaled Nitric Oxide (FeNO) at Week 52

    Baseline , Week 52

  • Change From Baseline in Standardized Asthma Quality of Life Questionnaire for 12 years and Older (AQLQ + 12) at Week 52

    Baseline, Week 52

  • Change From Baseline in Asthma Rescue Medication Use at Week 52

    Baseline, Week 52

  • +2 more secondary outcomes

Study Arms (3)

Lebrikizumab High

EXPERIMENTAL

Participants with uncontrolled asthma on ICS therapy (total daily dose of 500-2000 micrograms \[mcg\] of fluticasone propionate dry powder inhaler \[DPI\] or equivalent) and a second controller medication, will receive SC injection of lebrikizumab (high dose) Q4W for 52 weeks during placebo-controlled period and up to 76 weeks or 104 weeks for participants who will be willing to take part in optional active-treatment extension period.

Drug: LebrikizumabDrug: Standard of Care

Lebrikizumab Low

EXPERIMENTAL

Participants with uncontrolled asthma on ICS therapy (total daily dose of 500-2000 mcg of fluticasone propionate DPI or equivalent) and a second controller medication, will receive SC injection of lebrikizumab (low dose) Q4W for 52 weeks during placebo-controlled period and up to 76 weeks or 104 weeks for participants who will be willing to take part in optional active-treatment extension period.

Drug: LebrikizumabDrug: Standard of Care

Placebo

PLACEBO COMPARATOR

Participants with uncontrolled asthma on ICS therapy (total daily dose of 500-2000 mcg of fluticasone propionate DPI or equivalent) and a second controller medication, will receive SC injection of lebrikizumab matching placebo Q4W for 52 weeks during placebo-controlled period and then SC injection of lebrikizumab at high or low dose will be administered from Weeks 52 to 76 or 104 to participants who are willing to take part in optional active-treatment extension period.

Drug: LebrikizumabDrug: PlaceboDrug: Standard of Care

Interventions

Lebrikizumab will be administered as SC injection at high or low dose Q4W.

Lebrikizumab HighLebrikizumab LowPlacebo

Lebrikizumab matching placebo will be administered as SC injection Q4W.

Placebo

Participants will continue to receive ICS therapy (total daily dose of 500-2000 mcg fluticasone propionate DPI or equivalent) along with at least one second controller medications (e.g. long-acting beta agonists \[LABAs\], leukotriene receptor antagonists (LTRAs), long-acting muscarinic antagonists (LAMAs), or theophylline) as standard of care.

Lebrikizumab HighLebrikizumab LowPlacebo

Eligibility Criteria

Age12 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Asthma diagnosis for greater than or equal to (\>/=) 12 months prior to Visit 1
  • Bronchodilator response during screening
  • Pre-bronchodilator FEV1 of 40 percent (%) - 90% predicted at both Visits 2 and 3
  • On high dose ICS therapy for \>/= 6 months prior to Visit 1
  • On an eligible second controller medication for 6 months prior to Visit 1
  • Uncontrolled asthma as defined by the protocol both during screening and at the time of randomization
  • Demonstrated adherence with controller medication during the screening period

You may not qualify if:

  • History of severe allergic reaction or anaphylactic reaction to a biologic agent or known hypersensitivity to any component of the lebrikizumab injection
  • Maintenance oral corticosteroid therapy within 3 months prior to Visit 1
  • Treatment with systemic (oral, intravenous \[IV\], or intramuscular \[IM\]) corticosteroids within 4 weeks prior to Visit 1 or during the screening period
  • Treatment with intra-articular corticosteroids within 4 weeks prior to Visit 1 or during the screening period or anticipated need for intra-articular corticosteroids during the course of the study
  • Infection that meets the following criteria: Any infection requiring hospital admission or requiring treatment with IV or IM antibiotics within 4 weeks prior to Visit 1 or during screening; any active infection that required treatment with oral antibiotics within 2 weeks prior to Visit 1 or during screening; upper or lower respiratory tract infection within 4 weeks prior to Visit 1 or during screening; active parasitic infection or Listeria monocytogenes infection within 6 months prior to Visit 1 or during screening
  • History of active tuberculosis requiring treatment
  • Known immunodeficiency, including, but not limited to, human immunodeficiency virus (HIV) infection
  • Evidence of acute or chronic hepatitis or known liver cirrhosis
  • History of cystic fibrosis, bronchiectasis, and/or other clinically significant lung disease other than asthma
  • Diagnosis or history of malignancy or current evaluation for potential malignancy
  • Current smoker or former smoker with a history of greater than (\>) 10 pack-years
  • History of alcohol or drug abuse
  • Past and/or current use of any anti- interleukin (IL) -13 or anti-IL-4/IL-13 therapy, including lebrikizumab
  • Use of other monoclonal antibody therapy, including omalizumab, within 6 months or 5 drug half-lives (whichever is longer) prior to Visit 1
  • Initiation of or change in allergen immunotherapy within 3 months prior to Visit 1 or during screening
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (165)

Allergy Associates of Tucson

Tucson, Arizona, 85716, United States

Location

Kaiser Permanente Los Angeles

Los Angeles, California, 90027, United States

Location

Southern California Research Center

Mission Viejo, California, 92691, United States

Location

Allergy & Asthma Consultants

Redwood City, California, 94063, United States

Location

Dignity Health Medical Foundation

Sacramento, California, 95823, United States

Location

Bensch Research Associates

Stockton, California, 95207, United States

Location

Allergy & Asthma Medical Group; Clinical Research Division

Walnut Creek, California, 94598, United States

Location

Colorado Children's Hospital; The Breathing Institute

Aurora, Colorado, 80045, United States

Location

IMMUNOe International Research Centers

Centennial, Colorado, 80112, United States

Location

Asthma & Allergy; Associates, P.C.

Colorado Springs, Colorado, 80907, United States

Location

National Jewish Medical and Research Center

Denver, Colorado, 80206, United States

Location

Abel and Buchheim

Miami, Florida, 33165, United States

Location

Compass Research East, LLC

Orlando, Florida, 32806, United States

Location

Sarasota Clinical Research

Sarasota, Florida, 34239, United States

Location

University of South Florida

Tampa, Florida, 33613, United States

Location

Brookstone Clinical Res Ctr

Columbus, Georgia, 31904, United States

Location

Georgia Pain Clinic

Marietta, Georgia, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

The Clinical Research Center

Shiloh, Illinois, 62269, United States

Location

Riley Hospital for Children; Pediatric Nephrology

Indianapolis, Indiana, 46202, United States

Location

Abraham Research PLLC

Florence, Kentucky, 41042, United States

Location

Breathe America Shreveport Inc

Shreveport, Louisiana, 71106, United States

Location

Asthma, Allergy & Sinus Center

Baltimore, Maryland, 21236, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02115, United States

Location

Univ of Michigan Medical Ctr

Ann Arbor, Michigan, 48109-0718, United States

Location

Cardinal Glennon Child's Hosp; Endrocrinology

St Louis, Missouri, 63104-1095, United States

Location

Parikh Institute for Research LLC

New Jersey, New Jersey, 08904, United States

Location

University of New Mexico; School of Med

Albuquerque, New Mexico, 87131, United States

Location

Parikh Institute for Research LLC

New York, New York, United States

Location

Urban Health Plan, Inc.

The Bronx, New York, 10459, United States

Location

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Promedica Toledo Children's Hospital

Toledo, Ohio, 43606, United States

Location

Bend Memorial Clinic

Bend, Oregon, 97701, United States

Location

Allergy, Asthma, & Dermatology Research Center, Llc

Lake Oswego, Oregon, 97035, United States

Location

Clinical Research Inst. of Southern Oregon, Pc

Medford, Oregon, 97504, United States

Location

TTS Research

Boerne, Texas, 78006, United States

Location

Allergy & Asthma Research Center of El Paso

El Paso, Texas, 79925, United States

Location

Allergy & Asthma Res Ctr PA

San Antonio, Texas, 78251, United States

Location

South Texas Allergy and Asthma Medical Professionals

San Antonio, Texas, 78251, United States

Location

Bridgerland Clinical Research

North Logan, Utah, 84341, United States

Location

O & O Alpan, LLC

Fairfax, Virginia, 22030, United States

Location

Bellingham Asthma, Allergy & Immunology

Bellingham, Washington, 98225, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Centro Médico Vitae

Buenos Aires, B6500BWQ, Argentina

Location

Fundación Faicep

Buenos Aires, C1122AAK, Argentina

Location

Fundacion Cidea

Buenos Aires, C1125 ABE, Argentina

Location

INAER

Buenos Aires, C1425BEN, Argentina

Location

Instituto Respirar

Mendoza, 5500, Argentina

Location

INSARES

Mendoza, Mendoza City, M5500CCG, Argentina

Location

Centro Respiratorio Infantil

Rosario, 2000, Argentina

Location

Investigaciones en Patologias Respiratorias

San Miguel de Tucumán, 4000, Argentina

Location

Centro Integral de Medicina Respiratoria (CIMER)

San Miguel de Tucumán, T4000CHE, Argentina

Location

Instituto Del Buen Aire

Santa Fe, 3000, Argentina

Location

Sanatorio Británico de Rosario

Santa Fé, Argentina

Location

CEMER Centro Médico de Enfermedades Respiratorias

Vicente López, B1602DQD, Argentina

Location

Centro de Referencia em Enfermidades Respiratorias e Alergia - CEAR

Salvador, Estado de Bahia, 41940-455, Brazil

Location

Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, 90020-090, Brazil

Location

Hospital Sao Lucas - PUCRS

Porto Alegre, Rio Grande do Sul, 90610-000, Brazil

Location

Faculdade de Medicina do ABC - FMABC

Santo André, São Paulo, 09060-650, Brazil

Location

Pesquisare Saúde Sociedade Simples

Santo André, São Paulo, 09080-000, Brazil

Location

Hospital Alemao Oswaldo Cruz; Pesquisa Clinica

São Paulo, São Paulo, 01323-020, Brazil

Location

Instituto de Pesquisa Clínica e Medicina Avançada Ltda

São Paulo, São Paulo, 05437-010, Brazil

Location

CMPC/Clinica de Alergia Martti Antila

Sorocaba, São Paulo, 18040-425, Brazil

Location

Dr. Tharwat A. Fera Inc.

Vancouver, British Columbia, V5Z 4E1, Canada

Location

Brian Lyttle's Private Practice

London, Ontario, N6A 5B8, Canada

Location

Centre de Recherche Applique En Allergie de Quebec

Québec, Quebec, G1V 4M6, Canada

Location

Hospital Santa Clara

Bogotá, Colombia

Location

Hospital Pablo Tobon Uribe

Medellin-Antioquia, Colombia

Location

Hofstetr Alois MUDr. s.r.o.

Jihlava, 586 01, Czechia

Location

Alergologie Teplice, s.r.o.

Teplice, 415 01, Czechia

Location

Groupe Hospitalier Pellegrin; Pharmacie

Bordeaux, 33076, France

Location

Groupe Hospitalier Necker Enfants Malades

Paris, 75015, France

Location

Hopital Armand Trousseau

Paris, 75571, France

Location

Hopital Charles Nicolle; cic

Rouen, 76031, France

Location

Universitaetsklinikum Frankfurt

Frankfurt, 60528, Germany

Location

Evangelisches Krankenhaus Hamm

Hamm, 59063, Germany

Location

Praxis Dr. med. Jan Feimer

München, 80539, Germany

Location

Semmelweis Egyetem

Budapest, 1083, Hungary

Location

Heim Pál Gyermekkórház

Budapest, 1089, Hungary

Location

Kenezy Korhaz Rendelointezet

Debrecen, 4031, Hungary

Location

Borsod-Abaúj-Zemplén Megyei Kórház és Egyetemi Oktató Kórház

Miskolc, 3526, Hungary

Location

Szegedi Tudományegyetem Szent-Györgyi Albert Klinikai Központ

Szeged, 6720, Hungary

Location

Papp és Társa Bt.

Szigetvár, 7900, Hungary

Location

Tudogyogyintezet Torokbalint

Törökbálint, 2045, Hungary

Location

Barzilai Medical Center

Ashkelon, 78278, Israel

Location

Rambam Health Care Campus

Haifa, 31096, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 91031, Israel

Location

Schneider Children's Medical Center

Petah Tikva, 49100, Israel

Location

Chaim Sheba Medical Center

Tel Litwinsky, 52661, Israel

Location

Azienda Policlinico Umberto I; Dipartimento Integrato di Pediatria e Neuropsichiatria Infantile

Rome, Lazio, 00161, Italy

Location

Ospedale Pediatrico Bambino Gesu

Rome, Lazio, 00165, Italy

Location

Fondazione IRCCS Policlinico San Matteo

Pavia, Lombardy, 27100, Italy

Location

Azienda Ospedaliero - Universitaria Policlinico - Vittorio Emanuele

Catania, Sicily, 95123, Italy

Location

National Hospital Organization Mie Hospital

Tsu, 514-0125, Japan

Location

National Hospital Organization Shimoshizu National Hospital

Yotsukaidō, 284-0003, Japan

Location

Grupo Medico Camino

DF, 03310, Mexico

Location

Instituto Jalisciense de Investigacion Clinica S.A. de C.V.

Guadalajara, 44100, Mexico

Location

Centro de Investigacion Medico Biologico y Terapia Avanzada, S.C.

Guadalajara, 44130, Mexico

Location

Unidad Medica de Occidente

Guadalajara, 44220, Mexico

Location

Instituto Nacional de Pediatría

Mexico City, 04530, Mexico

Location

Hospital Universitario Dr. Jose Eleuterio González; Enfermedades Pulmonares Crónicas

Monterrey, 64460, Mexico

Location

Unidad de Investigacion Clinica En Medicina (Udicem) S.C.

Monterrey, 64718, Mexico

Location

Consultorio Especialidad Alergologia Pediatrica

Villahermosa, 86035, Mexico

Location

Hospital Dos de Mayo; Parque Historia De la Medicina Peruana S/n

Lima, Lima 01, Peru

Location

Hospital Nacional Luis N Saenz PNP

Lima, Lima 11, Peru

Location

Clinica Internacional

Lima, Lima 1, Peru

Location

Centro de Investigación Ricardo Palma

Lima, LIMA 27, Peru

Location

Clinica Anglo Americana

Lima, Lima 27, Peru

Location

Clinica San Borja

Lima, Lima 41, Peru

Location

Prywatna Praktyka Lekarska

Bialystok, 15-430, Poland

Location

Malopolskie Centrum Alergologii

Krakow, 31-624, Poland

Location

SPZOZ Uniwersytecki Szpital Kliniczny nr 1 im. Norberta Barlickiego Uniwersytetu Medycznego w Lodzi

Lodz, 90-153, Poland

Location

Wojewodzki Szpital Specjalistyczny im. M. Kopernika w Lodzi

Lodz, 93-513, Poland

Location

Centrum Alergologii NZOZ

Lublin, 20-552, Poland

Location

Centrum Alergologii Teresa Hofman

Poznan, 60-214, Poland

Location

ALERGO-MED Specjalistyczna Przychodnia Lekarska Sp. z o. o

Tarnów, 33-100, Poland

Location

Klinika Chorób Wewnetrznych i Alergologii MSW

Warsaw, 02-507, Poland

Location

Hospital Infante D. Pedro; Servico de Imunoalergologia

Aveiro, 3814-501, Portugal

Location

Hospital Particular do Algarve - Unidade de Faro

Faro, 8005-226, Portugal

Location

Hospital Dona Estefania; Servico de Imunoalergologia

Lisbon, 1169-045, Portugal

Location

Hospital CUF Porto; Servico de Imunoalergologia

Senhora Da Hora - Porto, 4460-188, Portugal

Location

Alersa

Košice, 040 11, Slovakia

Location

ALERGOMEA s.r.o.

Lučenec, 984 01, Slovakia

Location

Imunoalergologia Dzurilla s.r.o.

Nitra, 949 01, Slovakia

Location

Uni of Cape Town Lung Inst.

Cape Town, 7925, South Africa

Location

Westville Hospital

Durban, 3630, South Africa

Location

Sebastian Peter

Durban, 4001, South Africa

Location

WWCT Lakeview Hospital

Johannesburg, 1501, South Africa

Location

Medicross Sophiatown

Johannesburg, 2113, South Africa

Location

GCT Mercantile; Clinical Research Centre

Port Elizabeth, 6014, South Africa

Location

Bothe ke Bontle Health Services

Pretoria, 0101, South Africa

Location

Soweto Clinical Trial Centre

Soweto, 1818, South Africa

Location

Limpopo Clinical Research Initiative; Tamboti Medical Centre

Tabazimbi, 0380, South Africa

Location

Inha University Hospital

Incheon, 22332, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

KyungHee Medical Center

Seoul, 130-702, South Korea

Location

Hospital Universitario Germans Trias i Pujol; Servicio de Farmacia

Badalona, Barcelona, 08916, Spain

Location

Hospital Sant Joan De Deu

Esplugues de Llobregas, Barcelona, 08950, Spain

Location

Corporacio Sanitaria Parc Tauli; Servicio de Oncologia

Sabadell, Barcelona, 08208, Spain

Location

Hospital de Manises

Manises, Valencia, 46940, Spain

Location

Hospital Quiron Teknon

Barcelona, 08017, Spain

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

Clínica Dr. Lobatón

Cadiz, 11008, Spain

Location

Clinica Ojeda de Asma Y Alergia

Madrid, 28006, Spain

Location

Hospital Regional Universitario Carlos Haya

Málaga, 29010, Spain

Location

Chung Shan M. U. H.

Taichung, 402, Taiwan

Location

China Medical University Hospital

Taichung, 40447, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 407, Taiwan

Location

National Cheng Kung Univ Hosp

Tainan, 00704, Taiwan

Location

Chang Gung Memorial Hospital

Taoyuan District, 333, Taiwan

Location

Municipal Medical Institution; Chernivtsi Regional Children's Hospital

Chernivtsi, 58023, Ukraine

Location

Public Institution City Clinical Hospital # 6 of Dnipropetrovsk Regional Board

Dnipro, 49000, Ukraine

Location

State Institution of Pediatrics Obstetrics and Gynecology of NAMSU

Kiev, 04050, Ukraine

Location

Municipal Institution "Kryvyi Rih City Clinical Hospital #8" of Dnipropetrovsk Regional Council

Kryvyi Rih, 50082, Ukraine

Location

SI National Institute of Phthisiology and Pulmonology n.a. F.G.Yanovskyi under NAMS of Ukraine

Kyiv, 03680, Ukraine

Location

SI Research Centre of Radiation Medicine of AMSU

Kyiv, 3115, Ukraine

Location

Municipal Institution Zaporizhzhya Regional Clinical Child Hospital

Zaporizhzhya, 69063, Ukraine

Location

Birmingham Children's Hospital NHS Foundation Trust

Birmingham, B4 6NH, United Kingdom

Location

Birmingham Heartlands Hospital

Birmingham, B9 5SS, United Kingdom

Location

Dumfries and Galloway Royal Infirmary; Department of Paediatrics

Dumfries, DG1 4AP, United Kingdom

Location

Royal Hospital For Children

Glasgow, G51 4TF, United Kingdom

Location

University of Leicester

Leicester, LE1 7RH, United Kingdom

Location

Royal Brompton Hospital; Respiratory Department

London, SW3 6NP, United Kingdom

Location

Sheffield Childrens Hospital

Sheffield, S102TH, United Kingdom

Location

Southampton General Hospital

Southampton, SO16 6YD, United Kingdom

Location

Related Publications (1)

  • Szefler SJ, Roberts G, Rubin AS, Zielen S, Kuna P, Alpan O, Anzures-Cabrera J, Chen Q, Holweg CTJ, Kaminski J, Putnam WS, Matthews JG, Kamath N. Efficacy, safety, and tolerability of lebrikizumab in adolescent patients with uncontrolled asthma (ACOUSTICS). Clin Transl Allergy. 2022 Jul 14;12(7):e12176. doi: 10.1002/clt2.12176. eCollection 2022 Jul.

MeSH Terms

Conditions

Asthma

Interventions

lebrikizumabStandard of Care

Condition Hierarchy (Ancestors)

Bronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesRespiratory HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Intervention Hierarchy (Ancestors)

Quality Indicators, Health CareQuality of Health CareHealth Services AdministrationHealth Care Quality, Access, and Evaluation

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 7, 2013

First Posted

June 11, 2013

Study Start

August 31, 2013

Primary Completion

December 28, 2016

Study Completion

December 28, 2016

Last Updated

May 16, 2017

Record last verified: 2017-05

Locations