NCT01768286

Brief Summary

This study is to evaluate the safety, tolerability, and antiviral efficacy of ledipasvir/sofosbuvir fixed dose combination (FDC) with or without ribavirin (RBV) administered for 12 or 24 weeks in treatment-experienced subjects with chronic genotype 1 hepatitis C virus (HCV) infection.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
441

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jan 2013

Shorter than P25 for phase_3

Geographic Reach
1 country

53 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2013

Completed
9 days until next milestone

First Submitted

Initial submission to the registry

January 10, 2013

Completed
5 days until next milestone

First Posted

Study publicly available on registry

January 15, 2013

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2013

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2014

Completed
10 months until next milestone

Results Posted

Study results publicly available

November 26, 2014

Completed
Last Updated

November 16, 2018

Status Verified

November 1, 2014

Enrollment Period

10 months

First QC Date

January 10, 2013

Results QC Date

November 21, 2014

Last Update Submit

October 19, 2018

Conditions

Keywords

HCV genotype 1 (GT-1)HCVSustained Virologic ResponseDirect Acting AntiviralCombination TherapyGS-7977GS-5885RibavirinOpen LabelSofosbuvirAdditional relevant MeSH terms:HepatitisHepatitis, ChronicHepatitis CHepatitis C, ChronicLiver DiseasesDigestive System DiseasesHepatitis, Viral, HumanVirus DiseasesEnterovirus InfectionsPicornaviridae InfectionsRNA Virus InfectionsFlaviviridae InfectionsAntiviral AgentsAnti-Infective AgentsTherapeutic UsesPharmacologic ActionsAntimetabolitesMolecular Mechanisms of Pharmacological Action

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants With Sustained Virologic Response (SVR) 12 Weeks After Discontinuation of Therapy (SVR12)

    SVR12 was defined as HCV RNA \< the lower limit of quantitation (LLOQ; ie, 25 IU/mL) 12 weeks following the last dose of study drug.

    Posttreatment Week 12

  • Incidence of Adverse Events Leading to Permanent Discontinuation From Any Study Drug

    The percentage of participants who experienced an adverse event leading to permanent discontinuation from any study drug was summarized.

    Up to 24 weeks

Secondary Outcomes (12)

  • Percentage of Participants With SVR at 4 and 24 Weeks After Discontinuation of Therapy (SVR4 and SVR24)

    Posttreatment Weeks 4 and 24

  • Percentage of Participants With HCV RNA < LLOQ at Week 1

    Week 1

  • Percentage of Participants With HCV RNA < LLOQ at Week 2

    Week 2

  • Percentage of Participants With HCV RNA < LLOQ at Week 4

    Week 4

  • Percentage of Participants With HCV RNA < LLOQ at Week 8

    Week 8

  • +7 more secondary outcomes

Study Arms (4)

LDV/SOF 12 Weeks

EXPERIMENTAL

Participants will receive LDV/SOF FDC for 12 weeks.

Drug: LDV/SOF

LDV/SOF+RBV 12 Weeks

EXPERIMENTAL

Participants will receive LDV/SOF FDC plus RBV for 12 weeks.

Drug: LDV/SOFDrug: RBV

LDV/SOF 24 Weeks

EXPERIMENTAL

Participants will receive LDV/SOF FDC for 24 weeks.

Drug: LDV/SOF

LDV/SOF+RBV 24 Weeks

EXPERIMENTAL

Participants will receive LDV/SOF FDC plus RBV for 24 weeks.

Drug: LDV/SOFDrug: RBV

Interventions

Ledipasvir (LDV) 90 mg/sofosbuvir (SOF) 400 mg fixed-dose combination (FDC) tablet administered orally once daily

Also known as: Harvoni®, GS-5885/GS-7997
LDV/SOF 12 WeeksLDV/SOF 24 WeeksLDV/SOF+RBV 12 WeeksLDV/SOF+RBV 24 Weeks
RBVDRUG

Ribavirin (RBV) tablets administered orally in a divided daily dose according to package insert weight-based dosing recommendations (\< 75 kg = 1000 mg and ≥ 75 kg = 1200 mg)

LDV/SOF+RBV 12 WeeksLDV/SOF+RBV 24 Weeks

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age \> 18, with chronic genotype 1 HCV infection
  • HCV treatment-experienced, including patients who have previously failed a nonstructural protein (NS)3/4A protease inhibitor plus pegylated interferon (PEG)/RBV regimen
  • HCV RNA \> 10,000 IU/mL at screening
  • Cirrhosis determination; a liver biopsy may be required
  • Screening laboratory values within defined thresholds
  • Use of two effective contraception methods if female of childbearing potential or sexually active male

You may not qualify if:

  • Pregnant or nursing female or male with pregnant female partner
  • Coinfection with HIV or hepatitis B virus
  • Current or prior history of clinical hepatic decompensation
  • Hepatocellular carcinoma or other malignancy (with exception of certain resolved skin cancers)
  • Chronic use of systemic immunosuppressive agents
  • History of clinically significant illness or any other medical disorder that may interfere with subject treatment, assessment or compliance with the protocol

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (53)

Unknown Facility

Phoenix, Arizona, United States

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Tucson, Arizona, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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Palo Alto, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Englewood, Colorado, United States

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Washington D.C., District of Columbia, United States

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Gainesville, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Atlanta, Georgia, United States

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Marietta, Georgia, United States

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Chicago, Illinois, United States

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Indianapolis, Indiana, United States

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Bowling Green, Kentucky, United States

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Baton Rouge, Louisiana, United States

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Baltimore, Maryland, United States

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Lutherville, Maryland, United States

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Boston, Massachusetts, United States

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Springfield, Massachusetts, United States

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Detroit, Michigan, United States

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Rochester, Minnesota, United States

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Saint Louis, Minnesota, United States

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Saint Paul, Minnesota, United States

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Kansas City, Missouri, United States

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Berlin, New Jersey, United States

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Hillsborough, New Jersey, United States

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Albuquerque, New Mexico, United States

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Santa Fe, New Mexico, United States

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Binghamton, New York, United States

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Manhasset, New York, United States

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New York, New York, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Fayetteville, North Carolina, United States

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Statesville, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Philadelphia, Pennsylvania, United States

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Providence, Rhode Island, United States

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Germantown, Tennessee, United States

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Nashville, Tennessee, United States

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Arlington, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Fairfax, Virginia, United States

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Newport News, Virginia, United States

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Norfolk, Virginia, United States

Location

Related Publications (2)

  • Grebely J, Mauss S, Brown A, Bronowicki JP, Puoti M, Wyles D, Natha M, Zhu Y, Yang J, Kreter B, Brainard DM, Yun C, Carr V, Dore GJ. Efficacy and Safety of Ledipasvir/Sofosbuvir With and Without Ribavirin in Patients With Chronic HCV Genotype 1 Infection Receiving Opioid Substitution Therapy: Analysis of Phase 3 ION Trials. Clin Infect Dis. 2016 Dec 1;63(11):1405-1411. doi: 10.1093/cid/ciw580. Epub 2016 Aug 23.

  • Afdhal N, Reddy KR, Nelson DR, Lawitz E, Gordon SC, Schiff E, Nahass R, Ghalib R, Gitlin N, Herring R, Lalezari J, Younes ZH, Pockros PJ, Di Bisceglie AM, Arora S, Subramanian GM, Zhu Y, Dvory-Sobol H, Yang JC, Pang PS, Symonds WT, McHutchison JG, Muir AJ, Sulkowski M, Kwo P; ION-2 Investigators. Ledipasvir and sofosbuvir for previously treated HCV genotype 1 infection. N Engl J Med. 2014 Apr 17;370(16):1483-93. doi: 10.1056/NEJMoa1316366. Epub 2014 Apr 11.

MeSH Terms

Conditions

Hepatitis C, ChronicHepatitisHepatitis, ChronicHepatitis CLiver DiseasesDigestive System DiseasesHepatitis, Viral, HumanVirus DiseasesEnterovirus InfectionsPicornaviridae InfectionsRNA Virus InfectionsFlaviviridae Infections

Interventions

ledipasvir, sofosbuvir drug combination

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences, Inc.

Study Officials

  • Jenny Yang, PharmD

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 10, 2013

First Posted

January 15, 2013

Study Start

January 1, 2013

Primary Completion

November 1, 2013

Study Completion

February 1, 2014

Last Updated

November 16, 2018

Results First Posted

November 26, 2014

Record last verified: 2014-11

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations