NCT01701401

Brief Summary

The purpose of this study is to evaluate the safety, tolerability, and antiviral efficacy of ledipasvir (LDV)/sofosbuvir (SOF) fixed-dose combination (FDC) tablets with or without ribavirin (RBV) administered for 12 and 24 weeks in treatment-naive subjects with chronic genotype 1 HCV infection.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
870

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Sep 2012

Geographic Reach
7 countries

88 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2012

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

October 2, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

October 5, 2012

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2014

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2014

Completed
12 months until next milestone

Results Posted

Study results publicly available

March 27, 2015

Completed
Last Updated

November 16, 2018

Status Verified

March 1, 2015

Enrollment Period

1.5 years

First QC Date

October 2, 2012

Results QC Date

March 17, 2015

Last Update Submit

October 19, 2018

Conditions

Keywords

HCV genotype 1 (GT-1)HCVSustained Virologic ResponseDirect Acting AntiviralCombination TherapyGS-7977GS-5885RibavirinOpen LabelSofosbuvirAdditional relevant MeSH terms:HepatitisHepatitis, ChronicHepatitis CHepatitis C, ChronicLiver DiseasesDigestive System DiseasesHepatitis, Viral, HumanVirus DiseasesEnterovirus InfectionsPicornaviridae InfectionsRNA Virus InfectionsFlaviviridae InfectionsAntiviral AgentsAnti-Infective AgentsTherapeutic UsesPharmacologic ActionsAntimetabolitesMolecular Mechanisms of Pharmacological Action

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants With Sustained Virologic Response (SVR) 12 Weeks After Discontinuation of Study Drug (SVR12)

    SVR12 was defined as HCV RNA level \< the lower limit of quantification (LLOQ, ie, \< 25 copies/mL) 12 weeks after last dose of study drug.

    Posttreatment Week 12

  • Incidence of Adverse Events Leading to Permanent Discontinuation From Any Study Drug

    The percentage of participants who experienced an adverse event leading to permanent discontinuation from any study drug was summarized.

    Up to 24 weeks

Secondary Outcomes (8)

  • Percentage of Participants With SVR at 4 and 24 Weeks After Discontinuation of Study Drug

    Posttreatment Weeks 4 and 24

  • Percentage of Participants With HCV RNA < LLOQ at Week 2

    Week 2

  • Percentage of Participants With HCV RNA < LLOQ at Week 4

    Week 4

  • Percentage of Participants With HCV RNA < LLOQ at Week 8

    Week 8

  • Change From Baseline in HCV RNA at Week 2

    Baseline; Week 2

  • +3 more secondary outcomes

Study Arms (4)

LDV/SOF 12 weeks

EXPERIMENTAL

LDV/SOF administered for 12 weeks

Drug: LDV/SOF

LDV/SOF+RBV 12 weeks

EXPERIMENTAL

LDV/SOF+RBV administered for 12 weeks.

Drug: LDV/SOFDrug: RBV

LDV/SOF 24 weeks

EXPERIMENTAL

LDV/SOF administered for 24 weeks

Drug: LDV/SOF

LDV/SOF+RBV 24 weeks

EXPERIMENTAL

LDV/SOF+RBV administered for 24 weeks.

Drug: LDV/SOFDrug: RBV

Interventions

LDV/SOF 90/400 mg FDC tablet administered orally once daily

Also known as: Harvoni®, GS-5885/GS-7977
LDV/SOF 12 weeksLDV/SOF 24 weeksLDV/SOF+RBV 12 weeksLDV/SOF+RBV 24 weeks
RBVDRUG

RBV tablets administered orally in a divided daily dose according to package insert weight-based dosing recommendations (\< 75 kg = 1000 mg and ≥ 75 kg = 1200 mg)

LDV/SOF+RBV 12 weeksLDV/SOF+RBV 24 weeks

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 18, with chronic genotype 1 HCV infection
  • HCV treatment-naive
  • HCV RNA \> 10,000 IU/mL at screening
  • Cirrhosis determination; a liver biopsy may be required
  • Screening laboratory values within defined thresholds
  • Use of two effective contraception methods if female of childbearing potential or sexually active male

You may not qualify if:

  • Pregnant or nursing female or male with pregnant female partner
  • Co-infection with HIV or hepatitis B virus (HBV)
  • Current or prior history of clinical hepatic decompensation
  • Hepatocellular carcinoma (HCC) or other malignancy (with exception of certain resolved skin cancers)
  • Chronic use of systemic immunosuppressive agents
  • History of clinically significant illness or any other medical disorder that may interfere with subject treatment, assessment or compliance with the protocol

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

Unknown Facility

Birmingham, Alabama, United States

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La Jolla, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Palo Alto, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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Aurora, Colorado, United States

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Englewood, Colorado, United States

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Washington D.C., District of Columbia, United States

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Gainesville, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Tampa, Florida, United States

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Wellington, Florida, United States

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Atlanta, Georgia, United States

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Decatur, Georgia, United States

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Marietta, Georgia, United States

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Chicago, Illinois, United States

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Indianapolis, Indiana, United States

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Baltimore, Maryland, United States

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Lutherville, Maryland, United States

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Boston, Massachusetts, United States

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Detroit, Michigan, United States

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Rochester, Minnesota, United States

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Saint Paul, Minnesota, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Hillsborough, New Jersey, United States

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Albuquerque, New Mexico, United States

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Santa Fe, New Mexico, United States

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Manhasset, New York, United States

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New York, New York, United States

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The Bronx, New York, United States

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Asheville, North Carolina, United States

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Chapel Hill, North Carolina, United States

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Durham, North Carolina, United States

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Fayetteville, North Carolina, United States

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Statesville, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cincinnati, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Germantown, Tennessee, United States

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Nashville, Tennessee, United States

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Arlington, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Fairfax, Virginia, United States

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Falls Church, Virginia, United States

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Norfolk, Virginia, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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CHRU Lille, France

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Clichy, France

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Créteil, France

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La Tronche, France

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Lyon, France

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Marseille, France

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Nice, France

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Paris, France

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Berlin, Germany

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Cologne, Germany

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Düsseldorf, Germany

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Essen, Germany

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Frankfurt, Germany

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Freiburg im Breisgau, Germany

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Hamburg, Germany

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Hanover, Germany

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Mainz, Germany

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Bologna, Italy

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Brescia, Italy

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Milan, Italy

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Padua, Italy

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Palermo, Italy

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Roma, Italy

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San Giovanni Rotondo, Italy

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Torino, Italy

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San Juan, Puerto Rico

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Barcelona, Spain

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Madrid, Spain

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Málaga, Spain

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Santander, Spain

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Seville, Spain

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Birmingham, Wstmid, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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Plymouth, United Kingdom

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Related Publications (3)

  • Grebely J, Mauss S, Brown A, Bronowicki JP, Puoti M, Wyles D, Natha M, Zhu Y, Yang J, Kreter B, Brainard DM, Yun C, Carr V, Dore GJ. Efficacy and Safety of Ledipasvir/Sofosbuvir With and Without Ribavirin in Patients With Chronic HCV Genotype 1 Infection Receiving Opioid Substitution Therapy: Analysis of Phase 3 ION Trials. Clin Infect Dis. 2016 Dec 1;63(11):1405-1411. doi: 10.1093/cid/ciw580. Epub 2016 Aug 23.

  • Younossi ZM, Elsheikh E, Stepanova M, Gerber L, Nader F, Stamm LM, Brainard DM, McHutchinson JG. Ledipasvir/sofosbuvir treatment of hepatitis C virus is associated with reduction in serum apolipoprotein levels. J Viral Hepat. 2015 Dec;22(12):977-82. doi: 10.1111/jvh.12448. Epub 2015 Aug 17.

  • Afdhal N, Zeuzem S, Kwo P, Chojkier M, Gitlin N, Puoti M, Romero-Gomez M, Zarski JP, Agarwal K, Buggisch P, Foster GR, Brau N, Buti M, Jacobson IM, Subramanian GM, Ding X, Mo H, Yang JC, Pang PS, Symonds WT, McHutchison JG, Muir AJ, Mangia A, Marcellin P; ION-1 Investigators. Ledipasvir and sofosbuvir for untreated HCV genotype 1 infection. N Engl J Med. 2014 May 15;370(20):1889-98. doi: 10.1056/NEJMoa1402454. Epub 2014 Apr 11.

MeSH Terms

Conditions

Hepatitis C, ChronicHepatitisHepatitis, ChronicHepatitis CLiver DiseasesDigestive System DiseasesHepatitis, Viral, HumanVirus DiseasesEnterovirus InfectionsPicornaviridae InfectionsRNA Virus InfectionsFlaviviridae Infections

Interventions

ledipasvir, sofosbuvir drug combination

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences, Inc.

Study Officials

  • Jenny Yang, Pharm D

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 2, 2012

First Posted

October 5, 2012

Study Start

September 1, 2012

Primary Completion

March 1, 2014

Study Completion

April 1, 2014

Last Updated

November 16, 2018

Results First Posted

March 27, 2015

Record last verified: 2015-03

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations