NCT01740336

Brief Summary

This multicenter, randomized, single-blind, placebo-controlled, two arm study will evaluate the efficacy and safety of paclitaxel with GDC-0941 versus paclitaxel with placebo in participants with locally recurrent or metastatic breast cancer.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
183

participants targeted

Target at P75+ for phase_2 breast-cancer

Timeline
Completed

Started Feb 2013

Geographic Reach
7 countries

84 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 30, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

December 4, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

February 6, 2013

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 20, 2015

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 10, 2015

Completed
Last Updated

April 24, 2017

Status Verified

April 1, 2017

Enrollment Period

2.7 years

First QC Date

November 30, 2012

Last Update Submit

April 21, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival (PFS) Assessed as per Modified Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1 (v1.1)

    From the time of randomization until disease progression or death from any cause (up to approximately 3 years)

Secondary Outcomes (6)

  • Percentage of Participants With Adverse Events

    From randomization up to approximately 3 years

  • Percentage of Participants With Objective Tumor Response Assessed as per Modified RECIST v1.1

    From first observation of an objective tumor response until disease progression (up to approximately 3 years)

  • Percentage of Participants Acheiving Clinical Benefit (Partial Response, Complete Response or Stable Disease Lasting for at Least 6 Months) Assessed as per Modified RECIST v1.1

    From randomization until disease progression (up to approximately 3 years)

  • Duration of Confirmed Objective Response Assessed as per Modified RECIST v1.1

    From first observation of an objective tumor response until disease progression (up to approximately 3 years)

  • Population Pharmacokinetics (PK) for GDC-0941

    Day 8 of Cycle 1 and Day 1 of Cycle 6 (cycle length=28 days)

  • +1 more secondary outcomes

Study Arms (2)

A: Paclitaxel, GDC-0941

EXPERIMENTAL

Participants will receive GDC-091 260 milligrams (mg) orally in repeated rounds of once daily (QD) dosing for 5 consecutive days followed by 2 consecutive days during which GDC-0941 will not be administered (5/7-day schedule). This 5/7-day schedule will be repeated weekly in each 28-day cycle until disease progression or intolerable toxicity. Participants will receive 90 milligrams per square meter (mg/m\^2) intravenously (IV) weekly for 3 out of 4 weeks in every 28-day cycle.

Drug: GDC-0941Drug: Paclitaxel

B: Paclitaxel, Placebo

PLACEBO COMPARATOR

Participants will receive placebo matching to GDC-0941 on the 5/7-day schedule along with 90 mg/m\^2 IV weekly for 3 out of 4 weeks in every 28-day cycle.

Drug: PlaceboDrug: Paclitaxel

Interventions

GDC-0941 will be administered QD orally for 5 consecutive days each week.

A: Paclitaxel, GDC-0941

Placebo matching to GDC-0941

B: Paclitaxel, Placebo

Paclitaxel will be administered IV weekly for 3 out of 4 weeks in every 28-day cycle.

A: Paclitaxel, GDC-0941B: Paclitaxel, Placebo

Eligibility Criteria

Age18 Years+
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the breast, with measurable or non-measurable locally recurrent or metastatic disease
  • Human epidermal growth factor receptor 2 (HER2)-negative and hormone receptor (HR) (estrogen receptor and/or progesterone receptor)-positive disease as defined by local guidelines
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
  • Adequate hematologic and end organ function
  • Women of childbearing potential must agree to remain abstinent or to use two adequate methods of contraception, including at least one method with a failure rate of less than (\<) 1 percent (%) per year, during the treatment period and for at least 30 days after the last dose of study treatment or 6 months after discontinuation of paclitaxel, whichever is longer

You may not qualify if:

  • Prior non-capecitabine chemotherapy for locally recurrent or metastatic disease
  • Prior treatment with a phosphoinositide 3-kinase (PI3K) inhibitor for advanced or metastatic breast cancer
  • History of intolerance to a taxane-containing therapy
  • History of clinically significant cardiac or pulmonary dysfunction
  • History of malabsorption syndrome or other condition that would interfere with enteral absorption
  • Clinically significant history of liver disease
  • Active autoimmune disease or active inflammatory disease
  • Immunocompromised status due to current known active infection with human immunodeficiency virus (HIV) or due to the use of immunosuppressive therapies for other conditions
  • Need for current chronic corticosteroid therapy
  • Pregnant, lactating, or breastfeeding women
  • Current severe, uncontrolled systemic disease
  • Known untreated or active central nervous system (CNS) metastases

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (97)

Arizona Oncology Associates, PC - NAHOA

Sedona, Arizona, 86336, United States

Location

Pacific Cancer Medical Center

Anaheim, California, 92801, United States

Location

California Cancer Associates for Research & Excellence, Inc.

Encinitas, California, 92008, United States

Location

Kaiser Permanente - Hayward

Hayward, California, 94545, United States

Location

Kaiser Permanente - Oakland

Oakland, California, 94611, United States

Location

Bay Area Cancer Research Group, LLC

Pleasant Hill, California, 94523, United States

Location

Kaiser Permanente Medical Center - Roseville

Roseville, California, 95661, United States

Location

Kaiser Permanente Sacramento Medical Center

Sacramento, California, 95825, United States

Location

Kaiser Permanente - San Francisco (2238 Geary)

San Francisco, California, 94115, United States

Location

University of California at San Francisco

San Francisco, California, 94115, United States

Location

Kaiser Permanente - San Jose

San Jose, California, 95119, United States

Location

Kaiser Permanente - Santa Clara

Santa Clara, California, 95051, United States

Location

Kaiser Permanente - South San Francisco

South San Francisco, California, 94080, United States

Location

Kaiser Permanente - Vallejo

Vallejo, California, 94589, United States

Location

Kaiser Permanente - Walnut Creek

Walnut Creek, California, 94596, United States

Location

Helen & Harry Gray Cancer Center-Hartford Hospital-CCD PRIME; Research

Hartford, Connecticut, 06102-5037, United States

Location

Clinical Research of South Florida

Coral Gables, Florida, 33134, United States

Location

Cancer Specialists of North Florida

Orange Park, Florida, 32073, United States

Location

Hematology - Oncology Associates of Treasure Coast

Port Saint Lucie, Florida, 34952, United States

Location

Phoebe Putney Memorial Hospital

Albany, Georgia, 31701, United States

Location

Joliet Oncology-Hematology; Associates, Ltd.

Joliet, Illinois, 60435, United States

Location

Oncology Specialists, S.C.

Park Ridge, Illinois, 60068, United States

Location

Illinois Cancer Care

Peoria, Illinois, 61615, United States

Location

Cotton-O'Neil Clinical Research Center, Hematology and Oncology; Cotton O'Neil Cancer Center

Topeka, Kansas, 66606, United States

Location

Hematology Oncology Clinic

Baton Rouge, Louisiana, 70808, United States

Location

Metairie Oncologist, LLC

Metairie, Louisiana, 70006, United States

Location

Maine Research Associates

Auburn, Maine, 04210, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Beth Israel Deaconess Med Ctr

Brookline, Massachusetts, 02445, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Billings Clinic Cancer Center-CCD PRIME

Billings, Missouri, Montana, United States

Location

Nebraska Cancer Specialists; Oncology Hematology West, PC

Omaha, Nebraska, 68130, United States

Location

ProHEALTH Care Associates LLP

Lake Success, New York, 11042, United States

Location

Summa Health System

Akron, Ohio, 44304, United States

Location

Aultman Hospital; Aultman Hospital Cancer Center

Canton, Ohio, 44710, United States

Location

TriHealth Oncology Institute

Cincinnati, Ohio, 45247, United States

Location

Abington Memorial Hospital

Abington, Pennsylvania, 19001, United States

Location

Hematology and Oncology Associates of Sc

Greenville, South Carolina, 29615, United States

Location

Shivers Cancer Center at University Medical Center Brackenridge

Austin, Texas, 78701, United States

Location

Texas Oncology

Bedford, Texas, 76022, United States

Location

Texas Oncology, P.A. - El Paso; West

El Paso, Texas, 79902, United States

Location

Texas Oncology - Memorial City

Houston, Texas, 77024, United States

Location

Texas Oncology, P.A. ;Sherman Cancer Center

Sherman, Texas, 75090-0504, United States

Location

Northern Utah Associates

Ogden, Utah, 84403, United States

Location

Shenandoah Oncology Associates

Winchester, Virginia, 22601, United States

Location

Puget Sound Cancer Centers

Edmonds, Washington, 98026, United States

Location

Swedish Health Services

Seattle, Washington, 98122, United States

Location

Royal Prince Alfred Hospital

Camperdown, New South Wales, 2050, Australia

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

Port Macquarie Base Hospital;North Coast Cancer Institute

Port Macquarie, New South Wales, 2444, Australia

Location

Sydney Haematology & Oncology Clinic

Wahroonga, New South Wales, 2076, Australia

Location

Calvary Mater Newcastle; Medical Oncology

Waratah, New South Wales, 2298, Australia

Location

Border Medical Oncology

Wodonga, New South Wales, 3690, Australia

Location

Royal Brisbane and Women's Hospital

Herston, Queensland, 4029, Australia

Location

Mater Adult Hospital

Mackay, Queensland, 4740, Australia

Location

Ashford Cancer Center Research

Kurralta Park, South Australia, 5037, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Bendigo Hospital; Oncology

Bendigo, Victoria, 3550, Australia

Location

Peninsula and South Eastern Haematology and Oncology Grou

Frankston, Victoria, 3199, Australia

Location

Royal Perth Hospital; Medical Oncology

Perth, Western Australia, 6000, Australia

Location

Lkh-Univ. Klinikum Graz

Graz, 8036, Austria

Location

LKH - Universitätsklinikum der PMU Salzburg

Salzburg, 5020, Austria

Location

Krankenhaus Hietzing m.Neurolog. Zentrum Rosenhuegel

Vienna, 1130, Austria

Location

Klinikum Wels-Grieskirchen

Wels, 4600, Austria

Location

Institut Jules Bordet

Brussels, 1000, Belgium

Location

UZ Antwerpen

Edegem, 2650, Belgium

Location

UZ Leuven Gasthuisberg

Leuven, 3000, Belgium

Location

CHU Ambroise Paré

Mons, 7000, Belgium

Location

Clinique Ste-Elisabeth

Namur, 5000, Belgium

Location

Sint Augustinus Wilrijk

Wilrijk, 2610, Belgium

Location

Fakultni nemocnice Brno

Brno, 613 00, Czechia

Location

Masarykuv onkologicky ustav

Brno, 656 53, Czechia

Location

Krajska nemocnice Liberec a.s.

Liberec, 460 63, Czechia

Location

Multiscan s.r.o.

Pardubice, 532 03, Czechia

Location

Vseobecna fakultni nemocnice v Praze

Prague, 128 08, Czechia

Location

Nemocnice Na Bulovce

Prague, 180 01, Czechia

Location

Thomayerova nemocnice

Praha 4 - Krc, 140 59, Czechia

Location

Chungbuk National University Hospital

Cheongju-si, 28644, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Institut Catala d´Oncologia Hospital Germans Trias i Pujol

Badalona, Barcelona, 08916, Spain

Location

Institut Catala d Oncologia Hospital Duran i Reynals

Barcelona, 08908, Spain

Location

Complejo Hospitalario de Jaen

Jaén, 23007, Spain

Location

Hospital General Univ. Gregorio Maranon

Madrid, 28009, Spain

Location

START Madrid. Centro Integral Oncologico Clara Campal; CIOCC

Madrid, 28050, Spain

Location

Royal Sussex County Hospital

Brighton, BN2 5BE, United Kingdom

Location

Royal Surrey County Hospital

Guildford, GU2 7XX, United Kingdom

Location

Leicester Royal Infirmary

Leicester, LE1 5WW, United Kingdom

Location

Barts Hospital

London, E1 2EF, United Kingdom

Location

The Christie

Manchester, M20 4BX, United Kingdom

Location

Freeman Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Nottingham University Hospitals City Campus

Nottingham, NG5 1PB, United Kingdom

Location

Royal Stoke University Hospital

Stoke-on-Trent, ST4 6QG, United Kingdom

Location

Royal Cornwall Hospital

Truro, TR1 3LQ, United Kingdom

Location

New Cross Hospital

Wolverhampton, WV10 0QP, United Kingdom

Location

Related Publications (1)

  • Vuylsteke P, Huizing M, Petrakova K, Roylance R, Laing R, Chan S, Abell F, Gendreau S, Rooney I, Apt D, Zhou J, Singel S, Fehrenbacher L. Pictilisib PI3Kinase inhibitor (a phosphatidylinositol 3-kinase [PI3K] inhibitor) plus paclitaxel for the treatment of hormone receptor-positive, HER2-negative, locally recurrent, or metastatic breast cancer: interim analysis of the multicentre, placebo-controlled, phase II randomised PEGGY study. Ann Oncol. 2016 Nov;27(11):2059-2066. doi: 10.1093/annonc/mdw320. Epub 2016 Aug 29.

MeSH Terms

Conditions

Breast Neoplasms

Interventions

2-(1H-indazol-4-yl)-6-(4-methanesulfonylpiperazin-1-ylmethyl)-4-morpholin-4-ylthieno(3,2-d)pyrimidinePaclitaxel

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

TaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenes

Study Officials

  • Clinical Trials

    Genentech, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 30, 2012

First Posted

December 4, 2012

Study Start

February 6, 2013

Primary Completion

October 20, 2015

Study Completion

December 10, 2015

Last Updated

April 24, 2017

Record last verified: 2017-04

Locations