NCT01690299

Brief Summary

This study will test the clinical effectiveness and safety of apremilast compared with placebo as well as etanercept compared with placebo in the same group of patients with moderate to severe plaque psoriasis.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
250

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2012

Typical duration for phase_3

Geographic Reach
11 countries

82 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 19, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 21, 2012

Completed
10 days until next milestone

Study Start

First participant enrolled

October 1, 2012

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 3, 2014

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

August 4, 2015

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 4, 2016

Completed
Last Updated

March 15, 2022

Status Verified

April 1, 2020

Enrollment Period

1.8 years

First QC Date

September 19, 2012

Results QC Date

July 2, 2015

Last Update Submit

March 3, 2022

Conditions

Keywords

Psoriasisarthritispsoriaticpalmoplantarscalppsoriasis pillpsoriasis tabletplaque psoriasisplaque type psoriasismoderate to severe plaque type psoriasispsoriatic arthritis

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Who Achieved a 75% Improvement (Response) in the Psoriasis Area Severity Index (PASI-75) for the Comparison Between Apremilast and Placebo at Week 16 From Baseline

    PASI-75 response is the percentage of participants who achieved at least a 75% reduction (improvement) from baseline in PASI score at Week 16. The improvement in PASI score was used as a measure of efficacy. The PASI was a measure of psoriatic disease severity taking into account qualitative lesion characteristics (erythema, thickness, and scaling) and degree of skin surface area involvement on defined anatomical regions. PASI scores range from 0 to 72, with higher scores reflecting greater disease severity. Erythema, thickness, and scaling are scored on a scale of 0 (none) to 4 (very severe) on 4 anatomic regions of the body: head, trunk, upper limbs, and lower limbs. Degree of involvement on each of the 4 anatomic regions is scored on a scale of 0 (no involvement) to 6 (90% to 100% involvement). The PASI score was set to missing if any severity score or degree of involvement was missing.

    Baseline to Week 16

Secondary Outcomes (11)

  • Percentage of Participants Who Achieved a 75% Improvement (Response) in the Psoriasis Area and Severity Index (PASI) for the Comparison Between Etanercept 50mg SC QW and Placebo at Week 16

    Baseline and Week 16

  • Percentage of Participants Who Achieved a Static Physician Global Assessment (sPGA) Score of Clear (0) or Almost Clear (1) With at Least 2 Points Reduction for Comparison Between Apremilast and Placebo and Etanercept and Placebo at Week 16

    Baseline and Week 16

  • Percent Change From Baseline in the Affected Body Surface Area (BSA) for Comparison Between Apremilast and Placebo and Etanercept and Placebo at Week 16

    Baseline to Week 16

  • Percentage of Participants Who Achieved a 50% Improvement (Response) in the Psoriasis Area Severity Index (PASI-50) for Comparison Between Apremilast and Placebo and Etanercept and Placebo at Week 16

    Baseline to Week 16

  • Change From Baseline in Dermatology Life Quality Index (DLQI) Total Score In Comparison Between Apremilast and Placebo and Etanercept and Placebo at Week 16

    Baseline to Week 16

  • +6 more secondary outcomes

Study Arms (3)

Apremilast 30 mg plus placebo injection

EXPERIMENTAL

Apremilast 30 mg tablets orally twice a day (BID) plus once weekly (QW) evaluator/subject-blinded subcutaneous (SC) saline (placebo) injections

Drug: ApremilastDrug: Placebo injection

Etanercept 50 mg plus placebo tablet

EXPERIMENTAL

Etanercept 50 mg evaluator/subject-blinded SC QW injections plus placebo tablets orally BID

Drug: EtanerceptDrug: Placebo tablet

Oral placebo tablets plus SC placebo injections

PLACEBO COMPARATOR

Identically matching placebo tablets and evaluator/subject-blinded SC injections

Drug: Placebo tabletDrug: Placebo injection

Interventions

Apremilast 30 mg tablet orally BID

Also known as: CC-10004, Otezla
Apremilast 30 mg plus placebo injection

Etanercept 50 mg evaluator/subject-blinded SC QW injection

Also known as: Enbrel
Etanercept 50 mg plus placebo tablet

Placebo tablets BID

Etanercept 50 mg plus placebo tabletOral placebo tablets plus SC placebo injections

Once weekly evaluator/subject-blinded SC placebo (1 mL x 2 injections SC)

Apremilast 30 mg plus placebo injectionOral placebo tablets plus SC placebo injections

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males or females, ≥ 18 years of age
  • Diagnosis of chronic, moderate to severe plaque psoriasis for at least 12 months prior to Screening, and a candidate for phototherapy and/or systemic (including etanercept) therapy
  • Had an inadequate response, intolerance, or contraindication to at least 1 conventional systemic agent for the treatment of psoriasis.
  • No prior exposure to biologics for treatment of psoriatic arthritis or psoriasis

You may not qualify if:

  • Other than psoriasis, history of any clinically significant and uncontrolled systemic diseases; any condition, including the presence of laboratory abnormalities, which would place the subject at unacceptable risk if he/she were to participate in the study.
  • Pregnant or breast feeding.
  • Have failed more than 3 systemic agents for treatment of psoriasis.
  • History of allergy to any component of the investigational product (IP), including human immunoglobulin (Ig) proteins or allergy to etanercept.
  • Hepatitis B surface antigen or anti-hepatitis C antibody positive at Screening.
  • Latent, active tuberculosis (TB) or inadequately treated TB; nontuberculous mycobacterial infection or opportunistic infection (eg, cytomegalovirus, Pneumocystis carinii, aspergillosis, Clostridium difficile).
  • Have a history of, or ongoing, chronic or recurrent infectious disease
  • Have received, or are expected to receive, any live virus or bacterial vaccination within 3 months before first administration of IP, or through Week 20 during the study.
  • Had a Bacillus Calmette-Guérin (BCG) vaccination within 1 year prior to screening.
  • History of positive human immunodeficiency virus (HIV), or have congenital or acquired immunodeficiency (eg, common variable immunodeficiency disease).
  • Active substance abuse or a history of substance abuse within 6 months prior to Screening.
  • Malignancy or history of malignancy, except for treated \[ie, cured\] basal cell or squamous cell in situ skin carcinomas and cervical intraepithelial neoplasia \[CIN\] or carcinoma in situ of the cervix with no evidence of recurrence within the previous 5 years.
  • Psoriasis flare or rebound within 4 weeks prior to Screening.
  • Topical therapy within 2 weeks of randomization or systemic therapy for psoriasis within 4 weeks prior to randomization
  • Use of phototherapy within 4 weeks prior to randomization or prolonged sun exposure or use of tanning booths or other ultraviolet (UV) light sources.
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (82)

Arizona Research Center

Phoenix, Arizona, 85023, United States

Location

Bakersfield Dermatology and Skin Cancer Medical Group

Bakersfield, California, 93309, United States

Location

University of California Irvine-Department of Dermatology

Irvine, California, 92697, United States

Location

University of California San Diego Medical Center

San Diego, California, 92122, United States

Location

Horizons Clinical Research

Denver, Colorado, 80220, United States

Location

George Washington University

Washington D.C., District of Columbia, 20037, United States

Location

Florida Center for Dermatology, PA

Jacksonville, Florida, 32204, United States

Location

Florida Academic Dermatology Center

Miami, Florida, 33136, United States

Location

International Dermatology Research

Miami, Florida, 33144, United States

Location

Renstar Medical Research

Ocala, Florida, 34471, United States

Location

Atlanta Dermatology, Vein and Research Center, PC

Alpharetta, Georgia, 30022, United States

Location

NorthShore University HealthSystem

Skokie, Illinois, 60077, United States

Location

Southern Illinois University School of Medicine

Springfield, Illinois, 62702, United States

Location

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, 46256, United States

Location

Dermatology and Advanced Aesthetics

Lake Charles, Louisiana, 70605, United States

Location

Lawrence Green, MD, LLC

Rockville, Maryland, 20850, United States

Location

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Robert Wood Johnson Medical School

Somerset, New Jersey, 08873, United States

Location

Forest Hills Dermatology Group

Forest Hills, New York, 11375, United States

Location

NYU Department of Dermatology

New York, New York, 10016, United States

Location

University of North Carolina

Chapel Hill, North Carolina, 27516, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Wake Forest University Health Sciences

Winston-Salem, North Carolina, 27104, United States

Location

University Hospitals Case Medical Center

Cleveland, Ohio, 44106, United States

Location

Ohio State University Medical Center

Columbus, Ohio, 43230, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Tennesse Clinical Research Center

Nashville, Tennessee, 37215, United States

Location

Teckton Research

Austin, Texas, 78745, United States

Location

The Education and Research Foundation

Lynchburg, Virginia, 24501, United States

Location

Virginia Clinical Research Inc

Norfolk, Virginia, 23507, United States

Location

Dermatology Associates of Seattle

Seattle, Washington, 98101, United States

Location

The Skin Centre

Benowa, Queensland, 4217, Australia

Location

Sinclair Dermatology

East Melbourne, Victoria, 3002, Australia

Location

Fremantle Dermatology

Fremantle, Western Australia, 6160, Australia

Location

Gairdner Hospital

Victoria Park, 6100, Australia

Location

Rheumatology unit Ward 5C Queen Elizabeth Hospital

Woodville, 5011, Australia

Location

Veracity Clinical Research

Woolloongabba, 4102, Australia

Location

Cliniques Universitaires St-Luc

Brussels, 1200, Belgium

Location

University Hospital Ghent

Ghent, 9000, Belgium

Location

University Hospital of Liege CHU Liege

Liège, 4000, Belgium

Location

Eastern Canada Cutaneous Research Associates Ltd

Halifax, Nova Scotia, B3H 1Z4, Canada

Location

Skin Center for Dermatology

Peterborough, Ontario, K9J 5K2, Canada

Location

K. Papp Clinical Research Inc.

Waterloo, Ontario, N2J 1C4, Canada

Location

Siena Medical Research

Montreal, Quebec, H3Z 2S6, Canada

Location

Q & T Research Sherbrooke Inc.

Sherbrooke, Quebec, J1H 4J6, Canada

Location

Dorothea, Kožní a korektivne dermatologické pracovište

Chomutov, 430 04, Czechia

Location

Dermamedica

Náchod, 54701, Czechia

Location

Východoceské dermatologické centrum Homea s.r.o.

Pardubice, 530 02, Czechia

Location

Krajská nemocnice Pardubice, Kožní oddelení

Pardubice, 532 03, Czechia

Location

Dermatovenerologicka ambulance

Svitavy, 568 02, Czechia

Location

Koznia zilni ambulance

Ústí nad Labem, 400 10, Czechia

Location

South Estonian Hospital Ltd

Meegomäe Village, Võru County, 65526, Estonia

Location

Dermatology Clinic of Tartu University Hospital

Tartu, 50417, Estonia

Location

Psoriasis Study Center

Berlin, 10117, Germany

Location

Dermatologische Praxis

Berlin, 10827, Germany

Location

Klinische Forschung Berlin - Buch GmbH

Berlin, 13125, Germany

Location

University Hospital Carl Gustav Carus

Dresden, 1307, Germany

Location

Hautklinik Universitatsklinikum Erlangen

Erlangen, 91054, Germany

Location

University Hospital Frankfurt

Frankfurt, 60590, Germany

Location

SCIderm GmbH

Hamburg, 20354, Germany

Location

Institute for Health Services Research in Dermatology and Nursing - IVDP, University Medical Center

Hamburg, D-20246, Germany

Location

Universitatsklinikum Heidelberg

Heidelberg, 69115, Germany

Location

UniversitatsKlinikum Leipzig A.o.R.

Leipzig, 4103, Germany

Location

Comprehensive Center of Inflammatory Medicine (CCIM) University Medical Center Schleswig-Holstein

Lübeck, 23538, Germany

Location

Gemeinschaftspraxis Mahlow

Mahlow, 15831, Germany

Location

University Hospital Munster

Münster, 48143, Germany

Location

Praxis fr Dermatologie und Venerologie

Wuppertal, 42275, Germany

Location

Tolna Megyei Balassa Janos Korhaz

Szekszárd, 7100, Hungary

Location

Allergo-Derm Bakos Kft.

Szolnok, 5000, Hungary

Location

LTD M & M centrs

Ādaži, 2164, Latvia

Location

Arija's Ancane's Family Doctor Private Practice

Baldone, 2125, Latvia

Location

Riga 1st Hospital Skin and Sexually Transmitted Diseases Clinical Centre

Riga, 1001, Latvia

Location

Adoria Ltd

Riga, 1011, Latvia

Location

Family Doctor's Indra's Kenina's Practice

Riga, 1011, Latvia

Location

Health Center of Talsi Ltd

Talsi, 3201, Latvia

Location

Academic Medical Center

Amsterdam, 1105 AZ, Netherlands

Location

Radboud University Medical Centre

Nijmegen, 6500HB, Netherlands

Location

University Hospital of Wales

Cardiff, CF14 4XN, United Kingdom

Location

Leeds Teaching Hospitals Trust

Leeds, LS7 4SA, United Kingdom

Location

Whipps Cross University Hospital

London, E11 1NR, United Kingdom

Location

St Helier Hospital

London, SM5 1AA, United Kingdom

Location

George Eliot Hospital

Nuneaton, CV10 7DJ, United Kingdom

Location

Related Publications (3)

  • Reich K, Mrowietz U, Menter A, Griffiths CEM, Bagel J, Strober B, Nunez Gomez N, Shi R, Guerette B, Lebwohl M. Effect of baseline disease severity on achievement of treatment target with apremilast: results from a pooled analysis. J Eur Acad Dermatol Venereol. 2021 Dec;35(12):2409-2414. doi: 10.1111/jdv.17520. Epub 2021 Aug 23.

    PMID: 34255891BACKGROUND
  • Mease PJ, Hatemi G, Paris M, Cheng S, Maes P, Zhang W, Shi R, Flower A, Picard H, Stein Gold L. Apremilast Long-Term Safety Up to 5 Years from 15 Pooled Randomized, Placebo-Controlled Studies of Psoriasis, Psoriatic Arthritis, and Behcet's Syndrome. Am J Clin Dermatol. 2023 Sep;24(5):809-820. doi: 10.1007/s40257-023-00783-7. Epub 2023 Jun 14.

  • Reich K, Gooderham M, Green L, Bewley A, Zhang Z, Khanskaya I, Day RM, Goncalves J, Shah K, Piguet V, Soung J. The efficacy and safety of apremilast, etanercept and placebo in patients with moderate-to-severe plaque psoriasis: 52-week results from a phase IIIb, randomized, placebo-controlled trial (LIBERATE). J Eur Acad Dermatol Venereol. 2017 Mar;31(3):507-517. doi: 10.1111/jdv.14015. Epub 2016 Dec 19.

MeSH Terms

Conditions

PsoriasisArthritis, PsoriaticArthritis

Interventions

apremilastEtanercept

Condition Hierarchy (Ancestors)

Skin Diseases, PapulosquamousSkin DiseasesSkin and Connective Tissue DiseasesSpondylarthropathiesSpondylarthritisSpondylitisSpinal DiseasesBone DiseasesMusculoskeletal DiseasesJoint Diseases

Intervention Hierarchy (Ancestors)

Immunoglobulin Fc FragmentsImmunoglobulin FragmentsPeptide FragmentsPeptidesAmino Acids, Peptides, and ProteinsImmunoglobulin Constant RegionsImmunoglobulinsImmunoproteinsBlood ProteinsProteinsSerum GlobulinsGlobulinsReceptors, Tumor Necrosis FactorReceptors, CytokineReceptors, ImmunologicReceptors, Cell SurfaceMembrane Proteins

Results Point of Contact

Title
Anne McClain, Senior Manager, Clinical Trial Disclosure
Organization
Celgene Corporation

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 19, 2012

First Posted

September 21, 2012

Study Start

October 1, 2012

Primary Completion

July 3, 2014

Study Completion

April 4, 2016

Last Updated

March 15, 2022

Results First Posted

August 4, 2015

Record last verified: 2020-04

Data Sharing

IPD Sharing
Will share

De-identified individual patient data for variables necessary to address the specific research question in an approved data sharing request

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
Data sharing requests relating to this study will be considered beginning 18 months after the study has ended and either 1) the product and indication have been granted marketing authorization in both the US and Europe or 2) clinical development for the product and/or indication discontinues and the data will not be submitted to regulatory authorities. There is no end date for eligibility to submit a data sharing request for this study.
Access Criteria
Qualified researchers may submit a request containing the research objectives, the Amgen product(s) and Amgen study/studies in scope, endpoints/outcomes of interest, statistical analysis plan, data requirements, publication plan, and qualifications of the researcher(s). In general, Amgen does not grant external requests for individual patient data for the purpose of re-evaluating safety and efficacy issues already addressed in the product labelling. Requests are reviewed by a committee of internal advisors. If not approved, a Data Sharing Independent Review Panel will arbitrate and make the final decision. Upon approval, information necessary to address the research question will be provided under the terms of a data sharing agreement. This may include anonymized individual patient data and/or available supporting documents, containing fragments of analysis code where provided in analysis specifications. Further details are available at the URL below.
More information

Locations