NCT01607957

Brief Summary

The purpose of this study is to compare the efficacy and safety of TAS-102 versus placebo in patients with refractory metastatic colorectal cancer.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
800

participants targeted

Target at P50-P75 for phase_3 colorectal-cancer

Timeline
Completed

Started Jun 2012

Geographic Reach
12 countries

110 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 24, 2012

Completed
6 days until next milestone

First Posted

Study publicly available on registry

May 30, 2012

Completed
18 days until next milestone

Study Start

First participant enrolled

June 17, 2012

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 31, 2014

Completed
2.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 23, 2016

Completed
3 years until next milestone

Results Posted

Study results publicly available

May 21, 2019

Completed
Last Updated

September 19, 2024

Status Verified

August 1, 2024

Enrollment Period

1.6 years

First QC Date

May 24, 2012

Results QC Date

April 1, 2019

Last Update Submit

August 30, 2024

Conditions

Keywords

Refractory, metastatic colorectal cancer

Outcome Measures

Primary Outcomes (1)

  • Overall Survival

    Overall survival was defined as the time from the date of randomization to the date of death for participants. If a participant discontinued study medication for reasons other than radiologic disease progression, the participant was followed for tumor response until radiologic disease progression or initiation of new anticancer therapy.

    Every 8 weeks, up to 12 months after the last participant was randomized or until the target number of events (deaths) was met, whichever was later. (Overall survival data was collected till 24 Jan 2014 which was date of observation of the 571st death)

Secondary Outcomes (2)

  • Progression-free Survival

    Every 8 weeks, up to 12 months after the last participant was randomized or until the date of the investigator-assessed radiological disease progression or death due to any cause,whichever was later. (Progression free survival cutoff: 31 Jan 2014)

  • Percentage of Participants With Adverse Events (AE), Treatment-Related AEs, Discontinuations, Serious Adverse Events (SAEs) and Deaths

    From the time of signing the informed consent form until the period of participant follow up (30 days following after the administration of last dose of study medication or until initiation of new antitumor therapy, whichever was earlier

Study Arms (2)

TAS-102

EXPERIMENTAL
Drug: TAS-102

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

35 mg/m2/dose, orally, twice daily on days 1-5 and 8-12 of each 28-day cycle. Number of cycles: until at least one of the discontinuation criteria are met.

TAS-102

Placebo tablets, orally, twice daily on days 1-5 and 8-12 of each 28-day cycle. Number of cycles: until at least one of the discontinuation criteria are met.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has provided written informed consent
  • Has adenocarcinoma of the colon or rectum
  • Has failed at least 2 prior regimens of standard chemotherapies for metastatic colorectal cancer
  • ECOG performance status of 0 or 1
  • Is able to take medications orally
  • Has adequate organ function (bone marrow, kidney and liver)
  • Women of childbearing potential must have a negative pregnancy test and must agree to adequate birth control if conception is possible. Males must agree to adequate birth control.

You may not qualify if:

  • Certain serious illnesses or medical condition(s)
  • Has had certain other recent treatment e.g. major surgery, anticancer therapy, extended field radiation, received investigational agent, within the specified time frames prior to study drug administration
  • Has received TAS-102
  • Has unresolved toxicity of greater than or equal to CTCAE Grade 2 attributed to any prior therapies
  • Is a pregnant or lactating female

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (115)

Arizona Center for Cancer Care

Glendale, Arizona, 85306, United States

Location

California Cancer Associates for Research and Excellence

Fresno, California, 93720, United States

Location

Ronald H. Yanagihara, MD

Gilroy, California, 95020, United States

Location

LAC and USC Medical Center

Los Angeles, California, 90033, United States

Location

USC Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

Pacific Hematology Oncology Associates

San Francisco, California, 94115, United States

Location

San Jose Medical Group

San Jose, California, 95124, United States

Location

Coastal Integrative Cancer Care

San Luis Obispo, California, 93401, United States

Location

Yale Cancer Center

New Haven, Connecticut, 06520, United States

Location

MD Anderson Cancer Center Orlando

Orlando, Florida, 32806, United States

Location

Illinois Cancer Care, P.C.

Peoria, Illinois, 61615, United States

Location

Indiana University Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

Mary Bird Perkins Cancer Center

Baton Rouge, Louisiana, 70809, United States

Location

Ochsner Clinic Fndtn

New Orleans, Louisiana, 70121-2429, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

St. Joseph Mercy Hospital

Ann Arbor, Michigan, 48106, United States

Location

Jefferson City Medical Group

Jefferson City, Missouri, 65109-6023, United States

Location

Saint Luke's Cancer Institute

Kansas City, Missouri, 64111, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

Hickman Cancer Center at Flower Hospital

Sylvania, Ohio, 43560, United States

Location

Hematology/Oncology Associates of Fredericksburg

Fredericksburg, Virginia, 22408, United States

Location

Royal North Shore Hospital

Sydney, New South Wales, 2065, Australia

Location

The Queen Elisabeth Hospital

Woodville South, South Australia, 5011, Australia

Location

Austin Hospital

Heidelberg, Victoria, 3084, Australia

Location

The Royal Melbourne Hospital

Parkville, Victoria, 3050, Australia

Location

Sir Charles Gairdner Hospital

Perth, Western Australia, 6009, Australia

Location

Krankenhaus der Barmherzigen Schwestern Linz

Linz, 4010, Austria

Location

Universitaet Wien

Vienna, 1090, Austria

Location

Universitaetsklinik fur Innere Medizin

Vienna, 1090, Austria

Location

Wilhelminenspital Wien

Vienna, 1160, Austria

Location

Klinikum Wels-Grieskirchen GmbH

Wels, 4600, Austria

Location

Cliniques Universitaires UCL St. Luc

Brussels, 1200, Belgium

Location

Erasme University Hospital-ULB-Brussels

Brussels, B-1070, Belgium

Location

Grand Hospital de Charleroi

Charleroi, 6000, Belgium

Location

Antwerp University Hospital

Edegem, 2650, Belgium

Location

University Hospital Gent

Edegem, 2650, Belgium

Location

University Hospital Gent

Ghent, 9000, Belgium

Location

Leuven University Hospital - Campus Gasthuiseberg

Leuven, 3000, Belgium

Location

University Hospital Gasthuisberg

Leuven, 3000, Belgium

Location

Klinika onkologie a radioteraie, Facultni nemocnice Hradec Kralove

Hradec Králové, 50005, Czechia

Location

Institute of Oncology and Rehabilitation Ples

Nová Ves pod Pleší, 26204, Czechia

Location

CHU de Becançon

Besançon, 25030, France

Location

University Hospital of Bordeaux

Bordeaux, 33075, France

Location

Centre Oscar Lambret

Lille, 59020, France

Location

CRLC Val d'Aurelle

Montpellier, 34298, France

Location

Hopital Saint Antoine

Paris, 75571, France

Location

Centre Eugene Marquis

Rennes, 35042, France

Location

Onkologische Schwerpunktpraxis Kurfuerstendamm

Berlin, 10707, Germany

Location

Praxiskooperation Bonn-Euskirchen-Rheinbach

Bonn, 53123, Germany

Location

Uniklinik Koeln

Cologne, 50937, Germany

Location

Universitatsklinikum Carl Gustav Carus - Dresden

Dresden, 1307, Germany

Location

Medizinische Klinik am Krankenhaus Nordwest GmbH

Frankfurt, 60488, Germany

Location

Uniklinik der Martin-Luther-Universitaet Halle-Wittenberg

Halle, 6120, Germany

Location

Universitätsklinikum Hamburg-Eppendorf

Hamburg, 20246, Germany

Location

Johannes Gutenberg Universität Mainz

Mainz, 55131, Germany

Location

Interdisziplinaeres Tumorzentrum Mannheim

Mannheim, 68167, Germany

Location

Klinikum der Universität München - Großhadern

München, 81377, Germany

Location

Staedtisches Klinikum Muenchen / Klinikum Neuperlach

München, 81737, Germany

Location

Klinikum Oldenburg gGmbH

Oldenburg, 26133, Germany

Location

Universitaetsklinikum Ulm

Ulm, 89081, Germany

Location

Bon Secours Hospital

Cork, Ireland

Location

Adelaide and Meath Hospital

Dublin, 24, Ireland

Location

St. Vincent's University Hospital

Dublin, 4, Ireland

Location

Fondazione Poliambulanza

Brescia, Lombardy, 25124, Italy

Location

Universita Delgi Studi de Genova (UNIGE)- Azienda Ospedaliera. Universitaria "San Martino" (Ospedale San Martino)

Genova, 16132, Italy

Location

A.O. Ospedale Niguarda Ca' Granda

Milan, 20162, Italy

Location

Fondazione IRCCS Instituto Nazionale dei Tumori Milano

Milan, 20133, Italy

Location

A.O. R.N. "A.Cardarelli"

Naples, 80131, Italy

Location

Seconda Universita degli Studi de Napoli

Napoli, 80131, Italy

Location

AOU San Luidi di Orbassano

Orbassano, 1010043, Italy

Location

Azienda Ospedaliero

Pisa, 6756126, Italy

Location

Arcispidale S Maria Nuova

Reggio Emilia, 42123, Italy

Location

Ospedale di Rimini

Rimini, 47923, Italy

Location

Ospedale di Sondrio

Sondrio, 23100, Italy

Location

Aichi Cancer Center Hospital

Nagoya, Aichi-ken, 4648681, Japan

Location

National Cancer Center Hospital East

Kashiwa, Chiba, 277-0882, Japan

Location

National Cancer Center Hospital East

Kashiwa, Chiba, 2778577, Japan

Location

National Hospital Organization Shikoku Cancer Center

Matsuyama, Ehime, 7910280, Japan

Location

KKR Sapporo Medical Center TONAN-Hospital

Sapporo, Hokkaido, 0600001, Japan

Location

Hokkaido University Hospital

Sapporo, Hokkaido, 0608648, Japan

Location

Kobe City Medical Center General Hospital

Kobe, Hyōgo, 6500047, Japan

Location

Tsukuba University Hospital

Tsukuba, Ibaraki, 3058576, Japan

Location

Kanagawa Cancer Center

Yokohama, Kanagawa, 2418515, Japan

Location

Osaka Medical College Hospital

Takatsuki, Osaka, 5698686, Japan

Location

Saitama Cancer Center

Kita-adachi-gun, Saitama, 3620806, Japan

Location

Shizuoka Cancer Center

Sunto-gun, Shizuoka, 4118777, Japan

Location

Jichi Medical University Hospital

Shimotsuke, Tochigi, 3290498, Japan

Location

National Cancer Center Hospital

Chuo-ku, Tokyo, 1040045, Japan

Location

The Cancer Institute Hospital of Japanese Foundation for Cancer Research

Koto-ku, Tokyo, 1358550, Japan

Location

Keio University Hospital

Shinjuku-ku, Tokyo, 1608582, Japan

Location

Chiba Cancer Center

Chiba, 2608717, Japan

Location

National Hospital Organization Kyushu Cancer Center

Fukuoka, 8111395, Japan

Location

Kumamoto University Hospital

Kumamoto, 8608556, Japan

Location

Osaka Medical Center for Cancer and Cardiovascular Diseases

Osaka, 5378511, Japan

Location

Tokushima University Hospital

Tokushima, 7708503, Japan

Location

Hospital Universitario Vall d'Hebrón

Barcelona, 8035, Spain

Location

Hospital Arnau de Vilanova

Lleida, 25198, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, 28034, Spain

Location

Fundacion Jimenez Diaz - Universidad Autonoma de Madrid

Madrid, 28040, Spain

Location

Hospital 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Carlos Haya

Málaga, 29010, Spain

Location

Hospital Universitario Morales Messeguer

Murcia, 30008, Spain

Location

Corporacion Sanitaria Parc Tauli

Sabadell, 8916, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Clínico Universitario de Valencia

Valencia, 46010, Spain

Location

Hospital General Universitario de Valencia

Valencia, 46014, Spain

Location

Karolinska University Hospital

Stockholm, 17176, Sweden

Location

Akademiska Sjukhuset

Uppsala, 75185, Sweden

Location

Aberdeen Royal Infirmary

Aberdeen, AB25 2ZN, United Kingdom

Location

University Hospitals Bristol NHS Foundation Trust

Bristol, BS2 8ED, United Kingdom

Location

St James' Institute of Oncology

Leeds, LS9 7TF, United Kingdom

Location

University College London Hospitals Foundation NHS Trust

London, NW1 2PG, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

Surrey, SM2 5PT, United Kingdom

Location

Related Publications (4)

  • Yoshino T, Cleary JM, Van Cutsem E, Mayer RJ, Ohtsu A, Shinozaki E, Falcone A, Yamazaki K, Nishina T, Garcia-Carbonero R, Komatsu Y, Baba H, Argiles G, Tsuji A, Sobrero A, Yamaguchi K, Peeters M, Muro K, Zaniboni A, Sugimoto N, Shimada Y, Tsuji Y, Hochster HS, Moriwaki T, Tran B, Esaki T, Hamada C, Tanase T, Benedetti F, Makris L, Yamashita F, Lenz HJ. Neutropenia and survival outcomes in metastatic colorectal cancer patients treated with trifluridine/tipiracil in the RECOURSE and J003 trials. Ann Oncol. 2020 Jan;31(1):88-95. doi: 10.1016/j.annonc.2019.10.005.

  • Van Cutsem E, Mayer RJ, Laurent S, Winkler R, Gravalos C, Benavides M, Longo-Munoz F, Portales F, Ciardiello F, Siena S, Yamaguchi K, Muro K, Denda T, Tsuji Y, Makris L, Loehrer P, Lenz HJ, Ohtsu A; RECOURSE Study Group. The subgroups of the phase III RECOURSE trial of trifluridine/tipiracil (TAS-102) versus placebo with best supportive care in patients with metastatic colorectal cancer. Eur J Cancer. 2018 Feb;90:63-72. doi: 10.1016/j.ejca.2017.10.009. Epub 2017 Dec 21.

  • Longo-Munoz F, Argiles G, Tabernero J, Cervantes A, Gravalos C, Pericay C, Gil-Calle S, Mizuguchi H, Carrato-Mena A, Limon ML, Garcia-Carbonero R. Efficacy of trifluridine and tipiracil (TAS-102) versus placebo, with supportive care, in a randomized, controlled trial of patients with metastatic colorectal cancer from Spain: results of a subgroup analysis of the phase 3 RECOURSE trial. Clin Transl Oncol. 2017 Feb;19(2):227-235. doi: 10.1007/s12094-016-1528-7. Epub 2016 Jul 21.

  • Mayer RJ, Van Cutsem E, Falcone A, Yoshino T, Garcia-Carbonero R, Mizunuma N, Yamazaki K, Shimada Y, Tabernero J, Komatsu Y, Sobrero A, Boucher E, Peeters M, Tran B, Lenz HJ, Zaniboni A, Hochster H, Cleary JM, Prenen H, Benedetti F, Mizuguchi H, Makris L, Ito M, Ohtsu A; RECOURSE Study Group. Randomized trial of TAS-102 for refractory metastatic colorectal cancer. N Engl J Med. 2015 May 14;372(20):1909-19. doi: 10.1056/NEJMoa1414325.

MeSH Terms

Conditions

Colorectal Neoplasms

Interventions

trifluridine tipiracil drug combination

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Results Point of Contact

Title
Taiho
Organization
Taiho Oncology, Inc.

Study Officials

  • From - Boston, MA

    Dana-Farber Cancer Institute

    PRINCIPAL INVESTIGATOR
  • From - Leuven, Belgium

    University Hospital, Gasthuisberg

    PRINCIPAL INVESTIGATOR
  • From - Kashiwa, Chiba Japan

    National Cancer Center Hospital East

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 24, 2012

First Posted

May 30, 2012

Study Start

June 17, 2012

Primary Completion

January 31, 2014

Study Completion

May 23, 2016

Last Updated

September 19, 2024

Results First Posted

May 21, 2019

Record last verified: 2024-08

Locations