NCT01602380

Brief Summary

The purpose of the study is to compare how treatment with Fulvestrant (FASLODEX) or Anastrozole (ARIMIDEX) effects disease progression for women with locally advanced or metastatic breast cancer who have not had prior hormonal treatment.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
462

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2012

Longer than P75 for phase_3

Geographic Reach
20 countries

118 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 11, 2012

Completed
10 days until next milestone

First Posted

Study publicly available on registry

May 21, 2012

Completed
5 months until next milestone

Study Start

First participant enrolled

October 17, 2012

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 11, 2016

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 17, 2017

Completed
8.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 16, 2026

Completed
Last Updated

February 27, 2026

Status Verified

February 1, 2026

Enrollment Period

3.5 years

First QC Date

May 11, 2012

Results QC Date

March 23, 2017

Last Update Submit

February 6, 2026

Conditions

Keywords

hormone receptor positive breast cancerendocrineno hormone therapyhormonebreastcancerneoplasmmetastatictumour

Outcome Measures

Primary Outcomes (1)

  • Comparison of Progression-Free Survival (PFS) in Patients Treated With Fulvestrant With Those Treated With Anastrozole

    PFS was defined as the time from randomisation until objective disease progression according to Response Evaluation Criteria in Solid Tumours version 1.1 (RECIST 1.1), surgery or radiotherapy to manage worsening of disease or death by any cause (in the absence of progression). Outcome measure is reported as median time from randomisation to PFS, calculated using the Kaplan-Meier technique.

    Baseline RECIST 1.1 assessments (Day 0) and then every 12 weeks until the earliest of disease progression evident, patient dies or has surgery/radiotherapy for their disease (up to approximately 38 months)

Secondary Outcomes (8)

  • Comparison of Overall Survival (OS) in Patients Treated With Fulvestrant With Those Treated With Anastrozole; Percentage of Patients With Events

    Baseline (Day 0) up to data cut-off for final analysis (up to approximately 116 months). Following disease progression, patients were to be contacted at 12 weekly intervals to determine survival status

  • Objective Response Rate (ORR) for Fulvestrant Treatment Versus Anastrozole Treatment

    Baseline RECIST 1.1 assessments (Day 0) and then every 12 weeks until disease progression or treatment discontinuation (up to approximately 38 months)

  • Duration of Response (DoR) for Fulvestrant Treatment Versus Anastrozole Treatment

    Baseline RECIST 1.1 assessments (Day 0) and then every 12 weeks until disease progression or treatment discontinuation (up to approximately 38 months)

  • Expected Duration of Response (EDoR) for Fulvestrant Treatment Versus Anastrozole Treatment

    Baseline RECIST 1.1 assessments and then every 12 weeks until disease progression or treatment discontinuation (up to approximately 38 months)

  • Clinical Benefit Rate (CBR) for Fulvestrant Treatment Versus Anastrozole Treatment

    Baseline RECIST 1.1 assessments (Day 0) and then every 12 weeks until disease progression or treatment discontinuation (up to approximately 38 months)

  • +3 more secondary outcomes

Study Arms (2)

faslodex+placebo

EXPERIMENTAL

Blinded: Fulvestrant 500mg intramuscular injection (2x250mg) plus dummy Anastrozole tablets

Drug: faslodex 500mgDrug: arimidex dummy

arimidex +placebo

ACTIVE COMPARATOR

Blinded: Anastrozole 1mg tablets plus dummy Fulvestrant intramuscular injection (2x0mg)

Drug: arimidex 1mgDrug: faslodex dummy

Interventions

2 x intramuscular injections at day 1, 14, 28 and every 28 days thereafter

faslodex+placebo

oral tablet 1 daily

arimidex +placebo

2 x intramuscular injections at day 1, 14, 28 and every 28 days thereafter

arimidex +placebo

oral tablet 1 daily

faslodex+placebo

Eligibility Criteria

Age18 Years - 130 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histological confirmation of breast cancer in post menopausal women (age \>=60). Positive hormone receptor status (ER +ve and/or PgR +ve) of primary or metastatic tumour tissue based on local laboratory assessment.
  • EITHER locally advanced disease (1 line of chemotherapy allowed only if remain unsuitable for therapy of curative intent) OR Metastatic disease. (1 line of chemotherapy for breast cancer allowed only if subsequent evidence of further progressive disease)
  • At least 1 lesion (measurable and/or non-measurable) that can be accurately assessed at baseline and is suitable for repeated assessment.
  • Postmenopausal women, fulfilling 1 of:
  • Prior bilateral oophorectomy
  • Age \>60 years
  • Age \< 60 years and amenorrheic for 12+months in the absence of chemotherapy, tamoxifen, toremifene, or ovarian suppression and FSH and oestradiol in the postmenopausal range

You may not qualify if:

  • Presence of life-threatening metastatic disease
  • Any of:
  • Extensive hepatic involvement
  • involving brain or meninges
  • symptomatic pulmonary lymph spread
  • Discrete lung metastases are acceptable if respiratory function is not significantly compromised
  • Prior systemic therapy for breast cancer other than one line of cytotoxic chemotherapy (the last dose of chemotherapy must have been received more than 28 days prior to randomisation)
  • Radiation therapy if not completed within 28 days prior to randomisation (with the exception of radiotherapy given for control of bone pain, started prior to randomisation). Prior hormonal treatment for breast cancer.
  • Current or prior malignancy within previous 3 years (other than breast cancer or adequately treated basal cell or squamous cell carcinoma of the skin or in situ carcinoma of the cervix).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (118)

Research Site

Modesto, California, 95355, United States

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Savannah, Georgia, 31405, United States

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Auburn, Maine, 04212, United States

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Worcester, Massachusetts, 01608, United States

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Detroit, Michigan, 48202, United States

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St Louis, Missouri, 63110, United States

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Lincoln, Nebraska, 68506, United States

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Somerset, New Jersey, 08873, United States

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Columbus, Ohio, 43202, United States

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Montgomery, Ohio, 45242, United States

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Memphis, Tennessee, 38120, United States

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Salt Lake City, Utah, 84107, United States

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La Rioja, 5300, Argentina

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Mar del Plata, B7600CTO, Argentina

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Pergamino, B2700CPM, Argentina

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Rosario, S2000KZE, Argentina

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Porto Alegre, 91350-200, Brazil

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Santo André, 09060-870, Brazil

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Abbotsford British Columbia, British Columbia, V2S0C2, Canada

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Vancouver, British Columbia, V5Z 4E6, Canada

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Kitchener, Ontario, N2G 1G3, Canada

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Thunder Bay, Ontario, P7B 6V4, Canada

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Montreal, Quebec, H3T 1E2, Canada

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Montreal, Quebec, H4A 3J1, Canada

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Chengdu, 610041, China

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Dalian, 116011, China

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Fuzhou, 350025, China

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Guangzhou, 510060, China

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Shanghai, 200032, China

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Shenyang, 110001, China

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Suzhou, 215004, China

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Tianjin, 300060, China

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Prague, 150 06, Czechia

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Příbram, 261 01, Czechia

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Avellino, 83100, Italy

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Bari, 70124, Italy

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Benevento, 82100, Italy

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Catania, 95126, Italy

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Genova, 16128, Italy

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Pisa, 56100, Italy

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Roma, 00100, Italy

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Roma, 00144, Italy

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Roma, 00161, Italy

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Treviglio, 24047, Italy

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Fukuoka, 811-1395, Japan

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Hamamatsu, 430-0906, Japan

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Kagoshima, 892-0833, Japan

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Kumamoto, 860-8556, Japan

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Matsuyama, 791-0280, Japan

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Mitaka-shi, 181-8611, Japan

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Nishinomiya-shi, 663-8501, Japan

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Osaka, 540-0006, Japan

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Sakaishi, 590-0064, Japan

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Suita-shi, 565-0871, Japan

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Mexico City, 6760, Mexico

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Mérida, 97000, Mexico

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Monterrey, 64000, Mexico

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Monterrey, 64060, Mexico

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Monterrey, 64710, Mexico

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Lima, Lima 18, Peru

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Lima, LIMA 27, Peru

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Lima, LIMA 33, Peru

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Lima, LIMA 41, Peru

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Katowice, 40-635, Poland

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Lodz, 90-242, Poland

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Lublin, 20-718, Poland

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Brăila, 810325, Romania

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Craiova, 200347, Romania

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Onești, 601048, Romania

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Timișoara, 300239, Romania

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Barnaul, 656052, Russia

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Moscow, 115478, Russia

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Omsk, 644013, Russia

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Ryazan, 390046, Russia

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Saint Petersburg, 191014, Russia

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Saint Petersburg, 195271, Russia

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Saint Petersburg, 197022, Russia

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Saint Petersburg, 197758, Russia

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Tomsk, 634028, Russia

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Bardejov, 085 01, Slovakia

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Bratislava, 814 65, Slovakia

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Bratislava, 833 10, Slovakia

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Trenčín, 91171, Slovakia

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Cape Town, 7570, South Africa

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Cape Town, 7700, South Africa

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Cape Town, 7925, South Africa

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Pietermaritzburg, 3201, South Africa

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Pretoria, 0001, South Africa

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Pretoria, 0081, South Africa

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Madrid, 28034, Spain

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Madrid, 28050, Spain

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Pamplona, 31008, Spain

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Pozuelo de Alarcón, 28223, Spain

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Sabadell, 8208, Spain

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Seville, 41009, Spain

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Seville, 41013, Spain

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Seville, 41014, Spain

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Valencia, 46014, Spain

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Valencia, 46026, Spain

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Taichung, 40447, Taiwan

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Taipei, 10449, Taiwan

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Taipei, 112, Taiwan

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Taipei, 235, Taiwan

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Ankara, 06100, Turkey (Türkiye)

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Gaziantep, 27310, Turkey (Türkiye)

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Cherkasy, 18009, Ukraine

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Dnipro, 49102, Ukraine

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Donetsk, 83092, Ukraine

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Ivano-Frankivsk, 76014, Ukraine

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Kharkiv Region, 61070, Ukraine

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Kyiv, 3115, Ukraine

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Lviv, 79031, Ukraine

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Mariupol, 87500, Ukraine

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Uzhhorod, 88000, Ukraine

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Vinnytsia, 21029, Ukraine

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Airdrie, ML6 0JS, United Kingdom

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Derby, DE22 3NE, United Kingdom

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Stoke-on-Trent, ST4 6QG, United Kingdom

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Related Publications (4)

  • Robertson JFR, Shao Z, Noguchi S, Bondarenko I, Panasci L, Singh S, Subramaniam S, Ellis MJ. Fulvestrant Versus Anastrozole in Endocrine Therapy-Naive Women With Hormone Receptor-Positive Advanced Breast Cancer: Final Overall Survival in the Phase III FALCON Trial. J Clin Oncol. 2025 May;43(13):1539-1545. doi: 10.1200/JCO.24.00994. Epub 2025 Jan 7.

  • Robertson JFR, Cheung KL, Noguchi S, Shao Z, Degboe A, Lichfield J, Thirlwell J, Fazal M, Ellis MJ. Health-related quality of life from the FALCON phase III randomised trial of fulvestrant 500 mg versus anastrozole for hormone receptor-positive advanced breast cancer. Eur J Cancer. 2018 May;94:206-215. doi: 10.1016/j.ejca.2018.02.026. Epub 2018 Mar 22.

  • Robertson JFR, Bondarenko IM, Trishkina E, Dvorkin M, Panasci L, Manikhas A, Shparyk Y, Cardona-Huerta S, Cheung KL, Philco-Salas MJ, Ruiz-Borrego M, Shao Z, Noguchi S, Rowbottom J, Stuart M, Grinsted LM, Fazal M, Ellis MJ. Fulvestrant 500 mg versus anastrozole 1 mg for hormone receptor-positive advanced breast cancer (FALCON): an international, randomised, double-blind, phase 3 trial. Lancet. 2016 Dec 17;388(10063):2997-3005. doi: 10.1016/S0140-6736(16)32389-3. Epub 2016 Nov 29.

  • Ellis MJ, Llombart-Cussac A, Feltl D, Dewar JA, Jasiowka M, Hewson N, Rukazenkov Y, Robertson JF. Fulvestrant 500 mg Versus Anastrozole 1 mg for the First-Line Treatment of Advanced Breast Cancer: Overall Survival Analysis From the Phase II FIRST Study. J Clin Oncol. 2015 Nov 10;33(32):3781-7. doi: 10.1200/JCO.2015.61.5831. Epub 2015 Sep 14.

Related Links

MeSH Terms

Conditions

NeoplasmsNeoplasm Metastasis

Interventions

FulvestrantAnastrozole

Condition Hierarchy (Ancestors)

Neoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

EstradiolEstrenesEstranesSteroidsFused-Ring CompoundsPolycyclic CompoundsEstradiol CongenersGonadal Steroid HormonesGonadal HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNitrilesOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca

Study Officials

  • Shankar S, MD

    AstraZeneca

    STUDY DIRECTOR
  • John Robertson, MD

    Graduate Medicine and Health School, University of Nottingham, UK

    PRINCIPAL INVESTIGATOR
  • Matthew Ellis, DM

    Washington University School of Medicine, USA

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 11, 2012

First Posted

May 21, 2012

Study Start

October 17, 2012

Primary Completion

April 11, 2016

Study Completion

January 16, 2026

Last Updated

February 27, 2026

Results First Posted

May 17, 2017

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
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