NCT01562899

Brief Summary

This is a multi-center, open-label, phase Ib/II study. First, the aim of the phase Ib part is to estimate the MTD(s) and/or to identify the recommended phase II dose(s) (RP2D) for the combination of MEK162 and AMG 479 (ganitumab), followed by the phase II part to assess the clinical efficacy and to further assess the safety of the combination in selected patient populations. The dose escalation part of the study will be guided by a Bayesian Logistic Regression Model (BLRM). At least 18 patients are expected to be enrolled in the dose escalation part. Following MTD/ RP2D declaration, patients will be enrolled in three phase II arms to assess efficacy of the combination as well as to better understand the safety, tolerability, PK, antibody concentrations and PD of the combination at MTD/RP2D. Phase II arm 1 will consist of approximately 25 patients with KRAS-mutant colorectal adenocarcinoma. Phase II arm 2 will consist of approximately 20 patients with metastatic pancreatic adenocarcinoma. Phase II arm 3 will consist of approximately 28 patients with mutant BRAFV600 melanoma. Patients will be treated until progression of disease, unacceptable toxicity develops, or withdrawal of informed consent, whichever occurs first. All patients will be followed up - at minimum patients must complete the safety follow-up assessments 30 days after the last dose of the study treatment.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
77

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Aug 2012

Typical duration for phase_1

Geographic Reach
8 countries

9 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 22, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

March 26, 2012

Completed
5 months until next milestone

Study Start

First participant enrolled

August 27, 2012

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2015

Completed
Last Updated

December 10, 2020

Status Verified

December 1, 2020

Enrollment Period

2.6 years

First QC Date

March 22, 2012

Last Update Submit

December 9, 2020

Conditions

Keywords

MEK162AMG 479Ganitumabcolorectal adenocarcinomapancreatic adenocarcinomamelanomaKRASBRAF

Outcome Measures

Primary Outcomes (2)

  • Phase Ib: Estimation of Maximum Tolerated Doses (MTDs) and/or recommended Phase II doses (RP2Ds) by measuring incidence of dose limiting toxicities

    To estimate the MTDs and/or RP2Ds of MEK162 in combination with AMG479 by measuring incidence of dose limiting toxicities in Cycle 1 (Cycle 1 = 28 days)

    Approximately 6 months

  • Phase II: Antitumor activity of MEK162 in combination with AMG 479 by evaluating Objective Response Rate (ORR) in colorectal carcinoma and melanoma and by evaluating Disease Control Rate (DCR) at week 10 in pancreatic carcinoma

    To estimate the antitumor activity of MEK162 in combination with AMG479 by evaluating Objective Response Rate (ORR) according to RECIST 1.1 in colorectal carcinoma and melanoma and by evaluating the Disease Control Rate (DCR) per RECIST 1.1 at week 10 in pancreatic carcinoma

    Approximately 24 months

Secondary Outcomes (4)

  • Both Phases: Safety and tolerability of MEK162 & AMG 479 (ganitumab) in combination by evaluating the adverse events, serious adverse events, changes in hematology and chemistry values, vital signs, ECGs; dose interruptions, reductions and dose intensity

    Phase Ib: Approximately 6 months; Phase II: Approximately 24 months

  • Both Phases: Determination of single and multiple dose pharmacokinetics (PK) profile of MEK162 in combination with AMG 479 (ganitumab) by measuring time vs. plasma concentrations and basic PK parameters of MEK162

    Phase Ib: Approximately 6 months; Phase II: Approximately 24 months

  • Phase Ib: Preliminary anti-tumor activity of MEK162 and AMG 479 (ganitumab) in combination by evaluating the Overall Response Rate (ORR), Duration of Response (DOR) and Progression Free Survival (PFS)

    Approximately 6 months

  • Phase II: Further anti-tumor activity of MEK162 & AMG 479 (ganitumab) in combination by evaluating the DOR, PFS and OS by evaluating Disease Control Rate for colorectal carcinoma and melanoma; Overall Response Rate for pancreatic carcinoma patients

    Approximately 24 months

Study Arms (4)

Dose escalation

EXPERIMENTAL

Dose finding group chosen in order to establish a safe and tolerated dose of binimetinib in combination with ganitumab in patients with selected advanced solid tumors.

Drug: MEK162Drug: AMG 479

KRAS mutated colorectal adenocarcinoma

EXPERIMENTAL

Patients with KRAS mutant colorectal cancer. The starting dose (30 mg bid) of binimetinib chosen for this study was a fraction of the MTD (60 mg bid) and the RP2D (45 mg bid) determined for single agent use. The starting dose for ganitumab was 12 mg/kg q2w which had been shown to be a well-tolerated dose in combination with other anti-cancer agents.

Drug: MEK162Drug: AMG 479

Metastatic pancreatic adenocarcinoma

EXPERIMENTAL

Patients with metastatic pancreatic cancer. The starting dose (30 mg bid) of binimetinib chosen for this study was a fraction of the MTD (60 mg bid) and the RP2D (45 mg bid) determined for single agent use. The starting dose for ganitumab was 12 mg/kg q2w which had been shown to be a well-tolerated dose in combination with other anti-cancer agents.

Drug: MEK162Drug: AMG 479

BRAF mutated melanoma

EXPERIMENTAL

Patients with mutant BRAF V600 melanoma. The starting dose (30 mg bid) of binimetinib chosen for this study was a fraction of the MTD (60 mg bid) and the RP2D (45 mg bid) determined for single agent use. The starting dose for ganitumab was 12 mg/kg q2w which had been shown to be a well-tolerated dose in combination with other anti-cancer agents.

Drug: MEK162Drug: AMG 479

Interventions

MEK162DRUG

Supplied as tablets of dosage strength 15 mg in high-density polyethylene bottles with child-resistant closure.

Also known as: Binimetinib
BRAF mutated melanomaDose escalationKRAS mutated colorectal adenocarcinomaMetastatic pancreatic adenocarcinoma

Supplied as sterile liquid for intravenous infusion in vials in boxes. Until April 2013 a frozen formulation with a concentration of 30 mg/ml was used; from May 2013 onwards a refrigerated formulation with a concentration of 70 mg/ml was used.

Also known as: Ganitumab
BRAF mutated melanomaDose escalationKRAS mutated colorectal adenocarcinomaMetastatic pancreatic adenocarcinoma

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients aged ≥ 18 years
  • Patients with advanced solid tumors (CRC, melanoma) with documented somatic KRAS or BRAFV600 mutations in tumor tissue. Patients with metastatic pancreatic adenocarcinoma may be enrolled irrespectively of KRAS or BRAFV600 mutational status.
  • Patients must have relapsed or progressed following standard therapy or patients for whom no standard anticancer therapy exists.
  • Measurable disease as determined by RECIST v1.1. World Health Organization (WHO) Performance Status (PS) ≤ 2.
  • Adequate organ function
  • Negative serum pregnancy test

You may not qualify if:

  • Prior therapy with MEK- or IGF-1R- inhibitor
  • History or current evidence of central serous retinopathy (CSR), retinal vein occlusion (RVO) or retinal degenerative disease
  • Patients with known history of severe infusion reactions to monoclonal antibodies
  • Patients with primary CNS tumor or CNS tumor involvement
  • History of thromboembolic event requiring full-dose anticoagulation therapy
  • Clinically significant cardiac disease
  • History of another malignancy within 2 years
  • Pregnant or nursing (lactating) women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

Massachusetts General Hospital Mass General 2

Boston, Massachusetts, 02114, United States

Location

University of Utah / Huntsman Cancer Institute Huntsman

Salt Lake City, Utah, 84103, United States

Location

Pfizer Investigative Site

Parkville, Victoria, 3050, Australia

Location

Pfizer Investigative Site

Leuven, 3000, Belgium

Location

Pfizer Investigative Site

Toronto, Ontario, M5G 2M9, Canada

Location

Pfizer Investigative Site

Toulouse, 31059, France

Location

Pfizer Investigative Site

Napoli, 80131, Italy

Location

Pfizer Investigative Site

Barcelona, Catalonia, 08035, Spain

Location

Pfizer Investigative Site

Sutton, Surrey, SM2 5PT, United Kingdom

Location

MeSH Terms

Conditions

Melanoma

Interventions

binimetinibganitumab

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue Diseases

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 22, 2012

First Posted

March 26, 2012

Study Start

August 27, 2012

Primary Completion

April 1, 2015

Study Completion

April 1, 2015

Last Updated

December 10, 2020

Record last verified: 2020-12

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations