NCT01530997

Brief Summary

The purpose of this research study is to learn about the effectiveness of using lower-intensity radiation and chemotherapy to treat human papillomavirus (HPV) associated low-risk oropharyngeal and/or unknown primary squamous cell carcinomas of the head and neck. The cure rate for this type of cancer is estimated to be high, \> 90%. The standard treatment for this cancer is 7 weeks of radiation with 3 high doses of cisplatin. Sometimes surgery is performed afterwards. This standard regimen causes a lot of side effects and long term complications. This study is evaluating whether a lower dose of radiation and chemotherapy may provide a similar cure rate as the longer, more intensive standard regimen. Patients in this study will receive 1 less week of radiation and a lower weekly dose of chemotherapy followed by a limited surgical evaluation.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
45

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Feb 2012

Longer than P75 for phase_2

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 20, 2012

Completed
18 days until next milestone

Study Start

First participant enrolled

February 7, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 10, 2012

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2014

Completed
2.8 years until next milestone

Results Posted

Study results publicly available

August 9, 2017

Completed
2.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2019

Completed
Last Updated

November 13, 2024

Status Verified

November 1, 2024

Enrollment Period

2.7 years

First QC Date

January 20, 2012

Results QC Date

March 30, 2017

Last Update Submit

November 11, 2024

Conditions

Keywords

Human Papilloma VirusOropharynxOropharyngeal Squamous Cell CarcinomaSquamous Cell CarcinomaRadiation TherapyChemotherapyp16

Outcome Measures

Primary Outcomes (1)

  • Pathologic Complete Response Rate After De-escalated CRT in HPV-positive and/or p16 Positive Oropharyngeal Squamous Cell Carcinoma (OPSCC).

    Pathologic Complete Response Rate is defined as no evidence of residual viable cancer in the evaluated pathological specimens.

    6 to 14 weeks after the last patient is enrolled, or approximately 24 to 32 months after study being opened

Secondary Outcomes (9)

  • Two-Year Local Control

    Median follow-up was 36 months with a range of 5-53 months

  • Regional Control

    Median follow-up was 36 months with a range of 5-53 months

  • Cause-Specific Survival

    The median follow-up was 36 months with a range of 5-53 months

  • Distant Metastases Free Survival

    the median follow-up was 36 months with a range of

  • Overall Survival Rate

    Median follow-up was 36 months with a range of 5-53 months.

  • +4 more secondary outcomes

Study Arms (1)

De-escalated Radiation and Chemotherapy

EXPERIMENTAL

Patients will receive 54 to 60 Gy of Intensity Modulated Radiotherapy (IMRT) with concurrent weekly intravenous cisplatin (30 mg/m2). Diagnostic imaging (CT and/or MRI) will be obtained 4 to 8 weeks after completion of CRT to assess response. All patients will have surgical resection of any clinically apparent residual primary tumor or biopsy of the primary site if there is no evidence of residual tumor and will undergo a limited neck dissection to encompass at least those nodal level(s) that were positive pre-treatment, 4 to 14 weeks after CRT.

Radiation: Intensity Modulated Radiotherapy (IMRT)Drug: CisplatinProcedure: Limited surgical evaluation

Interventions

All patients will receive IMRT. Dose painting IMRT will be used and all doses will be specified to the planning target volume (PTV). The high risk planning target volume (PTV-HR) and standard risk planning target volume (PTV-SR) will be treated to the following respective total doses: 60 Gy and 54 Gy. The dose per fraction to the PTV-HR and PTV-SR will be 2 Gy per day and 1.8 Gy per day, respectively. The PTV-HR will include the gross tumor and the PTV-SR will include the lymph nodes at risk for harboring micro-metastatic disease (i.e. subclinical disease).

De-escalated Radiation and Chemotherapy

Cisplatin, 30mg/m2, will be given intravenously over 60 minutes weekly during IMRT; 6 total doses for a total of 180 mg/m2. It is preferred that the doses be administered on days 1, 8, 15, 22, and 29, and 36 of IMRT; however, this is not mandatory.

Also known as: Platinol
De-escalated Radiation and Chemotherapy

4 to 14 weeks after completion of CRT, patients will have at least a biopsy of the primary tumor and limited neck surgery to remove those lymph nodes that were involved with cancer prior to CRT.

De-escalated Radiation and Chemotherapy

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • ≥ 18 years of age
  • T0-3, N0 to N2c, M0 squamous cell carcinoma of the oropharynx
  • Biopsy proven squamous cell carcinoma that is HPV and/or p16 positive
  • ≤ 10 pack-years smoking history or \> 5 years of abstinence from smoking
  • History/physical examination within 8 weeks prior to registration
  • Radiologic confirmation of the absence of hematogenous metastasis within 12 weeks prior to registration.
  • The Eastern Cooperative Oncology Group (ECOG) Performance Status 0-1
  • Complete Blood Count (CBC)/differential obtained within 4 weeks prior to registration, with adequate bone marrow function defined as follows: Absolute neutrophil count (ANC) ≥ 1,800 cells/mm3; Platelets ≥ 100,000 cells/mm3; Hemoglobin ≥ 8.0 g/dl.
  • Adequate renal and hepatic function within 4 weeks prior to registration, defined as follows: Serum creatinine \< 2.0 mg/dl; Total bilirubin \< 2 x the institutional upper limit of normal (ULN); aspartate aminotransferase (AST) or alanine aminotransferase (ALT) \< 3 x the institutional ULN.
  • Negative serum pregnancy test within 2 weeks prior to registration for women of childbearing potential.
  • Women of childbearing potential and male participants who are sexually active must practice adequate contraception during treatment and for 6 weeks following treatment.
  • Patients must be deemed able to comply with the treatment plan and follow-up schedule.
  • Patients must provide study specific informed consent prior to study entry.

You may not qualify if:

  • Prior history of radiation therapy to the head and neck
  • Prior history of head and neck cancer.
  • Severe, active co-morbidity, defined as follows: Unstable angina and/or congestive heart failure requiring hospitalization within the last 6 months; Transmural myocardial infarction within the last 6 months; Acute bacterial or fungal infection requiring intravenous antibiotics at the time of registration; Chronic Obstructive Pulmonary Disease exacerbation or other respiratory illness requiring hospitalization or precluding study therapy at the time of registration; Hepatic insufficiency resulting in clinical jaundice and/or coagulation defects; Note, however, coagulation parameters are not required for entry into this protocol; Pre-existing ≥ grade 2 neuropathy; Prior organ transplant.
  • Known HIV positive
  • Significant pre-existing hearing loss, as defined by the patient or treating physician.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Penrose Cancer Center

Colorado Springs, Colorado, 80907, United States

Location

University of Florida, Department of Radiation Oncology

Gainesville, Florida, 32610-0385, United States

Location

University of North Carolina at Chapel Hill, Department of Radiation Oncology

Chapel Hill, North Carolina, 27599, United States

Location

Rex Healthcare

Raleigh, North Carolina, 27607, United States

Location

Rex Cancer Center of Wakefield

Raleigh, North Carolina, 27614, United States

Location

Related Publications (3)

  • Ang KK, Harris J, Wheeler R, Weber R, Rosenthal DI, Nguyen-Tan PF, Westra WH, Chung CH, Jordan RC, Lu C, Kim H, Axelrod R, Silverman CC, Redmond KP, Gillison ML. Human papillomavirus and survival of patients with oropharyngeal cancer. N Engl J Med. 2010 Jul 1;363(1):24-35. doi: 10.1056/NEJMoa0912217. Epub 2010 Jun 7.

    PMID: 20530316BACKGROUND
  • Mavroidis P, Price A, Fried D, Kostich M, Amdur R, Mendenhall W, Liu C, Das S, Marks LB, Chera B. Dose-volume toxicity modeling for de-intensified chemo-radiation therapy for HPV-positive oropharynx cancer. Radiother Oncol. 2017 Aug;124(2):240-247. doi: 10.1016/j.radonc.2017.06.020. Epub 2017 Jul 13.

  • Chera BS, Amdur RJ, Tepper J, Qaqish B, Green R, Aumer SL, Hayes N, Weiss J, Grilley-Olson J, Zanation A, Hackman T, Funkhouser W, Sheets N, Weissler M, Mendenhall W. Phase 2 Trial of De-intensified Chemoradiation Therapy for Favorable-Risk Human Papillomavirus-Associated Oropharyngeal Squamous Cell Carcinoma. Int J Radiat Oncol Biol Phys. 2015 Dec 1;93(5):976-85. doi: 10.1016/j.ijrobp.2015.08.033. Epub 2015 Aug 22.

Related Links

MeSH Terms

Conditions

Carcinoma, Squamous CellHead and Neck NeoplasmsOropharyngeal NeoplasmsSquamous Cell Carcinoma of Head and Neck

Interventions

Radiotherapy, Intensity-ModulatedCisplatin

Condition Hierarchy (Ancestors)

CarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsNeoplasms, Squamous CellNeoplasms by SitePharyngeal NeoplasmsOtorhinolaryngologic NeoplasmsPharyngeal DiseasesStomatognathic DiseasesOtorhinolaryngologic Diseases

Intervention Hierarchy (Ancestors)

Radiotherapy, ConformalRadiotherapy, Computer-AssistedRadiotherapyTherapeuticsChlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum Compounds

Limitations and Caveats

Per the protocol, affiliate sites will only report grade 3/4 and all fatal (grade 5) toxicities. 1/2 toxicities were not reported for affiliate sites.

Results Point of Contact

Title
Robin V. Johnson
Organization
UNC Lineberger Comprehensive Cancer Center

Study Officials

  • Bhishamjit Chera, MD

    University of North Carolina, Chapel Hill

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 20, 2012

First Posted

February 10, 2012

Study Start

February 7, 2012

Primary Completion

November 1, 2014

Study Completion

November 1, 2019

Last Updated

November 13, 2024

Results First Posted

August 9, 2017

Record last verified: 2024-11

Locations