NCT01478594

Brief Summary

The objective of this study is to compare the progression free survival (PFS), overall survival (OS), objective response rate (ORR), time to treatment failure (TTF), duration of response (DoR), quality of life, safety and tolerability of tivozanib in combination with mFOLFOX6 and bevacizumab in combination with mFOLFOX6.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
265

participants targeted

Target at P75+ for phase_2 colorectal-cancer

Timeline
Completed

Started Dec 2011

Geographic Reach
11 countries

65 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 21, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 23, 2011

Completed
8 days until next milestone

Study Start

First participant enrolled

December 1, 2011

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2013

Completed
1.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2015

Completed
3 months until next milestone

Results Posted

Study results publicly available

April 3, 2015

Completed
Last Updated

July 8, 2015

Status Verified

June 1, 2015

Enrollment Period

1.8 years

First QC Date

November 21, 2011

Results QC Date

February 19, 2015

Last Update Submit

June 9, 2015

Conditions

Keywords

metastatic colorectal cancerAvastinbevacizumabtivozanibmFOLFOX6BATON-CRCAV951ASP4130

Outcome Measures

Primary Outcomes (1)

  • Investigator-assessed Progression-Free Survival (PFS)

    The time from the date of randomization until objective tumor progression or death due to any cause. Objective tumor progression was determined through radiological imaging and based on the requirements of the Response Evaluation Criteria in Solid Tumors (RECIST Version 1.1): Progressive Disease (PD): At least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study and an absolute increase of at least 5 mm, or unequivocal progression of existing non-target lesions or the appearance of one or more new lesions. Participants who did not progress or had not died at the time of the analysis were censored at the date of last tumor assessment where non-progression was documented.

    From randomization until the analysis cut-off date of 13 September 2013; median time on study drug was 167 days in the tivozanib group and 162 days in the bevacizumab group.

Secondary Outcomes (20)

  • Progression-Free Survival (PFS) Based on Independent Radiological Review (IRR)

    3 years

  • Overall Survival (OS)

    From randomization until the analysis cut-off date of 13 September 2013; median time on study drug was 167 days in the tivozanib group and 162 days in the bevacizumab group.

  • Objective Response Rate (ORR)

    From randomization until the analysis cut-off date of 13 September 2013; median time on study drug was 167 days in the tivozanib group and 162 days in the bevacizumab group.

  • Duration of Response (DoR)

    From randomization until the analysis cut-off date of 13 September 2013; median time on study drug was 167 days in the tivozanib group and 162 days in the bevacizumab group.

  • Time to Treatment Failure (TTF)

    From randomization until the analysis cut-off date of 13 September 2013; median time on study drug was 167 days in the tivozanib group and 162 days in the bevacizumab group.

  • +15 more secondary outcomes

Study Arms (2)

Tivozanib + mFOLFOX6

EXPERIMENTAL

Participants received 1.5 mg of tivozanib orally once daily beginning on Day 1 of each cycle for 21 days followed by 7 days off treatment. Participants also received modified FOLFOX6 (mFOLFOX6) chemotherapy every 2 weeks on Days 1 and 15 of each cycle.

Drug: TivozanibDrug: mFOLFOX6

Bevacizumab + mFOLFOX6

ACTIVE COMPARATOR

Participants received a dose of 5 mg/kg bevacizumab via intravenous infusion every 2 weeks on Days 1 and 15 of each cycle. Participants also received mFOLFOX6 chemotherapy every 2 weeks on Days 1 and 15 of each cycle.

Drug: BevacizumabDrug: mFOLFOX6

Interventions

Capsules for oral administration

Also known as: AV951, ASP4130
Tivozanib + mFOLFOX6

Solution for intravenous infusion

Also known as: Avastin
Bevacizumab + mFOLFOX6

mFOLFOX6 regimen is a combination therapy of oxaliplatin 85 mg/m\^2 administered as an intravenous bolus over 2 hours on Days 1 and 15, leucovorin calcium 400 mg/m\^2 administered as an intravenous bolus over 2 hours on Days 1 and 15, fluorouracil 400 mg/m\^2 administered as an intravenous bolus over 5 to 15 minutes on Days 1 and 15, then 2400 mg/m\^2 continuous intravenous infusion over 46 hours on Days 1 to 3 and 15 to 17.

Bevacizumab + mFOLFOX6Tivozanib + mFOLFOX6

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Documented diagnosis of metastatic colorectal cancer
  • One measurable lesion per Response Evaluation Criteria in Solid Tumors (RECIST) 1.1
  • No prior systemic chemotherapy for advanced colorectal cancer; no fluorouracil containing adjuvant therapy in previous 6 months
  • Eastern Cooperative Oncology Group (ECOG) status of 0 or 1

You may not qualify if:

  • Any prior Vascular Endothelial Growth Factor (VEGF)-directed therapy or any other agent or investigational agent targeting the VEGF pathway
  • Primary Central Nervous System (CNS) malignancies or CNS metastases
  • Hematologic abnormalities:
  • Hemoglobin \< 9.0 g/dL,
  • Absolute neutrophil count (ANC) \< 2000 per mm\^3,
  • Platelet count \< 100,000 per mm\^3,
  • Prothrombin (PT) or Partial Thromboplastin Time (PTT) \> 1.5 X Upper Limit of Normal (ULN)
  • Serum chemistry abnormalities:
  • Total bilirubin \> 1.5 X ULN,
  • Aspartate aminotransferase (AST) or Alanine Aminotransferase (ALT) \> 2.5 X ULN,
  • Alkaline phosphatase \> 2.5 X ULN,
  • Serum albumin \< 2.0 g/dL,
  • Creatinine \> 1.5 X ULN,
  • Proteinuria \> 2+ by urine dipstick
  • Significant cardiovascular disease
  • +16 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (73)

Banner MD Anderson Cancer Research Center

Gilbert, Arizona, 85234, United States

Location

Genesis Cancer Center

Hot Springs, Arizona, 71913, United States

Location

Arizona Clinical Research Center

Tucson, Arizona, 85715, United States

Location

University of California San Diego-Morris Cancer Center

La Jolla, California, 92093, United States

Location

UC Irvine Medical Center, Division of Hematology/Oncology

Orange, California, 92868, United States

Location

Desert Hematology Oncology Medical Group, Inc.

Rancho Mirage, California, 92270, United States

Location

Mountain Blue Cancer Care Center

Golden, Colorado, 80033, United States

Location

University of Florida, Davis Cancer Center (VA)

Gainesville, Florida, 32610, United States

Location

Cleveland Clinic Florida

Weston, Florida, 33331, United States

Location

Queen's Medical Center

Honolulu, Hawaii, 96813, United States

Location

University of Hawaii

Honolulu, Hawaii, 96813, United States

Location

Kaiser Foundation Hospitals

Honolulu, Hawaii, 96819, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Illinios Cancer Care

Peoria, Illinois, 61615, United States

Location

Investigative Clinical Research of Indiana, LLC

Indianapolis, Indiana, 46260, United States

Location

Horizon Oncology Research, Inc.

Lafayette, Indiana, 47905, United States

Location

Associates of Oncology Hematology, P.C.

Rockville, Maryland, 20850, United States

Location

University of Michigan Health

Ann Arbor, Michigan, 48109, United States

Location

NYU Cancer Institute

New York, New York, 10016, United States

Location

Alamance Regional Medical Center

Burlington, North Carolina, 27215, United States

Location

Tri Country Hematology / Oncology

Canton, Ohio, 44718, United States

Location

Signal Point Clinical Research Center, LLC

Middletown, Ohio, 45042, United States

Location

Cancer Care Associates

Tulsa, Oklahoma, 74136, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Oncology Hematology of Lehigh Valley

Bethlehem, Pennsylvania, 18015, United States

Location

Northern Utah Associates

Ogden, Utah, 84403, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

St George Hospital

Kogarah, New South Wales, 2217, Australia

Location

Tweed Hospital

Tweed Heads, New South Wales, 2485, Australia

Location

Calvary Mater Newcastle

Waratah, New South Wales, 2298, Australia

Location

Flinders Medical Centre

Bedford Park, South Australia, 5042, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Ballarat Health Services

Ballarat, Victoria, 3350, Australia

Location

Cabrini Hospital Malvern

Malvern, Victoria, 3144, Australia

Location

Border Medical Oncology

Wodonga, Victoria, 3690, Australia

Location

Medizinische Universitat Graz

Graz, 8036, Austria

Location

Salzburger Landesklinken

Salzburg, 5020, Austria

Location

Klinikum Wels-Grieskirchen GmbH

Wels, 4600, Austria

Location

Ziekenhuisnetwerk Antwerpen - AZ Middelheim

Antwerp, 2020, Belgium

Location

Imelda VZW

Bonheiden, 2820, Belgium

Location

AZ Sint-Lucas Brugge

Bruges, 8310, Belgium

Location

AZ Groeninge - Campus Sint-Niklaas

Kortrijk, 8500, Belgium

Location

British Columbia Cancer Agency

Vancouver, British Columbia, V5Z 4E6, Canada

Location

QEII Health Science Centre

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

Hopital De La Cite-De-La-Sante

Laval, Quebec, H7M 3L9, Canada

Location

Hopital Saint-Luc - Pavillon Principal

Montreal, Quebec, H2X 3J4, Canada

Location

Chuq Centre Hospitalier Universitaire De Quebec

Québec, Quebec, G1R 2J6, Canada

Location

Masarykuv onkologicky ustav

Brno, 656 53, Czechia

Location

Fakultni nemocnice Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

Tampereen yliopistollinen sairaala

Tampere, FI-33520, Finland

Location

Turun yliopistollinen keskussairaala

Turku, FI-20520, Finland

Location

Orszagos Onkologiai Intezet

Budapest, 1122, Hungary

Location

Petz Aladar Megyei Oktato Korhaz

Győr, 9024, Hungary

Location

Bekes Megyei Kepviselotestulet Pandy Kalman Korhaza

Gyula, 5700, Hungary

Location

Fejer Megyei Szent Gyorgy Korhaz

Székesfehérvár, 8000, Hungary

Location

Azienda Ospedaliero- Universitaria di Bologna - Policlinico S.Orsola-Malpighi

Bologna, 40128, Italy

Location

Fondazione del Piemonte per I'Oncologia IRCC

Candiolo, 10060, Italy

Location

IRCCS Azienda Ospedaliera Universitaria San Martino - Istituto Nazionale per la Ricerca sul Cancro

Genova, 16132, Italy

Location

Istituto Clinico Humanitas

Rozzano (MI), 20089, Italy

Location

Amphia Ziekenhuis

Breda, 4819 EV, Netherlands

Location

Hospital Universitario Miguel Servet

Zaragoza, Aragon, 50009, Spain

Location

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, 39008, Spain

Location

Corporacio Sanitaria Parc Tauli

Sabadell, Catalonia, 08208, Spain

Location

Hospital Mutua de Terrassa

Terrassa, Catalonia, 08221, Spain

Location

Centro Oncologico de Galicia

Galicia, 15009, Spain

Location

Centro Integral Oncologico Clara Campal

Madrid, 28050, Spain

Location

Addenbrooke's Hospital

Cambridge, CB2 2QQ, United Kingdom

Location

Western General Hospital

Edinburgh, EH4 2XU, United Kingdom

Location

Beatson West of Scotland Cancer Center

Glasgow, G12 0YN, United Kingdom

Location

University College Hospital

London, NW1 2BU, United Kingdom

Location

Maidstone Hospital

Maidstone, ME16 9QQ, United Kingdom

Location

Christie Hospital

Manchester, M20 4BX, United Kingdom

Location

Peterborough and Stamford Hospitals NHS Foundation Trust

Peterborough, PE3 6DA, United Kingdom

Location

MeSH Terms

Conditions

Colorectal Neoplasms

Interventions

tivozanibBevacizumab

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Medical Director
Organization
AVEO

Study Officials

  • Medical Director

    AVEO Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 21, 2011

First Posted

November 23, 2011

Study Start

December 1, 2011

Primary Completion

September 1, 2013

Study Completion

January 1, 2015

Last Updated

July 8, 2015

Results First Posted

April 3, 2015

Record last verified: 2015-06

Locations