NCT01460160

Brief Summary

The purpose of this study is to determine whether Dasatinib when added to standard chemotherapy is effective and safe in the treatment of pediatric philadelphia chromosome positive acute lymphoblastic leukemia

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
106

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Apr 2012

Longer than P75 for phase_2

Geographic Reach
6 countries

128 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 25, 2011

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 26, 2011

Completed
6 months until next milestone

Study Start

First participant enrolled

April 13, 2012

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 28, 2017

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

August 21, 2018

Completed
2.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2021

Completed
Last Updated

December 8, 2021

Status Verified

November 1, 2021

Enrollment Period

5.1 years

First QC Date

October 25, 2011

Results QC Date

May 25, 2018

Last Update Submit

November 8, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • 3-year Event-free Survival (EFS) Rate

    3-year EFS rate is defined as the percentage of participants without event after 3 years since the start of study treatment. Events for EFS are defined as ANY first one of the following: * Lack of complete response in bone marrow * Relapse at any site * Development of second malignant neoplasm * Death from any cause

    From first dose to 3 years following first dose

Secondary Outcomes (5)

  • Number of Participants Experiencing Adverse Events

    From first dose to 100 days following last dose (up to approximately 23 months)

  • Event-Free Survival (EFS) Rate (Kaplan-Meier Estimates)

    From first dose to 3 years or 5 years following first dose

  • Complete Remission Rate

    From first dose to End of Induction Period Ia (up to 5 weeks) or Ib (up to 9 weeks) or End of Consolidation Period (up to 22 weeks)

  • Percentage of Participants Negative for Minimal Residual Disease (MRD)

    From first dose to End of Induction Period Ia (up to 5 weeks) or Ib (up to 9 weeks) or End of Consolidation Period (up to 22 weeks)

  • Percentage of Participants With BCR-ABL Mutations at Baseline and at Time of Disease Progression or Relapse

    At baseline (prior to start of study treatment) and at disease progression or relapse (up to approximately 3 years)

Study Arms (1)

Arm 1: Dasatinib

EXPERIMENTAL
Drug: Dasatinib

Interventions

Tablets, Oral, 60 mg/m2, Once daily, 2 years or until unacceptable toxicity

Also known as: Sprycel
Arm 1: Dasatinib

Eligibility Criteria

Age1 Year - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Newly diagnosed Philadelphia chromosome positive Acute Lymphoblastic Leukemia (ALL)
  • Age \>1 year and \< less than 18 years old
  • Induction chemotherapy ≤ 14 days according to institutional standard of care
  • Adequate liver, renal and cardiac function

You may not qualify if:

  • Prior treatment with a Oncogene fusion protein (BCR-ABL) inhibitor
  • Extramedullary involvement of the testicles
  • Active systemic bacterial, fungal or viral infection
  • Down syndrome

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (128)

University Of Alabama At Birmingham

Birmingham, Alabama, 35233, United States

Location

Phoenix Children'S Hospital/Ctr. For Cancer & Blood Ctr.

Phoenix, Arizona, 85016, United States

Location

University Of Arkansas For Medical Sciences

Little Rock, Arkansas, 72202, United States

Location

Antranik Agop Bedros

Loma Linda, California, 92350, United States

Location

Miller Children's and Women Hospital

Long Beach, California, 90806, United States

Location

Children'S Hospital Of L.A.

Los Angeles, California, 90027, United States

Location

Southern California Permanente Medical Group

Los Angeles, California, 90027, United States

Location

Valley Children's Hospital

Madera, California, 93636, United States

Location

Children's Hospital of Orange County

Orange, California, 92868, United States

Location

Lpch & Sumc

Palo Alto, California, 94304, United States

Location

Kaiser Medical Center

Roseville, California, 95661, United States

Location

Ucsf - Hematology/Oncology

San Francisco, California, 94143-0106, United States

Location

Children'S Hospital Colorado

Aurora, Colorado, 80045, United States

Location

Connecticut Children's Medical Center

Hartford, Connecticut, 06106, United States

Location

A. I. Dupont Hospital For Children

Wilmington, Delaware, 19803, United States

Location

Children'S National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Lee Memorial Health System

Fort Myers, Florida, 33908, United States

Location

University Of Florida

Gainesville, Florida, 32610, United States

Location

Nemours Children'S Clinic

Jacksonville, Florida, 32207, United States

Location

Md Anderson Cancer Center Orlando

Orlando, Florida, 32806, United States

Location

Nemours Childrens Hospital

Orlando, Florida, 32827, United States

Location

All Children'S Hospital

St. Petersburg, Florida, 33629, United States

Location

St. Joseph's Children's Hospital

Tampa, Florida, 33607, United States

Location

St. Mary'S

West Palm Beach, Florida, 33407, United States

Location

Children's Healthcare Of Atlanta

Atlanta, Georgia, 30322, United States

Location

Kapiolani Medical Center For Women & Children

Honolulu, Hawaii, 96826, United States

Location

Mountain States Tumor Institute

Boise, Idaho, 83712, United States

Location

Ann & Robert H Lurie Children's Hospital Of Chicago

Chicago, Illinois, 60611, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Southern Illinois University School Of Medicine

Springfield, Illinois, 62794-9635, United States

Location

James Whitcomb Riley Hospital For Children

Indianapolis, Indiana, 46202-5225, United States

Location

Children'S Center For Cancer And Blood Diseases

Indianapolis, Indiana, 46260, United States

Location

University Of Kentucky

Lexington, Kentucky, 40536-0284, United States

Location

Norton Children's Hospital

Louisville, Kentucky, 40202, United States

Location

Sinai Hospital Of Baltimore

Baltimore, Maryland, 21215, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21231, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

UMass Memorial Medical Center

Worcester, Massachusetts, 01655, United States

Location

Children'S Hospital Of Michigan

Detroit, Michigan, 48201, United States

Location

Helen Devos Children'S Hospital

Grand Rapids, Michigan, 49503, United States

Location

Michigan State University

Lansing, Michigan, 48912, United States

Location

Childrens Hospitals And Clinics Of Minnesota

Minneapolis, Minnesota, 55404, United States

Location

Univ Of Mississippi Med Ctr

Jackson, Mississippi, 39216, United States

Location

University Of Missouri Health Care

Columbia, Missouri, 65212, United States

Location

Children'S Mercy Hospital And Clinics

Kansas City, Missouri, 64108, United States

Location

Washington University Medical Center

St Louis, Missouri, 63110, United States

Location

Children'S Specialty Center Of Nevada

Las Vegas, Nevada, 89109, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Goryeb Children'S Hospital

Morristown, New Jersey, 07962, United States

Location

The Cancer Institute Of New Jersey

New Brunswick, New Jersey, 08901, United States

Location

Newark Beth Israel Medical Center

Newark, New Jersey, 07112, United States

Location

St. Joseph's Regional Medical Center

Paterson, New Jersey, 07503, United States

Location

University Of New Mexico

Albuquerque, New Mexico, 87131-0001, United States

Location

New York University

New York, New York, 10016, United States

Location

The Herbert Irving Pavilion

New York, New York, 10032, United States

Location

New York Presbyterian/Weill Cornell

New York, New York, 10065, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

New York Medical College

Valhalla, New York, 10595, United States

Location

Levine Children's Hospital

Charlotte, North Carolina, 28203, United States

Location

Wake Forest University

Winston-Salem, North Carolina, 27157-1081, United States

Location

Cincinnati Children'S Hospital Medical Center

Cincinnati, Ohio, 45229-3039, United States

Location

Nationwide Children'S Hospital

Columbus, Ohio, 43205, United States

Location

The Children'S Medical Center Of Dayton

Dayton, Ohio, 45404-1815, United States

Location

The Toledo Children'S Hospital

Toledo, Ohio, 43606, United States

Location

Mercy Children's Hospital

Toledo, Ohio, 43608, United States

Location

University Of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Legacy Emanuel Hospital & Health Center

Portland, Oregon, 97227, United States

Location

Oregon Health & Sci Univ

Portland, Oregon, 97239, United States

Location

Geisinger Medical Center

Danville, Pennsylvania, 17822-1320, United States

Location

Penn State Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Children'S Hospital Of Philadelphia

Philadelphia, Pennsylvania, 19104-4318, United States

Location

Children's Hospital Of Pittsburgh Of UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

East Tennessee Children'S Hosp

Knoxville, Tennessee, 37916, United States

Location

Vanderbilt University

Nashville, Tennessee, 37232-6310, United States

Location

Dell Children'S Medical Center Of Central Texas

Austin, Texas, 78723, United States

Location

Driscoll Children'S Hospital

Corpus Christi, Texas, 78411, United States

Location

Ut Southwestern

Dallas, Texas, 75390-9063, United States

Location

Cook Children'S Hem/Onc Center

Fort Worth, Texas, 76104, United States

Location

Texas Children'S Cancer Center

Houston, Texas, 77030, United States

Location

Scott & White - McLane Children's Specialty Clinic

Temple, Texas, 76508, United States

Location

Primary Children's Medical Center

Salt Lake City, Utah, 84113, United States

Location

Inova Pediatric Specialty Center Ii

Fairfax, Virginia, 22031, United States

Location

Children'S Hosp-Kings Daughter

Norfolk, Virginia, 23507, United States

Location

Seattle Children'S

Seattle, Washington, 98105, United States

Location

St Vincent Hospital

Green Bay, Wisconsin, 54301, United States

Location

Kenneth Desantes, Md

Madison, Wisconsin, 53705-2275, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Local Institution

Sth Brisbane, Queensland, 4101, Australia

Location

Local Institution

Parkville, Victoria, 3052, Australia

Location

Local Institution

Nedlands, Western Australia, 6009, Australia

Location

Alberta Children'S Hospital

Calgary, Alberta, T3B 6A8, Canada

Location

Stollery Children'S Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

Local Institution

London, Ontario, N6A 5W9, Canada

Location

Children'S Hospital Of Eastern Ontario

Ottawa, Ontario, K1H 8L1, Canada

Location

Chu Ste-Justine

Montreal, Quebec, H3T 1C5, Canada

Location

The Montreal Children's Hospital of the MUHC

Montreal, Quebec, H4A 3J1, Canada

Location

Local Institution

Saskatoon, Saskatchewan, S7N 4H4, Canada

Location

Local Institution

Bologna, 40138, Italy

Location

Local Institution

Cagliari, 09121, Italy

Location

Local Institution

Catania, 95123, Italy

Location

Local Institution

Florence, 50139, Italy

Location

Local Institution

Genova, 16147, Italy

Location

Local Institution

Monza, 20900, Italy

Location

Local Institution

Napoli, 80123, Italy

Location

Local Institution

Palermo, 90134, Italy

Location

Local Institution

Roma, 00161, Italy

Location

Local Institution

Roma, 00165, Italy

Location

Local Institution

Torino, 10126, Italy

Location

Local Institution

Trieste, 34137, Italy

Location

Local Institution

San Juan, 00912, Puerto Rico

Location

Local Institution

Bristol, Avon, BS2 8BJ, United Kingdom

Location

Local Institution

Cardiff, Glamorgan, CF14 4XW, United Kingdom

Location

Local Institution

Aberdeen, Grampian, AB25 2ZG, United Kingdom

Location

Local Institution

London, Greater London, WC1N3JH, United Kingdom

Location

Local Institution

Manchester, Greater Manchester, M27 4HA, United Kingdom

Location

Local Institution

Southampton, Hampshire, SO9 4XY, United Kingdom

Location

Local Institution

Glasgow, Lanarkshire, G3 8SJ, United Kingdom

Location

Local Institution

Edinburgh, Lothian, EH9 1LF, United Kingdom

Location

Local Institution

Liverpool, Merseyside, L12 2AP, United Kingdom

Location

Local Institution

Leeds, North Yorkshire, LS1 3EX, United Kingdom

Location

Local Institution

Nottingham, Nottinghamshire, NG7 2UH, United Kingdom

Location

Local Institution

Oxford, Oxfordshire, OX 39DU, United Kingdom

Location

Local Institution

Sheffield, South Yorkshire, S10 2TH, United Kingdom

Location

Local Institution

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Local Institution

Newcastle upon Tyne, Tyne and Wear, NE1 4LP, United Kingdom

Location

Local Institution

Birmingham, West Midlands, B4 6NH, United Kingdom

Location

Local Institution

Cambridge, CB2 2QQ, United Kingdom

Location

Related Publications (2)

  • Hunger SP, Tran TH, Saha V, Devidas M, Valsecchi MG, Gastier-Foster JM, Cazzaniga G, Reshmi SC, Borowitz MJ, Moorman AV, Heerema NA, Carroll AJ, Martin-Regueira P, Loh ML, Raetz EA, Schultz KR, Slayton WB, Cario G, Schrappe M, Silverman LB, Biondi A. Dasatinib with intensive chemotherapy in de novo paediatric Philadelphia chromosome-positive acute lymphoblastic leukaemia (CA180-372/COG AALL1122): a single-arm, multicentre, phase 2 trial. Lancet Haematol. 2023 Jul;10(7):e510-e520. doi: 10.1016/S2352-3026(23)00088-1.

  • Tasian SK, Peters C. Targeted therapy or transplantation for paediatric ABL-class Ph-like acute lymphocytic leukaemia? Lancet Haematol. 2020 Dec;7(12):e858-e859. doi: 10.1016/S2352-3026(20)30369-0. No abstract available.

Related Links

MeSH Terms

Conditions

Leukemia

Interventions

Dasatinib

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

ThiazolesSulfur CompoundsOrganic ChemicalsAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidines

Results Point of Contact

Title
Bristol-Myers Squibb Study Director
Organization
Bristol-Myers Squibb

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 25, 2011

First Posted

October 26, 2011

Study Start

April 13, 2012

Primary Completion

May 28, 2017

Study Completion

June 1, 2021

Last Updated

December 8, 2021

Results First Posted

August 21, 2018

Record last verified: 2021-11

Locations