NCT00777036

Brief Summary

The purpose of this study is to determine whether dasatinib is safe and effective in children and adolescents with newly diagnosed chronic myeloid leukemia (CML), or in children with Ph+ acute lymphoblastic leukemia (ALL), accelerated or blast phases CML who relapse after imatinib or who are resistant or intolerant to imatinib. The side effects of this oral investigational drug in children and adolescents will be evaluated

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
133

participants targeted

Target at P75+ for phase_2 leukemia

Timeline
Completed

Started Mar 2009

Longer than P75 for phase_2 leukemia

Geographic Reach
18 countries

174 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 21, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 22, 2008

Completed
5 months until next milestone

Study Start

First participant enrolled

March 20, 2009

Completed
7.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2016

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

January 5, 2018

Completed
7.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 27, 2025

Completed
Last Updated

August 29, 2025

Status Verified

August 1, 2025

Enrollment Period

7.5 years

First QC Date

October 21, 2008

Results QC Date

December 6, 2017

Last Update Submit

August 12, 2025

Conditions

Keywords

Leukemia, Pediatric

Outcome Measures

Primary Outcomes (3)

  • Major Cytogenetic Response (MCyR) Rate

    Major Cytogenetic Response (MCyR) rate is defined as the proportion of all treated participants who achieved a complete (0%) or partial (1%-35% Ph+ metaphases in at least 20 metaphases in bone marrow) cytogenetic response, expressed as percentage. The denominator of the MCyR response rate consists of all treated participants in Cohort 1, and the numerator is all participants in Cohort 1 achieving MCyR. 95% confidence interval was calculated by Clopper-Pearson exact method.

    From first dose of study therapy until 30 days after last dose (Assessed up to September 2016, approximately 90 months)

  • Complete Hematologic Response (CHR) Rate

    Complete Hematologic Response (CHR) rate is defined as the proportion of all treated participants who achieve a confirmed CHR while on-study, expressed as percentage. CHR is defined as including no more than 5% blasts in bone marrow and normal white blood cell count without blasts in peripheral blood, expressed as percentage. The denominator of the CHR response rate consists of all treated participants in Cohort 2, and the numerator is all participants in Cohort 2 achieving CHR. 95% confidence interval was calculated by Clopper-Pearson exact method.

    From first dose of study therapy until 30 days after last dose (Assessed up to September 2016, approximately 90 months)

  • Complete Cytogenetic Response (CCyR) Rate

    Complete Cytogenetic Response (CCyR) rate is defined as the proportion of all treated participants who achieve a CCyR while on-study, expressed as a percentage. CCyR rate is defined as 0% Ph+ metaphases in at least 20 metaphases in bone marrow. The denominator of the CCyR response rate consists of all treated participants in Cohort 3, and the numerator is all participants in Cohort 3 achieving CCyR. 95% confidence interval was calculated by Clopper-Pearson exact method.

    From first dose of study therapy until 30 days after last dose (Assessed up to September 2016, approximately 90 months)

Secondary Outcomes (18)

  • Major Cytogenetic Response (MCyR) Rate in Cohort 2

    From first dose of study therapy until 30 days after last dose (Assessed up to September 2016, approximately 90 months)

  • Complete Hematologic Response (CHR) Rate in Cohorts 1 and 3

    From first dose of study therapy until 30 days after last dose (Assessed up to September 2016, approximately 90 months)

  • Rate of Best Cytogenetic Response

    From first dose of study therapy until 30 days after last dose (Assessed up to September 2016, approximately 90 months)

  • Time to Major Cytogenetic Response (MCyR)

    From first dose until MCyR criteria are met (assessed up to September 2016, approximately 90 months)

  • Duration of Major Cytogenetic Response (MCyR)

    From first day criteria are met for MCyR until the date PD is reported or death (assessed up to September 2016, approximately 90 months)

  • +13 more secondary outcomes

Study Arms (3)

Cohort 1: Imatinib-resistant/intolerant CP-CML

EXPERIMENTAL

Dasatinib 60 mg/m² tablet every day (QD) \[with a maximum dose of 100 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit OR Dasatinib 72 mg/m² powder for oral suspension (PFOS) QD \[with a maximum dose of 120 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

Drug: Dasatinib

Cohort 2: Ph+ALL or AP- or BP-CML

EXPERIMENTAL

Dasatinib 80 mg/m² tablet QD \[with a maximum dose of 140 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit OR Dasatinib 96 mg/m² PFOS QD \[with a maximum dose of 170 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

Drug: Dasatinib

Cohort 3: Newly diagnosed, treatment naïve CP-CML

EXPERIMENTAL

Dasatinib 60 mg/m² tablet QD \[with a maximum dose of 100 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit OR Dasatinib 72 mg/m² PFOS QD \[with a maximum dose of 120 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

Drug: Dasatinib

Interventions

Also known as: Sprycel (BMS-354825)
Cohort 1: Imatinib-resistant/intolerant CP-CMLCohort 2: Ph+ALL or AP- or BP-CMLCohort 3: Newly diagnosed, treatment naïve CP-CML

Eligibility Criteria

Age1 Day - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • CP-CML who prove resistant or intolerant to imatinib (Cohort 1)
  • Ph+ ALL, AP-CML, or BP-CML who are resistant or intolerant to or who relapse after imatinib therapy (Cohort 2)
  • Newly diagnosed, treatment naive CP-CML (Cohort 3)
  • Lansky or Karnofsky scale \>50
  • Life expectancy ≥12 weeks
  • Adequate hepatic and renal function
  • Written informed consent
  • Target Population for the PK substudy must obtain written informed consent from subject, or from parents or legal guardians for minor subjects, according to local law and regulation
  • Target Population for the PK substudy subjects must have CP-CML and be taking daily dasatinib (tablets or PFOS) either as part of Cohort 1 or Cohort 3 of this protocol. Patients receiving commercial dasatinib tablets outside of this protocol may be invited to participate in this PK substudy
  • Target Population for the PK substudy subjects with CP-CML who are tolerating dasatinib tablet dose of at least 60 mg/m2 or dasatinib PFOS dose of at least 72 mg/m2
  • Target Population for the PK substudy prior exposure to imatinib or other TKI therapy is permissible

You may not qualify if:

  • Eligibility for potentially-curative therapy including hematopoietic stem-cell transplantation
  • Symptomatic CNS involvement (other than signs and symptoms caused by leptomeningeal disease)
  • Isolated extramedullary disease
  • Prior therapy with Dasatinib
  • Target Population for the PK substudy subjects are not allowed to use proton pump inhibitors, H2 antagonists, CYP3A4 inhibitors and inducers when entering the PK substudy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (174)

Local Institution

Birmingham, Alabama, 35233, United States

Location

Local Institution - 0005

Phoenix, Arizona, 85016, United States

Location

Phoenix Children'S Hospital

Phoenix, Arizona, 85016, United States

Location

Jonathan Jaques Children'S Cancer Center

Long Beach, California, 90801-1428, United States

Location

Jonathan Jaques Children'S Cancer Center

Long Beach, California, 90806, United States

Location

Local Institution - 0001

Long Beach, California, 90806, United States

Location

Children'S Hospital Of Orange County

Orange, California, 92868, United States

Location

Local Institution - 0024

Orange, California, 92868, United States

Location

Children'S Hospital

Aurora, Colorado, 80045, United States

Location

Local Institution - 0004

Aurora, Colorado, 80045, United States

Location

Children's Healthcare Of Atlanta - Egleston

Atlanta, Georgia, 30322, United States

Location

Local Institution - 047

Atlanta, Georgia, 30322, United States

Location

Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

Location

Local Institution - 0072

Chicago, Illinois, 60611, United States

Location

Local Institution

Chicago, Illinois, 60611, United States

Location

Dana Faber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Dana Farber Cancer Institute.

Boston, Massachusetts, 02215, United States

Location

Local Institution - 0040

Boston, Massachusetts, 02215, United States

Location

Stephen D. Hassenfeld Children'S Center

New York, New York, 10016, United States

Location

Local Institution - 0061

New York, New York, 10021, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Memorial Sloan Kettering Nassau

New York, New York, 10065, United States

Location

Oregon Health & Sci Univ

Portland, Oregon, 97239-3098, United States

Location

Local Institution - 0002

Portland, Oregon, 97239, United States

Location

Oregon Health & Sci Univ

Portland, Oregon, 97239, United States

Location

Children'S Hospital Of Philadelphia

Philadelphia, Pennsylvania, 19104-4318, United States

Location

Local Institution - 0014

Philadelphia, Pennsylvania, 19104-4318, United States

Location

Children'S Hospital Of Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

Location

Local Institution - 0003

Pittsburgh, Pennsylvania, 15224, United States

Location

Local Institution - 0035

Houston, Texas, 77030-4009, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030-4009, United States

Location

Local Institution - 0048

Houston, Texas, 77030, United States

Location

Texas Children'S Cancer Center

Houston, Texas, 77030, United States

Location

Local Institution - 0028

Seattle, Washington, 98105, United States

Location

Seattle Children'S

Seattle, Washington, 98105, United States

Location

Local Institution - 0043

Bunos Aires, Buenos Aires, 1425, Argentina

Location

Local Institution

Bunos Aires, Buenos Aires, 1425, Argentina

Location

Hospital Nacional Profesor Alejandro Posadas

El Palomar, Buenos Aires, 1684, Argentina

Location

Local Institution - 0049

El Palomar, Buenos Aires, 1684, Argentina

Location

Local Institution - 0042

Córdoba, 5016, Argentina

Location

Local Institution

Córdoba, 5016, Argentina

Location

Local Institution - 065

Randwick, New South Wales, 2031, Australia

Location

Local Institution

Randwick, New South Wales, 2031, Australia

Location

Local Institution - 069

Westmead, New South Wales, 2145, Australia

Location

Local Institution

Westmead, New South Wales, 2145, Australia

Location

Local Institution - 0064

Sth Brisbane, Queensland, 4101, Australia

Location

Local Institution

Sth Brisbane, Queensland, 4101, Australia

Location

Local Institution - 067

North Adelaide, South Australia, 5006, Australia

Location

Local Institution

North Adelaide, South Australia, 5006, Australia

Location

Local Institution - 0066

Parkville, Victoria, 3052, Australia

Location

Local Institution

Parkville, Victoria, 3052, Australia

Location

Local Institution - 0021

Curitiba, Paraná, 80060-900, Brazil

Location

Local Institution

Curitiba, Paraná, 80060-900, Brazil

Location

Local Institution - 0022

Porto Alegre, Rio Grande do Sul, 90035-003, Brazil

Location

Local Institution

Porto Alegre, Rio Grande do Sul, 90035-003, Brazil

Location

Local Institution - 0019

São Paulo, São Paulo, 04520-013, Brazil

Location

Local Institution - 0020

Campinas, 13083-970, Brazil

Location

Local Institution

Campinas, 13083-970, Brazil

Location

Local Institution - 0039

São Paulo, 01401-000, Brazil

Location

Local Institution

São Paulo, 01401-000, Brazil

Location

Local Institution

São Paulo, 04023-062, Brazil

Location

Alberta Children'S Hospital

Calgary, Alberta, T3B 6A8, Canada

Location

Local Institution - 0079

Calgary, Alberta, T3B 6A8, Canada

Location

Local Institution - 0078

Edmonton, Alberta, T6G 2B7, Canada

Location

Stollery Children'S Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

Bc Children'S Hospital

Vancouver, British Columbia, V6H 3V4, Canada

Location

Local Institution - 077

Vancouver, British Columbia, V6H 3V4, Canada

Location

Iwk Health Centre

Halifax, Nova Scotia, B3K 6R8, Canada

Location

Local Institution - 073

Halifax, Nova Scotia, B3K 6R8, Canada

Location

Children'S Hospital Of Eastern Ontario

Ottawa, Ontario, K1H 8L1, Canada

Location

Local Institution - 086

Ottawa, Ontario, K1H 8L1, Canada

Location

Local Institution - 076

Toronto, Ontario, M5G 1X8, Canada

Location

The Hospital For Sick Children

Toronto, Ontario, M5G 1X8, Canada

Location

Chu Ste-Justine

Montreal, Quebec, H3T 1C5, Canada

Location

Local Institution - 080

Montreal, Quebec, H3T 1C5, Canada

Location

Local Institution - 0030

Lyon, 69008, France

Location

Local Institution

Lyon, 69008, France

Location

Local Institution - 0032

Nantes, 44093, France

Location

Local Institution

Nantes, 44093, France

Location

Local Institution - 0037

Paris, 75012, France

Location

Local Institution

Paris, 75012, France

Location

Local Institution

Paris, 75571, France

Location

Local Institution - 0029

Paris, 75935, France

Location

Local Institution

Paris, 75935, France

Location

Local Institution - 036

Poitiers, 86000, France

Location

Local Institution

Poitiers, 86000, France

Location

Local Institution - 075

Frankfurt, 60590, Germany

Location

Local Institution

Frankfurt, 60590, Germany

Location

Local Institution - 0074

Hanover, 30625, Germany

Location

Local Institution

Hanover, 30625, Germany

Location

Local Institution - 0089

Navrangpura, Ahmedabad, Gujarat, 380009, India

Location

Local Institution

Navrangpura, Ahmedabad, Gujarat, 380009, India

Location

Local Institution

Bangalore, Karnataka, 560027, India

Location

Local Institution

Mumbai, Maharashtra, 400010, India

Location

Local Institution - 0094

Pune, Maharashtra, 411001, India

Location

Local Institution

Pune, Maharashtra, 411001, India

Location

Local Institution - 0093

Madurai, Tamil Nadu, 625107, India

Location

Local Institution

Madurai, Tamil Nadu, 625107, India

Location

Local Institution

Vellore, Tamil Nadu, 632004, India

Location

Local Institution - 0088

Bangalore, 560027, India

Location

Local Institution - 0082

Kolkata, 700 016, India

Location

Local Institution

Kolkata, 700 016, India

Location

Local Institution - 0085

Mumbai, 400010, India

Location

Local Institution

Mumbai, 400010, India

Location

Local Institution - 0084

Trivandrum, 695011, India

Location

Local Institution

Trivandrum, 695011, India

Location

Local Institution - 038

Bologna, 40138, Italy

Location

Local Institution

Bologna, 40138, Italy

Location

Local Institution - 006

Monza, 20900, Italy

Location

Local Institution

Monza (MB), 20900, Italy

Location

Local Institution - 070

Roma, 00161, Italy

Location

Local Institution

Roma, 00161, Italy

Location

Local Institution - 0059

Roma, 00165, Italy

Location

Local Institution

Roma, 00165, Italy

Location

Local Institution - 015

Torino, 10126, Italy

Location

Local Institution

Torino, 10126, Italy

Location

Hospital Civil De Guadalajara - Nuevo Dr. Juan I. Menchaca

Guadalajara, Jalisco, 44340, Mexico

Location

Local Institution - 0054

Guadalajara, Jalisco, 44340, Mexico

Location

Local Institution - 0051

Cuauhtémoc, Mexico City, 06720, Mexico

Location

Local Institution

Df, Mexico City, 06720, Mexico

Location

Local Institution - 0053

Mexico City, Mexico City, 04530, Mexico

Location

Local Institution

Mexico City, Mexico City, 04530, Mexico

Location

Local Institution - 0052

Mexico City, Mexico City, 06726, Mexico

Location

Local Institution

Mexico City, Mexico City, 06726, Mexico

Location

Local Institution

Mexico, D. F., Mexico City, 06726, Mexico

Location

Local Institution - 0050

Monterrey, Nuevo León, 64460, Mexico

Location

Local Institution

Monterrey, Nuevo León, 64460, Mexico

Location

Local Institution - 0060

Monterrey, N.l., Nuevo León, 64180, Mexico

Location

Local Institution

Monterrey, N.l., Nuevo León, 64180, Mexico

Location

Local Institution - 0007

Rotterdam, 3015 GJ, Netherlands

Location

Local Institution

Rotterdam, 3015 GJ, Netherlands

Location

Local Institution - 0099

Utrecht, 3584 CS, Netherlands

Location

Local Institution - 0095

Bucharest, 022322, Romania

Location

Local Institution

Bucharest, 022322, Romania

Location

Local Institution - 0097

Sector 2, 022328, Romania

Location

Local Institution - 0017

Moscow, 115478, Russia

Location

Local Institution

Moscow, 115478, Russia

Location

Local Institution - 0023

Moscow, 117198, Russia

Location

Local Institution

Moscow, 117198, Russia

Location

Local Institution - 0018

Saint Petersburg, 197022, Russia

Location

Local Institution

Saint Petersburg, 197022, Russia

Location

Local Institution - 0071

Singapore, 119074, Singapore

Location

Local Institution

Singapore, 119228, Singapore

Location

Local Institution - 0055

Bloemfontein, Free State, 9301, South Africa

Location

Local Institution

Bloemfontein, Free State, 9301, South Africa

Location

Local Institution - 058

Pretoria, Gauteng, 0001, South Africa

Location

Local Institution

Pretoria, Gauteng, 0001, South Africa

Location

Local Institution - 0057

Cape Town, Western Cape, 7925, South Africa

Location

Local Institution

Cape Town, Western Cape, 7925, South Africa

Location

Local Institution - 062

Tygerberg, Western Cape, 7505, South Africa

Location

Local Institution

Tygerberg, Western Cape, 7505, South Africa

Location

Local Institution - 0092

Seoul, 05505, South Korea

Location

Local Institution

Seoul, 05505, South Korea

Location

Local Institution - 0091

Seoul, 137-701, South Korea

Location

Local Institution

Seoul, 137-701, South Korea

Location

Local Institution - 0013

Barcelona, 08025, Spain

Location

Local Institution

Barcelona, 08025, Spain

Location

Local Institution - 0012

Barcelona, 08035, Spain

Location

Local Institution

Barcelona, 08035, Spain

Location

Local Institution - 0011

Madrid, 28009, Spain

Location

Local Institution

Madrid, 28009, Spain

Location

Local Institution - 0010

Madrid, 28046, Spain

Location

Local Institution

Madrid, 28046, Spain

Location

Local Institution - 0041

Málaga, 29010, Spain

Location

Local Institution

Málaga, 29010, Spain

Location

Local Institution - 0033

Valencia, 46009, Spain

Location

Local Institution

Valencia, 46009, Spain

Location

Local Institution

Valencia, Spain

Location

Local Institution - 0016

Glasgow, Central, G3 8SJ, United Kingdom

Location

Local Institution

Glasgow, Central, G3 8SJ, United Kingdom

Location

Local Institution - 0009

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Local Institution

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Local Institution - 0008

Birmingham, West Midlands, B4 6NH, United Kingdom

Location

Local Institution

Birmingham, West Midlands, B4 6NH, United Kingdom

Location

Related Publications (1)

  • Gore L, Kearns PR, de Martino ML, Lee, De Souza CA, Bertrand Y, Hijiya N, Stork LC, Chung NG, Cardos RC, Saikia T, Fagioli F, Seo JJ, Landman-Parker J, Lancaster D, Place AE, Rabin KR, Sacchi M, Swanink R, Zwaan CM. Dasatinib in Pediatric Patients With Chronic Myeloid Leukemia in Chronic Phase: Results From a Phase II Trial. J Clin Oncol. 2018 May 1;36(13):1330-1338. doi: 10.1200/JCO.2017.75.9597. Epub 2018 Mar 2.

Related Links

MeSH Terms

Conditions

Leukemia

Interventions

Dasatinib

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

ThiazolesSulfur CompoundsOrganic ChemicalsAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidines

Results Point of Contact

Title
Bristol-Myers Squibb Study Director
Organization
Bristol-Myers Squibb

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 21, 2008

First Posted

October 22, 2008

Study Start

March 20, 2009

Primary Completion

September 1, 2016

Study Completion

January 27, 2025

Last Updated

August 29, 2025

Results First Posted

January 5, 2018

Record last verified: 2025-08

Locations