NCT01458951

Brief Summary

This study is designed to evaluate the efficacy and safety of tofacitinib (CP-690,550) in patients with moderate to severe ulcerative colitis who have failed or be intolerant to one of following treatments for ulcerative colitis: oral steroids, azathiopurine/6-mercaptopurine, or anti-TNF-alpha therapy.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
547

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jun 2012

Typical duration for phase_3

Geographic Reach
27 countries

169 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 21, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 25, 2011

Completed
7 months until next milestone

Study Start

First participant enrolled

June 1, 2012

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2015

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2015

Completed
1 year until next milestone

Results Posted

Study results publicly available

June 1, 2016

Completed
Last Updated

June 1, 2016

Status Verified

April 1, 2016

Enrollment Period

2.9 years

First QC Date

October 21, 2011

Results QC Date

April 26, 2016

Last Update Submit

April 26, 2016

Conditions

Keywords

TofacitinibCP-690550Moderate to severe ulcerative colitisphase 3 clinical trialMayo score

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Remission at Week 8

    Remission in participants was defined by a total Mayo score of 2 points or lower, with no individual subscore exceeding 1 point and a rectal bleeding subscore of 0. Mayo score is an instrument designed to measure disease activity of Ulcerative Colitis . It consisted of 4 subscores: stool frequency, rectal bleeding, findings of centrally read flexible proctosigmoidoscopy and physician global assessment (PGA), each graded from 0 to 3 with higher scores indicating more severe disease. These scores were summed up to give a total score range of 0 to 12; where higher score indicating more severe disease.

    Week 8

Secondary Outcomes (9)

  • Percentage of Participants Achieving Mucosal Healing at Week 8

    Week 8

  • Percentage of Participants Achieving Clinical Response at Week 8

    Week 8

  • Percentage of Participants With Endoscopic Remission at Week 8

    Week 8

  • Percentage of Participants With Clinical Remission at Week 8

    Week 8

  • Percentage of Participants With Symptomatic Remission at Week 8

    Week 8

  • +4 more secondary outcomes

Study Arms (2)

tofacitinib 10 mg BID

EXPERIMENTAL
Drug: tofacitinib

Placebo BID

PLACEBO COMPARATOR
Drug: Placebo

Interventions

10 mg oral BID

Also known as: CP-690,550
tofacitinib 10 mg BID

Placebo oral BID

Placebo BID

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject must be at least 18 years of age.
  • Males and females with a documented diagnosis of UC at least 4 months prior to entry into the study.
  • Subjects with moderately to severely active UC based on Mayo score criteria.
  • Subjects must have failed or be intolerant of at least one of the following treatments for UC:
  • Corticosteroids (oral or intravenous).
  • Azathioprine or 6 mercaptopurine (6 MP).
  • Anti TNF therapy.

You may not qualify if:

  • Presence of indeterminate colitis, microscopic colitis, ischemic colitis, infectious colitis, or clinical findings suggestive of Crohn's disease.
  • Subjects with disease limited to distal 15 cm.
  • Subjects without previous treatment for UC (ie, treatment naïve).
  • Subjects displaying clinical signs of fulminant colitis or toxic megacolon.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (182)

Desert Sun Clinical Research, LLC

Tucson, Arizona, 85710, United States

Location

Desert Sun Gastroenterology

Tucson, Arizona, 85710, United States

Location

Desert Sun Surgery Center

Tucson, Arizona, 85710, United States

Location

Alliance Clinical Research

Oceanside, California, 92056, United States

Location

Clinical Application Laboratories

San Diego, California, 92103, United States

Location

San Diego Endoscopy Center

San Diego, California, 92103, United States

Location

UCSF Endoscopy Unit at Mount Zion

San Francisco, California, 94115, United States

Location

University of California San Francisco

San Francisco, California, 94115, United States

Location

Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center

Torrance, California, 90502, United States

Location

Bristol Hospital

Bristol, Connecticut, 06010, United States

Location

Connecticut Clinical Research Foundation

Bristol, Connecticut, 06010, United States

Location

Yale New Haven Hospital

New Haven, Connecticut, 06510, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06510, United States

Location

Central Connecticut Endoscopy Center

Plainville, Connecticut, 06062, United States

Location

Citrus Surgery & Endoscopy Center (Colonoscopy)

Crystal River, Florida, 34429, United States

Location

Nature Coast Clinical Research

Inverness, Florida, 34452, United States

Location

Suncoast Endoscopy Center (colonoscopy)

Inverness, Florida, 34453, United States

Location

Gastroenterology Group of Naples

Naples, Florida, 34102, United States

Location

Advanced Gastroenterology Center

Port Orange, Florida, 32127, United States

Location

Advanced Medical Research Center

Port Orange, Florida, 32127, United States

Location

Endoscopy Center

Port Orange, Florida, 32127, United States

Location

Port Orange Urgent Care

Port Orange, Florida, 32127, United States

Location

Atlanta Center for Gastroenterology, P.C.

Decatur, Georgia, 30033, United States

Location

Cotton-O'Neil Clinical Research Center, Digestive Health

Topeka, Kansas, 66606, United States

Location

Gastrointestinal Specialists, A.M.C.

Shreveport, Louisiana, 71103, United States

Location

Shreveport Endoscopy Center, A.M.C.

Shreveport, Louisiana, 71103, United States

Location

Louisiana Research Center, LLC

Shreveport, Louisiana, 71105, United States

Location

Chevy Chase Endoscopy Center (Endoscopies Only)

Chevy Chase, Maryland, 20815, United States

Location

MGG Group Co., Inc., Chevy Chase Clinical Research

Chevy Chase, Maryland, 20815, United States

Location

Clinical Research Institute of Michigan, LLC

Chesterfield, Michigan, 48047, United States

Location

Center for Digestive Health

Troy, Michigan, 48098, United States

Location

Surgical Centers of Michigan

Troy, Michigan, 48098, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Surgery Center of Columbia

Columbia, Missouri, 65201, United States

Location

Hannibal Regional Hospital

Hannibal, Missouri, 63401, United States

Location

Audrain Medical Center

Mexico, Missouri, 65265, United States

Location

Center for Digestive & Liver Disease, Inc.

Mexico, Missouri, 65265, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

AGA Clinical Research Associates, LLC

Egg Harbor, New Jersey, 08234, United States

Location

South Jersey Gastroenterology

Marlton, New Jersey, 08053, United States

Location

The Gastroenterology Group of South Jersey

Vineland, New Jersey, 08360, United States

Location

The Endo Center at Voorhees

Voorhees Township, New Jersey, 08043, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

Carolina Research - Carolina Digestive Diseases

Greenville, North Carolina, 27834, United States

Location

Regional Gastroenterology Associates of Lancaster, Ltd.

Lancaster, Pennsylvania, 17604, United States

Location

Vanderbilt University Medical Center - IBD Clinic

Nashville, Tennessee, 37212-1375, United States

Location

Vanderbilt University Medical Center - GI Research Office

Nashville, Tennessee, 37212-1610, United States

Location

Vanderbilt University Medical Center - Drug Shipment

Nashville, Tennessee, 37232-7610, United States

Location

Vanderbilt University Medical Center - GCRC

Nashville, Tennessee, 37232, United States

Location

Vanderbilt University Medical Center - Heart Station

Nashville, Tennessee, 37232, United States

Location

Vanderbilt University Medical Center - Radiology

Nashville, Tennessee, 37232, United States

Location

Texas Clinical Research Institiute

Arlington, Texas, 76012, United States

Location

Austin Gastroenterology PA/Professional Quality Research, Inc.

Austin, Texas, 78705, United States

Location

Austin Gastroenterology PA

Austin, Texas, 78745, United States

Location

Austin Endoscopy Center II

Austin, Texas, 78746, United States

Location

Memorial Hermann Hospital

Houston, Texas, 77030, United States

Location

The University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

Digestive Health Specialists of Tyler

Tyler, Texas, 75701, United States

Location

VCU Health System Digestive Health Center

Richmond, Virginia, 23298, United States

Location

VCU Health System Endoscopy Suite

Richmond, Virginia, 23298, United States

Location

VCU Medical Center Investigational Drug Service (IDS)

Richmond, Virginia, 23298, United States

Location

Virginia Commonwealth University, Clinical Research Services (CRSU)

Richmond, Virginia, 23298, United States

Location

The Canberra Hospital

Garran, Australian Capital Territory, 2605, Australia

Location

Concord Hospital -Concord Repatriation Hospital

Concord, New South Wales, 2139, Australia

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

Liverpool Hospital Eastern Campus

Liverpool, New South Wales, 2170, Australia

Location

Monash Medical Centre

Clayton, Victoria, 3168, Australia

Location

Medizinische Universitat Innsbruck

Innsbruck, 6020, Austria

Location

Krankenhaus Barmherzige Brueder St. Veit/Glan

Sankt Veit an der Glan, 9300, Austria

Location

GZA St Vincentius

Antwerp, 2018, Belgium

Location

AZ Groeninge, Campus Kennedylaan

Kortrijk, 8500, Belgium

Location

H-Hartziekenhuis Roeselare-Menen vzw

Roeselare, 8800, Belgium

Location

Hospital de Clinicas de Porto Alegre - HCPA

Porto Alegre, Rio Grande do Sul, 90035-003, Brazil

Location

University of Alberta Hospital - Walter C. Mackenzie Health Sciences Centre

Edmonton, Alberta, T6G 2B7, Canada

Location

University of Alberta - Zeidler Ledcor Centre

Edmonton, Alberta, T6G 2X8, Canada

Location

Montreal General Hospital - McGill University Health Centre

Montreal, Quebec, H3G 1A4, Canada

Location

Saskatoon City Hospital

Saskatoon, Saskatchewan, S7K 0M7, Canada

Location

Royal University Hospital

Saskatoon, Saskatchewan, S7N 0W8, Canada

Location

Instituto de Coloproctologia ICO S.A.S.

Medellín, Antioquia, 00000, Colombia

Location

University Hospital Center Osijek, Clinic of Internal Medicine,

Osijek, 31000, Croatia

Location

University Hospital Center Rijeka

Rijeka, 51000, Croatia

Location

University Hospital Center Zagreb,Department of Gastroenterology

Zagreb, 10000, Croatia

Location

Nemocnice Strakonice, a.s., Interni oddeleni

Strakonice, 386 29, Czechia

Location

Krajska Zdravotni a.s., Masarykova nemocnice Usti nad Labem, o.z.

Ústí nad Labem, 40113, Czechia

Location

Bispebjerg Hospital

Copenhagen, NV, 2400, Denmark

Location

Hvidovre University Hospital

Hvidovre, 2650, Denmark

Location

Odense University Hospital

Odense C, 5000, Denmark

Location

ECG Unit, Innomedica OU and Qualitas AS (ECG Only)

Tallinn, 10117, Estonia

Location

Innomedica OU

Tallinn, 10117, Estonia

Location

X-Ray Unit, Qualitas AS (X-Ray Only)

Tallinn, 10117, Estonia

Location

East Tallinn Central Hospital Internal Medicine Clinic

Tallinn, 10138, Estonia

Location

ECG Unit, East Tallinn Central Hospital

Tallinn, 10138, Estonia

Location

X-Ray Unit, East Tallinn Central Hospital

Tallinn, 10138, Estonia

Location

Quattromed HTI Laboratorid OU

Tallinn, 12618, Estonia

Location

Mammograaf OU (Endoscopy Only)

Tallinn, 13419, Estonia

Location

Hopital Saint Andre

Bordeaux, France, 33075, France

Location

CHU Amiens PICARDIE - Hopital SUD

Amiens, 80054, France

Location

Hopital Beaujon

Clichy, 92110, France

Location

Hopital Saint Antoine

Paris, 75571, France

Location

C.H.U. de Reims - Hôpital Robert Debré

Reims, 51092, France

Location

Hopital Nord

Saint-Priest-en-Jarez, 42270, France

Location

Universitäetsklinik Schleswig-Holstein, Campus Kiel

Kiel, Schlewig Holstein, 24105, Germany

Location

Klinikum der Johann Wolfgang Goethe-Universitaet

Frankfurt, 60590, Germany

Location

Gastroenterologische Gemeinschaftspraxis Minden

Minden, 32423, Germany

Location

University Hospital Munich-Grosshadern

Munich, 81377, Germany

Location

Universitaetsklinikum Ulm

Ulm, 89081, Germany

Location

Dr. Rethy Pal Korhaz-Rendelointezet- III. Belgyogyaszat

Békéscsaba, Europe, 5600, Hungary

Location

Szent Janos Korhaz és Eszak-budai Egyesített Korhazak I Belgyogyaszat-Gasztroenterologiai Osztaly

Budapest, 1125, Hungary

Location

Peterfy Sandor utcai Korhaz- Rendelointezet es Baleseti Kozpontl. Belgyogyaszat

Budapest, H-1076, Hungary

Location

MH Honvedkorhaz

Budapest, H-1134, Hungary

Location

Pannonia Maganorvosi Centrum Kft.

Budapest, H-1135, Hungary

Location

Debreceni Egyetem Klinikai Központ Belgyógyászati Intézet, Gasztroenterológiai Tanszék

Debrecen, 4032, Hungary

Location

Bekes Megyei Pandy Kalman Korhaz

Gyula, H-5700, Hungary

Location

Borsod-Abauj-Zemplen Megyei Korhaz es Egyetemi Oktato Korhaz

Miskolc, 3526, Hungary

Location

"Karolina Korhaz Rendelointezet,Belgyogyaszat

Mosonmagyaróvár, 9200, Hungary

Location

Rambam Health Care Campus

Haifa, 31096, Israel

Location

The Edith Wolfson Medical Center/Gastroenterology Institute

Holon, 58100, Israel

Location

Kaplan Medical Center

Rehovot, 76100, Israel

Location

Daugavpils Regional Hospital

Daugavpils, LV-5417, Latvia

Location

VU University Medical Center (VUMC)

Amsterdam, 1081 HV, Netherlands

Location

Academic Medical Centre (AMC),

Amsterdam, 1105AZ, Netherlands

Location

University Medical Center Groningen (UMCG)

Groningen, 9713 GZ, Netherlands

Location

Christchurch Hospital

Christchurch, Canterbury, 8011, New Zealand

Location

Auckland City Hospital

Auckland, 1023, New Zealand

Location

Waikato Hospital

Hamilton, 3240, New Zealand

Location

P3 Research Limited

Wellington, 6021, New Zealand

Location

Pacific Radiology (X-rays only)

Wellington, 6021, New Zealand

Location

Bowen Hospital

Wellington, 6035, New Zealand

Location

Centrum Medyczne Szpital Sw. Rodziny Sp. z o. o.

Lodz, Iodzkie, 90-302, Poland

Location

Centrum Endoskopii Zabiegowej, Poradnia Chorob Jelitowych,

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, 85-168, Poland

Location

Oddzial Chorob Wewnetrznych i Gastroenterologii,

Bialystok, Podlaskie Voivodeship, 15-950, Poland

Location

H-T Centrum Medyczne sp. z o.o. sp. komandytowa

Tychy, Silesian Voivodeship, 43100, Poland

Location

Gabinet Endoskopii Przewodu Pokarmowego

Krakow, 31-009, Poland

Location

Endoskopia Sp. z.o.o.

Sopot, 81-756, Poland

Location

Nzoz Vivamed

Warsaw, 03-580, Poland

Location

Spitalul Universitar de Urgenta Bucuresti, Sectia de Medicina Interna 2 si Gastroenterologie

Bucharest, Sector 5, cod 050098, Romania

Location

Spitalul Clinic Judetean Mures, Sectia Clinica de Gastroenterologie

Jud. Mures, 540103, Romania

Location

State budget institution of healthcare "City Clinical Hospital # 51 healthcare department of Moscow"

Moscow, Russia, 121309, Russia

Location

Municipal institution of healthcare "Clinical Hospital # 2"

Yaroslavl, Russia, 150010, Russia

Location

OOO Medical Center of Diagnostics and Prophylaxis "Sodruzhestvo"

Yaroslavl, Russia, 150040, Russia

Location

Federal state budget institution "State scientific centre of coloproctology"

Moscow, 123423, Russia

Location

State budget Healthcare Institution Moscow regional scientific research clinical institute

Moscow, 129110, Russia

Location

Federal State Budgetary Institution "Scientific Research Institute of Physiology and

Novosibirsk, 630117, Russia

Location

Municipal institution of healthcare "City clinical hospital 12"

Saratov, 410039, Russia

Location

State budget institution of healthcare of Yaroslavl region Regional clinical hospital

Yaroslavl, 150062, Russia

Location

Clinical Centre of Serbia, Clinic for Gastroenterology and Hepatology

Belgrade, 11000, Serbia

Location

Clinical Centre of Vojvodina, Clinic for Gastroenterology and Hepatology

Novi Sad, 21000, Serbia

Location

Clinical Centre of Vojvodina, Emergency Internal Medicine Division

Novi Sad, 21000, Serbia

Location

General Hospital Subotica

Subotica, 24000, Serbia

Location

Lama Medical Care s.r.o., Gastroenterologicko-Hepatologicke centrum Thalion

Bratislava, 831 04, Slovakia

Location

KM Management spol. s r.o.

Nitra, 949 01, Slovakia

Location

Aura SA, s.r.o.

Nové Mesto nad Váhom, 91501, Slovakia

Location

Gastro I., s.r.o.

Prešov, 08001, Slovakia

Location

Panorama Medi-Clinic

Cape Town, Western Cape, 7500, South Africa

Location

The Louis Leipoldt Medical Centre

Cape Town, Western Cape, 7530, South Africa

Location

Dr JP Wright

Claremont, Cape Town, Western Cape, 7708, South Africa

Location

Hanyang University Guri Hospital, Clinical Laboratory

Guri-si, Gyeonggi-do, 471-701, South Korea

Location

CHA Bundang Medical Center, CHA University

Seongnam-si, Gyeonggi-do, 463-712, South Korea

Location

Pusan National University Hospital

Busan, 602-739, South Korea

Location

Gachon University Gil Medical Center

Incheon, 405-760, South Korea

Location

Seoul National University Hospital

Seoul, 110-744, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 120-752, South Korea

Location

Kyung Hee University Hospital

Seoul, 130-872, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

Corporacio Sanitaria Parc Tauli

Sabadell, Barcelona, 08208, Spain

Location

Hospital Universitario de Bellvitge

Barcelona, 08907, Spain

Location

Chung Shan Medical University Hospital

Taichung, 40201, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

Kyiv City Clinical Hospital #8,

Kiev, Ukraine, 04201, Ukraine

Location

Regional Municipal Institution "Chernivtsi Regional Clinical Hospital"

Chernivtsi, 58001, Ukraine

Location

Regional Municipal Institution Chernivtsi Regional Clinical Hospital

Chernivtsi, 58001, Ukraine

Location

State Institution Institute of Gastroenterology of the National Academy of Medical Sciences

Dnipropetrovsk, 49074, Ukraine

Location

Municipal Healthcare Institution Kharkiv City Clinical Hospital #2, Proctology Department

Kharkiv, 61037, Ukraine

Location

Municipal Institution "Odesa Regional Clinical Hospital"

Odesa, 65025, Ukraine

Location

Medical Clinical Research Center "Health Clinic" on the base of

Vinnytsia, 21029, Ukraine

Location

Motor-Sich clinic, LLC

Zaporizhzhia, 69068, Ukraine

Location

Minicipal Institution "City Hospital #7" Therapeutic Department,

Zaporizhzhia, 69118, Ukraine

Location

Department of Gastroenterology, Old Building

Bristol, England, BS2 8HW, United Kingdom

Location

St Mark's Hospital

Harrow, Middlesex, HA1 3UJ, United Kingdom

Location

Norfolk and Norwich University Hospital

Norwich, Norfolk, NR4 7UY, United Kingdom

Location

Norfolk and Norwich University Hospital

Norwich, NR4 7UY, United Kingdom

Location

Related Publications (36)

  • Panes J, D'Haens GR, Sands BE, Ng SC, Lawendy N, Kulisek N, Guo X, Wu J, Vranic I, Panaccione R, Vermeire S. Analysis of tofacitinib safety in ulcerative colitis from the completed global clinical developmental program up to 9.2 years of drug exposure. United European Gastroenterol J. 2024 Jul;12(6):793-801. doi: 10.1002/ueg2.12584. Epub 2024 May 22.

  • Rubin DT, Torres J, Regueiro M, Reinisch W, Prideaux L, Kotze PG, Tan FH, Gardiner S, Mundayat R, Cadatal MJ, Ng SC. Association Between Smoking Status and the Efficacy and Safety of Tofacitinib in Patients with Ulcerative Colitis. Crohns Colitis 360. 2024 Jan 20;6(1):otae004. doi: 10.1093/crocol/otae004. eCollection 2024 Jan.

  • Rubin DT, Salese L, Cohen M, Kotze PG, Woolcott JC, Su C, Mundayat R, Paulissen J, Torres J, Long MD. Presence of risk factors associated with colectomy among patients with ulcerative colitis: a post hoc analysis of data from the tofacitinib OCTAVE ulcerative colitis clinical program. Therap Adv Gastroenterol. 2023 Aug 7;16:17562848231189122. doi: 10.1177/17562848231189122. eCollection 2023.

  • Schreiber S, Rubin DT, Ng SC, Peyrin-Biroulet L, Danese S, Modesto I, Guo X, Su C, Kwok KK, Jo H, Chen Y, Yndestad A, Reinisch W, Dubinsky MC. Major Adverse Cardiovascular Events by Baseline Cardiovascular Risk in Patients with Ulcerative Colitis Treated with Tofacitinib: Data from the OCTAVE Clinical Programme. J Crohns Colitis. 2023 Nov 24;17(11):1761-1770. doi: 10.1093/ecco-jcc/jjad104.

  • Kristensen LE, Danese S, Yndestad A, Wang C, Nagy E, Modesto I, Rivas J, Benda B. Identification of two tofacitinib subpopulations with different relative risk versus TNF inhibitors: an analysis of the open label, randomised controlled study ORAL Surveillance. Ann Rheum Dis. 2023 Jul;82(7):901-910. doi: 10.1136/ard-2022-223715. Epub 2023 Mar 17.

  • Lichtenstein GR, Cohen BL, Salese L, Modesto I, Wang W, Chan G, Ahmed HM, Su C, Peyrin-Biroulet L. Impact of Concomitant Corticosteroids on Tofacitinib Induction Efficacy and Infection Rates in Ulcerative Colitis. Dig Dis Sci. 2023 Jun;68(6):2624-2634. doi: 10.1007/s10620-022-07794-0. Epub 2023 Feb 4.

  • Dubinsky MC, Armuzzi A, Gecse KB, Ullman T, Bushmakin AG, DiBonaventura M, Cappelleri JC, Connelly SB, Woolcott JC, Salese L. Improvements in Disease Activity Partially Mediate the Effect of Tofacitinib Treatment on Generic and Disease-Specific Health-Related Quality of Life in Patients with Ulcerative Colitis: Data from the OCTAVE Program. Dig Dis. 2023;41(4):604-614. doi: 10.1159/000528788. Epub 2023 Jan 5.

  • Winthrop KL, Yndestad A, Henrohn D, Danese S, Marsal S, Galindo M, Woolcott JC, Jo H, Kwok K, Shapiro AB, Jones TV, Diehl A, Su C, Panes J, Cohen SB. Influenza Adverse Events in Patients with Rheumatoid Arthritis, Ulcerative Colitis, or Psoriatic Arthritis in the Tofacitinib Clinical Development Programs. Rheumatol Ther. 2023 Apr;10(2):357-373. doi: 10.1007/s40744-022-00507-z. Epub 2022 Dec 17.

  • Sandborn WJ, Sands BE, Vermeire S, Leung Y, Guo X, Modesto I, Su C, Wang W, Panes J. Modified Mayo score versus Mayo score for evaluation of treatment efficacy in patients with ulcerative colitis: data from the tofacitinib OCTAVE program. Therap Adv Gastroenterol. 2022 Dec 5;15:17562848221136331. doi: 10.1177/17562848221136331. eCollection 2022.

  • Lichtenstein GR, Bressler B, Francisconi C, Vermeire S, Lawendy N, Salese L, Sawyerr G, Shi H, Su C, Judd DT, Jones T, Loftus EV. Assessment of Safety and Efficacy of Tofacitinib, Stratified by Age, in Patients from the Ulcerative Colitis Clinical Program. Inflamm Bowel Dis. 2023 Jan 5;29(1):27-41. doi: 10.1093/ibd/izac084.

  • Hudesman DP, Torres J, Salese L, Woolcott JC, Mundayat R, Su C, Mosli MH, Allegretti JR. Long-Term Improvement in the Patient-Reported Outcomes of Rectal Bleeding, Stool Frequency, and Health-Related Quality of Life with Tofacitinib in the Ulcerative Colitis OCTAVE Clinical Program. Patient. 2023 Mar;16(2):95-103. doi: 10.1007/s40271-022-00603-w. Epub 2022 Nov 7.

  • Targownik L, Dubinsky MC, Steinwurz F, Bushmakin AG, Cappelleri JC, Tai E, Gardiner S, Hur P, Panes J. Disease Activity and Health-related Quality of Life Relationships with Work Productivity in Patients with Ulcerative Colitis in OCTAVE Induction 1 and 2 and OCTAVE Sustain. J Crohns Colitis. 2023 Apr 19;17(4):513-523. doi: 10.1093/ecco-jcc/jjac161.

  • Sandborn WJ, D'Haens GR, Sands BE, Panaccione R, Ng SC, Lawendy N, Kulisek N, Modesto I, Guo X, Mundayat R, Su C, Vranic I, Panes J. Tofacitinib for the Treatment of Ulcerative Colitis: An Integrated Summary of up to 7.8 Years of Safety Data from the Global Clinical Programme. J Crohns Colitis. 2023 Apr 3;17(3):338-351. doi: 10.1093/ecco-jcc/jjac141.

  • Loftus EV, Baumgart DC, Gecse K, Kinnucan JA, Connelly SB, Salese L, Su C, Kwok KK, Woolcott JC, Armuzzi A. Clostridium difficile Infection in Patients with Ulcerative Colitis Treated with Tofacitinib in the Ulcerative Colitis Program. Inflamm Bowel Dis. 2023 May 2;29(5):744-751. doi: 10.1093/ibd/izac139.

  • Winthrop KL, Vermeire S, Long MD, Panes J, Ng SC, Kulisek N, Mundayat R, Lawendy N, Vranic I, Modesto I, Su C, Melmed GY. Long-term Risk of Herpes Zoster Infection in Patients With Ulcerative Colitis Receiving Tofacitinib. Inflamm Bowel Dis. 2023 Jan 5;29(1):85-96. doi: 10.1093/ibd/izac063.

  • Mukherjee A, Tsuchiwata S, Nicholas T, Cook JA, Modesto I, Su C, D'Haens GR, Sandborn WJ. Exposure-Response Characterization of Tofacitinib Efficacy in Moderate to Severe Ulcerative Colitis: Results From Phase II and Phase III Induction and Maintenance Studies. Clin Pharmacol Ther. 2022 Jul;112(1):90-100. doi: 10.1002/cpt.2601. Epub 2022 Apr 27.

  • Dubinsky MC, Magro F, Steinwurz F, Hudesman DP, Kinnucan JA, Ungaro RC, Neurath MF, Kulisek N, Paulissen J, Su C, Ponce de Leon D, Regueiro M. Association of C-reactive Protein and Partial Mayo Score With Response to Tofacitinib Induction Therapy: Results From the Ulcerative Colitis Clinical Program. Inflamm Bowel Dis. 2023 Jan 5;29(1):51-61. doi: 10.1093/ibd/izac061.

  • Feagan BG, Khanna R, Sandborn WJ, Vermeire S, Reinisch W, Su C, Salese L, Fan H, Paulissen J, Woodworth DA, Niezychowski W, Sands BE. Agreement between local and central reading of endoscopic disease activity in ulcerative colitis: results from the tofacitinib OCTAVE trials. Aliment Pharmacol Ther. 2021 Dec;54(11-12):1442-1453. doi: 10.1111/apt.16626. Epub 2021 Oct 6.

  • Farraye FA, Qazi T, Kotze PG, Moore GT, Mundayat R, Lawendy N, Sharma PP, Judd DT. The impact of body mass index on efficacy and safety in the tofacitinib OCTAVE ulcerative colitis clinical programme. Aliment Pharmacol Ther. 2021 Aug;54(4):429-440. doi: 10.1111/apt.16439. Epub 2021 Jun 24.

  • Rubin DT, Reinisch W, Greuter T, Kotze PG, Pinheiro M, Mundayat R, Maller E, Fellmann M, Lawendy N, Modesto I, Vavricka SR, Lichtenstein GR. Extraintestinal manifestations at baseline, and the effect of tofacitinib, in patients with moderate to severe ulcerative colitis. Therap Adv Gastroenterol. 2021 May 16;14:17562848211005708. doi: 10.1177/17562848211005708. eCollection 2021.

  • Sandborn WJ, Peyrin-Biroulet L, Sharara AI, Su C, Modesto I, Mundayat R, Gunay LM, Salese L, Sands BE. Efficacy and Safety of Tofacitinib in Ulcerative Colitis Based on Prior Tumor Necrosis Factor Inhibitor Failure Status. Clin Gastroenterol Hepatol. 2022 Mar;20(3):591-601.e8. doi: 10.1016/j.cgh.2021.02.043. Epub 2021 Mar 6.

  • Vong C, Martin SW, Deng C, Xie R, Ito K, Su C, Sandborn WJ, Mukherjee A. Population Pharmacokinetics of Tofacitinib in Patients With Moderate to Severe Ulcerative Colitis. Clin Pharmacol Drug Dev. 2021 Mar;10(3):229-240. doi: 10.1002/cpdd.899. Epub 2021 Jan 29.

  • Curtis JR, Regueiro M, Yun H, Su C, DiBonaventura M, Lawendy N, Nduaka CI, Koram N, Cappelleri JC, Chan G, Modesto I, Lichtenstein GR. Tofacitinib Treatment Safety in Moderate to Severe Ulcerative Colitis: Comparison of Observational Population Cohort Data From the IBM MarketScan(R) Administrative Claims Database With Tofacitinib Trial Data. Inflamm Bowel Dis. 2021 Aug 19;27(9):1394-1408. doi: 10.1093/ibd/izaa289.

  • Sandborn WJ, Peyrin-Biroulet L, Quirk D, Wang W, Nduaka CI, Mukherjee A, Su C, Sands BE. Efficacy and Safety of Extended Induction With Tofacitinib for the Treatment of Ulcerative Colitis. Clin Gastroenterol Hepatol. 2022 Aug;20(8):1821-1830.e3. doi: 10.1016/j.cgh.2020.10.038. Epub 2020 Oct 27.

  • Sands BE, Colombel JF, Ha C, Farnier M, Armuzzi A, Quirk D, Friedman GS, Kwok K, Salese L, Su C, Taub PR. Lipid Profiles in Patients With Ulcerative Colitis Receiving Tofacitinib-Implications for Cardiovascular Risk and Patient Management. Inflamm Bowel Dis. 2021 May 17;27(6):797-808. doi: 10.1093/ibd/izaa227.

  • Panaccione R, Isaacs JD, Chen LA, Wang W, Marren A, Kwok K, Wang L, Chan G, Su C. Characterization of Creatine Kinase Levels in Tofacitinib-Treated Patients with Ulcerative Colitis: Results from Clinical Trials. Dig Dis Sci. 2021 Aug;66(8):2732-2743. doi: 10.1007/s10620-020-06560-4. Epub 2020 Aug 20.

  • Dubinsky MC, DiBonaventura M, Fan H, Bushmakin AG, Cappelleri JC, Maller E, Thorpe AJ, Salese L, Panes J. Tofacitinib in Patients with Ulcerative Colitis: Inflammatory Bowel Disease Questionnaire Items in Phase 3 Randomized Controlled Induction Studies. Inflamm Bowel Dis. 2021 Jun 15;27(7):983-993. doi: 10.1093/ibd/izaa193.

  • Lichtenstein GR, Rogler G, Ciorba MA, Su C, Chan G, Pedersen RD, Lawendy N, Quirk D, Nduaka CI, Thorpe AJ, Panes J. Tofacitinib, an Oral Janus Kinase Inhibitor: Analysis of Malignancy (Excluding Nonmelanoma Skin Cancer) Events Across the Ulcerative Colitis Clinical Program. Inflamm Bowel Dis. 2021 May 17;27(6):816-825. doi: 10.1093/ibd/izaa199.

  • Sandborn WJ, Panes J, Sands BE, Reinisch W, Su C, Lawendy N, Koram N, Fan H, Jones TV, Modesto I, Quirk D, Danese S. Venous thromboembolic events in the tofacitinib ulcerative colitis clinical development programme. Aliment Pharmacol Ther. 2019 Nov;50(10):1068-1076. doi: 10.1111/apt.15514. Epub 2019 Oct 9.

  • Sands BE, Taub PR, Armuzzi A, Friedman GS, Moscariello M, Lawendy N, Pedersen RD, Chan G, Nduaka CI, Quirk D, Salese L, Su C, Feagan BG. Tofacitinib Treatment Is Associated With Modest and Reversible Increases in Serum Lipids in Patients With Ulcerative Colitis. Clin Gastroenterol Hepatol. 2020 Jan;18(1):123-132.e3. doi: 10.1016/j.cgh.2019.04.059. Epub 2019 May 8.

  • Sandborn WJ, Panes J, D'Haens GR, Sands BE, Su C, Moscariello M, Jones T, Pedersen R, Friedman GS, Lawendy N, Chan G. Safety of Tofacitinib for Treatment of Ulcerative Colitis, Based on 4.4 Years of Data From Global Clinical Trials. Clin Gastroenterol Hepatol. 2019 Jul;17(8):1541-1550. doi: 10.1016/j.cgh.2018.11.035. Epub 2018 Nov 23.

  • Hanauer S, Panaccione R, Danese S, Cheifetz A, Reinisch W, Higgins PDR, Woodworth DA, Zhang H, Friedman GS, Lawendy N, Quirk D, Nduaka CI, Su C. Tofacitinib Induction Therapy Reduces Symptoms Within 3 Days for Patients With Ulcerative Colitis. Clin Gastroenterol Hepatol. 2019 Jan;17(1):139-147. doi: 10.1016/j.cgh.2018.07.009. Epub 2018 Sep 10.

  • Winthrop KL, Melmed GY, Vermeire S, Long MD, Chan G, Pedersen RD, Lawendy N, Thorpe AJ, Nduaka CI, Su C. Herpes Zoster Infection in Patients With Ulcerative Colitis Receiving Tofacitinib. Inflamm Bowel Dis. 2018 Sep 15;24(10):2258-2265. doi: 10.1093/ibd/izy131.

  • Motoya S, Watanabe M, Kim HJ, Kim YH, Han DS, Yuasa H, Tabira J, Isogawa N, Arai S, Kawaguchi I, Hibi T. Tofacitinib induction and maintenance therapy in East Asian patients with active ulcerative colitis: subgroup analyses from three phase 3 multinational studies. Intest Res. 2018 Apr;16(2):233-245. doi: 10.5217/ir.2018.16.2.233. Epub 2018 Apr 30.

  • Panes J, Vermeire S, Lindsay JO, Sands BE, Su C, Friedman G, Zhang H, Yarlas A, Bayliss M, Maher S, Cappelleri JC, Bushmakin AG, Rubin DT. Tofacitinib in Patients with Ulcerative Colitis: Health-Related Quality of Life in Phase 3 Randomised Controlled Induction and Maintenance Studies. J Crohns Colitis. 2018 Jan 24;12(2):145-156. doi: 10.1093/ecco-jcc/jjx133.

  • Sandborn WJ, Su C, Sands BE, D'Haens GR, Vermeire S, Schreiber S, Danese S, Feagan BG, Reinisch W, Niezychowski W, Friedman G, Lawendy N, Yu D, Woodworth D, Mukherjee A, Zhang H, Healey P, Panes J; OCTAVE Induction 1, OCTAVE Induction 2, and OCTAVE Sustain Investigators. Tofacitinib as Induction and Maintenance Therapy for Ulcerative Colitis. N Engl J Med. 2017 May 4;376(18):1723-1736. doi: 10.1056/NEJMoa1606910.

Related Links

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

tofacitinib

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 21, 2011

First Posted

October 25, 2011

Study Start

June 1, 2012

Primary Completion

May 1, 2015

Study Completion

June 1, 2015

Last Updated

June 1, 2016

Results First Posted

June 1, 2016

Record last verified: 2016-04

Locations