NCT01456052

Brief Summary

This is a multicenter, placebo-controlled, parallel-group, pilot study to evaluate safety and preliminary effectiveness of two blinded dose levels of telotristat etiprate (LX1606) in participants with acute, mild to moderate ulcerative colitis on 5-aminosalicylic acid/mesalamine therapy.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
59

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2012

Geographic Reach
4 countries

24 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 17, 2011

Completed
3 days until next milestone

First Posted

Study publicly available on registry

October 20, 2011

Completed
3 months until next milestone

Study Start

First participant enrolled

January 30, 2012

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 3, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 3, 2013

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

March 11, 2015

Completed
Last Updated

May 23, 2019

Status Verified

May 1, 2019

Enrollment Period

1.6 years

First QC Date

October 17, 2011

Results QC Date

October 15, 2014

Last Update Submit

May 9, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of Participants Experiencing a Treatment Emergent Adverse Event

    8 weeks

Secondary Outcomes (3)

  • Number of Participants Achieving Clinical Response

    Baseline to 8 weeks

  • Number of Participants Achieving Clinical Remission

    Baseline to 8 weeks

  • Change From Baseline in Total Modified Mayo Score

    Baseline to 8 weeks

Study Arms (3)

Low Dose Telotristat Etiprate

EXPERIMENTAL

500 mg telotristat etiprate (LX1606) administered orally once daily (QD).

Drug: Telotristat Etiprate

High Dose Telotristat Etiprate

EXPERIMENTAL

500 mg telotristat etiprate (LX1606) administered orally three times daily (TID).

Drug: Telotristat Etiprate

Placebo

PLACEBO COMPARATOR

Matching placebo administered orally.

Drug: Placebo

Interventions

500 mg telotristat etiprate (LX1606) administered orally.

High Dose Telotristat EtiprateLow Dose Telotristat Etiprate

Matching placebo administered orally.

Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of ulcerative colitis of at least 6 months duration
  • Disease extends at least 15 cm proximally from the anal verge, documented within the past 3 years
  • Flare occurs on 5-aminosalicylic acid (5-ASA)/mesalamine therapy and subject is willing to remain on a stable dose for the duration of the study
  • Age ≥18 and \<70 years of age
  • Able and willing to provide written informed consent

You may not qualify if:

  • Prior terminal ileum or colonic surgery, except appendectomy or hemorrhoid surgery
  • Presence of indeterminate colitis, microscopic colitis, ischemic colitis, infectious colitis, or clinical findings suggestive of Crohn's disease
  • Clinical signs of fulminant colitis or toxic megacolon
  • History of dysplasia associated lesion or mass (DALM)
  • Subjects who have had surgery for ulcerative colitis, or in the opinion of the investigator, are likely to require surgery for ulcerative colitis during the study
  • History of primary sclerosing cholangitis
  • Any physical or laboratory abnormality deemed by the investigator as clinically significant
  • Major surgery within 60 days of Screening
  • Use of any investigational agent within 30 days of Screening or any therapeutic protein or antibody within 90 days of Screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

Lexicon Investigational Site

Little Rock, Arkansas, 72205, United States

Location

Lexicon Investigational Site

Anaheim, California, 92801, United States

Location

Lexicon Investigational Site

Santa Monica, California, 90404, United States

Location

Lexicon Investigational Site

Great Neck, New York, 11021, United States

Location

Lexicon Investigational Site

New York, New York, 10017, United States

Location

Lexicon Investigational Site

Tulsa, Oklahoma, 74135, United States

Location

Lexicon Investigational Site

Houston, Texas, 77030, United States

Location

Lexicon Investigational Site

San Antonio, Texas, 78229, United States

Location

Lexicon Investigational Site

Ogden, Utah, 84405, United States

Location

Lexicon Investigational Site

Sandy City, Utah, 84094, United States

Location

Lexicon Investigational Site

Seattle, Washington, 98195, United States

Location

Lexicon Investigational Site

Kaunas, LT-50009, Lithuania

Location

Lexicon Investigational Site

Klaipėda, LT-92288, Lithuania

Location

Lexicon Investigational Site

Šiauliai, LT-76231, Lithuania

Location

Lexicon Investigational Site

Vilnius, LT-03215, Lithuania

Location

Lexicon Investigational Site

Vilnius, LT-08661, Lithuania

Location

Lexicon Investigational Site

Krakow, 31531, Poland

Location

Lexicon Investigational Site

Lodz, 90302, Poland

Location

Lexicon Investigational Site

Sopot, 81756, Poland

Location

Lexicon Investigational Site

Warsaw, 03580, Poland

Location

Lexicon Investigational Site

Wroclaw, 53025, Poland

Location

Lexicon Investigational Site

Wroclaw, 54144, Poland

Location

Lexicon Investigational Site

Nitra, 94901, Slovakia

Location

Lexicon Investigational Site

Nové Mesto nad Váhom, 91501, Slovakia

Location

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

telotristat

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Results Point of Contact

Title
Manager of Regulatory Affairs
Organization
Lexicon Pharmaceuticals, Inc.

Study Officials

  • Doug Fleming, MD

    Lexicon Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 17, 2011

First Posted

October 20, 2011

Study Start

January 30, 2012

Primary Completion

September 3, 2013

Study Completion

September 3, 2013

Last Updated

May 23, 2019

Results First Posted

March 11, 2015

Record last verified: 2019-05

Locations