NCT01562314

Brief Summary

This study was conducted to determine the efficacy and safety of GWP42003 compared with placebo by the percentage of participants achieving remission quantified as a Mayo score of 2 or less (with no sub-score \>1) after 10 weeks of treatment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
60

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started May 2012

Geographic Reach
1 country

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 21, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 23, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

May 9, 2012

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 5, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 5, 2014

Completed
1 year until next milestone

Results Posted

Study results publicly available

August 14, 2015

Completed
Last Updated

August 9, 2018

Status Verified

July 1, 2018

Enrollment Period

2.2 years

First QC Date

March 21, 2012

Results QC Date

June 22, 2015

Last Update Submit

July 11, 2018

Conditions

Keywords

Mild to Moderate Ulcerative ColitisGWP42003

Outcome Measures

Primary Outcomes (2)

  • Number Of Participants With A Mayo Score Of 2 Or Less (With No Sub-score >1) At EOT

    The Mayo score is an assessment of ulcerative colitis activity. The Mayo total score ranges from 0 to 12 points with higher scores indicating more severe disease. The total score is made up of 4 sub-scores, each of which is assessed using a 0 to 3 scale. Sub-scores are graded as follows: Stool Frequency: 0 = Normal number of stools, 1 = 1 to 2 stools more than normal, 2 = 3 to 4 stools more than normal, 3 = 5 or more stools more than normal; Rectal Bleeding: 0 = No blood seen, 1 = Streaks of blood with stool less than half the time, 2 = Obvious blood with stool most of the time or more, 3 = Blood alone passes; Findings on Endoscopy: 0 = Normal or inactive disease, 1 = Mild disease (erythema, decreased vascular pattern, mild friability), 2 = Moderate disease (marked erythema, lack of vascular pattern, friability, erosions), 3 = Severe disease (spontaneous bleeding, ulceration); Physician's Global Assessment of Illness Severity (PGAS): 0 = none, 1 = mild, 2 = moderate, and 3 = severe.

    Baseline to End of Treatment (EOT) (10 weeks) or Early Termination (ET)

  • Number Of Participants With A Mayo Score Of 2 Or Less (With No Sub-score >1) At EOT - PP Analysis

    The Mayo score is an assessment of ulcerative colitis activity. The Mayo total score ranges from 0 to 12 points with higher scores indicating more severe disease. The total score is made up of 4 sub-scores, each of which is assessed using a 0 to 3 scale. Sub-scores are graded as follows: Stool Frequency: 0 = Normal number of stools, 1 = 1 to 2 stools more than normal, 2 = 3 to 4 stools more than normal, 3 = 5 or more stools more than normal; Rectal Bleeding: 0 = No blood seen, 1 = Streaks of blood with stool less than half the time, 2 = Obvious blood with stool most of the time or more, 3 = Blood alone passes; Findings on Endoscopy: 0 = Normal or inactive disease, 1 = Mild disease (erythema, decreased vascular pattern, mild friability), 2 = Moderate disease (marked erythema, lack of vascular pattern, friability, erosions), 3 = Severe disease (spontaneous bleeding, ulceration); PGAS: 0 = none, 1 = mild, 2 = moderate, and 3 = severe.

    Baseline to EOT (10 weeks) or ET

Secondary Outcomes (15)

  • Distribution On The PGAS At EOT

    EOT (10 weeks) or ET

  • Distribution On The PGAS At EOT - PP Analysis

    EOT (10 weeks) or ET

  • Change From Baseline To EOT In The PGAS Score

    Baseline to EOT (10 weeks) or ET

  • Change From Baseline To EOT In The PGAS Score - PP Analysis

    Baseline to EOT (10 weeks) or ET

  • Change From Baseline To EOT In The Inflammatory Bowel Disease Questionnaire (IBDQ) Total Score

    Baseline to EOT (10 weeks) or ET

  • +10 more secondary outcomes

Study Arms (2)

GWP42003

EXPERIMENTAL

GWP42003 was administered orally at a dose of 50 mg up to 250 mg, BID, in the fasted state in the morning and evening, for 10 weeks. Following randomization, participants entered a 2-week dose escalation period to achieve their maximum tolerated dose, up to 500 mg, and maintained this dose for the rest of the treatment period. Participants were then followed for 1 week.

Drug: GWP42003

Placebo

PLACEBO COMPARATOR

Placebo capsules matching the study drug were administered orally, BID, in the fasted state in the morning and evening, for 10 weeks. Participants were then followed for 1 week.

Drug: Placebo

Interventions

1 to 5 50 mg capsules taken BID

Also known as: Cannabidiol (CBD) Botanical Drug Substance (BDS)
GWP42003

1 to 5 matching capsules taken BID

Also known as: Placebo control
Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female participants aged 18 years or above;
  • Participant diagnosed with mild to moderate ulcerative colitis and on a fixed dose of 5-Aminosalicylic (5-ASA) treatment and have been on a stable dose for at least 2 weeks prior to screening (0 mg dose of 5-ASA was acceptable);
  • Participants at screening and baseline with a Mayo assessment score of greater than or equal to 4 (≥4) but less than or equal to 10 (≤10) and with an endoscopy score of at least 1 (≥1) , following an adequate exposure to oral and/ or topical 5-ASA, in the opinion of the investigator;
  • In the opinion of the investigator, capable of complying with the study requirements and completing the study;
  • Willing and able to give informed consent;
  • Willing for his or her name to be notified to the responsible authorities for participation in this study, as applicable;
  • Willing to allow his or her primary care practitioner and consultant, if appropriate, to be notified of participation in the study;

You may not qualify if:

  • Severe ulcerative colitis (Mayo score of greater than 10 (\>10);
  • Ulcerative colitis only affecting the rectum (proctitis)
  • Gastrointestinal infection evident from stool culture and testing for Clostridium difficile toxin (in the opinion of the investigator);
  • Currently using or had used recreational cannabis, medicinal cannabis, cannabinoid medications (including Sativex®), or synthetic cannabinoid-based medications within 1 month prior to study entry and unwilling to abstain for the duration of the study;
  • Any known or suspected history of alcohol or substance abuse, epilepsy or recurrent seizures, or hypersensitivity to cannabinoids;
  • Was receiving a prohibited medication prior to screening and for the duration of the study;
  • Previous non-responders to mono or polyclonal anti-Tumor Necrosis Factor antibodies;
  • Personal or first degree relative, with history of schizophrenia or other psychosis;
  • History of other significant psychiatric disorder or severe personality disorder (at the discretion of the investigator);
  • Any known or suspected history of depression sufficient to require treatment with antidepressants or disrupt ordinary life (excluding episodes of reactive depression at the discretion of the investigator);
  • Clinically significant cardiac, renal or hepatic impairment in the opinion of the investigator;
  • Female participants who were pregnant, lactating or planning pregnancy during the course of the study and for 3 months from the date of last dose;
  • Female participants of child bearing potential, unless willing to use 2 forms of contraception, 1 of which must have been a barrier contraception (for example, a female condom or occlusive cap \[diaphragm or cervical vault/caps\] with spermicide) during the study and for 3 months from the date of last dose (however a male condom should not have been used in conjunction with the female condom);
  • Male participants whose partner was of child bearing potential, unless willing to use an appropriate barrier method of contraception (condom and spermicide) in addition to having their female partner use another form of barrier contraception (for example, an occlusive cap \[diaphragm or cervical vault/caps\] with spermicide) during the study and for 3 months from date of last dose (however a male condom should not have been used in conjunction with a female condom);
  • Planned to travel outside the country of residence during the treatment phase of the study;
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Unknown Facility

Birmingham, B15 2TH, United Kingdom

Location

Unknown Facility

Coventry, CV2 2DX, United Kingdom

Location

Unknown Facility

Liverpool, L7 8XP, United Kingdom

Location

Unknown Facility

London, NW1 2PG, United Kingdom

Location

Unknown Facility

London, NW3 2QG, United Kingdom

Location

Unknown Facility

London, SE1 7EH, United Kingdom

Location

Unknown Facility

Middlesex, HA1 3UJ, United Kingdom

Location

Unknown Facility

Wigan, WN1 2NN, United Kingdom

Location

Related Publications (1)

  • Irving PM, Iqbal T, Nwokolo C, Subramanian S, Bloom S, Prasad N, Hart A, Murray C, Lindsay JO, Taylor A, Barron R, Wright S. A Randomized, Double-blind, Placebo-controlled, Parallel-group, Pilot Study of Cannabidiol-rich Botanical Extract in the Symptomatic Treatment of Ulcerative Colitis. Inflamm Bowel Dis. 2018 Mar 19;24(4):714-724. doi: 10.1093/ibd/izy002.

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

Cannabidiol

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Intervention Hierarchy (Ancestors)

CannabinoidsTerpenesHydrocarbonsOrganic Chemicals

Results Point of Contact

Title
Medical Enquiries
Organization
GW Research Ltd

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 21, 2012

First Posted

March 23, 2012

Study Start

May 9, 2012

Primary Completion

August 5, 2014

Study Completion

August 5, 2014

Last Updated

August 9, 2018

Results First Posted

August 14, 2015

Record last verified: 2018-07

Locations