NCT01336465

Brief Summary

This Phase II study is a randomized, double-blind, placebo-controlled multicenter study to evaluate the efficacy and safety of rhuMAb Beta7 in patients with moderate to severe ulcerative colitis.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
124

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Sep 2011

Geographic Reach
11 countries

51 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 14, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 18, 2011

Completed
5 months until next milestone

Study Start

First participant enrolled

September 1, 2011

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2012

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2013

Completed
Last Updated

August 12, 2016

Status Verified

August 1, 2016

Enrollment Period

1 year

First QC Date

April 14, 2011

Last Update Submit

August 10, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Clinical remission defined as a Mayo Clinic Score (MCS) </= 2 with no individual subscore exceeding 1 point

    Week 10

Secondary Outcomes (3)

  • Clinical response as defined by at least a 3-point decrease and 30% reduction from baseline in MCS and a >/=1-point decrease in rectal bleeding subscore or absolute rectal bleeding score of 0 or 1

    Week 6 and Week 10

  • Clinical remission defined by a MCS </= 2 with no individual subscore exceeding 1 point

    Week 6

  • Proportion of patients with endoscopic score and rectal bleeding score of 0

    Week 6 and Week 10

Study Arms (2)

rhuMAb Beta7

EXPERIMENTAL
Drug: rhuMAb Beta7

placebo

PLACEBO COMPARATOR
Drug: placebo

Interventions

Repeating subcutaneous injection

placebo

Repeating subcutaneous injection

rhuMAb Beta7

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of moderate to severe ulcerative colitis outpatient
  • Disease duration at time of screening of \>/= 12 weeks

You may not qualify if:

  • Extensive colonic resection or subtotal or total colectomy
  • Presence of an ileostomy or colostomy
  • Moderate to severe anemia
  • A history or evidence of colonic mucosal dysplasia
  • Pregnant or lactating
  • Significant uncontrolled co-morbidity, such as neurological, cardiac, pulmonary, renal, hepatic, endocrine, or gastrointestinal (GI) disorders
  • Significant screening ECG abnormalities, including evidence of acute myocardial infarction, complete left bundle branch block, second-degree heart block, or complete heart block
  • Poorly controlled diabetes
  • Impaired renal function
  • Impaired hepatic function in the absence of a diagnosis of primary sclerosing cholangitis
  • Positive tests for antibodies indicating active or prior infection with HIV or hepatitis B (HBV) or C (HCV)
  • Positive screening test for latent mycobacterium tuberculosis (TB) infection
  • Demyelinating disease
  • Received any investigational treatment within 12 weeks prior to initiation of study treatment
  • Previous exposure to rhuMAb Beta7

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (51)

Unknown Facility

San Diego, California, 92103, United States

Location

Unknown Facility

Gainesville, Florida, 32610, United States

Location

Unknown Facility

Atlanta, Georgia, 30308, United States

Location

Unknown Facility

Chevy Chase, Maryland, 20815, United States

Location

Unknown Facility

Ann Arbor, Michigan, 48109-0682, United States

Location

Unknown Facility

Rochester, Minnesota, 55905, United States

Location

Unknown Facility

Great Neck, New York, 11021, United States

Location

Unknown Facility

Cincinnati, Ohio, 45219, United States

Location

Unknown Facility

Garran, Australian Capital Territory, 2605, Australia

Location

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Clayton, Victoria, 3168, Australia

Location

Unknown Facility

Fitzroy, Victoria, 3065, Australia

Location

Unknown Facility

Melbourne, Victoria, 3181, Australia

Location

Unknown Facility

Parkville, Victoria, 3050, Australia

Location

Unknown Facility

Bonheiden, 2820, Belgium

Location

Unknown Facility

Ghent, 9000, Belgium

Location

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

Location

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Edmonton, Alberta, T6G 2X8, Canada

Location

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Edmonton, Alberta, V6Z 1Y6, Canada

Location

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London, Ontario, N6A 5W9, Canada

Location

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Woodbridge, Ontario, L4L 4Y7, Canada

Location

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Hradec Králové, 500 12, Czechia

Location

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Náchod, 547 01, Czechia

Location

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Ostrava - Poruba, 708 52, Czechia

Location

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Zlín, 762 75, Czechia

Location

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Berlin, 13353, Germany

Location

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Hanover, 30625, Germany

Location

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Kiel, 24105, Germany

Location

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Minden, 32423, Germany

Location

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Ulm, 89081, Germany

Location

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Budapest, 1073, Hungary

Location

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Budapest, 1136, Hungary

Location

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Gyöngyös, 3200, Hungary

Location

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Győr, 9024, Hungary

Location

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Mosonmagyaróvár, 9200, Hungary

Location

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Beersheba, 84105, Israel

Location

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Haifa, 31096, Israel

Location

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Jerusalem, 91031, Israel

Location

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Ramat Gan, 52621, Israel

Location

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Tel Aviv, 64239, Israel

Location

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Auckland, 1023, New Zealand

Location

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Auckland, 1640, New Zealand

Location

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Christchurch, 8011, New Zealand

Location

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Dunedin, 9054, New Zealand

Location

Unknown Facility

Takapuna, 0620, New Zealand

Location

Unknown Facility

Barcelona, Barcelona, 08003, Spain

Location

Unknown Facility

Barcelona, Barcelona, 08036, Spain

Location

Unknown Facility

Harrow, HA1 3UJ, United Kingdom

Location

Unknown Facility

London, N6A 4L6, United Kingdom

Location

Unknown Facility

London, SW10 9NH, United Kingdom

Location

Unknown Facility

Newcastle upon Tyne, NE1 4LP, United Kingdom

Location

Related Publications (1)

  • Vermeire S, O'Byrne S, Keir M, Williams M, Lu TT, Mansfield JC, Lamb CA, Feagan BG, Panes J, Salas A, Baumgart DC, Schreiber S, Dotan I, Sandborn WJ, Tew GW, Luca D, Tang MT, Diehl L, Eastham-Anderson J, De Hertogh G, Perrier C, Egen JG, Kirby JA, van Assche G, Rutgeerts P. Etrolizumab as induction therapy for ulcerative colitis: a randomised, controlled, phase 2 trial. Lancet. 2014 Jul 26;384(9940):309-18. doi: 10.1016/S0140-6736(14)60661-9. Epub 2014 May 9.

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

etrolizumab

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Study Officials

  • Sharon O'Byrne, M.D.

    Genentech, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 14, 2011

First Posted

April 18, 2011

Study Start

September 1, 2011

Primary Completion

September 1, 2012

Study Completion

June 1, 2013

Last Updated

August 12, 2016

Record last verified: 2016-08

Locations