NCT01435044

Brief Summary

This study was designed to assess the safety and efficacy of multiple interferon-free treatment regimens of sofosbuvir (Sovaldi™; GS-7977; PSI-7977) and GS-0938 (PSI-352938) alone and in combination, with and without ribavirin (RBV). Each regimen was to be evaluated over 12 and 24 weeks to identify the optimal duration of therapy to maximize the benefit (sustained virologic response \[SVR\]) versus risk (safety and resistance).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
239

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Sep 2011

Geographic Reach
2 countries

44 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2011

Completed
8 days until next milestone

First Submitted

Initial submission to the registry

September 9, 2011

Completed
6 days until next milestone

First Posted

Study publicly available on registry

September 15, 2011

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2013

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2013

Completed
Last Updated

February 6, 2014

Status Verified

January 1, 2014

Enrollment Period

1.6 years

First QC Date

September 9, 2011

Last Update Submit

January 7, 2014

Conditions

Keywords

Hepatitis CChronicHCV

Outcome Measures

Primary Outcomes (1)

  • Percentage of participants with sustained virologic response (SVR) 12 weeks after discontinuation of study drug (SVR12)

    SVR12 was defined as HCV RNA \< LLOQ 12 weeks after the last dose of all study drugs.

    Post-treatment Week 12

Secondary Outcomes (6)

  • Percentage of Participants Who Experienced Adverse Events

    Baseline to Week 24 plus 30 days

  • Change from baseline in HCV RNA

    Baseline to Week 12

  • Percentage of Participants With HCV RNA < LLOQ during treatment

    Baseline to Week 12

  • Percentage of Participants With ALT Normalization

    Baseline to post-treatment Week 4

  • Percentage of participants with SVR at 4 and 24 weeks after discontinuation of study drug (SVR4; SVR24)

    Post-treatment Weeks 4 and 24

  • +1 more secondary outcomes

Study Arms (7)

SOF+RBV 12 Weeks

EXPERIMENTAL

Participants were randomized to receive sofosbuvir plus RBV plus placebo to match GS-0938 for 12 weeks.

Drug: SofosbuvirDrug: RBV

SOF+RBV 24 Weeks

EXPERIMENTAL

Participants were randomized to receive sofosbuvir plus RBV plus placebo to match GS-0938 for 24 weeks.

Drug: SofosbuvirDrug: RBV

GS-0938 Alone

EXPERIMENTAL

Participants were randomized to receive GS-0938 plus placebo to match sofosbuvir for up to 24 weeks.

Drug: GS-0938Drug: Placebo to match sofosbuvir

GS-0938+SOF

EXPERIMENTAL

Participants were randomized to receive GS-0938 plus sofosbuvir for up to 24 weeks.

Drug: SofosbuvirDrug: GS-0938

GS-0938+SOF+RBV

EXPERIMENTAL

Participants were randomized to receive GS-0938 plus sofosbuvir plus RBV for up to 24 weeks.

Drug: SofosbuvirDrug: GS-0938Drug: RBV

Placebo

EXPERIMENTAL

Deferred start group: Participants were randomized to receive placebo to match GS-0938 plus placebo to match sofosbuvir for 24 Weeks.

Drug: Placebo to match sofosbuvirDrug: Placebo to match GS-0938

Retreatment Group - SOF+RBV 24 Weeks

EXPERIMENTAL

After discontinuing a regimen containing GS-0938, participants received sofosbuvir plus RBV for up to 24 weeks.

Drug: SofosbuvirDrug: RBV

Interventions

Sofosbuvir 400 mg (2 × 200 mg tablets) administered orally once daily

Also known as: Sovaldi™, GS-7977, PSI-7977
GS-0938+SOFGS-0938+SOF+RBVRetreatment Group - SOF+RBV 24 WeeksSOF+RBV 12 WeeksSOF+RBV 24 Weeks

GS-0938 300 mg (3 × 100 mg tablets) administered orally once daily

Also known as: PSI-352938
GS-0938 AloneGS-0938+SOFGS-0938+SOF+RBV
RBVDRUG

Ribavirin (RBV) tablets administered orally in a divided daily dose according to package insert weight-based dosing recommendations (\< 75kg = 1000 mg and ≥ 75 kg = 1200 mg)

Also known as: Ribasphere®
GS-0938+SOF+RBVRetreatment Group - SOF+RBV 24 WeeksSOF+RBV 12 WeeksSOF+RBV 24 Weeks

Placebo to match sofosbuvir administered orally once daily

GS-0938 AlonePlacebo

Placebo to match GS-0938 administered orally once daily

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Chronic HCV-infection
  • Naive to all HCV antiviral treatment
  • Otherwise healthy patients

You may not qualify if:

  • Positive test at Screening for HBsAg, anti-HBc IgM Ab, or anti-HIV Ab
  • History of any other clinically significant chronic liver disease
  • Medical history which the investigator considers the patient unsuitable for the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (44)

Alabama Liver & Digestive Specialists

Montgomery, Alabama, 36116, United States

Location

Unknown Facility

Bakersfield, California, 93301, United States

Location

Unknown Facility

Coronado, California, 92118, United States

Location

Unknown Facility

La Mesa, California, 91942, United States

Location

Unknown Facility

Los Angeles, California, 90036, United States

Location

CLI

Los Angeles, California, 90048, United States

Location

UCSD Antiviral Research Center

San Diego, California, 92103, United States

Location

eStudy Site

San Diego, California, 92120, United States

Location

Medical Associates Research Group

San Diego, California, 92193, United States

Location

Quest Clinical Research

San Francisco, California, 94115, United States

Location

Unknown Facility

Denver, Colorado, 80220, United States

Location

Unknown Facility

Engelwood, Colorado, 80113, United States

Location

South Denver Gastroenterology

Englewood, Colorado, 80113, United States

Location

Unknown Facility

Washington D.C., District of Columbia, 20009, United States

Location

Avail Clinical Research

DeLand, Florida, 32720, United States

Location

University of Florida Hepatology

Gainesville, Florida, 32610, United States

Location

University of Miami Center for Liver Diseases

Miami, Florida, 33136, United States

Location

Orlando Immunology Center

Orlando, Florida, 32803, United States

Location

Internal Medicine Specialists

Orlando, Florida, 32806, United States

Location

Miami Research Associates

South Miami, Florida, 33143, United States

Location

Advanced Research Institute

Trinity, Florida, 34655, United States

Location

South Florida Center of Gastroenterology

Wellington, Florida, 33414, United States

Location

AIDS Research Consortium of Atlanta

Atlanta, Georgia, 30308, United States

Location

Unknown Facility

Atlanta, Georgia, 30308, United States

Location

Unknown Facility

Marietta, Georgia, 30060, United States

Location

Digestive Health Services

Downers Grove, Illinois, 60515, United States

Location

Investigative Clinical Research

Annapolis, Maryland, 21401, United States

Location

Unknown Facility

Baltimore, Maryland, 21229, United States

Location

ID Care

Hillsborough, New Jersey, 08844, United States

Location

Concorde Medical Group

New York, New York, 10016, United States

Location

Mount Sinai Medical Center

New York, New York, 10029, United States

Location

Ashville Gastroenterology Associates

Ashville, North Carolina, 28801, United States

Location

Carolina's Center for Liver Disease

Statesville, North Carolina, 28677, United States

Location

Digestive Health Specialists

Winston-Salem, North Carolina, 27103, United States

Location

Unknown Facility

Cincinnati, Ohio, United States

Location

Gastro One

Germantown, Tennessee, 38138, United States

Location

Nashville Gastrointestinal Specialists

Nashville, Tennessee, 37211, United States

Location

Texas Clinical Research Institute

Arlington, Texas, 76012, United States

Location

Central Texas Clinical Research

Austin, Texas, 78705, United States

Location

Alamo Medical Research

San Antonio, Texas, 78215, United States

Location

Digestive and Liver Disease Specialists

Norfolk, Virginia, 23502, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

Unknown Facility

San Juan, Puerto Rico, 00909, Puerto Rico

Location

Fundacion de Investigacion de Diego

San Juan, 00927, Puerto Rico

Location

MeSH Terms

Conditions

Hepatitis C, ChronicHepatitis CBronchiolitis Obliterans Syndrome

Interventions

SofosbuvirPSI 352938Ribavirin

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsHepatitis, Viral, HumanVirus DiseasesFlaviviridae InfectionsRNA Virus InfectionsHepatitis, ChronicHepatitisLiver DiseasesDigestive System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsOrganizing PneumoniaBronchiolitis ObliteransBronchiolitisBronchitisBronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesGraft vs Host DiseaseImmune System Diseases

Intervention Hierarchy (Ancestors)

Uridine MonophosphateUracil NucleotidesPyrimidine NucleotidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleotidesNucleic Acids, Nucleotides, and NucleosidesRibonucleotidesRibonucleosidesNucleosides

Study Officials

  • Robert H. Hyland, DPhil

    Gilead Sciences

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 9, 2011

First Posted

September 15, 2011

Study Start

September 1, 2011

Primary Completion

April 1, 2013

Study Completion

May 1, 2013

Last Updated

February 6, 2014

Record last verified: 2014-01

Locations