NCT01393639

Brief Summary

The purpose of this study is to compare the safety and efficacy of multiple doses of PF-04171327, an experimental glucocorticoid drug, to prednisone at 5 mg or 10 mg and placebo in the treatment of rheumatoid arthritis. All subjects will also be receiving background treatment of methotrexate for their rheumatoid arthritis. Study medication will be given for eight weeks followed by a 4 week period during which the dose of study medication will be gradually reduced. The efficacy of the study medications will be determined by assessing severity of the rheumatoid arthritis during the study and safety will be determined by adverse event reporting, laboratory tests and biomarker analysis.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
323

participants targeted

Target at P75+ for phase_2 rheumatoid-arthritis

Timeline
Completed

Started Sep 2011

Longer than P75 for phase_2 rheumatoid-arthritis

Geographic Reach
18 countries

93 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 13, 2011

Completed
1 month until next milestone

First Posted

Study publicly available on registry

July 13, 2011

Completed
3 months until next milestone

Study Start

First participant enrolled

September 27, 2011

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 3, 2014

Completed
6 days until next milestone

Study Completion

Last participant's last visit for all outcomes

June 9, 2014

Completed
10.2 years until next milestone

Results Posted

Study results publicly available

September 4, 2024

Completed
Last Updated

September 4, 2024

Status Verified

August 1, 2024

Enrollment Period

2.7 years

First QC Date

June 13, 2011

Results QC Date

January 12, 2023

Last Update Submit

August 12, 2024

Conditions

Keywords

treatment of rheumatoid arthritistreatment of RApatients on methotrexate for rheumatoid arthritisprednisone for rheumatoid arthritis

Outcome Measures

Primary Outcomes (3)

  • Percentage of Participants Achieving a 20% Improvement in American College of Rheumatology (ACR) Criteria at Week 8

    ACR20 response: greater than or equal to (≥) 20 percent (%) improvement in tender joint count; ≥ 20% improvement in swollen joint count; and ≥ 20% improvement in at least 3 of 5 remaining ACR core measures: participant assessment of pain; participant global assessment of disease activity; physician global assessment of disease activity; self-assessed disability (disability index of the Health Assessment Questionnaire \[HAQ\]); and C-Reactive Protein (CRP).

    Week 8

  • Mean Percent Change From Baseline in 0 Hour Procollagen Type 1 N Terminal Propeptide (P1NP) at Week 8 (Comparisons to Prednisone 5 mg)

    Change from baseline in P1NP at week 8 is presented in this outcome measure.

    Week 8

  • Mean Percent Change From Baseline in 0 Hour Urinary N Telopeptide/Urinary Creatinine (uNTx/uCr) at Week 8 (Comparisons to Prednisone 5 mg)

    Change from baseline in uNTx/uCr at week 8 is presented in this outcome measure.

    Week 8

Secondary Outcomes (25)

  • Percentage of Participants Achieving ACR20 Response at Weeks 2, 4, and 12 (Comparisons to Placebo, and Prednisone 10 mg)

    Weeks 2, 4, and 12 (taper period)

  • Percentage of Participants Achieving ACR50 Response at Weeks 2, 4, 6, 8 and 12 (Comparisons to Placebo, and Prednisone 10 mg)

    Weeks 2, 4, 6, 8, and 12 (taper period)

  • Percentage of Participants Achieving ACR70 Response at Weeks 2, 4, 6, 8 and 12 (Comparisons to Placebo, and Prednisone 10 mg)

    Weeks 2, 4, 6, 8, and 12 (taper period)

  • Change From Baseline in Tender-Joint Counts at Weeks 2, 4, 6, 8 (Comparisons to Placebo, and Prednisone 10 mg)

    Weeks 2, 4, 6, and 8

  • Change From Baseline in Tender-Joint Counts at Week 12 (Descriptive Statistics)

    Week 12

  • +20 more secondary outcomes

Study Arms (7)

PF-04171327 1 mg QD

EXPERIMENTAL
Drug: PF-04171327

PF-04171327 5 mg QD

EXPERIMENTAL
Drug: PF-04171327

PF-04171327 10 mg QD

EXPERIMENTAL
Drug: PF-04171327

PF-04171327 15 mg QD

EXPERIMENTAL
Drug: PF-04171327

prednisone 5 mg QD

ACTIVE COMPARATOR
Drug: prednisone

prednisone 10 mg QD

ACTIVE COMPARATOR
Other: prednisone

placebo

PLACEBO COMPARATOR
Other: placebo

Interventions

1 mg tablet once daily (QD) for 8 weeks

PF-04171327 1 mg QD

5 mg capsule once daily for 8 weeks

prednisone 5 mg QD
placeboOTHER

placebo (tablet or capsule) once daily (QD) for 8 weeks

placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects must have documented rheumatoid arthritis with a duration of at least 3 months as determined by the investigator using standardly accepted criteria, must have been receiving methotrexate for at least 3 months to treat their rheumatoid arthritis, and must be free of any signs or symptoms of infection.

You may not qualify if:

  • Subjects cannot enter the study if they have recently received treatment with certain medications which might interfere with study medications;
  • subjects cannot enter if they have abnormalities in certain blood tests, history of cancer, recent bone fracture or other significant conditions.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (93)

Catalina Pointe Clinical Research, Inc.

Tucson, Arizona, 85704, United States

Location

C. Michael Neuwelt, MD, Inc.

San Leandro, California, 94578, United States

Location

Javed Rheumatology Associates, Inc.

Newark, Delaware, 19713, United States

Location

Allergy, Asthma, Arthritis, and Lung Center

Daytona Beach, Florida, 32114, United States

Location

Millennium Research

Ormond Beach, Florida, 32174, United States

Location

Alastair C. Kennedy, MD

Vero Beach, Florida, 32960, United States

Location

The Center for Arthritis and Rheumatism

Vero Beach, Florida, 32960, United States

Location

Arthritis and Osteoporosis Medical Associates, PLLC

Brooklyn, New York, 11201, United States

Location

Cincinnati Rheumatic Disease Study Group, Inc.

Cincinnati, Ohio, 45219, United States

Location

Altoona Center for Clinical Research

Duncansville, Pennsylvania, 16635, United States

Location

Low Country Rheumatology, PA

Charleston, South Carolina, 29406, United States

Location

Tricounty Radiology

Charleston, South Carolina, 29406, United States

Location

Accurate Clinical Research, Inc.

Houston, Texas, 77034, United States

Location

Arthritis Northwest, PLLC

Spokane, Washington, 99204, United States

Location

Revmatologichen kabinet, DKTs Sv. Pantaleimon OOD

Pleven, 5800, Bulgaria

Location

Revmatologichno Otdelenie, MBAL - Plovdiv

Plovdiv, 4000, Bulgaria

Location

MBAL "Sveti Ivan Rilski" Sofia; Klinika po Revmatologia

Sofia, 1612, Bulgaria

Location

MBAL Sveti Ivan Rilski Sofia; Klinika po Revmatologia

Sofia, 1612, Bulgaria

Location

Hospital Pablo Tobon Uribe

Medellín, Antioquia, Colombia

Location

Reumalab S.A.S

Medellín, Antioquia, Colombia

Location

Centro Integral de Reumatologia e Inmunologia CIREI

Bogota, Cundinamarca, 110221, Colombia

Location

Preventive Care SAS

Chía, Cundinamarca, 250001, Colombia

Location

Revmatologie Bruntal, S.R.O.

Bruntál, 79201, Czechia

Location

Revmatologicka ambulance

Ostrava - Poruba, 70800, Czechia

Location

Revmatologicka ambulance

Prague, 140 00, Czechia

Location

Thomayerova nemocnice

Prague, 140 59, Czechia

Location

Charite Universitaetsmedizin Berlin, Klinik fuer Rheumatologie

Berlin, 10117, Germany

Location

Klinische Forschung Berlin-Buch GmbH

Berlin, 13125, Germany

Location

CIRI GmbH

Frankfurt am Main, 60528, Germany

Location

Dr. Rethy Pal Korhaz es Rendelointezet, II. Reumatologia Szakrendeles

Békéscsaba, 5600, Hungary

Location

Budai Irgalmasrendi Korhaz, Reumatologia I.

Budapest, 1027, Hungary

Location

Revita Reumatologiai Rendelo

Budapest, 1027, Hungary

Location

Qualiclinic Kft.

Budapest, 1036, Hungary

Location

Fejer Megyei Szent Gyorgy Korhaz Reumatologia

Székesfehérvár, 8000, Hungary

Location

MAV Korhaz es Rendelointezet, Reumatologiai szakrendeles

Szolnok, 5000, Hungary

Location

Krishna Institute of Medical Sciences Ltd

Secunderabad, Andhra Pradesh, 500 003, India

Location

Shirdi Sai Hospital

Bangalore, Karnataka, 560 054, India

Location

Dapartment of Rheumatology

Lucknow, Uttar Pradesh, 226 018, India

Location

Hospital Raja Permaisuri Bainun

Ipoh, Perak, 30990, Malaysia

Location

Sunway Medical Centre

Petaling Jaya, Selangor, 46150, Malaysia

Location

Centro de Estudios de Investigacion Basica y Clinica SC.

Guadalajara, Jalisco, 44690, Mexico

Location

Unidad de Investigacion Biomedica del CEM

Mérida, Yucatán, 97000, Mexico

Location

Centro de Alta Especialidad en Reumatologia e Investigacion del Potosi S.C.

San Luis Potosí City, 78200, Mexico

Location

Centrum Kliniczno-Badawcze J. Brzezicki, B. Górniakiewicz-Brzezicka Lekarze Spółka Partnerska

Elblag, 82-300, Poland

Location

Nzoz "Lecznica Mak-Med S.C."

Nadarzyn, 05-830, Poland

Location

Wojewodzki Zespol Reumatologiczny im. dr J. Titz-Kosko

Sopot, 81-759, Poland

Location

Spitalul Clinic "Sfanta Maria", Clinica de Medicina Interna si Reumatologie

Bucharest, 800578, Romania

Location

Spitalul Clinic Judetean de Urgenta "Sfantul Apostol Andrei"

Galati, 800578, Romania

Location

Spitalul Clinic de Recuperare

Iași, 700656, Romania

Location

Spitalul Clinic Judetean de Urgenta Targu Mures, Reumatologic

Tg Mures, 540136, Romania

Location

GBOU VPO "Orenburg State Medical Academy of Ministry of Healthcare of Russian Federation"

Orenburg, Russian Federation, 460000, Russia

Location

Territorial Clinical Hospital

Barnaul, 656024, Russia

Location

GBUZ of Kemerovo region Regional clinical hospital for was veterans

Kemerovo, 650000, Russia

Location

Kemerovo Regional Clinical Hospital

Kemerovo, 650066, Russia

Location

FSBI Scientific - Research Institute of Rheumatology RAMS n.a. V.A. Nasonova.

Moscow, 115522, Russia

Location

LLC Consultative and Diagnostic Rheumatological Center Healthy Joints

Novosibirsk, 630091, Russia

Location

Republican Hospital V.A.Baranov

Petrozavodsk, 185019, Russia

Location

Ryazan Regional Clinical Cardiological Dispensary

Ryazan, 390026, Russia

Location

Clinical Rheumatological Hospital #25

Saint Petersburg, 190068, Russia

Location

Clinical Hospital #122 L.G. Sokolov

Saint Petersburg, 194291, Russia

Location

MUZ City Clinical Hospital #12

Saratov, 410039, Russia

Location

Smolensk Regional Clinical Hospital

Smolensk, 214018, Russia

Location

Tomsk Regional Clinical Hospital

Tomsk, 634063, Russia

Location

Vladimir Regional Clinical Hospital

Vladimir, 600023, Russia

Location

Clinical Hospital of Emergency Care N.V. Soloviev

Yaroslavl, 150003, Russia

Location

Yaroslavl Regional Clinical Hospital

Yaroslavl, 150062, Russia

Location

Sverdlovsk Regional Clinical Hospital # 1

Yekaterinburg, 620102, Russia

Location

Municilap Institution Central Clinical Hospital 6

Yekaterinburg, 620149, Russia

Location

Institute of Rheumatology

Belgrade, 11000, Serbia

Location

Institute for treatment and rehabilitation Niska Banja

Niška Banja, 18205, Serbia

Location

AAGS, s.r.o. , nestatne zdravotnicke zariadenie

Dunajská Streda, 92901, Slovakia

Location

Nestatna reumatologicka ambulancia

Považská Bystrica, 017 01, Slovakia

Location

Reumatologicka ambulancia, REUMEX, s.r.o.

Rimavská Sobota, 979 01, Slovakia

Location

Reumaglobal s.r.o.

Trnava, 917 01, Slovakia

Location

Nestatna reumatologicka ambulancia

Žilina, 010 01, Slovakia

Location

Panorama Medical Centre

Panorama, Cape Town, 7500, South Africa

Location

Emmed Research

Pretoria, Gauteng, 0084, South Africa

Location

KyungHee University Hospital

Seoul, Korea, 130-872, South Korea

Location

Daegu Catholic University Medical Center, Department of Rheumatology

Daegu, 705-718, South Korea

Location

Inha University Hospital, Medicine/Rheumatology

Incheon, 400-711, South Korea

Location

Seoul National University Hospital, Rheumatology, Internal Medicine

Seoul, 110-744, South Korea

Location

Konkuk University Medical Center, Department of Rheumatology

Seoul, 143-729, South Korea

Location

Complejo Hospitalario Universitario A Coruña. Hospital Materno Infantil Teresa Herrera

A Coruña, 15006, Spain

Location

Hospital SANITAS CIMA.

Barcelona, 08034, Spain

Location

Municipal Medical Institution "City Clinical Hospital #3"

Chernivtsi, 58022, Ukraine

Location

Municipal Medicoprophylactic Institution "Donetsk City Clinical Hospital #5".

Donetsk, 83001, Ukraine

Location

National Scientific Centre "Institute of Cardiology n.a. M.D. Strazheska of NAMS of Ukraine".

Kiev, 03680, Ukraine

Location

Komunalnyi zaklad Kyivskoi oblasnoi rady "Kyivska oblasna klinichna likarnia"

Kyiv, 04107, Ukraine

Location

Komunalnyi zaklad Lvivskoi oblasnoi rady "Lvivskyi oblasnyi klinichnyi diahnostychnyi tsentr"

Lviv, 79010, Ukraine

Location

Komunalna ustanova "Odeska oblasna klinichna likarnia"

Odesa, 65025, Ukraine

Location

Municipal Establishment "City Clinical Hospital #9 n.a. O.I. Minakov", Department of Rheumatology

Odesa, 65026, Ukraine

Location

Vinnytsya regional clinical hospital named after M.I. Pyrogova; Department of rheumatology

Vinnytsia, 21018, Ukraine

Location

Municipal Institution:"Zaporizhzhya Regional Clinical Hospital",Rheumatology Dep.

Zaporizhzhya, 69600, Ukraine

Location

Related Publications (1)

  • Buttgereit F, Strand V, Lee EB, Simon-Campos A, McCabe D, Genet A, Tammara B, Rojo R, Hey-Hadavi J. Fosdagrocorat (PF-04171327) versus prednisone or placebo in rheumatoid arthritis: a randomised, double-blind, multicentre, phase IIb study. RMD Open. 2019 Apr 16;5(1):e000889. doi: 10.1136/rmdopen-2018-000889. eCollection 2019.

Related Links

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

fosdagrocoratPrednisone

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

PregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 13, 2011

First Posted

July 13, 2011

Study Start

September 27, 2011

Primary Completion

June 3, 2014

Study Completion

June 9, 2014

Last Updated

September 4, 2024

Results First Posted

September 4, 2024

Record last verified: 2024-08

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations