NCT01851707

Brief Summary

The purpose of this study is to investigate the safety and efficacy of multiple dose levels of the investigational product (study drug), IPI-145, in combination with methotrexate compared to methotrexate alone in subjects with active moderate-to-severe Rheumatoid Arthritis.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
322

participants targeted

Target at P75+ for phase_2 rheumatoid-arthritis

Timeline
Completed

Started Apr 2013

Typical duration for phase_2 rheumatoid-arthritis

Geographic Reach
11 countries

64 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2013

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

May 8, 2013

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 10, 2013

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2014

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2015

Completed
Last Updated

March 17, 2021

Status Verified

March 1, 2021

Enrollment Period

1.7 years

First QC Date

May 8, 2013

Last Update Submit

March 15, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Proportion of subjects who achieve a 20% improvement in the American College of Rheumatology Criteria (ACR20) from Baseline to Week 12

    Baseline (Day 1), Weeks 2, 4, 6, 8, 10 and 12

Study Arms (4)

IPI-145, low dose BID

EXPERIMENTAL
Drug: IPI-145

IPI-145, medium dose BID

EXPERIMENTAL
Drug: IPI-145

IPI-145, high dose BID

EXPERIMENTAL
Drug: IPI-145

Placebo BID

PLACEBO COMPARATOR
Drug: Placebo

Interventions

2 blinded capsules will be administered twice a day (morning and night) for 12 weeks.

IPI-145, high dose BIDIPI-145, low dose BIDIPI-145, medium dose BID

2 blinded capsules will be administered twice a day (morning and night) for 12 weeks.

Placebo BID

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Documented diagnosis of Rheumatoid Arthritis for at least 6 months
  • Active disease, based on Screening clinical and laboratory criteria, despite taking methotrexate for at least 3 months

You may not qualify if:

  • Pregnant or lactating females
  • Previous failure or inadequate response to \>2 biologic disease-modifying anti-rheumatic drugs (DMARDs)
  • Concurrent DMARD treatment other than methotrexate, sulfasalazine, chloroquine, or hydroxychloroquine
  • Treatment with \> 10 mg daily prednisone (or equivalent) or more than one non-steroidal anti-inflammatory drug

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (64)

Unknown Facility

Pleven, Bulgaria

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Plovdiv, Bulgaria

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Rousse, Bulgaria

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Sofia, Bulgaria

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Stara Zagora, Bulgaria

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Targovishte, Bulgaria

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Varna, Bulgaria

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Medellín, Antioquia, Colombia

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Bogota, Cundinamarca, Colombia

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Bucaramanga, Santander Department, Colombia

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Frankfurt, Germany

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Halle, Germany

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Budapest, Hungary

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Kecskemét, Hungary

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Mezőkövesd, Hungary

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Nyíregyháza, Hungary

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Veszprém, Hungary

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Mexico City, Col Roam Sur, Mexico

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Mexico City, Del Cuautemoc, Mexico

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León, Guanajuato, Mexico

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Guadalajara, Jalisco, Mexico

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Madero, Mexico DF, Mexico

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Morelia, Michoacán, Mexico

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Monterrey, Nuevo León, Mexico

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San Luis Potosí City, San Luis Potosi, C.P., Mexico

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Mérida, Yucatán, Mexico

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Mexico City, Mexico

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Otahuhu, Auckland, New Zealand

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Wellington, New Zealand

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Grodzisk, Mazowiecki, Poland

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Krakow, Okulickiego, Poland

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Bialystok, Poland

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Elblag, Poland

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Krakow, Poland

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Lublin, Poland

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Nadarzyn, Poland

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Poznan, Poland

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Skierniewice, Poland

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Sosnowiec, Poland

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Stalowa Wola, Poland

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Starachowice, Poland

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Wroclaw, Poland

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Baia Mare, Romania

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Brăila, Romania

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Bucharest, Romania

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Oradea, Romania

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Timișoara, Romania

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Petrozavodsk, Republic of Karelia, Russia

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Ryazan, Ryazan Oblast, Russia

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Moscow, Russia

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Orenburg, Russia

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Saint Petersburg, Russia

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Saratov, Russia

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Vladimir, Russia

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Yaroslavl, Russia

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Belgrade, Serbia

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Novi Sad, Serbia

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Donetsk, Ukraine

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Kharkiv, Ukraine

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Kyiv, Ukraine

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Lviv, Ukraine

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Poltava, Ukraine

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Ternopil, Ukraine

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Zaporizhzhya, Ukraine

Location

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

duvelisib

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Hagop Youssoufian, MD

    Verastem, Inc.

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 8, 2013

First Posted

May 10, 2013

Study Start

April 1, 2013

Primary Completion

December 1, 2014

Study Completion

February 1, 2015

Last Updated

March 17, 2021

Record last verified: 2021-03

Locations