NCT01286272

Brief Summary

This randomized phase II trial studies how well ofatumumab and bendamustine hydrochloride with or without bortezomib works in treating patients with untreated follicular non-Hodgkin lymphoma. Monoclonal antibodies, such as ofatumumab, may block cancer growth in different ways by targeting certain cells. Drugs used in chemotherapy, such as bendamustine hydrochloride, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Bortezomib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. Bortezomib may also stop the growth of cancer cells by blocking blood flow to the tumor. It is not yet known whether ofatumumab and bendamustine hydrochloride are more effective with bortezomib in treating patients with follicular non-Hodgkin lymphoma.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
135

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2011

Longer than P75 for phase_2

Geographic Reach
1 country

96 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 27, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 31, 2011

Completed
3 months until next milestone

Study Start

First participant enrolled

April 28, 2011

Completed
6.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 24, 2017

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

January 10, 2019

Completed
6.6 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 2, 2025

Completed
Last Updated

November 24, 2025

Status Verified

October 1, 2025

Enrollment Period

6.1 years

First QC Date

January 27, 2011

Results QC Date

October 12, 2018

Last Update Submit

November 7, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Complete Response Rate

    A complete response was defined using International Harmonization Project Response Criteria as the complete disappearance of all detectable clinical evidence of disease and disease-related symptoms if present before therapy. If the bone marrow was involved by lymphoma before treatment, the infiltrate must have cleared on repeat bone marrow biopsy. The complete response (CR) rate was calculated in newly diagnosed untreated follicular lymphoma patients receiving 6 cycles of ofatumumab-bendamustine (ARM A) and 6 cycles of ofatumumab, bortezomib, and bendamustine (ARM B). The complete response rate was calculated as the number of patients with a complete response divided by the number of patients eligible for evaluation.

    From date of randomization until patient stops treatment for any reason, up to 484 days post-randomization

Secondary Outcomes (2)

  • Progression-free Survival (PFS)

    Up to 4 years

  • The Number of Patients Who Experienced Grade 3+ Hematologic and Non-hematologic Adverse Events at Least Possibly Related to Treatment

    From date of randomization until patient stops treatment for any reason, up to 484 days post-randomization

Other Outcomes (3)

  • Pre-treatment Single Nucleotide Polymorphisms (SNP)

    Up to 10 years

  • Immunohistochemical (IHC) Markers

    Up to 10 years

  • Predictive Value of Fludeoxyglucose-positron-emission Tomography

    Up to 36-38 weeks (6-8 weeks after course 6, day 1 after last course of induction chemotherapy)

Study Arms (2)

Arm A (ofatumumab, bendamustine hydrochloride)

EXPERIMENTAL

INDUCTION: Patients receive ofatumumab IV over 2-8 hours on day 1 and bendamustine hydrochloride IV over 30-60 minutes on days 1 and 2. Treatment repeats every 35 days for up to 6 courses. Patients without disease progression continue on to maintenance therapy. MAINTENANCE: Beginning 8 weeks after the start of induction course 6, patients receive ofatumumab IV over 2-8 hours on day 1. Treatment repeats every 56 days for up to 4 courses.

Drug: Bendamustine HydrochlorideRadiation: Fludeoxyglucose F-18Other: Laboratory Biomarker AnalysisBiological: OfatumumabProcedure: Positron Emission Tomography with Radiolabeled Targeting Agent

Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)

EXPERIMENTAL

INDUCTION: Patients receive ofatumumab IV over 2-8 hours on day 1, bendamustine hydrochloride IV over 30-60 minutes on days 1 and 2, and bortezomib IV over 3-5 seconds or SC on days 1, 8, 15, and 22. Treatment repeats every 35 days for up to 6 courses. Patients without disease progression continue on to maintenance therapy. MAINTENANCE: Beginning 8 weeks after the start of induction course 6, patients receive ofatumumab IV over 2-8 hours on day 1 and bortezomib IV over 3-5 seconds or SC on days 1, 8, 15, and 22. Treatment repeats every 56 days for up to 4 courses.

Drug: Bendamustine HydrochlorideDrug: BortezomibRadiation: Fludeoxyglucose F-18Other: Laboratory Biomarker AnalysisBiological: OfatumumabProcedure: Positron Emission Tomography with Radiolabeled Targeting Agent

Interventions

Given IV

Also known as: Belrapzo, Bendamustin Hydrochloride, Bendeka, CEP 18083, CEP-18083, CEP18083, Cytostasan Hydrochloride, Levact, Ribomustin, SyB L-0501, Treakisym, Treanda, VIVIMUSTA
Arm A (ofatumumab, bendamustine hydrochloride)Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)

Given IV or SC

Also known as: [(1R)-3-Methyl-1-[[(2S)-1-oxo-3-phenyl-2-[(pyrazinylcarbonyl)amino]propyl]amino]butyl]boronic Acid, LDP 341, LDP-341, LDP341, MLN 341, MLN-341, MLN341, PS 341, PS-341, PS341, Velcade
Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)

Undergo FDG-PET

Also known as: 18FDG, FDG, Fludeoxyglucose (18F), fludeoxyglucose F 18, Fludeoxyglucose F18, Fluorine-18 2-Fluoro-2-deoxy-D-Glucose, Fluorodeoxyglucose F18
Arm A (ofatumumab, bendamustine hydrochloride)Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)

Correlative studies

Arm A (ofatumumab, bendamustine hydrochloride)Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)
OfatumumabBIOLOGICAL

Given IV

Also known as: Arzerra, GSK1841157, HuMax-CD20, HuMax-CD20, 2F2, Kesimpta
Arm A (ofatumumab, bendamustine hydrochloride)Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)

Undergo FDG-PET

Also known as: Positron Emission Tomography with Radiolabeled Targeting Agents
Arm A (ofatumumab, bendamustine hydrochloride)Arm B (ofatumumab, bendamustine hydrochloride, bortezomib)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed follicular non-Hodgkin lymphoma, World Health Organization (WHO) classification grade 1, 2, or 3a (\> 15 centroblasts per high-power field with centrocytes present)
  • Bone marrow biopsies as the sole means of diagnosis are not acceptable, but they may be submitted in conjunction with nodal biopsies
  • Fine-needle aspirates are not acceptable
  • Failure to submit pathology within 60 days of patient registration will be considered a major protocol violation
  • Patients must have at least one of the following indicators of poor risk disease:
  • \>= 3 risk factors by the Follicular Lymphoma International Prognostic Index, or 2 risk factors by the Follicular Lymphoma International Prognostic Index and at least one bulky mass or lymph node \> 6 cm in size
  • Follicular Lymphoma International Prognostic Index (FLIPI score):
  • Age \> 60 years
  • Involvement of \> 4 nodal sites
  • Stage III-IV disease
  • Hemoglobin \< 12.0 g/dL
  • Lactate dehydrogenase (LDH) \> upper limit of normal (ULN)
  • of the above risk factors: low risk
  • risk factors: intermediate risk
  • \>= 3 risk factors: poor risk
  • +20 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (96)

UC San Diego Moores Cancer Center

La Jolla, California, 92093, United States

Location

Saint Helena Hospital

St. Helena, California, 94574, United States

Location

Middlesex Hospital

Middletown, Connecticut, 06457, United States

Location

Mount Sinai Medical Center

Miami Beach, Florida, 33140, United States

Location

Hawaii Cancer Care Inc - Waterfront Plaza

Honolulu, Hawaii, 96813, United States

Location

Queen's Medical Center

Honolulu, Hawaii, 96813, United States

Location

Straub Clinic and Hospital

Honolulu, Hawaii, 96813, United States

Location

Hawaii Cancer Care Inc-Liliha

Honolulu, Hawaii, 96817, United States

Location

Kuakini Medical Center

Honolulu, Hawaii, 96817, United States

Location

Kapiolani Medical Center for Women and Children

Honolulu, Hawaii, 96826, United States

Location

Castle Medical Center

Kailua, Hawaii, 96734, United States

Location

Wilcox Memorial Hospital and Kauai Medical Clinic

Lihue, Hawaii, 96766, United States

Location

Pali Momi Medical Center

‘Aiea, Hawaii, 96701, United States

Location

Queen's Cancer Center - Pearlridge

‘Aiea, Hawaii, 96701, United States

Location

Saint Alphonsus Cancer Care Center-Boise

Boise, Idaho, 83706, United States

Location

Kootenai Clinic Cancer Services - Post Falls

Post Falls, Idaho, 83854, United States

Location

University of Illinois

Chicago, Illinois, 60612, United States

Location

University of Chicago Comprehensive Cancer Center

Chicago, Illinois, 60637, United States

Location

Weiss Memorial Hospital

Chicago, Illinois, 60640, United States

Location

Cancer Care Specialists of Illinois - Decatur

Decatur, Illinois, 62526, United States

Location

Decatur Memorial Hospital

Decatur, Illinois, 62526, United States

Location

NorthShore University HealthSystem-Evanston Hospital

Evanston, Illinois, 60201, United States

Location

Ingalls Memorial Hospital

Harvey, Illinois, 60426, United States

Location

Southern Illinois University School of Medicine

Springfield, Illinois, 62702, United States

Location

Springfield Clinic

Springfield, Illinois, 62702, United States

Location

Springfield Memorial Hospital

Springfield, Illinois, 62781, United States

Location

Fort Wayne Medical Oncology and Hematology Inc-Parkview

Fort Wayne, Indiana, 46845, United States

Location

Franciscan Health Indianapolis

Indianapolis, Indiana, 46237, United States

Location

Memorial Regional Cancer Center Day Road

Mishawaka, Indiana, 46545, United States

Location

Michiana Hematology Oncology PC-Mishawaka

Mishawaka, Indiana, 46545, United States

Location

Memorial Hospital of South Bend

South Bend, Indiana, 46601, United States

Location

Michiana Hematology Oncology PC-Westville

Westville, Indiana, 46391, United States

Location

Mercy Hospital

Cedar Rapids, Iowa, 52403, United States

Location

Oncology Associates at Mercy Medical Center

Cedar Rapids, Iowa, 52403, United States

Location

Siouxland Regional Cancer Center

Sioux City, Iowa, 51101, United States

Location

Harold Alfond Center for Cancer Care

Augusta, Maine, 04330, United States

Location

Eastern Maine Medical Center

Bangor, Maine, 04401, United States

Location

Penobscot Bay Medical Center

Rockport, Maine, 04856, United States

Location

Sinai Hospital of Baltimore

Baltimore, Maryland, 21215, United States

Location

Trinity Health Saint Joseph Mercy Hospital Ann Arbor

Ann Arbor, Michigan, 48106, United States

Location

Henry Ford Health Saint John Hospital

Detroit, Michigan, 48236, United States

Location

Corewell Health Grand Rapids Hospitals - Butterworth Hospital

Grand Rapids, Michigan, 49503, United States

Location

Trinity Health Grand Rapids Hospital

Grand Rapids, Michigan, 49503, United States

Location

Fairview Ridges Hospital

Burnsville, Minnesota, 55337, United States

Location

Fairview Southdale Hospital

Edina, Minnesota, 55435, United States

Location

Minnesota Oncology Hematology PA-Maplewood

Maplewood, Minnesota, 55109, United States

Location

Saint John's Hospital - Healtheast

Maplewood, Minnesota, 55109, United States

Location

Minneapolis VA Medical Center

Minneapolis, Minnesota, 55417, United States

Location

Park Nicollet Clinic - Saint Louis Park

Saint Louis Park, Minnesota, 55416, United States

Location

Regions Hospital

Saint Paul, Minnesota, 55101, United States

Location

Central Care Cancer Center - Bolivar

Bolivar, Missouri, 65613, United States

Location

MU Health - University Hospital/Ellis Fischel Cancer Center

Columbia, Missouri, 65212, United States

Location

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, 64111, United States

Location

Mercy Hospital Springfield

Springfield, Missouri, 65804, United States

Location

CoxHealth South Hospital

Springfield, Missouri, 65807, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Missouri Baptist Medical Center

St Louis, Missouri, 63131, United States

Location

Mercy Hospital Saint Louis

St Louis, Missouri, 63141, United States

Location

Billings Clinic Cancer Center

Billings, Montana, 59101, United States

Location

Benefis Sletten Cancer Institute

Great Falls, Montana, 59405, United States

Location

Nevada Cancer Research Foundation NCORP

Las Vegas, Nevada, 89120, United States

Location

Dartmouth Hitchcock Medical Center/Dartmouth Cancer Center

Lebanon, New Hampshire, 03756, United States

Location

Hematology Oncology Associates of Central New York-East Syracuse

East Syracuse, New York, 13057, United States

Location

Northwell Health NCORP

Lake Success, New York, 11042, United States

Location

Northwell Health/Center for Advanced Medicine

Lake Success, New York, 11042, United States

Location

North Shore University Hospital

Manhasset, New York, 11030, United States

Location

Long Island Jewish Medical Center

New Hyde Park, New York, 11040, United States

Location

NYP/Weill Cornell Medical Center

New York, New York, 10065, United States

Location

State University of New York Upstate Medical University

Syracuse, New York, 13210, United States

Location

Randolph Hospital

Asheboro, North Carolina, 27203, United States

Location

UNC Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, 27599, United States

Location

Wayne Memorial Hospital

Goldsboro, North Carolina, 27534, United States

Location

Cone Health Cancer Center

Greensboro, North Carolina, 27403, United States

Location

ECU Health Oncology Kinston

Kinston, North Carolina, 28501, United States

Location

Annie Penn Memorial Hospital

Reidsville, North Carolina, 27320, United States

Location

Iredell Memorial Hospital

Statesville, North Carolina, 28677, United States

Location

Wake Forest University Health Sciences

Winston-Salem, North Carolina, 27157, United States

Location

Altru Cancer Center

Grand Forks, North Dakota, 58201, United States

Location

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210, United States

Location

Miami Valley Hospital North

Dayton, Ohio, 45415, United States

Location

Kettering Medical Center

Kettering, Ohio, 45429, United States

Location

Toledo Clinic Cancer Centers-Maumee

Maumee, Ohio, 43537, United States

Location

Saint Charles Hospital

Oregon, Ohio, 43616, United States

Location

ProMedica Flower Hospital

Sylvania, Ohio, 43560, United States

Location

Mercy Health - Saint Anne Hospital

Toledo, Ohio, 43623, United States

Location

Toledo Clinic Cancer Centers-Toledo

Toledo, Ohio, 43623, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Mercy Hospital Oklahoma City

Oklahoma City, Oklahoma, 73120, United States

Location

Providence Portland Medical Center

Portland, Oregon, 97213, United States

Location

Providence Saint Vincent Medical Center

Portland, Oregon, 97225, United States

Location

Guthrie Medical Group PC-Robert Packer Hospital

Sayre, Pennsylvania, 18840, United States

Location

Saint Francis Hospital

Greenville, South Carolina, 29601, United States

Location

Saint Francis Cancer Center

Greenville, South Carolina, 29607, United States

Location

Spartanburg Medical Center

Spartanburg, South Carolina, 29303, United States

Location

VCU Massey Comprehensive Cancer Center

Richmond, Virginia, 23298, United States

Location

West Virginia University Healthcare

Morgantown, West Virginia, 26506, United States

Location

Related Publications (2)

  • Rutherford SC, Yin J, Pederson L, Perez Burbano G, LaPlant B, Shadman M, Li H, LeBlanc ML, Kenkre VP, Hong F, Blum KA, Dockter T, Martin P, Jung SH, Grant B, Rosenbaum C, Ujjani C, Barr PM, Unger JM, Cheson BD, Bartlett NL, Kahl B, Friedberg JW, Mandrekar SJ, Leonard JP. Relevance of Bone Marrow Biopsies for Response Assessment in US National Cancer Institute National Clinical Trials Network Follicular Lymphoma Clinical Trials. J Clin Oncol. 2023 Jan 10;41(2):336-342. doi: 10.1200/JCO.21.02301. Epub 2022 Jul 5.

  • Blum KA, Polley MY, Jung SH, Dockter TJ, Anderson S, Hsi ED, Wagner-Johnston N, Christian B, Atkins J, Cheson BD, Leonard JP, Bartlett NL. Randomized trial of ofatumumab and bendamustine versus ofatumumab, bendamustine, and bortezomib in previously untreated patients with high-risk follicular lymphoma: CALGB 50904 (Alliance). Cancer. 2019 Oct 1;125(19):3378-3389. doi: 10.1002/cncr.32289. Epub 2019 Jun 7.

MeSH Terms

Interventions

Bendamustine HydrochlorideBortezomibFluorodeoxyglucose F18ofatumumabMagnetic Resonance Spectroscopy

Intervention Hierarchy (Ancestors)

ButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsBenzimidazolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsBoronic AcidsAcids, NoncarboxylicAcidsInorganic ChemicalsBoron CompoundsPyrazinesHeterocyclic Compounds, 1-RingDeoxyglucoseDeoxy SugarsCarbohydratesSpectrum AnalysisChemistry Techniques, AnalyticalInvestigative Techniques

Results Point of Contact

Title
Kristie A. Blum, MD
Organization
Alliance for Clinical Trials in Oncology

Study Officials

  • Kristie A Blum

    Alliance for Clinical Trials in Oncology

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 27, 2011

First Posted

January 31, 2011

Study Start

April 28, 2011

Primary Completion

May 24, 2017

Study Completion

September 2, 2025

Last Updated

November 24, 2025

Results First Posted

January 10, 2019

Record last verified: 2025-10

Locations