NCT01248494

Brief Summary

This is an open-label phase Ib multi-institution trial that evaluates the safety profile/tolerability and preliminary anti-tumor effect of BKM120 (a PI3K inhibitor) and endocrine therapy combination and BEZ235 (a PI3K/ mTOR inhibitor) and endocrine therapy combination in postmenopausal patients with hormone receptor-positive metastatic breast cancer.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
72

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Nov 2010

Longer than P75 for phase_1

Geographic Reach
1 country

6 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2010

Completed
22 days until next milestone

First Submitted

Initial submission to the registry

November 23, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 25, 2010

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2012

Completed
3.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2016

Completed
Last Updated

July 25, 2016

Status Verified

July 1, 2016

Enrollment Period

2.1 years

First QC Date

November 23, 2010

Last Update Submit

July 22, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Maximum Tolerated Dose of BKM120 or BEZ235 given in combination with endocrine therapy

    The maximum tolerated dose for each of the arms will be defined as the highest dose tested in which a DLT is experienced by 0 out of 3 or 1 out of 6 patients among the dose levels. The first cohort of patients (3 patients) in each arm will be started at dose level 1, and each patient will be observed for 4 weeks on the specified dose.

    at 4 weeks

Secondary Outcomes (2)

  • Number of Patients with Progression-free survival (PFS)

    4 weeks after off-treatment date

  • Response Rate (RR)

    4 weeks after off-treament date

Study Arms (3)

BEZ235 + Letrozole

EXPERIMENTAL
Drug: BEZ235Drug: Letrozole

BKM120 + Letrozole

EXPERIMENTAL
Drug: BKM 120Drug: Letrozole

Intermittent BKM120 + Letrozole

EXPERIMENTAL
Drug: LetrozoleDrug: BKM120

Interventions

BEZ235DRUG

* Dose level 1: 400mg PO BID * Dose level -1: 400mg PO in AM and 200mg PO in PM * Dose level -2: 200mg PO BID

BEZ235 + Letrozole

* Dose Level 1: BKM120, 100 mg PO daily * Dose level -1: BKM120, 80 mg PO daily * Dose Level -2: BKM120, 60 mg PO daily

BKM120 + Letrozole

All levels: 2.5mg/day PO

BEZ235 + LetrozoleBKM120 + LetrozoleIntermittent BKM120 + Letrozole
BKM120DRUG

* Dose Level 1: BKM120, 100 mg PO from Mondays through Fridays, weekly * Dose level -1: BKM120, 80 mg PO from Mondays through Fridays, weekly * Dose Level -2: BKM120, 60 mg PO from Mondays through Fridays, weekly

Intermittent BKM120 + Letrozole

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must provide informed written consent.
  • Patients must be \>/= 18 years of age.
  • ECOG performance status 0-1.
  • Clinical stage IV invasive mammary carcinoma, ER-positive and/or PR-positive by immunohistochemistry (IHC). Patients may have either measurable or nonmeasurable disease, both are allowed.
  • Patients whose breast cancers are also HER2-overexpressed (IHC 3+ or FISHpositive)need to have had previous treatment exposure to trastuzumab (Herceptin®)
  • Prior endocrine therapy (any) is allowed. There is not limit on lines of prior treatment in the metastatic setting.
  • Patients must have available tissue (archived formalin-fixed paraffin embedded blocks (FFPB) or fresh frozen tissue from original diagnosis or metastatic setting) for correlative studies. Tissue needs to be submitted at the time of registration. Patients will not be able to start study drugs without tissue availability.
  • Life expectancy \>/= 6 months
  • Patients must have adequate hematologic, hepatic, and renal function. All tests must be obtained less than 4 weeks from study entry. This includes:
  • ANC \>/= 1500/mm3
  • Platelet count \>/= 100,000/mm3
  • HgB \>/= 9 g/dL
  • Creatinine \</= 1.5X upper limits of normal
  • INR \</= 2Total serum bilirubin \</= 1.5 x ULN (in patients with known Gilbert Syndrome, a total bilirubin \</= 3.0 x ULN, with direct bilirubin \</= 1.5 x ULN)
  • AST and ALT \</= 3 x ULN (or \</= 5.0 x ULN if hepatic metastases are present)
  • +11 more criteria

You may not qualify if:

  • Locally recurrent resectable breast cancer.
  • Any kind of malabsorption syndrome significantly affecting gastrointestinal function.
  • Concurrent anti-cancer therapy (chemotherapy, radiation therapy, surgery, immunotherapy, hormonal therapy, biologic therapy) other than the ones specified in the protocol. Patients must have discontinued the above cancer therapies for 1 week prior to the first dose of study medication, as well as recovered from toxicity (to \</= than grade 1, except for alopecia) induced by previous treatments. Any investigational drugs should be discontinued 2 weeks prior to the first dose of study medication.
  • Prior therapy with a PI3K specific inhibitor. Prior use of Akt or mTOR inhibitors are allowed.
  • Use of any of the drugs (prohibited concomitant medications)
  • Patients with the following mood disorders as judged by the Investigator or a psychiatrist:
  • medically documented history of or active major depressive episode, bipolar disorder (I or II), obsessive-compulsive disorder, schizophrenia, a history of suicidal attempt or ideation, or homicidal ideation (immediate risk of doing harm to others)
  • \>/= CTCAE grade 3 anxiety
  • Meets the cut-off score of \>/= 10 in the PHQ-9 or a cut-off of \>/= 15 in the GAD-7 mood scale, respectively, or selects a positive response of "1, 2, or 3" to question number 9 regarding potential for suicidal thoughts in the PHQ-9 (independent of the total score of the PHQ-9) will be excluded from the study unless overruled by the psychiatric assessment
  • Uncontrolled intercurrent illness including, but not limited to:
  • ongoing or active infection requiring parenteral antibiotics
  • impairment of lung function (COPD \> grade 2, lung conditions requiring oxygen therapy)
  • symptomatic congestive heart failure (class III or IV of the New York Heart Association classification for heart disease)
  • Left Ventricular Ejection Fraction (LVEF) \< 50%
  • unstable angina pectoris, angioplasty, stenting, or myocardial infarction within 6 months
  • +10 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (6)

University of Alabama

Birmingham, Alabama, United States

Location

Massachusetts General Hospital, Dana Farber Cancer Center

Boston, Massachusetts, 02114, United States

Location

Columbia University Medical Center

New York, New York, United States

Location

Vanderbilt Cool Springs

Nashville, Tennessee, 37067, United States

Location

Vanderbilt Breast Center One Hundred Oaks

Nashville, Tennessee, 37204, United States

Location

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Related Links

MeSH Terms

Conditions

Breast Neoplasms

Interventions

dactolisibLetrozoleNVP-BKM120

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

NitrilesOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Ingrid Mayer, MD

    Vanderbilt-Ingram Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Assistant Professor of Medicine; Clinical Director, Breast Cancer Program; Medical Oncologist

Study Record Dates

First Submitted

November 23, 2010

First Posted

November 25, 2010

Study Start

November 1, 2010

Primary Completion

December 1, 2012

Study Completion

May 1, 2016

Last Updated

July 25, 2016

Record last verified: 2016-07

Locations