NCT01247922

Brief Summary

Participants that were assigned to the oral etoposide treatment arm in protocol OSI-774-205 and either progressed while on study or discontinued due to unacceptable toxicity related to etoposide were allowed to participate in this study to assess the safety profile of single-agent erlotinib in participants with recurrent or refractory pediatric ependymoma.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
4

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started May 2011

Shorter than P25 for phase_2

Geographic Reach
3 countries

21 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 23, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 25, 2010

Completed
6 months until next milestone

Study Start

First participant enrolled

May 23, 2011

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 13, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 13, 2012

Completed
3.3 years until next milestone

Results Posted

Study results publicly available

January 11, 2016

Completed
Last Updated

December 6, 2024

Status Verified

November 1, 2024

Enrollment Period

1.3 years

First QC Date

November 23, 2010

Results QC Date

October 26, 2015

Last Update Submit

November 19, 2024

Conditions

Keywords

Pediatric EpendymomaEpendymomaTarcevaErlotinib

Outcome Measures

Primary Outcomes (1)

  • Safety Assessed Through Evaluation of Physical Examinations, Vital Signs, Clinical Laboratory Tests, and Adverse Events (AEs)

    Safety is monitored through AEs, which includes abnormal or clinically significant vital sign assessments, laboratory test, physical examination findings associated with signs and/or symptoms requiring withdrawal, dose modification or medical intervention. A treatment-emergent adverse event (TEAE) was defined as an adverse event observed after starting administration of the study drug. An AE was considered serious (SAE) if it resulted in death, a life-threatening situation, inpatient hospitalization or prolongation of an existing hospitalization, persistent or significant disability/incapacity, congenital anomaly/birth defect in the offspring of a patient who received study drug or other important medical events.

    From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days)

Secondary Outcomes (2)

  • Best Overall Response

    End of treatment (The mean treatment duration was 170.5 days.)

  • Median Treatment Duration

    From first dose of study drug up to last dose of study drug (The mean treatment duration was 170.5 days)

Study Arms (1)

Erlotinib

EXPERIMENTAL

Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.

Drug: Erlotinib

Interventions

continuous oral Erlotinib 85 mg/m\^2 per day

Also known as: Tarceva, OSI-774
Erlotinib

Eligibility Criteria

Age1 Year - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients must have been enrolled in OSI-774-205, been randomized to oral etoposide and either progressed while on study or discontinued due to unacceptable toxicity related to etoposide
  • Performance status: Lansky ≥ 50% for patients ≤ 10 years of age or younger or Karnofsky ≥ 50% for patients greater than 10 years of age
  • Patients must have recovered from any acute toxicity to any prior anti-cancer treatment
  • Total bilirubin ≤ 1.5 x upper limit of normal (ULN) for age, serum glutamic pyruvic transaminase (SGPT) ALT ≤ 3 x ULN
  • Serum creatinine based on age OR Creatinine Clearance/Glomerular Filtration Rate (GFR) ≥ 70 mL/min/m2
  • Patients must be neurologically stable for at least 7 days before registration
  • Patients, both males and females, with reproductive potential must agree to practice effective contraceptive measures for the duration of study drug therapy and for at least 90 days after completion of study drug therapy
  • Patients must be able to take erlotinib orally

You may not qualify if:

  • Taking strong/moderate CYP3A4 or CYP1A2 inhibitors/inducers ≤ 14 days before registration
  • Have received any other chemotherapy or immunotherapy to treat ependymoma after discontinuation from OSI-774-205
  • Taking proton pump inhibitors ≤ 14 days before registration
  • Participating in another investigational drug trial while on study
  • Pregnant or breast-feeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (21)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Children's Hospital of Orange County (CHOC)

Orange, California, 92868, United States

Location

Packard Children's Hospital

Palo Alto, California, 94304, United States

Location

The Children's Hospital Center for Cancer and Blood Disorders

Aurora, Colorado, 80045, United States

Location

Children's National Medical Center -D.C. Center for Cancer and Blood Disorders

Washington D.C., District of Columbia, 20010, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Emory University Children's Healthcare of Atlanta

Atlanta, Georgia, 30322, United States

Location

University of Minnesota - Amplatz Children's Hospital

Minneapolis, Minnesota, 55455, United States

Location

Oregon Health & Sciences University Doernbecher Children's Hospital

Portland, Oregon, 97124, United States

Location

Childrens Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

University of Wisconsin

Madison, Wisconsin, 53705-2275, United States

Location

Stollery Children's Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

Children's and Women's Health Center of BC

Vancouver, British Columbia, V6H 3V4, Canada

Location

Hospital for Sick Children

Toronto, Ontario, M5G 1X8, Canada

Location

Birmingham Children's Hospital Oncology Department

Birmingham, B4 6NH, United Kingdom

Location

Royal Hospital for Sick Children

Glasgow, G3 8SJ, United Kingdom

Location

Paediatric Oncology and Haematology Offices,

Leeds, LS1 3EX, United Kingdom

Location

Alder Hey Children's NHS Foundation Trust

Liverpool, L12 1AP, United Kingdom

Location

Royal Manchester Children's Hospital Ward 84

Manchester, M13 9W2, United Kingdom

Location

University of Nottingham

Nottingham, NG7 2UH, United Kingdom

Location

Royal Marsden Hospital

Sutton, SM2 5pt, United Kingdom

Location

Related Links

MeSH Terms

Conditions

EpendymomaFamilial ependymoma

Interventions

Erlotinib Hydrochloride

Condition Hierarchy (Ancestors)

GliomaNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Intervention Hierarchy (Ancestors)

QuinazolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Limitations and Caveats

Company makes no warranties or representations of any kind as to the posting, expressed or implied, including warranties of merchantability and fitness for a particular purpose, and shall not be liable for any damages.

Results Point of Contact

Title
Sr. Medical Director
Organization
Astellas Pharma Global Development, Inc.

Study Officials

  • Medical Monitor

    Astellas Pharma Global Development

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 23, 2010

First Posted

November 25, 2010

Study Start

May 23, 2011

Primary Completion

September 13, 2012

Study Completion

September 13, 2012

Last Updated

December 6, 2024

Results First Posted

January 11, 2016

Record last verified: 2024-11

Data Sharing

IPD Sharing
Will not share

Access to anonymized individual participant level data will not be provided for this trial. Further details on Astellas' data sharing policy can be found at https://www.clinicaltrials.astellas.com/transparency/.

Locations