NCT01208831

Brief Summary

The purpose of this study is to determine Maximum Tolerated Dose (MTD) or recommended phase II dose of LDE225 when administered orally to two adult patient groups of East Asian (i.e., Japanese and Chinese/Taiwanese) with advanced solid tumors that have progressed despite standard therapy or for which no standard therapy exists.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
45

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Oct 2010

Typical duration for phase_1

Geographic Reach
3 countries

4 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 21, 2010

Completed
3 days until next milestone

First Posted

Study publicly available on registry

September 24, 2010

Completed
7 days until next milestone

Study Start

First participant enrolled

October 1, 2010

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2013

Completed
Last Updated

December 19, 2020

Status Verified

April 1, 2016

Enrollment Period

3 years

First QC Date

September 21, 2010

Last Update Submit

December 16, 2020

Conditions

Keywords

Advanced tumorshedgehogsmoothened inhibitor

Outcome Measures

Primary Outcomes (1)

  • determine maximum tolerated dose of single agent LDE225

    28 day cycles

Secondary Outcomes (3)

  • characterize safety and tolerability

    28 day cycles

  • characterize pharmacokinetics (PK) of single and repeated doses of LDE225

    28 day cycles

  • assess preliminary anti-tumor activity

    28 day cycles

Study Arms (1)

LDE225

EXPERIMENTAL
Drug: LDE225

Interventions

LDE225DRUG
LDE225

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • confirmed diagnosis of advanced solid tumor (including medulloblastoma and basal cell carcinoma)
  • blood work criteria

You may not qualify if:

  • patients with history of brain tumor (except recurrent medulloblastoma) or brain metastases
  • positive HIV, hepatitis B or C
  • impaired intestinal function
  • impaired heart function
  • pregnant or breast-feeding women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

Novartis Investigative Site

Hong Kong, Hong Kong

Location

Novartis Investigative Site

Nagoya, Aichi-ken, 466-8560, Japan

Location

Novartis Investigative Site

Kobe, Hyōgo, 650-0017, Japan

Location

Novartis Investigative Site

Taipei, 10048, Taiwan

Location

Related Publications (1)

  • Minami H, Ando Y, Ma BB, Hsiang Lee J, Momota H, Fujiwara Y, Li L, Fukino K, Ito K, Tajima T, Mori A, Lin CC. Phase I, multicenter, open-label, dose-escalation study of sonidegib in Asian patients with advanced solid tumors. Cancer Sci. 2016 Oct;107(10):1477-1483. doi: 10.1111/cas.13022. Epub 2016 Sep 24.

Related Links

MeSH Terms

Conditions

MedulloblastomaCarcinoma, Basal Cell

Interventions

sonidegib

Condition Hierarchy (Ancestors)

GliomaNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeuroectodermal Tumors, PrimitiveNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueCarcinomaNeoplasms, Basal Cell

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 21, 2010

First Posted

September 24, 2010

Study Start

October 1, 2010

Primary Completion

October 1, 2013

Study Completion

October 1, 2013

Last Updated

December 19, 2020

Record last verified: 2016-04

Locations