Medulloblastoma
114
19
32
43
Key Insights
Highlights
Success Rate
81% trial completion
Published Results
27 trials with published results (24%)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 49/100
8.8%
10 terminated out of 114 trials
81.1%
-5.5% vs benchmark
6%
7 trials in Phase 3/4
63%
27 of 43 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 43 completed trials
Clinical Trials (114)
Arsenic Trioxide Combined With Chemotherapy for Relapsed SHH-Activated and/or TP53-Mutant Medulloblastoma
Exploratory Study of Effects of Radiation Therapy in Pediatric Patients With Central Nervous System Tumors
Liothyronine in Combination With BIT Regimen for Medulloblastoma With or Without Minimal Residual Disease
Rare CNS Tumors Outcomes &Risk
Pharmacoscopy for Patients With Refractory Primary Brain Tumors
Molecular and Clinical Risk-Directed Therapy for Infants and Young Children With Newly Diagnosed Medulloblastoma
GPC2-CAR T Cell Therapy for Relapsed or Refractory Medulloblastoma in Children and Young Adults
PEP-CMV + Nivolumab for Newly Diagnosed Diffuse Midline Glioma/High-grade Glioma and Recurrent Diffuse Midline Glioma/High-grade Glioma, Medulloblastoma, and Ependymoma
B7-H3.CD28Z.CART in CNS Neoplasms
Digoxin Medulloblastoma Study
Parental Distress and Treatment Adherence in Pediatric Recurrent Medulloblastoma
Immune Checkpoint Inhibitor Nivolumab in People With Recurrent Select Rare CNS Cancers
Clinical Studies of Gemcitabine-Oxaliplatin
Phase I Study of APX005M in Pediatric Central Nervous System Tumors
Vaccine Immunotherapy for Recurrent Medulloblastoma and Primitive Neuroectodermal Tumor
DFMO as Maintenance Therapy for Molecular High/Very High Risk and Relapsed Medulloblastoma
PLX038 in Primary Central Nervous System Tumors Containing MYC or MYCN Amplifications
Individualized Treatment Plan in Children and Young Adults With Relapsed Medulloblastoma and Ependymoma
Accurate Diagnosis and Grading of Pediatric Solid Tumors Based on Pathological Large Models
Atovaquone Combined With Radiation in Children With Malignant Brain Tumors