Key Insights

Highlights

Success Rate

81% trial completion

Published Results

27 trials with published results (24%)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 49/100

Termination Rate

8.8%

10 terminated out of 114 trials

Success Rate

81.1%

-5.5% vs benchmark

Late-Stage Pipeline

6%

7 trials in Phase 3/4

Results Transparency

63%

27 of 43 completed with results

Key Signals

27 with results81% success

Data Visualizations

Phase Distribution

97Total
Not Applicable (8)
Early P 1 (3)
P 1 (48)
P 2 (31)
P 3 (5)
P 4 (2)

Trial Status

Completed43
Recruiting19
Active Not Recruiting13
Not Yet Recruiting10
Terminated10
Unknown10

Trial Success Rate

81.1%

Benchmark: 86.6%

Based on 43 completed trials

Clinical Trials (114)

Showing 20 of 20 trials
NCT07856069Phase 2Not Yet RecruitingPrimary

Arsenic Trioxide Combined With Chemotherapy for Relapsed SHH-Activated and/or TP53-Mutant Medulloblastoma

NCT01445288Completed

Exploratory Study of Effects of Radiation Therapy in Pediatric Patients With Central Nervous System Tumors

NCT07346157Phase 1RecruitingPrimary

Liothyronine in Combination With BIT Regimen for Medulloblastoma With or Without Minimal Residual Disease

NCT03251989Completed

Rare CNS Tumors Outcomes &Risk

NCT06804655Phase 2Recruiting

Pharmacoscopy for Patients With Refractory Primary Brain Tumors

NCT05535166Phase 2RecruitingPrimary

Molecular and Clinical Risk-Directed Therapy for Infants and Young Children With Newly Diagnosed Medulloblastoma

NCT07087002Phase 1RecruitingPrimary

GPC2-CAR T Cell Therapy for Relapsed or Refractory Medulloblastoma in Children and Young Adults

NCT06639607Phase 1Suspended

PEP-CMV + Nivolumab for Newly Diagnosed Diffuse Midline Glioma/High-grade Glioma and Recurrent Diffuse Midline Glioma/High-grade Glioma, Medulloblastoma, and Ependymoma

NCT07390539Phase 1Recruiting

B7-H3.CD28Z.CART in CNS Neoplasms

NCT06701812Phase 2RecruitingPrimary

Digoxin Medulloblastoma Study

NCT07660458WithdrawnPrimary

Parental Distress and Treatment Adherence in Pediatric Recurrent Medulloblastoma

NCT03173950Phase 2TerminatedPrimary

Immune Checkpoint Inhibitor Nivolumab in People With Recurrent Select Rare CNS Cancers

NCT00407433Phase 2CompletedPrimary

Clinical Studies of Gemcitabine-Oxaliplatin

NCT03389802Phase 1Completed

Phase I Study of APX005M in Pediatric Central Nervous System Tumors

NCT01326104Phase 2CompletedPrimary

Vaccine Immunotherapy for Recurrent Medulloblastoma and Primitive Neuroectodermal Tumor

NCT04696029Phase 2RecruitingPrimary

DFMO as Maintenance Therapy for Molecular High/Very High Risk and Relapsed Medulloblastoma

NCT06161519Phase 1Recruiting

PLX038 in Primary Central Nervous System Tumors Containing MYC or MYCN Amplifications

NCT05057702Not ApplicableRecruitingPrimary

Individualized Treatment Plan in Children and Young Adults With Relapsed Medulloblastoma and Ependymoma

NCT06822842Completed

Accurate Diagnosis and Grading of Pediatric Solid Tumors Based on Pathological Large Models

NCT06624371Phase 1Recruiting

Atovaquone Combined With Radiation in Children With Malignant Brain Tumors

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Research Network

Activity Timeline