NCT01155453

Brief Summary

This is an open label, dose finding, phase Ib clinical trial to determine the maximum tolerated dose (MTD) and /or recommended phase II dose (RP2D) and schedule for the PI3K (Phosphatidylinositol 3-Kinase) inhibitor BKM120 given in combination with the MEK inhibitor GSK1120212 in patients with selected, advanced solid tumors. The focus will be on tumors with RAS/RAF mutations and on triple negative breast cancer. Both study drugs will be administered once daily orally on a continuous schedule, a treatment cycle is defined as 28 days. Cohorts of at least 3 and up to a maximum of 6 patients eligible for the dose-determining set will be enrolled per dose combination below the MTD. The MTD is defined as the highest drug dosage not causing in the first cycle of treatment medically unacceptable, dose-limiting toxicity (DLT) in more than 33% of the treated patients.. At least 12 patients will be required at MTD and 6 patients at RP2D level to allow the evaluation of the combination's safety and pharmacokinetics or pharmacodynamics. Upon declaration of MTD and/or RP2D, patients will be enrolled to an expansion part of the study, to further assess safety, as well as to learn more about the efficacy of the study drug combination.

  • Expansion Arm 1 will consist of approximately 15 patients with RAS or BRAF mutant advanced NSCLC
  • Expansion Arm 2 will consist of approximately 15 patients with RAS or BRAF-mutant ovarian cancer
  • Expansion Arm 3 will consist of approximately 15 patients with RAS or BRAF-mutant pancreatic cancer

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
113

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Apr 2010

Longer than P75 for phase_1

Geographic Reach
5 countries

7 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2010

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

June 17, 2010

Completed
14 days until next milestone

First Posted

Study publicly available on registry

July 1, 2010

Completed
4.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2014

Completed
Last Updated

December 9, 2020

Status Verified

June 1, 2016

Enrollment Period

4.6 years

First QC Date

June 17, 2010

Last Update Submit

December 6, 2020

Conditions

Keywords

BKM120RAS RAF mutations,triple negative breast cancer,pancreatic cancer,PI3K inhibitor,MEK inhibitor

Outcome Measures

Primary Outcomes (1)

  • Maximum Tolerated Dose (MTD) and/or recommended phase II dose (RP2D) and schedule of BKM120+GSK1120212

    in average 1 year

Secondary Outcomes (5)

  • Measure the number of Adverse Event and laboratory values that fall outside of pre-determined ranges as a measure of Safety and tolerability of the oral combination of BKM120 and GSK1120212

    in average 1 year

  • Determine the single and multiple dose pharmacokinetics of BKM120 and GSK1120212 in measurement of the plasma concentration profiles of BKM120 and GSK1120212

    Assessed during the first Cycle (28 days) of treatment

  • Preliminary anti-tumor activity of the combination

    Assessed every 8 weeks of treatment

  • Treatment-induced PI3K and MEK/ERK(Mitogen-activated protein kinase /extracellular-signal-regulated kinases) pathway signaling inhibition and evidence of biological activity in tumor and skin

    Assessed every 2 weeks during the first cycle, then every 4 weeks

  • Molecular status (genetic alterations, protein expression and/or activation) of markers related to PI3K and ERK signaling in tumor tissue and blood and investigate their potential relationship to clinical responses

    Assessed at baseline (pre-treatment)

Study Arms (4)

BKM120 + GSK1120212 DE

EXPERIMENTAL

Dose Escalation

Drug: BKM120Drug: GSK1120212

BKM120 + GSK1120212 NSCLC patients

EXPERIMENTAL

Advanced RAS or BRAF mutant NSCLC patients

Drug: BKM120Drug: GSK1120212

BKM120 + GSK1120212 ovarian cancer patients

EXPERIMENTAL

Advanced RAS or BRAF mutant ovarian cancer patients

Drug: BKM120Drug: GSK1120212

BKM120 + GSK1120212 pancreatic cancer patients

EXPERIMENTAL

Advanced RAS or BRAF mutant pancreatic cancer patients

Drug: BKM120Drug: GSK1120212

Interventions

BKM120DRUG
BKM120 + GSK1120212 DEBKM120 + GSK1120212 NSCLC patientsBKM120 + GSK1120212 ovarian cancer patientsBKM120 + GSK1120212 pancreatic cancer patients
BKM120 + GSK1120212 DEBKM120 + GSK1120212 NSCLC patientsBKM120 + GSK1120212 ovarian cancer patientsBKM120 + GSK1120212 pancreatic cancer patients

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • histologically/ cytologically confirmed, advanced non resectable solid tumors
  • Measurable or non-measurable, but evaluable disease as determined by RECIST 1.0

You may not qualify if:

  • Patients with primary Central Nervous System (CNS) tumor or CNS tumor involvement.
  • Clinically manifested diabetes mellitus - Unacceptable ocular/retinal conditions

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (7)

University of California at Los Angeles Div. of Hematology/Oncology

Los Angeles, California, 90095, United States

Location

University of Texas/MD Anderson Cancer Center Dept of MD Anderson (8)

Houston, Texas, 77030-4009, United States

Location

Novartis Investigative Site

Leuven, 3000, Belgium

Location

Novartis Investigative Site

Toronto, Ontario, M5G 2M9, Canada

Location

Novartis Investigative Site

Seville, Andalusia, 41013, Spain

Location

Novartis Investigative Site

Barcelona, Catalonia, 08035, Spain

Location

Novartis Investigative Site

Bellinzona, 6500, Switzerland

Location

Related Links

MeSH Terms

Conditions

Triple Negative Breast NeoplasmsPancreatic Neoplasms

Interventions

NVP-BKM120trametinib

Condition Hierarchy (Ancestors)

Breast NeoplasmsNeoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesDigestive System NeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 17, 2010

First Posted

July 1, 2010

Study Start

April 1, 2010

Primary Completion

November 1, 2014

Study Completion

November 1, 2014

Last Updated

December 9, 2020

Record last verified: 2016-06

Locations