NCT01153919

Brief Summary

RATIONALE: Romiplostim may cause the body to make platelets. PURPOSE: This randomized phase II trial is studying how well romiplostim works in treating hepatitis C-infected patients with thrombocytopenia.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
27

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Jun 2010

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 24, 2010

Completed
6 days until next milestone

First Posted

Study publicly available on registry

June 30, 2010

Completed
Same day until next milestone

Study Start

First participant enrolled

June 30, 2010

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 14, 2014

Completed
4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 14, 2018

Completed
Last Updated

April 11, 2017

Status Verified

April 1, 2017

Enrollment Period

4 years

First QC Date

June 24, 2010

Last Update Submit

April 9, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean platelet count for actively treated and placebo treated subjects

    Weeks 6-8

Secondary Outcomes (5)

  • Incidence of adverse events, including clinically significant changes in laboratory values and the incidence of antibody formation

    Weeks 1-24

  • Number of subjects in each treatment group who achieve a platelet count of greater or equal to 100,000/L

    Week 8

  • Number of patients originally receiving active treatment who maintain a platelet count > 50,000/L while receiving anti-viral therapy with pegylated interferon and ribavirin

    Weeks 9-24

  • Changes in plasma HCV viral load during treatment with romiplostim alone

    Weeks 1-8

  • Incidence of sustained viral response achieved during treatment with anti-viral therapy in combination with romiplostim

    Weeks 9-24

Study Arms (2)

Arm I

ACTIVE COMPARATOR

Patients receive romiplostim subcutaneously once weekly for 8 weeks in the absence of disease progression or unacceptable toxicity.

Biological: romiplostimDrug: ribavirinBiological: PEG-interferon alfa-2aOther: laboratory biomarker analysis

Arm II

PLACEBO COMPARATOR

Patients receive placebo subcutaneously once weekly for 8 weeks. Patients failing to achieve a platelet count of \> 100,000/L cross over to arm I.

Drug: ribavirinOther: placeboBiological: PEG-interferon alfa-2aOther: laboratory biomarker analysis

Interventions

romiplostimBIOLOGICAL

Given subcutaneously

Also known as: AMG 531, Amgen megakaryopoiesis protein 2, Nplate
Arm I

Given orally

Also known as: ICN-1229, Rebetol, RIBA, RTCA, Viramide, Virazole
Arm IArm II
placeboOTHER

Given subcutaneously

Also known as: PLCB
Arm II

Given subcutaneously

Also known as: PEG-IFNA2a, PEGASYS, pegylated interferon alfa-2a
Arm IArm II

Correlative studies

Arm IArm II

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • All patients with HCV virus infection documented by detectable plasma HCV antibodies and RNA who would be excluded by FDA criteria for antiviral treatment with peginterferon-alpha 2a and ribavirin due to thrombocytopenia (platelets \< 70,000/L); patients cannot have received previous anti-viral therapy with interferon/ribavirin
  • Liver biopsy indicating chronic hepatitis within the previous 2 years
  • Mean platelet count of \< 70,000/L on two repeated measurements in a two week screening period with no single count \>= 75,000/L
  • Neutrophil count of \>= 1000/mcl
  • Hemoglobin \>= 11gm/dL and no evidence of active bleeding
  • Prothrombin Time (PT) INR \< 1.6 seconds
  • Albumin \>= 2.5 gm/dL
  • ALT \>= 1.2 and \< 10 times upper limit of normal
  • No evidence of either ischemic change or cardiac injury on 12-lead electrocardiogram (EKG)
  • Negative pregnancy test and women must be using adequate contraception for at least 2 weeks prior to enrollment and while enrolled in the study
  • Signed informed consent within 2 weeks of enrollment and randomization

You may not qualify if:

  • Received previous anti-viral therapy with interferon/ribavirin
  • Child's Class B and C or acute decompensated liver disease
  • Human Immunodeficiency Virus (HIV) infection or co-infected with hepatitis B virus
  • Any untreated active infection
  • Active malignancy, known primary bone marrow disorder (myelodysplasia, myeloproliferative disease, etc.), or history of blood or bone marrow transplantation; patients with documented hemoglobinopathies
  • Active vasculitis associated with cryoglobulinemia as manifested by either renal disease or dermatologic findings
  • Positive pregnancy test or men with pregnant partners
  • Creatinine and BUN of greater than twice (2x) the upper limits of normal
  • History of venous or arterial thrombosis, myocardial infarction or thrombotic stroke
  • Patients who in the investigators opinion will fail to be compliant or have other contraindication to treatment on this study
  • Other inherited or acquired liver disease
  • Previous solid organ transplant
  • Known hypersensitivity to E. coli derived recombinant proteins
  • Active rheumatologic disease including Systemic Lupus Erythematosis
  • Known history of Disseminated Intravascular Coagulation, Hemolytic Uremic Syndrome, or Thrombotic Thrombocytopenic Purpura

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

USC/Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

MeSH Terms

Conditions

Hepatitis CThrombocytopenia

Interventions

romiplostimRibavirinpeginterferon alfa-2a

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsHepatitis, Viral, HumanVirus DiseasesFlaviviridae InfectionsRNA Virus InfectionsHepatitisLiver DiseasesDigestive System DiseasesBlood Platelet DisordersHematologic DiseasesHemic and Lymphatic DiseasesCytopenia

Intervention Hierarchy (Ancestors)

RibonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Study Officials

  • Howard Liebman

    University of Southern California

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
CROSSOVER
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 24, 2010

First Posted

June 30, 2010

Study Start

June 30, 2010

Primary Completion

July 14, 2014

Study Completion

July 14, 2018

Last Updated

April 11, 2017

Record last verified: 2017-04

Locations