NCT01149096

Brief Summary

This randomized clinical trial is studying the side effects of collection of bone marrow from donors treated with or without filgrastim. Giving colony-stimulating factors, such as filgrastim (G-CSF), to donors helps the stem cells move from the bone marrow to the blood so they can be collected and stored.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
13

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jun 2010

Longer than P75 for phase_3

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 14, 2010

Completed
8 days until next milestone

First Submitted

Initial submission to the registry

June 22, 2010

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 23, 2010

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 14, 2011

Completed
4.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 30, 2016

Completed
3.4 years until next milestone

Results Posted

Study results publicly available

February 26, 2020

Completed
Last Updated

February 26, 2020

Status Verified

September 1, 2019

Enrollment Period

1.5 years

First QC Date

June 22, 2010

Results QC Date

December 18, 2019

Last Update Submit

February 13, 2020

Conditions

Outcome Measures

Primary Outcomes (7)

  • Percentage of Participants With Short-term Adverse Events in G-CSF (Filgrastim) Stimulated Bone Marrow (G-BM) Donors

    The Kaplan-Meier method will be used to estimate the cumulative incidence of short term adverse events defined by having any of the following events: 1) death due to a cause that is unknown or possibly related to G-CSF, 2) development of a malignancy, 3) development of a splenic rupture, or 4) development of a severe acute lung injury possibly related to GCSF therapy.

    Up to 1 year after donation

  • Percentage of Participants Who Experienced Death in G-CSF Stimulated-bone Marrow (G-BM) Donors

    The Kaplan-Meier method will be used to estimate the cumulative incidence of death event in G-BM donors only.

    Up to 1 year after donation

  • Percentage of Participants With Grade 1 or 2 Toxicities

    Estimate the percentage of patients having non-fatal complications of CTCAE Grades 1 or 2 in standard BM and G-CSF stimulated-bone marrow (G-BM) donors.

    Up to 1 year after donation

  • Percentage of Participants With Grade 3 or 4 Toxicities

    Estimate the percentage of patients having non-fatal complications of Grade 3 other than pain (consider Grade 4 for pain only), or any of Grade 4 in standard BM and G-CSF stimulated-bone marrow (G-BM) donors. Modified Toxicity Criteria and Pain Assessment was used with higher grades corresponding to more severe AEs.

    Up to 1 year after donation

  • 10-year Mortality Rate in Marrow Donors

    The Kaplan-Meier method will be used to estimate overall survival probabilities in standard BM and G-BM donors.

    Up to 10 years post bone marrow harvest

  • 10-year Overall Cancer Incidence

    The Kaplan-Meier method will be used to estimate overall cancer free probabilities in standard BM and G-BM donors.

    Up to 10 years post bone marrow harvest

  • 10-year Hematologic Cancer Rate

    The Kaplan-Meier method will be used to estimate hematologic cancer probabilities in standard BM and G-BM donors.

    Up to 10 years post bone marrow harvest

Secondary Outcomes (4)

  • Absolute T Cell Numbers

    Up to 1 year after donation

  • Th1 vs. Th2 Profile of T Cells

    Up to 1 year after donation

  • Dendritic Cell (DC) Populations

    Up to 1 year after donation

  • T Regulatory Cell Content

    Up to 1 year after donation

Study Arms (2)

Arm I (conventional bone marrow harvest)

ACTIVE COMPARATOR

Donors undergo conventional (i.e., unstimulated) bone marrow harvest on day 0.

Procedure: Bone Marrow DonationOther: Laboratory Biomarker Analysis

Arm II (filgrastim, bone marrow harvest)

EXPERIMENTAL

Donors receive filgrastim subcutaneously on days -4 through 0. Donors then undergo bone marrow harvest on day 0.

Procedure: Bone Marrow DonationBiological: FilgrastimOther: Laboratory Biomarker Analysis

Interventions

Undergo bone marrow harvest

Arm I (conventional bone marrow harvest)Arm II (filgrastim, bone marrow harvest)
FilgrastimBIOLOGICAL

Given subcutaneously

Also known as: G-CSF, Neupogen, r-metHuG-CSF, Recombinant Methionyl Human Granulocyte Colony Stimulating Factor, rG-CSF, Tevagrastim
Arm II (filgrastim, bone marrow harvest)

Optional correlative studies

Arm I (conventional bone marrow harvest)Arm II (filgrastim, bone marrow harvest)

Eligibility Criteria

Sexall
Healthy VolunteersYes
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Appropriately human leukocyte antigen (HLA)-matched (HLA, A, B, DRB1 identical or antigen mismatched \[i.e., 5/6 or 6/6 antigens matched\]) sibling of the bone marrow recipient enrolled on COG-ASCT0631
  • Adequate size relative to the recipient (i.e., harvesting the maximum of 20 cc/kg from the donor would result in a bone marrow graft that will provide an adequate cell and volume dose to the recipient, in the opinion of the treating physician)
  • Enrolled on the COG Umbrella Long-Term Follow-Up Study COG-ALTE05N1
  • Not pregnant or nursing
  • No human immunodeficiency virus (HIV) positivity
  • No sickle cell trait or sickle cell anemia/disease
  • Not at an increased risk from bone marrow donation after filgrastim administration due to a pre-existing medical condition, as determined by an independent physician separate from the research team
  • None of the following:
  • Active infection, especially pulmonary
  • Splenomegaly or a history of splenic injury
  • Active or recent pulmonary disease (i.e., pneumonia within the past 4 weeks)
  • A condition that would make the donor unsuitable to donate, as determined by an independent physician separate from the research team
  • No autoimmune disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

UCSF Medical Center-Parnassus

San Francisco, California, 94143, United States

Location

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

Location

Johns Hopkins All Children's Hospital

St. Petersburg, Florida, 33701, United States

Location

Lurie Children's Hospital-Chicago

Chicago, Illinois, 60611, United States

Location

Indiana University/Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

Norton Children's Hospital

Louisville, Kentucky, 40202, United States

Location

Johns Hopkins University/Sidney Kimmel Cancer Center

Baltimore, Maryland, 21287, United States

Location

C S Mott Children's Hospital

Ann Arbor, Michigan, 48109, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Children's Mercy Hospitals and Clinics

Kansas City, Missouri, 64108, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

New York Medical College

Valhalla, New York, 10595, United States

Location

UNC Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, 27599, United States

Location

Rainbow Babies and Childrens Hospital

Cleveland, Ohio, 44106, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Childrens Oncology Group

Philadelphia, Pennsylvania, 19104, United States

Location

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

Vanderbilt University/Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Primary Children's Hospital

Salt Lake City, Utah, 84113, United States

Location

Virginia Commonwealth University/Massey Cancer Center

Richmond, Virginia, 23298, United States

Location

MeSH Terms

Interventions

FilgrastimGranulocyte Colony-Stimulating Factor

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Results Reporting Coordinator
Organization
Children's Oncology Group

Study Officials

  • Stephan A Grupp

    Children's Oncology Group

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
SUPPORTIVE CARE
Intervention Model
PARALLEL
Sponsor Type
NETWORK
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 22, 2010

First Posted

June 23, 2010

Study Start

June 14, 2010

Primary Completion

December 14, 2011

Study Completion

September 30, 2016

Last Updated

February 26, 2020

Results First Posted

February 26, 2020

Record last verified: 2019-09

Locations