NCT01082640

Brief Summary

The purpose of this study is to determine the effect of febuxostat, once daily (QD) or twice daily (BID), on renal function in gout patients with elevated serum urate levels and who have moderate to severe renal impairment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
96

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Apr 2010

Geographic Reach
1 country

58 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 5, 2010

Completed
3 days until next milestone

First Posted

Study publicly available on registry

March 8, 2010

Completed
24 days until next milestone

Study Start

First participant enrolled

April 1, 2010

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2012

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

September 25, 2013

Completed
Last Updated

September 25, 2013

Status Verified

September 1, 2013

Enrollment Period

2.1 years

First QC Date

March 5, 2010

Results QC Date

May 31, 2013

Last Update Submit

September 23, 2013

Conditions

Keywords

GoutphysiologyHyperuricemiaUric AcidDrug Therapy

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline to Month 12 in Serum Creatinine

    Renal function was assessed by measuring the change from Baseline in serum creatinine. Analyses were conducted by the Central Laboratory.

    Baseline and Month 12

Secondary Outcomes (4)

  • Change From Baseline to Month 12 in Estimated Glomerular Filtration Rate (eGFR)

    Baseline and Month 12

  • Percentage of Participants With Serum Urate (sUA) Less Than 6 mg/dL at Month 12

    Month 12

  • Mean Clearance (CL/F) of Febuxostat at Steady State

    The 2 pre-dose PK samples collected were collected at any 2 of the following visits: Months 3, 6, 9, and/or 12, at -0.25 to 0 hours. The 4 postdose PK samples were collected at Months 3, 6, and/or 9, at 0.25; 0.75 to 2.0; 2.5 to 4.0; and 5 to 12 hours.

  • Mean Area Under the Concentration-Time Curve During the Dosing Interval (AUC[0-Ï„]) of Febuxostat at Steady State

    The 2 pre-dose PK samples collected were collected at any 2 of the following visits: Months 3, 6, 9, and/or 12, at -0.25 to 0 hours. The 4 postdose PK samples were collected at Months 3, 6, and/or 9, at 0.25; 0.75 to 2.0; 2.5 to 4.0; and 5 to 12 hours.

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Placebo-matching capsules, orally, twice daily for up to 12 months.

Drug: Placebo

Febuxostat 30 mg BID

EXPERIMENTAL

Febuxostat 30 mg, capsules, orally, twice daily (BID) for up to 12 months.

Drug: Febuxostat

Febuxostat 40/80 mg QD

EXPERIMENTAL

Participants initially received febuxostat 40 mg, capsules, once daily (QD) and one placebo-matching capsule QD and remained on this dose for up to 12 months if their serum urate (sUA) was \<6.0 mg/dL at the Day 14 visit. Participants whose sUA was ≥6.0 mg/dL at the Day 14 visit received febuxostat 80 mg, capsule, QD, and one placebo-matching capsule QD at the Month 1 visit, and for the remainder of the study.

Drug: FebuxostatDrug: Placebo

Interventions

Febuxostat capsules

Also known as: Uloric, TMX-67
Febuxostat 30 mg BIDFebuxostat 40/80 mg QD

Febuxostat placebo-matching capsules

Febuxostat 40/80 mg QDPlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have a serum urate greater than 7 mg/dL and a serum creatinine greater than or equal to 1.5 mg at Day -21
  • Must have a history or presence of gout defined as having one or more of the American Rheumatism Association criteria for the diagnosis of gout (the criteria related to tophi have been excluded for the purpose of the study)
  • Must have an estimated Glomerular Filtration Rate (eGFR) of 15 or greater, or less than or equal to 50 mL/min, AND a serum creatinine greater than 1.5 mg/dL at Screening Visit Day -21

You may not qualify if:

  • Has secondary hyperuricemia (eg, due to myeloproliferative disorder, or organ transplant)
  • Has tophaceous gout
  • Has a history of xanthinuria
  • Has received aspirin greater than 325 mg/day within 35 days prior to Day 1/Randomization Visit
  • Has known hypersensitivity or allergy to allopurinol or any component in its formulation
  • Has known hypersensitivity to febuxostat or colchicine or any components in their formulation
  • Has myocardial infarction or stroke within the 90 days prior to the Screening Visit
  • Has alanine aminotransferase and/or aspartate aminotransferase values greater than 2.0 times the upper limit of normal
  • Has end stage renal disease or is likely to be a candidate for dialysis over the 1 year study period
  • Has a serum creatinine less than or equal to 1.5 mg/dL, or an estimated Glomerular Filtration Rate at Day -21 Screening Visit less than 15 mL/min or greater than 50 mL/min as calculated by the central laboratory
  • Is required to take excluded medications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (58)

Unknown Facility

Birmingham, Alabama, United States

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Peoria, Arizona, United States

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Sierra Vista, Arizona, United States

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Tucson, Arizona, United States

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Little Rock, Arkansas, United States

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Huntington Park, California, United States

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Irvine, California, United States

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Lakewood, California, United States

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Long Beach, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Jose, California, United States

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Tustin, California, United States

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Arvada, Colorado, United States

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Westminster, Colorado, United States

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Wheat Ridge, Colorado, United States

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Middlebury, Connecticut, United States

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Brandon, Florida, United States

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Daytona Beach, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Pinellas Park, Florida, United States

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Port Charlotte, Florida, United States

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Port Orange, Florida, United States

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Augusta, Georgia, United States

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Conyers, Georgia, United States

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Dunwoody, Georgia, United States

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Honolulu, Hawaii, United States

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Boise, Idaho, United States

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Evergreen Park, Illinois, United States

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Springfield, Illinois, United States

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Valparaiso, Indiana, United States

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Wichita, Kansas, United States

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Elizabethtown, Kentucky, United States

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Paducah, Kentucky, United States

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Baltimore, Maryland, United States

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Detroit, Michigan, United States

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Kalamazoo, Michigan, United States

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Brooklyn Center, Minnesota, United States

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Neptune City, New Jersey, United States

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Morganton, North Carolina, United States

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Wilmington, North Carolina, United States

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Fargo, North Dakota, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Bethlehem, Pennsylvania, United States

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Anderson, South Carolina, United States

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Greer, South Carolina, United States

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Chattanooga, Tennessee, United States

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Houston, Texas, United States

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Odessa, Texas, United States

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San Antonio, Texas, United States

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Danville, Virginia, United States

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Fairfax, Virginia, United States

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Richmond, Virginia, United States

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Williamsburg, Virginia, United States

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Clarksburg, West Virginia, United States

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Wauwatosa, Wisconsin, United States

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Related Publications (1)

  • Saag KG, Whelton A, Becker MA, MacDonald P, Hunt B, Gunawardhana L. Impact of Febuxostat on Renal Function in Gout Patients With Moderate-to-Severe Renal Impairment. Arthritis Rheumatol. 2016 Aug;68(8):2035-43. doi: 10.1002/art.39654.

Related Links

MeSH Terms

Conditions

Renal InsufficiencyGoutHyperuricemia

Interventions

Febuxostat

Condition Hierarchy (Ancestors)

Kidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesArthritisJoint DiseasesMusculoskeletal DiseasesCrystal ArthropathiesRheumatic DiseasesPurine-Pyrimidine Metabolism, Inborn ErrorsMetabolism, Inborn ErrorsGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesMetabolic DiseasesNutritional and Metabolic DiseasesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

ThiazolesSulfur CompoundsOrganic ChemicalsAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Results Point of Contact

Title
Sr. VP, Clinical Science
Organization
Takeda Global Research and Development Center, Inc.

Study Officials

  • Medical Director

    Takeda

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 5, 2010

First Posted

March 8, 2010

Study Start

April 1, 2010

Primary Completion

May 1, 2012

Study Completion

May 1, 2012

Last Updated

September 25, 2013

Results First Posted

September 25, 2013

Record last verified: 2013-09

Locations