NCT01064401

Brief Summary

The primary study objective is to test the superiority of Daclizumab High Yield Process (DAC HYP) compared to interferon β 1a (IFN β-1a) in preventing multiple sclerosis (MS) relapse in participants with relapsing remitting multiple sclerosis. The secondary study objectives are to test the superiority of DAC HYP compared to IFN β-1a in slowing functional decline and disability progression and maintaining quality of life in this participant population.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,841

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started May 2010

Typical duration for phase_3

Geographic Reach
27 countries

224 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 26, 2010

Completed
13 days until next milestone

First Posted

Study publicly available on registry

February 8, 2010

Completed
3 months until next milestone

Study Start

First participant enrolled

May 1, 2010

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2014

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2014

Completed
2 years until next milestone

Results Posted

Study results publicly available

July 11, 2016

Completed
Last Updated

July 11, 2016

Status Verified

May 1, 2016

Enrollment Period

3.8 years

First QC Date

January 26, 2010

Results QC Date

May 31, 2016

Last Update Submit

May 31, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Adjusted Annualized Relapse Rate (ARR)

    Relapses are defined as new or recurrent neurological symptoms not associated with fever or infection, lasting at least 24 hours, and accompanied by new objective neurological findings upon examination by the examining neurologist. Only relapses confirmed by Independent Neurology Evaluation Committee (INEC) are included in this analysis. Adjusted ARR was estimated from a negative binomial regression model adjusted for the baseline relapse rate, history of prior IFN beta use, baseline Expanded Disability Status Scale score (EDSS; ≤ 2.5 vs \> 2.5) and baseline age (≤ 35 vs \> 35 years). Data after participants switched to alternative MS medications are excluded.

    Up to 144 weeks

Secondary Outcomes (4)

  • Adjusted Mean Number of New or Newly Enlarging T2 Hyperintense Lesions up to Week 96

    up to 96 weeks

  • Proportion of Participants With Sustained Disability Progression at 144 Weeks

    Baseline through 144 weeks

  • Proportion of Participants Relapse-free at Week 144

    144 weeks

  • Percentage of Participants With a ≥ 7.5 Point Worsening From Baseline in the Multiple Sclerosis Impact Scale (MSIS-29) Physical Impact Score at 96 Weeks

    Baseline and 96 weeks

Study Arms (2)

Daclizumab High Yield Process 150 mg SC

EXPERIMENTAL

Daclizumab High Yield Process (DAC HYP) 150mg subcutaneous (SC) injection once every 4 weeks plus placebo to IFN β-1a intramuscular (IM) injection once weekly for 96 to 144 weeks

Biological: BIIB019 (Daclizumab High Yield Process)Drug: Interferon beta-1a Placebo

IFN β-1a 30 µg IM

ACTIVE COMPARATOR

Interferon beta-1a (IFN β-1a) 30 µg IM once weekly plus placebo to DAC HYP SC once every 4 weeks for 96 to 144 weeks

Biological: Interferon beta-1aDrug: Daclizumab High Yield Process Placebo

Interventions

Daclizumab High Yield Process for subcutaneous injection

Also known as: DAC HYP
Daclizumab High Yield Process 150 mg SC

Placebo to interferon beta-1a intramuscular injection

Daclizumab High Yield Process 150 mg SC

Interferon beta-1a for intramuscular injection

Also known as: Avonex, IFN β-1a
IFN β-1a 30 µg IM

Placebo to Daclizumab High Yield Process subcutaneous injection

IFN β-1a 30 µg IM

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Must have a confirmed diagnosis of Relapsing Remitting Multiple Sclerosis (RRMS), and a cranial magnetic resonance imaging (MRI) demonstrating lesion(s) consistent with MS
  • Must have a baseline Expanded Disability Status Scale (EDSS) between 0.0 and 5.0, inclusive
  • Male subjects and female subjects of childbearing potential must be willing to practice effective contraception during the study and be willing and able to continue contraception for 4 months after their last dose of study treatment

You may not qualify if:

  • Known intolerance, contraindication to, or history of non-compliance with Avonex® 30 µg
  • History of treatment with Daclizumab High Yield Process (Dac HYP)
  • History of malignancy
  • History of severe allergic or anaphylactic reactions
  • Known hypersensitivity to study drugs or their excipients
  • History of abnormal laboratory results indicative of any significant disease
  • History of human immunodeficiency virus (HIV) or other immunodeficient conditions
  • History of drug or alcohol abuse (as defined by the Investigator) within the 2 years prior to randomization
  • History of seizure disorder or unexplained blackouts OR history of a seizure within 6 months prior to Baseline
  • History of suicidal ideation or an episode of clinically severe depression (as determined by the Investigator) within 3 months prior to Day 1
  • An MS relapse that has occurred within the 50 days prior to randomization AND/OR the subject has not stabilized from a previous relapse prior to randomization
  • Known history of, or positive screening test result for hepatitis C virus or hepatitis B virus
  • Varicella or herpes zoster virus infection or any severe viral infection within 6 weeks before screening
  • Exposure to varicella zoster virus within 21 days before screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (228)

Research Site

Gilbert, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Little Rock, Arkansas, United States

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La Jolla, California, United States

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Aurora, Colorado, United States

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Naples, Florida, United States

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Pompano Beach, Florida, United States

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St. Petersburg, Florida, United States

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Sunrise, Florida, United States

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Atlanta, Georgia, United States

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Evanston, Illinois, United States

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Fort Wayne, Indiana, United States

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Indianapolis, Indiana, United States

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Des Moines, Iowa, United States

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Kansas City, Kansas, United States

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Lexington, Kentucky, United States

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Baltimore, Maryland, United States

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Springfield, Massachusetts, United States

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Worchester, Massachusetts, United States

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Clinton Township, Michigan, United States

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St Louis, Missouri, United States

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Lebanon, New Hampshire, United States

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New Brunswick, New Jersey, United States

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Albuquerque, New Mexico, United States

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Buffalo, New York, United States

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Latham, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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Charlotte, North Carolina, United States

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Raleigh, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Medford, Oregon, United States

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Portland, Oregon, United States

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Allentown, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Providence, Rhode Island, United States

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Franklin, Tennessee, United States

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Knoxville, Tennessee, United States

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Salt Lake City, Utah, United States

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Burlington, Vermont, United States

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Kirkland, Washington, United States

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Seattle, Washington, United States

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Tacoma, Washington, United States

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Milwaukee, Wisconsin, United States

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Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

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Godoy Cruz, Mendoza Province, Argentina

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Rosario, Santa Fe Province, Argentina

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Camperdown, New South Wales, Australia

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New Lambton Heights, New South Wales, Australia

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Auchenflower, Queensland, Australia

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Woodville, South Australia, Australia

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Fitzroy, Victoria, Australia

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Heidelberg West, Victoria, Australia

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Belo Horizonte, Estado de Bahia, Brazil

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Brasília, Federal District, Brazil

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Recife, Pernambuco, Brazil

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Rio de Janeiro, Rio de Janeiro, Brazil

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Porto Alegre, Rio Grande, Brazil

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São Paulo, Rio Grande, Brazil

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Campinas, São Paulo, Brazil

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Ribeirão Preto, São Paulo, Brazil

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Vancouver, British Columbia, Canada

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St. John's, Newfoundland and Labrador, Canada

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Gatineau, Quebec, Canada

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Greenfield Park, Quebec, Canada

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Montreal, Quebec, Canada

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Regina, Saskatchewan, Canada

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Brno, Jihočeský kraj, Czechia

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Jihlava, Kraj Vysočina, Czechia

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Olomouc, Olomoucký kraj, Czechia

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Prague, Prague, Czechia

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Havířov, Severomoravksy Krav, Czechia

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Brno, Czechia

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Hradec Králové, Czechia

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Jihlava, Czechia

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Ostrava, Czechia

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Pardubice, Czechia

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Aarhus, Denmark

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Copenhagen, Denmark

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Glostrup Municipality, Denmark

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Odense C, Denmark

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Oulu, Oulu, Finland

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Tampere, Western Finalnd, Finland

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Helsinki, Finland

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Seinäjoki, Finland

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Turku, Finland

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Strasbourg, Alsace, France

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Lyon, Auvergne-Rhône-Alpes, France

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Caen, Basse-normandie, France

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Amiens, Picardie, France

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Nice, Provence-Alpes-Côte d'Azur Region, France

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Bourdeaux, France

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Dijon, France

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Lille, France

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Lomme, France

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Marseille, France

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Nancy, France

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Toulouse, France

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Bobigny, Île-de-France Region, France

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Paris, Île-de-France Region, France

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Tbilisi, Georgia

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Bad Mergentheim, Baden-Wurttemberg, Germany

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Freiburg im Breisgau, Baden-Wurttemberg, Germany

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Bamberg, Bavaria, Germany

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Bayreuth, Bavaria, Germany

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München, Bavaria, Germany

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Neuburg an der Donau, Bavaria, Germany

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Hamburg, Hamburg, Germany

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Marburg, Hesse, Germany

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Cologne, North Rhine-Westphalia, Germany

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Essen, North Rhine-Westphalia, Germany

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Münster, North Rhine-Westphalia, Germany

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Trier, Rhineland-Palatinate, Germany

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Dresden, Saxony, Germany

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Berlin, State of Berlin, Germany

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Tübingen, Germany

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Athens, Attica, Greece

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Heraklion, Crete, Greece

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Thessaloniki, Macedoni, Greece

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Budapest, Budapest, Hungary

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Székesfehérvár, Fejér, Hungary

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Győr, Győr-Moson-Sopron, Hungary

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Esztergom, Hungary

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Miskolc, Hungary

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Nyíregyháza, Hungary

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Veszprém, Hungary

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Hyderabad, Andhra Pradesh, India

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Delhi, Dwivdee, India

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Bangalore, Karnataka, India

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Trivandrum, Kerala, India

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Mumbai, Maharashtra, India

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Nagpur, Maharashtra, India

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New Delhi, India

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Dublin, Dublin, Ireland

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Ashkelon, Ashqelon, Israel

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Tzrifin, Beer Yaakov, Israel

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Petah Tikva, Petah Tiqwa, Israel

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Beersheba, Israel

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Haifa, Israel

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Kfar Saba, Israel

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Tzfat, Israel

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Bari, Bari, Italy

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Cagliari, Cagliari, Italy

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Catania, Catania, Italy

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Genova, Genova, Italy

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Cefalù, PA, Italy

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Roma, Roma, Italy

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Orbassano, Torino, Italy

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Florence, Italy

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Milan, Italy

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Padua, Italy

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Guadalajara, Jalisco, Mexico

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Mexico City, Mexico City, Mexico

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Chisinau, Moldova

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Poznan, Greater Poland Voivodeship, Poland

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Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

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Grudziądz, Kuyavian-Pomeranian Voivodeship, Poland

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Krakow, Lesser Poland Voivodeship, Poland

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Lublin, Lower Silesian Voivodeship, Poland

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Warsaw, Masovian Voivodeship, Poland

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Bialystok, Podlaskie Voivodeship, Poland

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Gdansk, Pomeranian Voivodeship, Poland

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Katowice, Silesian Voivodeship, Poland

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Kielce, Swietokrzycie, Poland

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Olsztyn, Warmian-Masurian Voivodeship, Poland

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Szczecin, West Pomeranian Voivodeship, Poland

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Bydgoszczas, Poland

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Plewiska, Poland

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Lódz, Łódź Voivodeship, Poland

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Bucurest, București, Romania

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Cluj-Napoca, Cluj, Romania

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Timișoara, Timiș County, Romania

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Iași, Romania

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Târgu Mures, Romania

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Kazan', Povolje-Tatarstan, Russia

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Yekaterinburg, Ural, Russia

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Yaroslavl, Yaroslavlr, Russia

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Chelyabinsk, Russia

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Kaluga, Russia

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Kemerovo, Russia

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Krasnoyarsk, Russia

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Moscow, Russia

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Nizhny Novgorod, Russia

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Novosibirsk, Russia

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Perm, Russia

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Saint Petersburg, Russia

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Smolensk, Russia

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Tomsk, Russia

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Tyumen, Russia

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Ufa, Russia

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Belgrade, Serbia

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Kragujevac, Serbia

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Niš, Serbia

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Novi Sad, Serbia

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Barcelona, Barcelona, Spain

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L'Hospitalet de Llobregat, Barcelona, Spain

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Córdoba, Cordoba, Spain

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Madrid, Madrid, Spain

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Seville, Sevilla, Spain

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Girona, Spain

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Gothenburg, Sweden

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Linköping, Sweden

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Malmo, Sweden

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Stockholm, Sweden

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Basel, Basel, Switzerland

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Lugano, Switzerland

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Dnipro, Ukraine

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Kharkiv, Ukraine

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Kyviv, Ukraine

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Odesa, Ukraine

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Poltava, Ukraine

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Vinnitsa, Ukraine

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Zaporizhzhya, Ukraine

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Brighton, United Kingdom

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Bristol, United Kingdom

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Edinburgh, United Kingdom

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London, United Kingdom

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New Castle Upon Tyne, United Kingdom

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Nottingham, United Kingdom

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Romford, United Kingdom

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Salford, United Kingdom

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Sheffield, United Kingdom

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Related Publications (7)

  • Loomis SJ, Sadhu N, Fisher E, Gafson AR, Huang Y, Yang C, Hughes EE, Marshall E, Herman A, John S, Runz H, Jia X, Bhangale T, Bronson PG. Genome-wide study of longitudinal brain imaging measures of multiple sclerosis progression across six clinical trials. Sci Rep. 2023 Aug 31;13(1):14313. doi: 10.1038/s41598-023-41099-0.

  • Castrogiovanni N, Mostert J, Repovic P, Bowen JD, Uitdehaag BMJ, Strijbis EMM, Cutter GR, Koch MW. Longitudinal Changes in Cognitive Test Scores in Patients With Relapsing-Remitting Multiple Sclerosis: An Analysis of the DECIDE Dataset. Neurology. 2023 Jul 4;101(1):e1-e11. doi: 10.1212/WNL.0000000000207301. Epub 2023 Apr 18.

  • Cohan S, Kappos L, Giovannoni G, Wiendl H, Selmaj K, Havrdova EK, Rose J, Greenberg S, Phillips G, Ma W, Wang P, Lima G, Sabatella G. Efficacy of daclizumab beta versus intramuscular interferon beta-1a on disability progression across patient demographic and disease activity subgroups in DECIDE. Mult Scler. 2018 Dec;24(14):1883-1891. doi: 10.1177/1352458517735190. Epub 2017 Oct 6.

  • Benedict RH, Cohan S, Lynch SG, Riester K, Wang P, Castro-Borrero W, Elkins J, Sabatella G. Improved cognitive outcomes in patients with relapsing-remitting multiple sclerosis treated with daclizumab beta: Results from the DECIDE study. Mult Scler. 2018 May;24(6):795-804. doi: 10.1177/1352458517707345. Epub 2017 May 9.

  • Liu Y, Vollmer T, Havrdova E, Riester K, Lee A, Phillips G, Wang P, Sabatella G. Impact of daclizumab versus interferon beta-1a on patient-reported outcomes in relapsing-remitting multiple sclerosis. Mult Scler Relat Disord. 2017 Jan;11:18-24. doi: 10.1016/j.msard.2016.11.005. Epub 2016 Nov 13.

  • Krueger JG, Kircik L, Hougeir F, Friedman A, You X, Lucas N, Greenberg SJ, Sweetser M, Castro-Borrero W, McCroskery P, Elkins J. Cutaneous Adverse Events in the Randomized, Double-Blind, Active-Comparator DECIDE Study of Daclizumab High-Yield Process Versus Intramuscular Interferon Beta-1a in Relapsing-Remitting Multiple Sclerosis. Adv Ther. 2016 Jul;33(7):1231-45. doi: 10.1007/s12325-016-0353-2. Epub 2016 Jun 1.

  • Kappos L, Wiendl H, Selmaj K, Arnold DL, Havrdova E, Boyko A, Kaufman M, Rose J, Greenberg S, Sweetser M, Riester K, O'Neill G, Elkins J. Daclizumab HYP versus Interferon Beta-1a in Relapsing Multiple Sclerosis. N Engl J Med. 2015 Oct 8;373(15):1418-28. doi: 10.1056/NEJMoa1501481.

MeSH Terms

Conditions

Multiple Sclerosis, Relapsing-Remitting

Interventions

daclizumab HYPInterferon beta-1a

Condition Hierarchy (Ancestors)

Multiple SclerosisDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Interferon-betaInterferon Type IInterferonsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Biogen Study Medical Director
Organization
Biogen

Study Officials

  • Medical Director

    Biogen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 26, 2010

First Posted

February 8, 2010

Study Start

May 1, 2010

Primary Completion

March 1, 2014

Study Completion

July 1, 2014

Last Updated

July 11, 2016

Results First Posted

July 11, 2016

Record last verified: 2016-05

Locations