NCT01058005

Brief Summary

This was a multicenter, randomized, open-label, parallel-group, active-controlled study. Prior to randomization, participants were to have been treated with glatiramer acetate or interferon β-1a (44 μg). Participants were to be randomized to receive natalizumab, interferon β-1a 44 μg, or glatiramer acetate.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
84

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Mar 2010

Geographic Reach
13 countries

42 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 26, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 28, 2010

Completed
1 month until next milestone

Study Start

First participant enrolled

March 1, 2010

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2012

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

August 13, 2014

Completed
Last Updated

September 3, 2014

Status Verified

August 1, 2014

Enrollment Period

2.1 years

First QC Date

January 26, 2010

Results QC Date

July 23, 2014

Last Update Submit

August 18, 2014

Conditions

Keywords

MS

Outcome Measures

Primary Outcomes (1)

  • Incidence of Treatment-emergent Serious Adverse Events (SAEs)

    An SAE was defined as any untoward medical occurrence that at any dose: results in death; in the view of the Investigator, places the subject at immediate risk of death (a life-threatening event; however, this does not include an event that, had it occurred in a more severe form, might have caused death); requires inpatient hospitalization or prolongation of existing hospitalization; results in persistent or significant disability/incapacity; or results in a congenital anomaly/birth defect. An SAE may also have been any other medically important event that, in the opinion of the Investigator, may jeopardize the subject or may require intervention to prevent one of the other outcomes listed in the definition above. See Adverse Events section below for further details.

    up to 108 Weeks

Study Arms (3)

Natalizumab

EXPERIMENTAL
Drug: BG00002 (natalizumab)

Interferon Beta-1a

ACTIVE COMPARATOR
Drug: interferon beta-1a

Glatiramer Acetate

ACTIVE COMPARATOR
Drug: glatiramer acetate

Interventions

300 mg intravenous injection every 4 weeks

Also known as: Tysabri
Natalizumab

44 mcg subcutaneous injection 3 times per week

Also known as: Rebif
Interferon Beta-1a

20 mg subcutaneous injection once daily

Also known as: Copaxone
Glatiramer Acetate

Eligibility Criteria

Age18 Years - 60 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Have a diagnosis of relapsing remitting multiple sclerosis (MS) as defined by the revised McDonald Committee criteria (Polman 2005).
  • Have had disease activity within 12 months prior to screening while on therapy; disease activity must be observed after a minimum of 6 months on therapy. Qualifying disease activity is defined as:
  • One or more clinical relapses OR
  • Be naïve to natalizumab.
  • Have a documented Expanded Disability Status Scale (EDSS) score between 0.0 and 5.5, inclusive.

You may not qualify if:

  • Have a diagnosis of primary progressive, secondary progressive, or progressive relapsing MS (as defined by Lublin and Reingold, 1996). These conditions require the presence of continuous clinical disease worsening over a period of at least 3 months. Patients with these conditions may also have superimposed relapses, but are distinguished from relapsing-remitting patients by the lack of clinically stable periods or clinical improvement.
  • Have known intolerance, contraindication to, or history of non-compliance with, the use of glatiramer acetate or interferon beta-1a.
  • Have had an MS exacerbation (relapse) within 30 days prior to randomization AND/OR the patient has not stabilized from a previous relapse, in the opinion of the Investigator, prior to randomization.
  • The patient is considered by the Investigator to be immunocompromised based on medical history, physical examination, laboratory testing, or due to prior immunosuppressive or immunomodulating treatment.
  • Subjects for whom MRI is contraindicated, i.e., have pacemakers or other contraindicated implanted metal devices, have suffered or are at risk for side effects from gadolinium (Gd), or have claustrophobia that cannot be medically managed.
  • History of any clinically significant (as determined by the Investigator) cardiac, endocrinologic, hematologic, hepatic, immunologic, metabolic, urologic, pulmonary, neurologic, dermatologic, psychiatric, renal, or other major disease that would preclude participation in a clinical trial.
  • History of malignant disease, including solid tumors and hematologic malignancies (with the exception of basal cell and squamous cell carcinomas of the skin that have been completely excised and are considered cured).
  • Known history of human immunodeficiency virus (HIV).
  • Positive test result for hepatitis C virus (test for hepatitis C virus antibody \[HCVAb\]) or hepatitis B virus (test for hepatitis B surface antigen \[HBsAg\] and/or hepatitis B core antibody \[HBcAb\]).
  • History of transplantation or any anti-rejection therapy.
  • History of progressive multifocal leukoencephalopathy (PML).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (42)

Research Site

Cullman, Alabama, United States

Location

Research Site

Phoenix, Arizona, United States

Location

Research Site

Fort Collins, Colorado, United States

Location

Research Site

Maitland, Florida, United States

Location

Research Site

St. Petersburg, Florida, United States

Location

Research Site

Tampa, Florida, United States

Location

Research Site

Atlanta, Georgia, United States

Location

Research Site

Lexington, Kentucky, United States

Location

Research Site

New Orleans, Louisiana, United States

Location

Research Site

Detroit, Michigan, United States

Location

Research Site

Patchogue, New York, United States

Location

Research Site

Charlotte, North Carolina, United States

Location

Research Site

Akron, Ohio, United States

Location

Research Site

Franklin, Tennessee, United States

Location

Research Site

Knoxville, Tennessee, United States

Location

Research Site

Round Rock, Texas, United States

Location

Research Site

Norfolk, Virginia, United States

Location

Research Site

Kirkland, Washington, United States

Location

Research Site

Morgantown, West Virginia, United States

Location

Research Site

Fitzroy, Victoria, Australia

Location

Research Site

Gatineau, Quebec, Canada

Location

Research Site

Pardubice, Czechia

Location

Research Site

Tampere, Finland

Location

Research Site

Strasbourg, Bas-Rhin, France

Location

Research Site

Esztergom, Komárom-Esztergom, Hungary

Location

Research Site

Budapest, Hungary

Location

Research Site

Nyíregyháza, Hungary

Location

Research Site

Catania, Catania, Italy

Location

Research Site

Napoli, Italy

Location

Research Site

Rome, Italy

Location

Research Site

Riga, Latvia

Location

Research Site

Bialystok, Podlaskie Voivodeship, Poland

Location

Research Site

Gdansk, Pomeranian Voivodeship, Poland

Location

Research Site

Lódz, Łódź Voivodeship, Poland

Location

Research Site

Ljubljana, Slovenia

Location

Research Site

Barcelona, Barcelona, Spain

Location

Research Site

Alicante, Spain

Location

Research Site

Girona, Spain

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Research Site

Madrid, Spain

Location

Research Site

Santa Cruz de Tenerife, Spain

Location

Research Site

Seville, Spain

Location

Research Site

Mölndal, Sweden

Location

MeSH Terms

Conditions

Multiple Sclerosis, Relapsing-Remitting

Interventions

NatalizumabInterferon beta-1aGlatiramer Acetate

Condition Hierarchy (Ancestors)

Multiple SclerosisDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsInterferon-betaInterferon Type IInterferonsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesBiological Factors

Limitations and Caveats

Due to early termination of the study and the small size of the study population, there was insufficient power for efficacy and safety analyses. Only serious adverse events were to be captured and reported under the protocol.

Results Point of Contact

Title
Biogen Idec Study Medical Director
Organization
Biogen Idec

Study Officials

  • Medical Director

    Biogen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 26, 2010

First Posted

January 28, 2010

Study Start

March 1, 2010

Primary Completion

April 1, 2012

Study Completion

April 1, 2012

Last Updated

September 3, 2014

Results First Posted

August 13, 2014

Record last verified: 2014-08

Locations