NCT00906399

Brief Summary

The primary objective of this study is to determine the efficacy of peginterferon beta-1a in reducing the annualized relapse rate (ARR) in participants with relapsing multiple sclerosis (RMS) at 1 year. The secondary objectives of this study are to determine whether peginterferon beta-1a, at 1 year when compared with placebo, is effective in reducing the total number of new or newly enlarging T2 hyperintense lesions on brain magnetic resonance imaging (MRI) scans, reducing the proportion of participants who relapse, and slowing the progression of disability.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,516

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jun 2009

Typical duration for phase_3

Geographic Reach
25 countries

173 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 20, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 21, 2009

Completed
11 days until next milestone

Study Start

First participant enrolled

June 1, 2009

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2012

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2013

Completed
12 months until next milestone

Results Posted

Study results publicly available

September 19, 2014

Completed
Last Updated

September 19, 2014

Status Verified

September 1, 2014

Enrollment Period

3.3 years

First QC Date

May 20, 2009

Results QC Date

July 28, 2014

Last Update Submit

September 15, 2014

Conditions

Keywords

interferoninjectableMSSCPEGylatedInterferon beta-1arelapsingPEGmultiple sclerosissubcutaneous

Outcome Measures

Primary Outcomes (1)

  • Annualized Relapse Rate (ARR) at 1 Year

    A relapse is defined as new or recurrent neurologic symptoms not associated with fever or infection, lasting for at least 24 hours, and accompanied by new objective neurologic findings. Only relapses confirmed by an independent neurology evaluation committee (INEC) are included in the analysis. Data after participants switched to alternative multiple sclerosis (MS) medications are excluded. Data were analyzed using negative binomial regression, adjusted for baseline Expanded Disability Status Scale (EDSS) score (\< 4 versus ≥ 4), baseline age (\< 40 versus ≥ 40 years), and baseline relapse rate (number of relapses in 3 years prior to study entry divided by 3).

    1 Year

Secondary Outcomes (3)

  • Number of New Or Newly Enlarging T2 Hyperintense Lesions at 1 Year

    1 Year

  • Proportion of Participants Relapsed at 1 Year

    Year 1

  • Estimated Proportion of Participants With Sustained Disability Progression at 1 Year

    1 Year

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Placebo every 2 weeks for 48 weeks followed by 125 µg peginterferon beta-1a subcutaneously every 2 or 4 weeks for 48 weeks.

Drug: BIIB017 (peginterferon beta-1a)Drug: Placebo

Peginterferon Beta-1a Q2W

EXPERIMENTAL

125 µg peginterferon beta-1a subcutaneously every 2 weeks (Q2W) for 96 weeks.

Drug: BIIB017 (peginterferon beta-1a)

Peginterferon Beta-1a Q4W

EXPERIMENTAL

125 µg peginterferon beta-1a subcutaneously every 4 weeks (Q4W) for 96 weeks. Participants received a placebo injection 2 weeks after each active injection (in order to maintain the blind with Q2W arm).

Drug: BIIB017 (peginterferon beta-1a)Drug: Placebo

Interventions

Supplied as a liquid in pre-filled syringes to deliver 0.5 mL of 0.25 mg/mL (125 µg dose), self-administered by subcutaneous injection.

Also known as: PEG IFN ß-1a, PEGylated interferon beta-1a, Plegridy
Peginterferon Beta-1a Q2WPeginterferon Beta-1a Q4WPlacebo

Matched placebo provided in pre-filled syringes, to deliver 0.5 mL self-administered by subcutaneous injection.

Peginterferon Beta-1a Q4WPlacebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have a confirmed diagnosis of relapsing multiple sclerosis (RMS), as defined by McDonald criteria 1 through 4 (Polman, 2005)
  • Must have an EDSS score between 0.0 and 5.0.
  • Must have experienced at least 2 relapses that have been medically documented within the last 3 years with at least one occurring in the last 12 months

You may not qualify if:

  • Other chronic disease of immune system, malignancies, urologic, pulmonary, gastrointestinal disease
  • Pregnant or nursing women
  • Prior treatment with interferon could not exceed 4 weeks and subjects must have discontinued interferon treatment 6 months prior to Baseline

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (178)

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Phoenix, Arizona, 85013, United States

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Ponte Vedra Beach, Florida, 32082 4040, United States

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Atlanta, Georgia, 30327, United States

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Des Moines, Iowa, 50314, United States

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Lexington, Kentucky, 40513, United States

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Baltimore, Maryland, 21287, United States

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Teaneck, New Jersey, 07666, United States

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Raleigh, North Carolina, 27607 6520, United States

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Akron, Ohio, 44320, United States

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Cleveland, Ohio, 44195, United States

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Franklin, Tennessee, 37064, United States

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Round Rock, Texas, 78681, United States

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Brussels, 1200, Belgium

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Sint-Truiden, 3800, Belgium

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Plovdiv, 4002, Bulgaria

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Sofia, 1113, Bulgaria

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Sofia, 1309, Bulgaria

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Sofia, 1407, Bulgaria

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Sofia, 1431, Bulgaria

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Sofia, 1527, Bulgaria

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Sofia, 1606, Bulgaria

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London, Ontario, N6A 5A5, Canada

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Montreal, Quebec, H2L4M1, Canada

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Santiago, 8207257, Chile

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Barranquilla, Atlántico, Colombia

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Bogota, Cundinamarca, Colombia

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Bogotá, Colombia

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Osijek, 31000, Croatia

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Zagreb, 10000, Croatia

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Brno, 62500, Czechia

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Olomouc, 77520, Czechia

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Ostrava, 70852, Czechia

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Ostrava - Vitkovice, 70200, Czechia

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Ostrava-Poruba, 70300, Czechia

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Prague, 12808, Czechia

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Prague, 15006, Czechia

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Teplice, 41529, Czechia

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Pärnu, EE 80010, Estonia

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Tallinn, EE 10617, Estonia

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Tartu, EE 51014, Estonia

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Amiens, 80054, France

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Clermont-Ferrand, 63003, France

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Lyon, 69394, France

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Marseille, 13385, France

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Nice, 6002, France

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Tbilisi, 112, Georgia

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Tbilisi, 141, Georgia

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Tbilisi, 179, Georgia

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Tbilisi, 186, Georgia

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Bayreuth, 95445, Germany

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Berlin, 10713, Germany

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Berlin, 14163, Germany

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Bochum, 44791, Germany

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Cologne, 50935, Germany

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Erbach im Odenwald, 64711, Germany

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Erlangen, 91054, Germany

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Hamburg, 20099, Germany

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Hanover, 30559, Germany

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Leipzig, 04103, Germany

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Marburg, 35043, Germany

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München, 80331, Germany

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Münster, 48149, Germany

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Prien am Chiemsee, 83209, Germany

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Ulm, 89079, Germany

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Westerstede, 26655, Germany

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Athens, 11521, Greece

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Athens, 11525, Greece

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Thessaloniki, 57010, Greece

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Ahmedabad, Gujarat, 380006, India

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Rajkot, Gujarat, 360001, India

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Bangalore, Karnataka, 560043, India

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Indore, Madhyr Pradesh, 452018, India

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Mumbai, Maharashtra, 400026, India

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Nagpur, Maharashtra, 440010, India

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Nashik, Maharashtra, 422004, India

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Pune, Maharashtra, 411004, India

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Pune, Maharashtra, 411030, India

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New Delhi, National Capital Territory of Delhi, 110029, India

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New Delhi, National Capital Territory of Delhi, 110060, India

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Saket, National Capital Territory of Delhi, 110017, India

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Amritsar, Punjab, 143001, India

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Jaipur, Rajasthan, 302004, India

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Chennai, Tamil Nadu, 600017, India

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Coimbatore, Tamil Nadu, 641014, India

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Kolkata, West Bengal, 700068, India

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Bangalore, 560017, India

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Mangalore, 575018, India

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Navi Mumbai, 400703, India

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Nehru Nagar, 110065, India

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Riga, LV 1005, Latvia

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Aquas Calientes, 20127, Mexico

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Chihuahua City, 31203, Mexico

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Mexico City, 03310, Mexico

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Mexico City, 10700, Mexico

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Monterrey, Nuevo Leon, 64710, Mexico

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Tijuana, Baja California, 22320, Mexico

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Breda, 4818CK, Netherlands

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Nieuwegein, 3435CM, Netherlands

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Auckland, 1023, New Zealand

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Christchurch, New Zealand

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Dunedin, New Zealand

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Lima, Lima 01, Peru

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Lima, Lima 1, Peru

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Lima, Lima 21, Peru

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San Isidro, Lima 27, Peru

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Bialystok, 15276, Poland

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Bialystok, 15402, Poland

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Bydgoszcz, 85681, Poland

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Gdansk, 80299, Poland

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Gdansk, 80803, Poland

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Gdansk, 80952, Poland

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Gmina Końskie, 26200, Poland

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Katowice, 40650, Poland

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Katowice, 40662, Poland

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Katowice, 40684, Poland

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Krakow, 31505, Poland

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Krakow, 31637, Poland

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Krakow, 31826, Poland

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Lodz, 90153, Poland

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Lublin, 20718, Poland

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Lublin, 20954, Poland

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Olsztyn, 10082, Poland

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Plewiska, 62064, Poland

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Poznan, 60355, Poland

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Poznan, 61853, Poland

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Szczecin, 70215, Poland

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Szczecin, 71252, Poland

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Warsaw, 00851, Poland

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Warsaw, 02957, Poland

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Warsaw, 04141, Poland

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Warsaw, 04749, Poland

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Wroclaw, 50556, Poland

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Zabrze, 41800, Poland

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Brasov, 500123, Romania

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Bucharest, 50098, Romania

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Campulung Muscel, 115100, Romania

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Iași, 700656, Romania

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Sibiu, 550166, Romania

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Târgu Mureş, 540136, Romania

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Chelyabinsk, 454136, Russia

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Kaluga, 248007, Russia

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Kazan', 420021, Russia

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Krasnodar, 350012, Russia

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Kursk, 305007, Russia

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Moscow, 107150, Russia

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Moscow, 119021, Russia

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Moscow, 125367, Russia

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Moscow, 127018, Russia

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Novosibirsk, 630007, Russia

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Perm, 614990, Russia

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Rostov-on-Don, 344015, Russia

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Smolensk, 214018, Russia

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Tomsk, 634050, Russia

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Ufa, 450005, Russia

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Belgrade, 11000, Serbia

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Kragujevac, 34000, Serbia

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Niš, 18000, Serbia

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Córdoba, 14008, Spain

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Madrid, 28041, Spain

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Madrid, 28046, Spain

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Málaga, 29010, Spain

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Seville, 41071, Spain

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Chernivtsi, 58018, Ukraine

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Dnipropetrovsk, 49027, Ukraine

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Donetsk, 83099, Ukraine

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Kharkiv, 61068, Ukraine

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Kharkiv, 61103, Ukraine

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Kyiv, 3110, Ukraine

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Kyiv, 4107, Ukraine

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Odesa, 65025, Ukraine

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Poltava, 26011, Ukraine

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Simferopol, 95017, Ukraine

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Ternopil, 46027, Ukraine

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Vinnytsia, 21005, Ukraine

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London, E1 1BB, United Kingdom

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Nottingham, NG7 2UH, United Kingdom

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Salford, M6 8HD, United Kingdom

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Sheffield, S10 2JF, United Kingdom

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Related Publications (11)

  • Calabresi PA, Kieseier BC, Arnold DL, Balcer LJ, Boyko A, Pelletier J, Liu S, Zhu Y, Seddighzadeh A, Hung S, Deykin A; ADVANCE Study Investigators. Pegylated interferon beta-1a for relapsing-remitting multiple sclerosis (ADVANCE): a randomised, phase 3, double-blind study. Lancet Neurol. 2014 Jul;13(7):657-65. doi: 10.1016/S1474-4422(14)70068-7. Epub 2014 Apr 30.

  • Loomis SJ, Sadhu N, Fisher E, Gafson AR, Huang Y, Yang C, Hughes EE, Marshall E, Herman A, John S, Runz H, Jia X, Bhangale T, Bronson PG. Genome-wide study of longitudinal brain imaging measures of multiple sclerosis progression across six clinical trials. Sci Rep. 2023 Aug 31;13(1):14313. doi: 10.1038/s41598-023-41099-0.

  • Calabresi PA, Arnold DL, Sangurdekar D, Singh CM, Altincatal A, de Moor C, Engle B, Goyal J, Deykin A, Szak S, Kieseier BC, Rudick RA, Plavina T. Temporal profile of serum neurofilament light in multiple sclerosis: Implications for patient monitoring. Mult Scler. 2021 Sep;27(10):1497-1505. doi: 10.1177/1352458520972573. Epub 2020 Dec 14.

  • Cleanthous S, Cano S, Kinter E, Marquis P, Petrillo J, You X, Wakeford C, Sabatella G. Measuring the impact of multiple sclerosis: Enhancing the measurement performance of the Multiple Sclerosis Impact Scale (MSIS-29) using Rasch Measurement Theory (RMT). Mult Scler J Exp Transl Clin. 2017 Aug 15;3(3):2055217317725917. doi: 10.1177/2055217317725917. eCollection 2017 Jul-Sep.

  • Scott TF, Kieseier BC, Newsome SD, Arnold DL, You X, Hung S, Sperling B. Improvement in relapse recovery with peginterferon beta-1a in patients with multiple sclerosis. Mult Scler J Exp Transl Clin. 2016 Nov 15;2:2055217316676644. doi: 10.1177/2055217316676644. eCollection 2016 Jan-Dec.

  • Newsome SD, Kieseier BC, Liu S, You X, Kinter E, Hung S, Sperling B. Peginterferon beta-1a reduces disability worsening in relapsing-remitting multiple sclerosis: 2-year results from ADVANCE. Ther Adv Neurol Disord. 2017 Jan;10(1):41-50. doi: 10.1177/1756285616676065. Epub 2016 Nov 16.

  • Arnold DL, Calabresi PA, Kieseier BC, Liu S, You X, Fiore D, Hung S. Peginterferon beta-1a improves MRI measures and increases the proportion of patients with no evidence of disease activity in relapsing-remitting multiple sclerosis: 2-year results from the ADVANCE randomized controlled trial. BMC Neurol. 2017 Feb 10;17(1):29. doi: 10.1186/s12883-017-0799-0.

  • Newsome SD, Guo S, Altincatal A, Proskorovsky I, Kinter E, Phillips G, You X, Sabatella G. Impact of peginterferon beta-1a and disease factors on quality of life in multiple sclerosis. Mult Scler Relat Disord. 2015 Jul;4(4):350-7. doi: 10.1016/j.msard.2015.06.004. Epub 2015 Jun 14.

  • Arnold DL, Calabresi PA, Kieseier BC, Sheikh SI, Deykin A, Zhu Y, Liu S, You X, Sperling B, Hung S. Effect of peginterferon beta-1a on MRI measures and achieving no evidence of disease activity: results from a randomized controlled trial in relapsing-remitting multiple sclerosis. BMC Neurol. 2014 Dec 31;14:240. doi: 10.1186/s12883-014-0240-x.

  • Kieseier BC, Arnold DL, Balcer LJ, Boyko AA, Pelletier J, Liu S, Zhu Y, Seddighzadeh A, Hung S, Deykin A, Sheikh SI, Calabresi PA. Peginterferon beta-1a in multiple sclerosis: 2-year results from ADVANCE. Mult Scler. 2015 Jul;21(8):1025-35. doi: 10.1177/1352458514557986. Epub 2014 Nov 28.

  • Hu X, Cui Y, White J, Zhu Y, Deykin A, Nestorov I, Hung S. Pharmacokinetics and pharmacodynamics of peginterferon beta-1a in patients with relapsing-remitting multiple sclerosis in the randomized ADVANCE study. Br J Clin Pharmacol. 2015 Mar;79(3):514-22. doi: 10.1111/bcp.12521.

MeSH Terms

Conditions

RecurrenceMultiple Sclerosis

Interventions

peginterferon beta-1a

Condition Hierarchy (Ancestors)

Disease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Biogen Idec Study Medical Director
Organization
Biogen Idec

Study Officials

  • Medical Director

    Biogen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 20, 2009

First Posted

May 21, 2009

Study Start

June 1, 2009

Primary Completion

October 1, 2012

Study Completion

October 1, 2013

Last Updated

September 19, 2014

Results First Posted

September 19, 2014

Record last verified: 2014-09

Locations