NCT00846053

Brief Summary

The purpose of this research is to determine how a person's lungs will uptake \[18F\]fluorodeoxyglucose (FDG), as measured with positron emission tomography (PET) scanning in young cystic fibrosis (CF) patients.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
21

participants targeted

Target at below P25 for not_applicable

Timeline
Completed

Started Feb 2009

Typical duration for not_applicable

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2009

Completed
15 days until next milestone

First Submitted

Initial submission to the registry

February 16, 2009

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 18, 2009

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2012

Completed
6.5 years until next milestone

Results Posted

Study results publicly available

July 24, 2018

Completed
Last Updated

July 24, 2018

Status Verified

June 1, 2018

Enrollment Period

3 years

First QC Date

February 16, 2009

Results QC Date

May 12, 2017

Last Update Submit

June 27, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Kinetic Influx Constant (Ki)

    The whole lung kinetic influx constant (Ki) is the primary outcome measure that is derived from the time-activity curves, which are generated from regions of interest placed over the whole lungs. Therefore, a single time-activity curves from each scan is used to derive the Ki.

    At the time of FDG scan, 1 to 2 hours

Secondary Outcomes (1)

  • Sputum Neutrophil Elastase (NE) Concentration

    Sample collected within 2-hours of PET scan

Study Arms (2)

Stable lung function

OTHER

\* Group S (n = 14) will consist of CF patients, aged 12-21 years old, who underwent FDG-PET with stable lung function during the past 4 years, defined as less than 2% decline per year. There is no therapeutic intervention and FDG-PET scan will be performed in both cohorts.

Diagnostic Test: FDG-PET

Rapidly deteriorating lung function

OTHER

\* Group R (n = 14) will contain CF patients, aged 12-21 years old, who underwent FDG-PET with rapidly deteriorating lung function during the past 4 years with greater than 4% per year decline. There is no therapeutic intervention and FDG-PET scan will be performed in both cohorts.

Diagnostic Test: FDG-PET

Interventions

FDG-PETDIAGNOSTIC_TEST

All subjects underwent FDG-PET and low-dose volumetric CT imaging. After completing a transmission scan, \[18F\]FDG was injected intravenously at the start of dynamic scan acquisition. Regions of interest were drawn over multiple tomographic slices to determine average whole-lung and regional lung tissue \[18F\] FDG uptake. Patlak graphical analysis was used to determine the rate of \[18F\]FDG uptake from the blood input function and lung tissue activity curves, measured as the influx constant Ki (slope of the linear regression from the Patlak plot). Corrected Ki (i.e., Ki divided by the initial volume of distribution). Lung density was calculated from the attenuation image by standard methods.

Rapidly deteriorating lung functionStable lung function

Eligibility Criteria

Age12 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Confirmed diagnosis of cystic fibrosis
  • Age 12 to 21 years old, of either gender, any race or ethnicity
  • Stable recent pulmonary status (defined as no new pulmonary symptoms, new antibiotic use, or hospitalization for pulmonary symptoms for at least 1 month).
  • We will permit patients treated with the macrolide antibiotic, azithromycin, to participate in this study. Azithromycin has recently become a virtual standard of care in CF, based on small but reproducible improvements in pulmonary function over 4 months of treatment with this drug. The mechanism of benefit is uncertain, but an anti-inflammatory effect has been suggested. The high prevalence of use means that a study without azithromycin would likely require a wash-out period, without data about the appropriate duration for such a wash-out, or whether inflammatory markers would reverse during that time.

You may not qualify if:

  • Failure to obtain informed consent
  • Positive pregnancy test or lactation
  • Currently enrolled in another study involving radioisotopes or an investigational drug
  • Recent (within 30 days of screening) hospitalization for any reason
  • New antibiotic use (within 30 days of screening).
  • Patient incapable of lying still and supine within the PET/computed X-ray tomography (CT) scanner for 90 minutes.
  • Patient incapable of completing other testing procedures (e.g., PFT, induced sputum)
  • Patient with serum glucose greater than 150 mg/dl at time of PET imaging study
  • Patient incapable of fasting for 4 to 6 hrs prior to PET imaging study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

MeSH Terms

Conditions

Cystic Fibrosis

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Results Point of Contact

Title
Thomas Ferkol, MD
Organization
Washington University

Study Officials

  • Thomas Ferkol, MD

    Washington University School of Medicine

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
DIAGNOSTIC
Intervention Model
SINGLE GROUP
Model Details: In this pilot study, we examined the value of FDG-PET scans as a noninvasive measure of neutrophilic inflammation in adolescents and young adults with cystic fibrosis. All subjects underwent scans.
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor of Pediatrics

Study Record Dates

First Submitted

February 16, 2009

First Posted

February 18, 2009

Study Start

February 1, 2009

Primary Completion

February 1, 2012

Study Completion

February 1, 2012

Last Updated

July 24, 2018

Results First Posted

July 24, 2018

Record last verified: 2018-06

Data Sharing

IPD Sharing
Will share

Data generated will be published at the end of the project, consistent with normal scientific practices. Such research data will be anonymized to prevent the disclosure of personal identifiers. In return for the use of data, investigators will acknowledge our grant number in publications and presentations, and in productivity reports on publications or funding that were derived from the project, and they will not distribute materials to third-parties without notification. There will be no charge for sharing data unless the request requires effort beyond what can be subsumed under normal project budgeted effort. If the request justifies a charge, the cost is kept to a minimum and based on actual expenses.

Shared Documents
STUDY PROTOCOL
Time Frame
Research data will be made available after the main findings from the final research data set have been accepted for publication. The data will be available indefinitely thereafter.
Access Criteria
Data may be shared with collaborators as approved by the Principal Investigator based on the following criteria: scientific merit, feasibility and IRB issues, appropriateness of principal investigator qualifications, and appropriateness to the project's overall goals and themes. Approval of the relevant co-investigators will be also sought and reviewed by the principal investigators.

Locations