NCT00705016

Brief Summary

The purpose of this open-label, randomized, controlled, Phase 1/2 study of the integrin inhibitor cilengitide is to evaluate the safety and efficacy of the combination of different regimens of cilengitide added to cisplatin, 5-fluorouracil (5-FU), and cetuximab in participants with recurrent/metastatic squamous cell carcinoma of the head and neck (SCCHN). The Phase 1 part was conducted in dedicated study centers. In the Phase 2 part of this trial, cilengitide is administered at two different doses to two experimental groups. The third group will only receive cisplatin, 5-FU and cetuximab. In the Phase 1 part of this trial, the dose of cilengitide in combination with cisplatin, 5-FU and cetuximab was determined. Cilengitide is an experimental anti-cancer substance interacting with so-called integrins. Integrins are protein molecules that are known to be present on the surface of certain cancer cells. Integrins are also found on certain cells that belong to growing blood vessels (endothelial cells). Integrins potentially facilitate the blood vessels' support of the tumor (angiogenesis) as well as the tumor's growth and further spread throughout the body (metastasis). By inhibiting integrins on the tumor cell surface, cilengitide potentially kills cancer cells, and potentially sensitizes cancer cells to other co-administered therapeutics. By inhibiting integrins on the endothelial cell surface, it potentially inhibits the ingrowth of additional blood vessels towards the tumor. Cilengitide is given as an intravenous infusion (given by a drip in one vein of your arm). If any unacceptable side effect occurs, treatment with the study drug will be stopped.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
184

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Oct 2008

Longer than P75 for phase_1

Geographic Reach
9 countries

37 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 24, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 25, 2008

Completed
3 months until next milestone

Study Start

First participant enrolled

October 1, 2008

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2011

Completed
1.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2013

Completed
11 months until next milestone

Results Posted

Study results publicly available

April 30, 2014

Completed
Last Updated

April 30, 2014

Status Verified

March 1, 2014

Enrollment Period

2.9 years

First QC Date

June 24, 2008

Results QC Date

March 28, 2014

Last Update Submit

March 28, 2014

Conditions

Keywords

Randomized treatmentopen-labelcontrolledrecurrentmetastaticSCCHNsuitablefor local therapy

Outcome Measures

Primary Outcomes (1)

  • Progression-free Survival (PFS) Time: Investigator Read

    The PFS is defined as the duration from randomization until radiological progression (based on response evaluation criteria in solid tumors \[RECIST\] Version 1.0) or death due to any cause. Only deaths within 84 days of last tumor assessment are considered. Participants without event are censored on the date of last tumor assessment. Investigator read is the assessment of all imaging by the treating physician at the local trial site.

    Time from randomization to disease progression, death or last tumor assessment, reported between day of first participant randomized, 03 July 2009, until cut-off date (03 September 2011)

Secondary Outcomes (6)

  • Overall Survival (OS) Time

    Time from randomization to death, reported between day of first participant randomized, 03 July 2009, until cut-off date (03 September 2011)

  • Best Overall Response (BOR) Rate

    Evaluations will be performed every 6 weeks until progression reported between day of first participant randomized, 03 July 2009, until cut-off date (03 September 2011)

  • Disease Control Rate

    Evaluations will be performed every 6 weeks until progression reported between day of first participant randomized, 03 July 2009, until cut-off date (03 September 2011)

  • Time to Treatment Failure (TTF)

    Time from randomization to disease progression, death or last tumor assessment, reported between day of first participant randomized, 03 July 2009, until cut-off date (03 September 2011)

  • Duration of Response

    Time from first assessment of CR or PR until PD, death or last tumor assessment, reported between day of first participant randomized, 03 July 2009, until cut-off date (03 September 2011)

  • +1 more secondary outcomes

Study Arms (3)

Cilengitide 2000 mg once weekly+Cetuximab+5-FU+Cisplatin

EXPERIMENTAL
Drug: Cilengitide 2000 mg once weeklyDrug: CetuximabDrug: 5-fluorouracil (5-FU)Drug: Cisplatin

Cilengitide 2000 mg twice weekly+Cetuximab+5-FU+Cisplatin

EXPERIMENTAL
Drug: Cilengitide 2000 mg twice weeklyDrug: CetuximabDrug: 5-fluorouracil (5-FU)Drug: Cisplatin

Cetuximab+5-FU+Cisplatin

ACTIVE COMPARATOR
Drug: CetuximabDrug: 5-fluorouracil (5-FU)Drug: Cisplatin

Interventions

Cilengitide 500 milligram (mg) will be administered as an intravenous infusion over 60 minutes, daily from Day 1 to 4 of the first week of each 3-week cycle, subsequently followed by 2000 mg dose of cilengitide on Day 8 and 15 of every cycle for a total of 6 cycles (18 weeks) or until PD, unacceptable toxicity or withdrawal for any other reason. After 6 cycles, participants received cilengitide 2000 mg once weekly until PD, unacceptable toxicity or withdrawal for any other reason.

Cilengitide 2000 mg once weekly+Cetuximab+5-FU+Cisplatin

Cilengitide 2000 mg will be administered as an intravenous infusion over 60 minutes, twice weekly on Day 1, 4, 8, 11, 15, and 18 of each 3-week cycle for a total of 6 cycles (18 weeks) or until PD, unacceptable toxicity or withdrawal for any other reason. After 6 cycles, participants will receive cilengitide 2000 mg once weekly until PD, unacceptable toxicity or withdrawal for any other reason.

Cilengitide 2000 mg twice weekly+Cetuximab+5-FU+Cisplatin

Cetuximab will be administered as 250 milligram per square meter (mg/m\^2) as infusion (initial starting dose of 400 mg/m\^2) on Day 1, 8 and 15 of each 3-week treatment cycle. Cetuximab will be administered for a total of 6 cycles (18 weeks) or until PD, unacceptable toxicity or withdrawal for any other reason. After 6 cycles, participants received Cetuximab 250 mg/m\^2 once weekly until PD, unacceptable toxicity or withdrawal for any other reason.

Also known as: Erbitux®
Cetuximab+5-FU+CisplatinCilengitide 2000 mg once weekly+Cetuximab+5-FU+CisplatinCilengitide 2000 mg twice weekly+Cetuximab+5-FU+Cisplatin

5-FU will be administered as an intravenous continuous infusion at a dose of 1000 mg/m\^2 daily from Day 1 to 4 of each 3-week treatment cycle. 5-FU will be administered for a total of 6 cycles (18 weeks), or until PD, unacceptable toxicity, or withdrawal for any other reason, whichever occur first.

Cetuximab+5-FU+CisplatinCilengitide 2000 mg once weekly+Cetuximab+5-FU+CisplatinCilengitide 2000 mg twice weekly+Cetuximab+5-FU+Cisplatin

Cisplatin will be administered as an intravenous infusion over 60 minutes, at a dose 100 mg/m\^2 on Day 1 of each 3-week treatment cycle. Cisplatin will be administered for a total of 6 cycles (18 weeks), or until PD, unacceptable toxicity, or withdrawal for any other reason, whichever occur first.

Cetuximab+5-FU+CisplatinCilengitide 2000 mg once weekly+Cetuximab+5-FU+CisplatinCilengitide 2000 mg twice weekly+Cetuximab+5-FU+Cisplatin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed diagnosis of SCCHN
  • At least one measurable lesion either by computerized tomography (CT) scan or magnetic resonance imaging (MRI)
  • Karnofsky performance status (KPS) of greater than or equal to 70 or eastern cooperative oncology group performance status (ECOG PS) of 0-1 at trial entry

You may not qualify if:

  • Prior systemic chemotherapy, except if given as part of a multimodal treatment for locally advanced disease, which was completed more than 6 months prior to trial entry
  • Surgery (excluding prior diagnostic biopsy) or irradiation within 4 weeks before trial entry
  • Nasopharyngeal Carcinoma
  • Documented or symptomatic brain or leptomeningeal metastasis
  • Previous treatment with epidermal growth factor receptor (EGFR) targeting therapy or signal transduction inhibitors

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (37)

Research Site

Salzburg, Austria

Location

Research Site

Vienna, Austria

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Antwerp, Belgium

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Brussels, Belgium

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Edegem (Antwerp), Belgium

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Ghent, Belgium

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Leuven, Belgium

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Namur, Belgium

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Lille, France

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Montpellier, France

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Nice, France

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Toulouse, France

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Tours, France

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Vandœuvre-lès-Nancy, France

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Villejuif, France

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Aachen, Germany

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Berlin, Germany

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Essen, Germany

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Hamburg, Germany

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Heidelberg, Germany

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Jena, Germany

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Leipzig, Germany

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Rostock, Germany

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Stuttgart, Germany

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Budapest, Hungary

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Győr, Hungary

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Nyíregyháza, Hungary

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La Spezia, Italy

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Milan, Italy

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Napoli, Italy

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Gliwice, Poland

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Warsaw, Poland

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L'Hospitalet de Llobregat, Spain

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Madrid, Spain

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Velencia, Spain

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Basel, Switzerland

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Geneva, Switzerland

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Related Publications (1)

  • Vermorken JB, Peyrade F, Krauss J, Mesia R, Remenar E, Gauler TC, Keilholz U, Delord JP, Schafhausen P, Erfan J, Brummendorf TH, Iglesias L, Bethe U, Hicking C, Clement PM. Cisplatin, 5-fluorouracil, and cetuximab (PFE) with or without cilengitide in recurrent/metastatic squamous cell carcinoma of the head and neck: results of the randomized phase I/II ADVANTAGE trial (phase II part). Ann Oncol. 2014 Mar;25(3):682-688. doi: 10.1093/annonc/mdu003.

MeSH Terms

Conditions

Neoplasms, Squamous CellRecurrenceNeoplasm Metastasis

Interventions

CilengitideCetuximabFluorouracilCisplatin

Condition Hierarchy (Ancestors)

Neoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsNeoplastic Processes

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsChlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum Compounds

Results Point of Contact

Title
Merck KGaA Communication Center
Organization
Merck Serono, a division of Merck KGaA

Study Officials

  • Jan Vermorken, MD, PhD

    University Hospital, Antwerp

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 24, 2008

First Posted

June 25, 2008

Study Start

October 1, 2008

Primary Completion

September 1, 2011

Study Completion

June 1, 2013

Last Updated

April 30, 2014

Results First Posted

April 30, 2014

Record last verified: 2014-03

Locations