NCT00682981

Brief Summary

The Phase I portion of this protocol will determine the best phase II dose and schedule of obatoclax with carboplatin and etoposide in patients with extensive-stage small cell lung cancer. The Phase II portion will evaluate the response rate to this regimen.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
218

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started May 2008

Typical duration for phase_1

Geographic Reach
10 countries

75 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2008

Completed
19 days until next milestone

First Submitted

Initial submission to the registry

May 20, 2008

Completed
3 days until next milestone

First Posted

Study publicly available on registry

May 23, 2008

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2011

Completed
Last Updated

July 21, 2016

Status Verified

July 1, 2016

Enrollment Period

3.5 years

First QC Date

May 20, 2008

Last Update Submit

July 19, 2016

Conditions

Keywords

ES-SCLCObatoclax

Outcome Measures

Primary Outcomes (1)

  • Determine the recommended Phase II dose of obatoclax administered as a 3-hour or 24-hour infusion for 3 consecutive days in Phase I, and response rate in Phase II.

    6 months

Study Arms (4)

Phase I A

EXPERIMENTAL

Obatoclax for 3 hours for 3 days with carboplatin/etoposide.

Drug: ObatoclaxDrug: Carboplatin/etoposide

Phase I B

EXPERIMENTAL

Obatoclax for 24 hours for 3 days with carboplatin/etoposide.

Drug: ObatoclaxDrug: Carboplatin/etoposide

Phase II A

EXPERIMENTAL

Obatoclax for 3 hours for 3 days with carboplatin/etoposide.

Drug: ObatoclaxDrug: Carboplatin/etoposide

Phase II B

ACTIVE COMPARATOR

Carboplatin/etoposide without continued study treatment

Drug: Carboplatin/etoposide

Interventions

IV Infusions for 3 consecutive days of either 3-hours, 2 hours duration

Also known as: GX15-070MS
Phase I APhase I BPhase II A

Carboplatin/etoposide combination

Also known as: Control
Phase I APhase I BPhase II APhase II B

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Phase I:
  • Pathological or cytological confirmation of SCLC
  • ES-SCLC
  • Measurable disease using Response Evaluation Criteria in Solid Tumors (RECIST) with at least one lesion ≥2.0 cm using conventional technique or ≥1.0 cm with spiral computed tomography (CT) scan in a single dimension
  • No previous chemotherapy
  • Age ≥18 years
  • Eastern Cooperative Oncology Group (ECOG) Performance Status ≤1
  • Normal organ function defined as: absolute neutrophil count (ANC)
  • /mm3, platelets ≥100,000/mm3, total bilirubin ≤ upper limit of normal (ULN) or total bilirubin ≤ 3.0 if liver metastases are present, alanine aminotransferase (serum glutamic pyruvic transaminase) (ALT \[SGPT\])
  • ´ ULN or ALT/SGPT ≤ 5 ´ ULN if liver metastases are present, and creatinine within normal institutional limits or calculated creatinine clearance ≥50 mL/min/1.73 m2 for patients with creatinine levels above institutional normal
  • Negative serum or urine pregnancy test result prior to study entry. In addition, women of child-bearing potential and men with partners of child-bearing potential must agree to use acceptable forms of birth control (those that result in less than 1% pregnancy/year when used correctly: implants, injectables, combined oral contraceptives, some IUDs, vasectomy of a male partner, sexual abstinence)
  • Ability to understand and willingness to sign a written informed consent form
  • Phase II:
  • Pathological or cytological confirmation of SCLC
  • ES-SCLC
  • +8 more criteria

You may not qualify if:

  • Phase I and II:
  • Other investigational or commercial agents or therapies administered with the intent to treat the patient's malignancy
  • History of allergic reactions attributed to components of the obatoclax formulation (Polysorbate 20 and PEG 300)
  • History of seizure disorders unrelated to SCLC brain metastases, or presence of symptomatic brain metastases
  • Uncontrolled,intercurrent illness including, but not limited to, symptomatic neurological illness; active, uncontrolled systemic infection considered opportunistic, lifethreatening,or clinically significant at the time of treatment; symptomatic congestive heart failure; unstable angina pectoris; clinically significant cardiac arrhythmia; significant pulmonary disease or hypoxia; or psychiatric illness/social situations that would limit compliance with study requirements
  • Pregnant women and women who are breast feeding;
  • human immunodeficiency virus (HIV)-positive patients receiving combination anti-retroviral therapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (75)

Clearview Cancer Institute

Huntsville, Alabama, 35805, United States

Location

Northwest Alabama Cancer Center

Muscle Shoals, Alabama, 35661, United States

Location

Mayo Clinic-Arizona

Scottsdale, Arizona, 85259, United States

Location

Arizona Clinical Research Center

Tucson, Arizona, 85715, United States

Location

City of Hope and Beckman Research Institute

Duarte, California, 91010, United States

Location

University of California-San Diego Moores Cancer Center

La Jolla, California, 92093-0987, United States

Location

Georgetown University Hospital-Lombardi Comprehensive Cancer Center

Washington D.C., District of Columbia, 20007, United States

Location

Integrated Community Oncology Network

Jacksonville, Florida, 32256, United States

Location

University of Miami-Sylvester Cancer Center

Miami, Florida, 33136, United States

Location

Florida Cancer Institute

New Port Richey, Florida, 34655-1112, United States

Location

H. Lee Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Northwest Georgia Oncology Centers

Marietta, Georgia, 30060, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Iowa Blood and Cancer Center, PLC

Cedar Rapids, Iowa, 52402, United States

Location

Cancer Center of Kansas

Wichita, Kansas, 67214, United States

Location

James Brown Cancer Center

Louisville, Kentucky, 40202, United States

Location

Center for Cancer and Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Kalamazoo Hematology and Oncology

Kalamazoo, Michigan, 49048, United States

Location

Mid Ohio Oncology/Hematology, Inc.

Columbus, Ohio, 43219, United States

Location

Cancer Care Associates-Oklahoma City

Oklahoma City, Oklahoma, 73112, United States

Location

Cancer Care Associates-Tulsa

Tulsa, Oklahoma, 74136, United States

Location

University of Pennsylvania Abramson Cancer Center

Philadelphia, Pennsylvania, 19104, United States

Location

Greater Philadelphia Cancer and Hematology Specialists

Philadelphia, Pennsylvania, 19114, United States

Location

Cancer Centers of the Carolinas

Greenville, South Carolina, 29605, United States

Location

McLeod Cancer & Blood Center

Johnson City, Tennessee, 37604, United States

Location

The West Clinic

Memphis, Tennessee, 38120, United States

Location

Baylor

Dallas, Texas, 75246, United States

Location

UT Southwestern Medical Center at Dallas

Dallas, Texas, 75390-8852, United States

Location

Tyler Cancer Center

Tyler, Texas, 75702, United States

Location

Peninsula Cancer Institute

Newport News, Virginia, 23601, United States

Location

Virginia Oncology Associates

Norfolk, Virginia, 23502, United States

Location

Wheeling Hospital

Wheeling, West Virginia, 26003, United States

Location

MHAT "Dr. Tota Venkova"

Gabrovo, Bulgaria

Location

District Dispensary for Cancer Diseases, Plovdiv

Plovdiv, Bulgaria

Location

District Dispensary for Oncology Diseases, Sofia City

Sofia, Bulgaria

Location

Specialized Hospital for Active Treatment in Oncology

Sofia, Bulgaria

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

McGill University

Montreal, Quebec, H2W 1S6, Canada

Location

Regional Hospital Kladno

Kladno, Czechia

Location

Hospital Kutna Hora

Kutná Hora, Czechia

Location

University Hospital Olomouc

Olomouc, Czechia

Location

Faculty Hospital Ostrava

Ostrava-Poruba, Czechia

Location

University Hospital Na Bulovce

Prague, Czechia

Location

National Institute of Tuberculosis & Pulmonology

Budapest, Hungary

Location

Semmelweis University Medical School, Budapest

Budapest, Hungary

Location

University Of Debrecen Medical and Health Science Centre

Debrecen, Hungary

Location

Csongrad County Council's Hospital for Chest Diseases

Deszk, Hungary

Location

Bacs-Kiskun County Hospital

Kecskemét, Hungary

Location

State Hospital Matrahaza

Mátraháza, Hungary

Location

Clinfan Ltd. SMO Tolna County Hospital

Szekszárd, Hungary

Location

Pest County Hospital

Törökbálint, Hungary

Location

Vedanta Institute of Medical Sciences

Ahmedabad, Gujarat, India

Location

Kailash Cancer Hospital and Research Centre

Goraj, Gujarat, India

Location

Jawaharlal Nehru Cancer Hospital and Research Centre

Bhopal, Madhya Pradesh, India

Location

Curie Manavata Cancer Centre

Nashik, Maharashtra, India

Location

Noble Hospital

Pune, Maharashtra, India

Location

Dr. Kamakshi Memorial Hospital

Chennai, Tamal Nadu, India

Location

Galaxy Cancer Institute, Pushpanjali Crosslay Hospital

Ghaziabad, Uttar Pradesh, India

Location

Orchid Nursing Home

Kolkata, West Bengal, India

Location

Wojewodzki Szpital Specjalistyczny im. K. Dluskiego

Bialystok, Poland

Location

SPZ Gruzlicy i Chorob Pluc

Olsztyn, Poland

Location

Mazowieckie Centrum Leczenia Chorob Pluc i Gruzlicy

Otwock, Poland

Location

Specjalistyczny Szpital im Prof Alfreda Sokolowskiego

Szczecin-Zdunowo, Poland

Location

Wojewodzki Szpital Chorob Pluc

Wodzisław Śląski, Poland

Location

Prof. Dr. Ion Chiricuta Oncology Institute Cluj Napoca

Cluj-Napoca, Romania

Location

Oncology Medical Centre SCM

Iași, Romania

Location

Emergency Clinical County Hospital Oradea

Oradea, Romania

Location

Institute for Pulmonary Diseases of Vojvodina

Kamenitz, Serbia

Location

Center for Pulmonary Diseases, Clinic for Internal Medicine

Kragujevac, Serbia

Location

Northern Ireland Cancer Centre Queens University Belfast

Belfast, Northern Ireland, United Kingdom

Location

Royal Bournemouth Hospital

Dorset, United Kingdom

Location

Nottingham University Hospital

Nottingham, United Kingdom

Location

Weston Park Hospital

Sheffield, United Kingdom

Location

Royal Surrey County Hospital

Surrey, United Kingdom

Location

Related Publications (1)

  • Langer CJ, Albert I, Ross HJ, Kovacs P, Blakely LJ, Pajkos G, Somfay A, Zatloukal P, Kazarnowicz A, Moezi MM, Schreeder MT, Schnyder J, Ao-Baslock A, Pathak AK, Berger MS; GEM017 Investigators. Randomized phase II study of carboplatin and etoposide with or without obatoclax mesylate in extensive-stage small cell lung cancer. Lung Cancer. 2014 Sep;85(3):420-8. doi: 10.1016/j.lungcan.2014.05.003. Epub 2014 May 13.

MeSH Terms

Conditions

Small Cell Lung Carcinoma

Interventions

obatoclaxEC regimen

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Study Officials

  • Jean Viallet, MD

    Gemin X Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 20, 2008

First Posted

May 23, 2008

Study Start

May 1, 2008

Primary Completion

November 1, 2011

Study Completion

November 1, 2011

Last Updated

July 21, 2016

Record last verified: 2016-07

Locations