NCT00338286

Brief Summary

The purpose of this study is to assess the impact on tumor progression as evaluated by progression-free survival (PFS) of epoetin alfa plus standard supportive care as compared with standard supportive care alone (packed red blood cell (RBC) transfusions), for treating anemia according to label guidance in patients with metastatic breast cancer receiving standard chemotherapy.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
2,098

participants targeted

Target at P75+ for phase_3 breast-cancer

Timeline
Completed

Started Mar 2006

Longer than P75 for phase_3 breast-cancer

Geographic Reach
21 countries

174 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 2, 2006

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

June 16, 2006

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 20, 2006

Completed
8.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 7, 2014

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

March 24, 2016

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 31, 2017

Completed
Last Updated

March 19, 2018

Status Verified

February 1, 2018

Enrollment Period

8.4 years

First QC Date

June 16, 2006

Results QC Date

December 22, 2015

Last Update Submit

February 15, 2018

Conditions

Keywords

anemiametastatic breast cancerHemoglobinprogression-free survival (PFS)erythropoiesis-stimulating agents (ESA)

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival

    Progression free survival was based in investigator-determined progressive disease (PD) and calculated from the date of randomization to the date of PD or the date of death, whichever occurred first. Participants who had not progressed and were still alive at the time of clinical cut off were censored at the last disease assessment prior to the clinical cutoff. For PD or death with a missing interval immediately preceding the event, progression-free survival (PFS) was censored at the last disease assessment prior to the missing interval. Participants who withdrew from the study (withdrawal of consent or lost to follow-up) without progression were censored at the time of the last disease assessment.

    From the date of randomization to the date of disease progression (PD) or death, whichever occurred first (up to 8.4 years)

Secondary Outcomes (4)

  • Overall Survival

    From randomization up to death from any cause (up to 8.4 years)

  • Time to Tumor Progression

    From date of randomization to the date of the first documented PD (up to 8.4 years)

  • Overall Response Rate (ORR)

    every 8 weeks for 1 year and then every 12 weeks until PD or death, whichever occurred first (up to 8.4 years)

  • Percentage of Participants With Suspected Thrombotic Vascular Events (TVEs)

    up to 8.4 years

Study Arms (2)

001

EXPERIMENTAL

epoetin alfa + packed RBC transfusion 40 000 IU SC once a week.

Drug: epoetin alfa + packed RBC transfusion

002

OTHER

Standard supportive care (packed RBC transfusion) Per doctor prescription

Other: Standard supportive care (packed RBC transfusion)

Interventions

40,000 IU SC once a week.

001

Eligibility Criteria

Age18 Years - 99 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed (e.g., slide of tissue) breast cancer
  • HER2/NEU positive or negative
  • Clinical evidence of metastasis (e.g., biopsy) with at least 1 measurable metastatic (M1) lesion prior to starting the current chemotherapy
  • Received 1st and 2nd line chemotherapy
  • Hemoglobin (Hb) \<= 11g/dL at the time of randomization
  • planned to receive at least 2 more cycles of chemotherapy
  • Life expectancy \> 6 months
  • Eastern Cooperative Oncology Group score 0 or 1
  • At least 18 years old using effective birth control or surgically sterile or postmenopausal for 1 year

You may not qualify if:

  • Active second cancer
  • no recent history of clinically relevant thrombovascular event
  • Current treatment with anticoagulants
  • Brain metastasis or CNS involvement
  • Anemia secondary to another cause
  • Recent (within prior 1 months) use of an ESA
  • Patient pregnant or breast feeding
  • Progressive disease during adjuvant/neoadjuvant chemotherapy
  • Rapidly progressive or life-threatening metastatic disease
  • Concomitant endocrine therapy
  • Patient in whom the only site of metastasis was local and was successfully treated surgically.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (174)

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Anaheim, California, United States

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Gainesville, Florida, United States

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Miami, Florida, United States

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New Port Richey, Florida, United States

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Rockledge, Florida, United States

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Hazard, Kentucky, United States

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Alexandria, Louisiana, United States

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Marrero, Louisiana, United States

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Jackson, Mississippi, United States

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Lake Success, New York, United States

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Staten Island, New York, United States

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Philadelphia, Pennsylvania, United States

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Corpus Christi, Texas, United States

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Houston, Texas, United States

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Buenos Aires, Argentina

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Capital Federal, Argentina

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Ciudad Autonoma de Buenos Airess, Argentina

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Córdoba, Argentina

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La Plata, Argentina

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Mendoza, Argentina

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Quilmes, Argentina

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Rosario, Argentina

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Santa Fe, Argentina

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Barretos, Brazil

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Curitiba, Brazil

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Goiânia/Go, Brazil

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Ijuí, Brazil

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Jaú, Brazil

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Piracicaba, Brazil

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Porto Alegre, Brazil

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Ribeirão Preto/Sp, Brazil

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Santo André, Brazil

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São José do Rio Preto, Brazil

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São Paulo, Brazil

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São Paulol, Brazil

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Plovdiv, Bulgaria

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Rousse, Bulgaria

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Sofia, Bulgaria

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Stara Zagora, Bulgaria

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Varna, Bulgaria

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Arica, Chile

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Santiago, Chile

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Temuco, Chile

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Valdivia, Chile

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Valparaíso, Chile

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Bogotá, Colombia

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Floridablanca-Santander, Colombia

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Montería, Colombia

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Cuenca, Ecuador

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Guayaquil, Ecuador

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Portoviejo, Ecuador

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Quito, Ecuador

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Batumi, Georgia

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Tbilisi, Georgia

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New Territories, Hong Kong

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Ahmedabad, India

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Andra Pradesh, India

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Bangalore, India

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Bengaluru, India

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Bhopal, India

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Delhi, India

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Hyderabad, India

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Jaipur, India

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Kārnād, India

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Kerala, India

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Kochi, India

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Kolkata, India

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Mangalore, India

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Mumbai, India

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Nashik, India

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New Delhi, India

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Pune, India

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Tamil Nadu Na, India

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Tamil Nadu, India

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Thiruvananthapuram, India

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Uttar Pradesh, India

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Vellore, India

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Bandung, Indonesia

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Jakarta, Indonesia

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Semarang, Indonesia

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Yogyakarta, Indonesia

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George Town, Malaysia

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Kampung Baharu Nilai, Malaysia

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Kelantan, Malaysia

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Kuala Lumpur, Malaysia

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Tanjung Bungah, Malaysia

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Chihuahua City, Mexico

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Guerrero, Mexico

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León, Mexico

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Mérida, Mexico

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Morelia, Mexico

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Puebla City, Mexico

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San Luis Potosí City, Mexico

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Sinaloa, Mexico

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Zapopan, Mexico

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Bitola, North Macedonia

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Skopje, North Macedonia

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Cebu, Philippines

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Davao City, Philippines

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Iloilo City, Philippines

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Manila, Philippines

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Quezon City, Philippines

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Bialystok, Poland

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Gdansk, Poland

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Gliwice, Poland

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Katowice, Poland

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Krakow, Poland

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Lodz, Poland

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Olsztyn, Poland

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Poznan, Poland

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Wroclaw, Poland

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Brasov, Romania

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Bucharest, Romania

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Cluj-Napoca, Romania

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Iași, Romania

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Onești, Romania

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Sibiu, Romania

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Suceava, Romania

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Timișoara, Romania

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Arkhangelsk, Russia

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Balashikha, Russia

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Belgorod, Russia

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Chelyabinsk, Russia

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Engels Saratov Region, Russia

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Ivanovo, Russia

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Kazan', Russia

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Krasnodar, Russia

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Leningrad Region, Russia

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Lipetsk, Russia

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Magnitogorsk, Russia

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Moscow, Russia

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Novosibirsk, Russia

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Obninsk, Russia

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Orenburg, Russia

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Perm, Russia

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Pyatigorsk, Russia

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Ryazan, Russia

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Saint Petersburg, Russia

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Smolensk, Russia

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Tyumen, Russia

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Ufa, Russia

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Voronezh, Russia

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Yekaterinburg, Russia

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Bloemfontein, South Africa

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Cape Town, South Africa

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Durban, South Africa

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Johannesburg, South Africa

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Klerksdorp, South Africa

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Port Elizabeth, South Africa

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Pretoria, South Africa

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Changhua, Taiwan

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Chiayi City, Taiwan

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Hualien City, Taiwan

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Kaohsiung City, Taiwan

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Taichung, Taiwan

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Tainan, Taiwan

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Taipei, Taiwan

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Taoyuan District, Taiwan

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Cherkassy, Ukraine

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Chernihiv, Ukraine

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Chernivtsi, Ukraine

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Dnipro, Ukraine

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Donetsk, Ukraine

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Ivano-Francovsk, Ukraine

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Kharkiv, Ukraine

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Kiev, Ukraine

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Lviv, Ukraine

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Odesa, Ukraine

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Poltava, Ukraine

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Sumy, Ukraine

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Uzhhorod, Ukraine

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Vinnitsa, Ukraine

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Vinnytsia, Ukraine

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Zaporizhzhya, Ukraine

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Related Publications (1)

  • Leyland-Jones B, Bondarenko I, Nemsadze G, Smirnov V, Litvin I, Kokhreidze I, Abshilava L, Janjalia M, Li R, Lakshmaiah KC, Samkharadze B, Tarasova O, Mohapatra RK, Sparyk Y, Polenkov S, Vladimirov V, Xiu L, Zhu E, Kimelblatt B, Deprince K, Safonov I, Bowers P, Vercammen E. A Randomized, Open-Label, Multicenter, Phase III Study of Epoetin Alfa Versus Best Standard of Care in Anemic Patients With Metastatic Breast Cancer Receiving Standard Chemotherapy. J Clin Oncol. 2016 Apr 10;34(11):1197-207. doi: 10.1200/JCO.2015.63.5649. Epub 2016 Feb 8.

MeSH Terms

Conditions

Breast NeoplasmsNeoplasm MetastasisAnemia

Interventions

Epoetin Alfa

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

ErythropoietinColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Director, Clinical Research
Organization
Janssen Research and Development

Study Officials

  • Janssen Research & Development, LLC C. Clinical Trial

    Janssen Research & Development, LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 16, 2006

First Posted

June 20, 2006

Study Start

March 2, 2006

Primary Completion

July 7, 2014

Study Completion

January 31, 2017

Last Updated

March 19, 2018

Results First Posted

March 24, 2016

Record last verified: 2018-02

Locations