NCT00314106

Brief Summary

Background:

  • In a study in humans with melanoma, patients given total body irradiation to suppress the immune system in conjunction with chemotherapy showed a significant clinical response.
  • In previous studies, about one-half of patients given tumor-fighting cells (cells created from the patient's tumor cells and grown in the laboratory) showed some anti-tumor response. Objective: To determine whether tumor-fighting cells taken from a melanoma tumor and grown in the lab can more effectively at fight melanoma when the patient's immune system is suppressed and cannot attack them. Eligibility: Patients 18 years of age or older with metastatic melanoma who have tumor reactive cells available. Design:
  • Patients are assigned to one of two groups - those having received prior therapy with Interleukin-2 (IL-2) and those who have not. After five days of injections of filgrastim, a medicine to stimulated the growth of white blood cells, patients undergo apheresis or bone marrow harvesting, or both, to collect stem cells for later re-infusion. For apheresis, whole blood is collected through a needle in an arm vein and circulated through a cell-separating machine where the stem cells are extracted. The rest of the blood is returned through the same needle or a needle in the other arm. Bone marrow harvesting is done under general anesthesia. Stem cells are collected through a large needle inserted into the hipbone.-Patients' immune system cells and bone marrow function are eliminated with chemotherapy (7 days) and total body irradiation (3 days) so the patient's immune system cells will not fight the tumor-fighting cells they are given in treatment.
  • 1 to 3 days after total body irradiation, patients receive the tumor-fighting cells by intravenous (IV) infusion. After the cells are infused, they receive interleukin-2 (IL-2) infusions every 8 hours for 5 days.
  • 2 days after infusion of the tumor-fighting cells, patients receive the stem cells collected earlier by apheresis.
  • Patients are evaluated 4 to 6 weeks after cell infusion to look for tumor response to treatment. Patients whose tumor has not grown return to the National Institutes of Health (NIH) every 1 to 3 months for blood tests, scans and x-rays.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
26

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Apr 2006

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2006

Completed
10 days until next milestone

First Submitted

Initial submission to the registry

April 11, 2006

Completed
1 day until next milestone

First Posted

Study publicly available on registry

April 12, 2006

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2009

Completed
28 days until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2009

Completed
3.6 years until next milestone

Results Posted

Study results publicly available

October 18, 2012

Completed
Last Updated

October 18, 2012

Status Verified

September 1, 2012

Enrollment Period

2.8 years

First QC Date

April 11, 2006

Results QC Date

September 18, 2012

Last Update Submit

September 18, 2012

Conditions

Keywords

Clinical ResponseStage IV MelanomaAdoptive Cell TherapyTumor Infiltrating LymphocytesImmunologic ResponseMetastatic Melanoma

Outcome Measures

Primary Outcomes (1)

  • Complete Response

    Determine if the combination of high dose aldesleukin, reinfused cells after lymphocyte depleting chemotherapy and 1200 cGy total body irradiation (TBI) is able to be associated with a modest fraction of patients with metastatic melanoma who can experience a complete response to therapy. Complete response (CR) is a disappearance of all target lesions.

    33 months

Secondary Outcomes (1)

  • Number of Participants With Adverse Events

    33 months

Study Arms (2)

TBI 1200 cGy + TIL +HD IL-2, prior IL-2

EXPERIMENTAL

Patients that received prior interleukin 2 (IL-2) therapy will receive a myeloablative lymphocyte depleting preparative regimen consisting of cyclophosphamide (60 mg/kg/day x 2 days intravenous (IV)), fludarabine (25mg/m\^2/day IV X 5 days) and 1200 cGy total body irradiation (TBI). Following the lymphodepleting regimen, patient will receive intravenous adoptive transfer of tumor reactive lymphocytes (minimum 3 X 10 (9) and up to a maximum of 3 X 10(11) lymphocytes) followed by high-dose intravenous (IV) IL-2 (720,000 IU/kg/dose every 8 hours for up to 15 doses).

Biological: Melanoma Reactive TILDrug: CyclophosphamideBiological: IL-2Drug: FludarabineRadiation: 1200 total body irradiation (TBI)

TBI 1200 cGy + TIL +HD IL-2, no prior IL-2

EXPERIMENTAL

Patients that have not received prior interleukin 2 (IL-2) therapy will receive a myeloablative lymphocyte depleting preparative regimen consisting of cyclophosphamide (60 mg/kg/day x 2 days intravenous (IV)), fludarabine (25mg/m\^2/day IV X 5 days) and 1200 cGy total body irradiation (TBI). Following the lymphodepleting regimen, patient will receive intravenous adoptive transfer of tumor reactive lymphocytes (minimum 3 X 10 (9) and up to a maximum of 3 X 10(11) lymphocytes) followed by high-dose intravenous (IV) IL-2 (720,000 IU/kg/dose every 8 hours for up to 15 doses)

Biological: Melanoma Reactive TILDrug: CyclophosphamideBiological: IL-2Drug: FludarabineRadiation: 1200 total body irradiation (TBI)

Interventions

Also known as: (TIL) tumor infiltrating lymphocytes
TBI 1200 cGy + TIL +HD IL-2, no prior IL-2TBI 1200 cGy + TIL +HD IL-2, prior IL-2

60 mg/kg/ day x 2 days intravenous

Also known as: Cytoxan
TBI 1200 cGy + TIL +HD IL-2, no prior IL-2TBI 1200 cGy + TIL +HD IL-2, prior IL-2
IL-2BIOLOGICAL

720,000 IU/kg/dose every 8 hours for up to 15 doses

Also known as: Aldesleukin
TBI 1200 cGy + TIL +HD IL-2, no prior IL-2TBI 1200 cGy + TIL +HD IL-2, prior IL-2

25 mg/m\^2/day intravenous x 5 days

Also known as: Fludara
TBI 1200 cGy + TIL +HD IL-2, no prior IL-2TBI 1200 cGy + TIL +HD IL-2, prior IL-2

1200 cGY total body radiation

Also known as: TBI
TBI 1200 cGy + TIL +HD IL-2, no prior IL-2TBI 1200 cGy + TIL +HD IL-2, prior IL-2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have tumor reactive cells obtained and evaluated while participating in the Surgery Branch protocol, "Cell Harvest and Preparation for Surgery Branch Adoptive Cell Therapy Protocols" or on another Institutional Review Board (IRB) approved Surgery Branch adoptive cell therapy study, i.e. 99-C-0158 or 03-C-0162.
  • The first ten patients enrolled must have previously received interleukin-2 (IL-2) and have been either non-responders (progressive disease) or have recurred.
  • Patients must be greater than or equal to 18 years of age and must have measurable metastatic melanoma.
  • Patients of both genders must be willing to practice birth control during treatment and for four months after receiving the preparative regimen.
  • Clinical performance status of Eastern Cooperative Oncology Group (ECOG) 0, 1.
  • Absolute neutrophil count greater than 1000/mm\^3 without support of filgrastim.
  • Platelet count greater than 100,000/mm\^3.
  • Serum alanine aminotransferase (ALT)/aspartate aminotransferase (AST) less than three times the upper limit of normal.
  • Serum creatinine less than or equal to 1.6 mg/dl.
  • Total bilirubin less than or equal to 2 mg/dl, except in patients with Gilbert's Syndrome who must have a total bilirubin less than 3 mg/dl.
  • Must be willing to sign a durable power of attorney.
  • Patients must be able to understand and sign the Informed Consent document.
  • Patients with resected or stable brain metastases will be eligible.
  • Left ventricular ejection fraction (LVEF) greater than or equal to 45%.
  • Carbon monoxide diffusing capacity (DLCO) greater than or equal to 60% predicted.

You may not qualify if:

  • Less than 30 days has elapsed since any prior systemic therapy at the time the patient receives the preparative regimen, or less than six weeks since prior nitrosurea therapy. All patients' toxicities must have recovered to a grade 1 or less or as specified in the eligibility criteria. Patients may have undergone minor surgical procedures within the past 3 weeks, as long as all toxicities have recovered to grade 1 or less or as specified in the eligibility criteria.
  • Women of child-bearing potential who are pregnant or breastfeeding because of the potentially dangerous effects of the preparative chemotherapy on the fetus or infant.
  • Life expectancy of less than three months.
  • Systemic steroid therapy required.
  • Hemoglobin less than 8 g/dl unable to be corrected with transfusion.
  • Any active systemic infections, coagulation disorders or other active major medical illnesses of the cardiovascular, respiratory or immune system, as evidenced by a positive stress thallium or comparable test, myocardial infarction, cardiac arrhythmias, obstructive or restrictive pulmonary disease.
  • Any form of primary or secondary immunodeficiency. Must have recovered immune competence after chemotherapy or radiation therapy as evidenced by normal ANC greater than 1000/mm\^3 and absence of opportunistic infections. (The experimental treatment being evaluated in this protocol depends on an intact immune system. Patients who have decreased immune competence may be less responsive to the experimental treatment and more susceptible to its toxicities.)
  • Seropositive for human immunodeficiency virus (HIV) antibody. (The experimental treatment being evaluated in this protocol depends on an intact immune system. Patients who are HIV seropositive can have decreased immune competence and thus be less responsive to the experimental treatment and more susceptible to its toxicities.)
  • Patients with hepatitis B or hepatitis C will be excluded.
  • Seronegative for Epstein-Barr virus (EBV).
  • Patients who are not willing to complete a durable power of attorney (DPA) will be excluded.
  • Patients who have received prior preparative regimens with cyclophosphamide and fludarabine on prior Surgery Branch adoptive cell therapies will be excluded.
  • The following patients will be excluded because of inability to receive high dose IL-2:
  • Patients will be excluded if they have a history of electrocardiogram (EKG) abnormalities, symptoms of cardiac ischemia or arrhythmias and have a LVEF less than 45% on a cardiac stress test (stress thallium, stress multi-gated acquisition scan (MUGA), dobutamine, echocardiogram or other stress test).
  • Similarly, patients who are 50 years old or greater with an LVEF less than 45% will be excluded.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Cancer Institute (NCI)

Bethesda, Maryland, 20892, United States

Location

Related Publications (2)

  • Rooney CM, Smith CA, Ng CY, Loftin S, Li C, Krance RA, Brenner MK, Heslop HE. Use of gene-modified virus-specific T lymphocytes to control Epstein-Barr-virus-related lymphoproliferation. Lancet. 1995 Jan 7;345(8941):9-13. doi: 10.1016/s0140-6736(95)91150-2.

    PMID: 7799740BACKGROUND
  • Yao X, Ahmadzadeh M, Lu YC, Liewehr DJ, Dudley ME, Liu F, Schrump DS, Steinberg SM, Rosenberg SA, Robbins PF. Levels of peripheral CD4(+)FoxP3(+) regulatory T cells are negatively associated with clinical response to adoptive immunotherapy of human cancer. Blood. 2012 Jun 14;119(24):5688-96. doi: 10.1182/blood-2011-10-386482. Epub 2012 May 3.

Related Links

MeSH Terms

Conditions

Melanoma

Interventions

Toll-Like Receptor 1CyclophosphamideInterleukin-2aldesleukinfludarabinefludarabine phosphate

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Toll-Like ReceptorsReceptors, Pattern RecognitionReceptors, ImmunologicReceptors, Cell SurfaceMembrane ProteinsProteinsAmino Acids, Peptides, and ProteinsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsInterleukinsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesLymphokinesBiological Factors

Results Point of Contact

Title
Steven A. Rosenberg, M.D.
Organization
National Cancer Institute, National Institutes of Health

Study Officials

  • Steven A Rosenberg, M.D.

    National Cancer Institute, National Institutes of Health

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH

Study Record Dates

First Submitted

April 11, 2006

First Posted

April 12, 2006

Study Start

April 1, 2006

Primary Completion

February 1, 2009

Study Completion

March 1, 2009

Last Updated

October 18, 2012

Results First Posted

October 18, 2012

Record last verified: 2012-09

Locations