NCT00300274

Brief Summary

This trial was to examine the impact of everolimus and reduced dose of cyclosporine on efficacy and safety compared to mycophenolate mofetil and a standard dose of cyclosporine in heart transplant recipients.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
721

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jan 2006

Longer than P75 for phase_3

Geographic Reach
14 countries

63 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2006

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

March 6, 2006

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 8, 2006

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2011

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

August 16, 2012

Completed
Last Updated

August 16, 2012

Status Verified

July 1, 2012

Enrollment Period

5.5 years

First QC Date

March 6, 2006

Results QC Date

July 6, 2012

Last Update Submit

July 10, 2012

Conditions

Keywords

Everolimusheart transplantheart diseasetransplantationheart IVUS assessment at 12 monthsrate of graft lossacute rejection episodessurvival

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Composite Efficacy Failure at 12 Months

    Composite efficacy failure was defined as Biopsy Proven Acute Rejection(BPAR) of International Society for Heart and Lung Transplantation(ISHLT) grade ≥3A, Acute Rejection associated with Hemodynamic Compromise, Graft loss/Retransplant, Death or Loss to follow-up. Identification of acute rejection was based on the local pathologist's evaluation of endomyocardial biopsy slides. Hemodynamic compromise was present if 1 or more of the following were met: Ejection fraction ≤30% or 25% lower than Baseline or Fractional shortening ≤20% or 25% lower than Baseline and/or use of inotropic treatment.

    12 Months

Secondary Outcomes (9)

  • Percentage of Participants With Graft Loss/Re-transplant, Death or Loss to Follow-up at 12 Months

    12 Months

  • Renal Function Measured by Glomerular Filtration Rate (GFR) at 12 Months

    12 Months

  • Change From Baseline in the Average Maximum Intimal Thickness at Month 12

    Baseline, Month 12

  • Percentage of Participants With Cardiac Allograft Vasculopathy (CAV) at Month 12

    12 Months

  • Percentage of Participants With Biopsy-proven Acute Rejection (BPAR of ISHLT Grade ≥ 3A), Acute Rejection Associated With Hemodynamic Compromise (HDC), Graft Loss/Re-transplant and Death at Month 12

    12 Months

  • +4 more secondary outcomes

Study Arms (3)

everolimus 1.5 mg

EXPERIMENTAL

Within 72 hours after transplantation participants received 0.75 mg everolimus tablets twice a day 12 hours apart for a total 1.5 mg daily dose in combination with reduced cyclosporine and standard dose corticosteroids for 24 months. The everolimus dose could be adjusted to maintain a target everolimus trough level of 3-8 ng/mL.

Drug: everolimusDrug: cyclosporineDrug: corticosteroids

everolimus 3.0 mg

EXPERIMENTAL

Within 72 hours after transplantation participants received 1.5 mg everolimus tablets twice a day 12 hours apart for a total 3.0 mg daily dose in combination with reduced cyclosporine and standard dose corticosteroids for 24 months. The everolimus dose could be adjusted to maintain a target everolimus trough level of 6-12 ng/mL. Randomization of new patients in this arm was prematurely stopped as of 27 March 2008 due to high mortality rate, as per Data Monitoring Committee.

Drug: everolimusDrug: cyclosporineDrug: corticosteroids

mycophenolate mofetil

ACTIVE COMPARATOR

Within 72 hours after transplantation participants received 3 tablets 500 mg mycophenolate mofetil twice a day 12 hours apart for a total daily dose of 3000 mg in combination with a standard cyclosporine dose and standard dose corticosteroids for 24 months.

Drug: mycophenolate mofetilDrug: cyclosporineDrug: corticosteroids

Interventions

Everolimus supplied as 0.75 mg tablets. Everolimus was also supplied in 0.25 mg and 0.5 mg tablets for dose adjustments.

Also known as: Zortress®, Certican®
everolimus 1.5 mgeverolimus 3.0 mg

Mycophenolate mofetil supplied as 500 mg tablets.

Also known as: Cellcept®
mycophenolate mofetil

Cyclosporine reduced dose in the everolimus arms (approximately half of the standard dose) and standard dose in the mycophenolate mofetil arm.

Also known as: Neoral®
everolimus 1.5 mgeverolimus 3.0 mgmycophenolate mofetil

Corticosteroids standard dose.

everolimus 1.5 mgeverolimus 3.0 mgmycophenolate mofetil

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female cardiac recipients 18-70 years of age undergoing primary heart transplantation.
  • The graft must be functional at time of randomization.

You may not qualify if:

  • Patients who are recipients of multiple solid organ transplants or tissue transplants or have previously received organ transplants.
  • Patients who are recipients of ABO incompatible transplants.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (64)

UCLA Medical Center

Los Angeles, California, United States

Location

California Pacific Medical Center

San Francisco, California, United States

Location

Stanford U Sch, Falk Cardiovasular Research Ctr.

Stanford, California, United States

Location

University of Florida Shands Hospital

Gainesville, Florida, United States

Location

Emory University Hospital

Atlanta, Georgia, United States

Location

Loyola Univerisity Medical School

Maywood, Illinois, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, United States

Location

Tufts Medical Center

Boston, Massachusetts, United States

Location

University of Michigan Health System

Ann Arbor, Michigan, United States

Location

Washington University School of Medicine

St Louis, Missouri, United States

Location

Columbia University Medical Center

New York, New York, United States

Location

Recanati Miller Transplant Institute

New York, New York, United States

Location

UNC Division of Cardiology

Chapel Hill, North Carolina, United States

Location

Duke University Heart Failure Research

Durham, North Carolina, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Location

Penn State College of Medicine

Hershey, Pennsylvania, United States

Location

Hahnemann University Hospital

Philadelphia, Pennsylvania, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, United States

Location

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Location

Medical University of South Carolina

Charleston, South Carolina, United States

Location

Texas Cardiovascular Consultants

Austin, Texas, United States

Location

University of Texas Medical Branch, Div of Cardio Thoracic

Galveston, Texas, United States

Location

Methodist Hospital/DeBakey Heart Failure Research Center

Houston, Texas, 77030, United States

Location

Intermountain Medical Center

Murray, Utah, United States

Location

University of Wisconsin - Madison Medical School

Madison, Wisconsin, 53792, United States

Location

St. Luke's Medical Center Cardiac Services

Milwakee, Wisconsin, United States

Location

Sanatorio Parque

Rosario, Santa Fe Province, Argentina

Location

Fundacion Favalaro

Buenos Aires, Argentina

Location

St Vincents Hospital

Darlinghurst, New South Wales, Australia

Location

Prince Charles Hospital

Chermside, Queensland, Australia

Location

Royal Perth Hospital

Perth, Western Australia, Australia

Location

Universitaet Wien

Vienna, Austria

Location

Cliniques Universitaires Saint-Luc

Brussels, Belgium

Location

University of Alberta Hospital

Edmonton, Alberta, Canada

Location

St Paul's Hospital

Vancouver, British Columbia, Canada

Location

New Halifax Infirmary

Halifax, Nova Scotia, Canada

Location

Toronto General Hospital

Toronto, Ontario, Canada

Location

Institut Univ. de cardiologie et pneumologie de Quebec

Sainte-Foy, Quebec, Canada

Location

Hopital Cardiologique de Lyon

Lyon, France

Location

Hopital Georges Pompidou

Paris, France

Location

Hopital Pitie Salpetriere

Paris, France

Location

CHU de Strasbourg Hopital Civil Medicale B

Strasbourg, France

Location

CHU Hopital de Brabois

Vandœuvre-lès-Nancy, France

Location

Herz- u. Diabeteszentrum NRW/Ruhr-Univ. Bochum

Bad Oeynhausen, Germany

Location

Deutsches Herzzentrum Berlin

Berlin, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, Germany

Location

Kliniken der Med. Hochschule

Hanover, Germany

Location

Universitaetsklinikum Kiel

Kiel, Germany

Location

Universitaetsklinik Regensburg

Regensburg, Germany

Location

Az. Osp. di Bologna Policl. S. Orsola-Malpighi Univ. degli Studi

Bologna, Italy

Location

Azienda Ospedaliera G. Brotzu

Cagliari, Italy

Location

A.O.-Universita di Padova-Universita degli Studi

Padua, Italy

Location

Fodazione IRCCS Policlinico S. Matteo

Pavia, Italy

Location

Azienda Ospedaliera S. Camillo-Forlanini

Roma, Italy

Location

Az. Ospedaliero-Universitaria S. Giovanni Battista di Torino

Torino, Italy

Location

Auckland Hospital

Auckland, New Zealand

Location

Rikshospitalet, Hjertemedisinskavdeling

Oslo, Norway

Location

Cardiovascular Center of Puerto Rico and the Caribbean

San Juan, Puerto Rico

Location

Hospital Universitario Reina Sofia

Córdoba, Spain

Location

Hospital Puerta de Hierro Majadahonda

Madrid, Spain

Location

National Taiwan University Hospital

Taipei, Taiwan

Location

Queen Elizabeth Hospital

Birmingham, United Kingdom

Location

Papworth Hospital

Cambridge, United Kingdom

Location

Wythenshawe Hospital

Manchester, United Kingdom

Location

MeSH Terms

Conditions

Heart Diseases

Interventions

EverolimusMycophenolic AcidCyclosporineAdrenal Cortex Hormones

Condition Hierarchy (Ancestors)

Cardiovascular Diseases

Intervention Hierarchy (Ancestors)

SirolimusMacrolidesLactonesOrganic ChemicalsCaproatesAcids, AcyclicCarboxylic AcidsFatty AcidsLipidsCyclosporinsPeptides, CyclicMacrocyclic CompoundsPolycyclic CompoundsPeptidesAmino Acids, Peptides, and ProteinsHormonesHormones, Hormone Substitutes, and Hormone Antagonists

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis

    Novartis

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 6, 2006

First Posted

March 8, 2006

Study Start

January 1, 2006

Primary Completion

July 1, 2011

Study Completion

July 1, 2011

Last Updated

August 16, 2012

Results First Posted

August 16, 2012

Record last verified: 2012-07

Locations