NCT00030966

Brief Summary

The purpose of this study is to determine if natalizumab in combination with AVONEX is safe and effective in delaying progression of individuals diagnosed with relapsing remitting Multiple Sclerosis (MS).

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,200

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jan 2002

Typical duration for phase_3

Geographic Reach
7 countries

88 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2002

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

February 15, 2002

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 18, 2002

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2005

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2005

Completed
Last Updated

June 18, 2009

Status Verified

June 1, 2009

Enrollment Period

3.2 years

First QC Date

February 15, 2002

Last Update Submit

June 17, 2009

Conditions

Keywords

Multiple SclerosisMS

Outcome Measures

Primary Outcomes (1)

  • Primary objectives of this study are to determine if natalizumab is effective in reducing the rate of clinical relapse at 1 year and in slowing the progression of disability at 2 years as measured by EDSS.

    1 year and 2 years

Secondary Outcomes (1)

  • If this combination reduces MRI lesions and the overall rate of clinical relapses

    1 year and 2 years

Study Arms (2)

Group 1

EXPERIMENTAL

Adding natalizumab monthly infusion to Avonex weekly injection for up to 116 weeks.

Drug: Natalizumab

Group 2

PLACEBO COMPARATOR

Adding placebo monthly infusion to Avonex weekly injection for up to 116 weeks.

Drug: Placebo

Interventions

Natalizumab, 300 mg, monthly IV infusion for up to 116 weeks.

Also known as: Tysabri
Group 1

Placebo monthly infusion for up to 116 weeks.

Group 2

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Diagnosis of MS as defined by McDonald et al, criteria, # 1- 4
  • Between the ages of 18 and 55, inclusive
  • Baseline EDSS score between 0.0 and 5.0, inclusive
  • Have been treated with Avonex for at least the 12 months prior to randomization
  • Have experienced at least one relapse (while on Avonex) within the 12 months prior to randomization.
  • Cranial MRI scan demonstrating lesions consistent with MS.
  • Have given written informed consent to participate in the study.

You may not qualify if:

  • Primary progressive, secondary progressive, or progressive relapsing MS.
  • MS relapse has occurred within 50 days of randomization
  • A clinically significant infectious illness within 30 days prior to randomization
  • History of, or abnormal lab result, indicative of significant disease, that in the opinion of the investigator, would preclude the administration of a recombinant humanized antibody immunomodulating agent or Avonex for 116 weeks.
  • History of severe allergic or anaphylactic reactions or known drug hypersensitivity.
  • Unable to perform the Timed 25-Foot Walk, 9HPT and PASAT 3
  • Abnormal blood tests at Screening Visit

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

University of Alabama-Birmingham, Department of Neurology

Birmingham, Alabama, 35233, United States

Location

Phoenix Neurological Associates, Ltd.

Phoenix, Arizona, 85008, United States

Location

University of Arkansas For Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

University of California - Irvine

Irvine, California, 92697, United States

Location

USC MS Comprehensive Care Center

Los Angeles, California, 90033, United States

Location

Kaiser-Permanente Medical Center

Redwood City, California, 94063, United States

Location

MS Center at UCSF

San Francisco, California, 94117, United States

Location

Healthsouth Rehabilitation Hospital

Colorado Springs, Colorado, 80910, United States

Location

University of Colorado MS Center

Denver, Colorado, 80262, United States

Location

Griffin Hospital

Derby, Connecticut, 06418, United States

Location

Georgetown Univesity Hospital, Research Pharmacy

Washington D.C., District of Columbia, 20007, United States

Location

George Washington University MS Center

Washington D.C., District of Columbia, 20037, United States

Location

North Ridge NeuroScience Center

Fort Lauderdale, Florida, 33334, United States

Location

Maitland Neurology

Maitland, Florida, 32751, United States

Location

University of Miami, Department of Neurology

Miami, Florida, 33136, United States

Location

The Multiple Sclerosis Center of Atlanta

Atlanta, Georgia, 30327, United States

Location

Marietta Neurological Associates

Marietta, Georgia, 30060, United States

Location

Northwestern University, Department of Neurology

Chicago, Illinois, 60611, United States

Location

Rush-Presbyterian St. Luke's Medical Center

Chicago, Illinois, 60612, United States

Location

Alexian Brothers Center for Clinical Research

Elk Grove Village, Illinois, 60007, United States

Location

Loyola Medical Center

Maywood, Illinois, 60153, United States

Location

Consultants in Neurology Northbrook

Northbrook, Illinois, 60062, United States

Location

Springfield Clinic Neuroscience Institute

Springfield, Illinois, 62702, United States

Location

Indiana University Medical Center

Indianapolis, Indiana, 46202, United States

Location

Mercy Hospital Outpatient Pharmacy

Des Moines, Iowa, 50314, United States

Location

LSU Neurolgoy Clinic in New Orleans

New Orleans, Louisiana, 70112, United States

Location

Maine Neurology

Scarborough, Maine, 04074-8926, United States

Location

University of Maryland Hospital, Department of Neurology

Baltimore, Maryland, 21201, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

University of Massachusetts Memorial Medical Center

Worcester, Massachusetts, 01655-0138, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202-2608, United States

Location

Michigan State University MS Clinic

East Lansing, Michigan, 48824, United States

Location

Michigan Institute for Neurological Disorders

Farmington Hills, Michigan, 48334, United States

Location

Noran Neurological Clinic

Minneapolis, Minnesota, 55404, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216-4505, United States

Location

St. John's Mercy Medical Center

St Louis, Missouri, 63141, United States

Location

Bernard W. Gimbel MS Center

Teaneck, New Jersey, 07666, United States

Location

Upstate Clinical Research, LLC

Albany, New York, 12205, United States

Location

Albany Medical Center

Albany, New York, 12208, United States

Location

Maimonides Medical Center, Division of Neurology

Brooklyn, New York, 11219, United States

Location

Buffalo General Hospital, Department of Neurology

Buffalo, New York, 14203, United States

Location

MS Care Center

New York, New York, 10003, United States

Location

St. Luke's Roosevelt Hospital, MS Research & Treatment Center

New York, New York, 10019, United States

Location

New York Hospital - Cornell Medical Center

New York, New York, 10021, United States

Location

New York State Psychiatric Institution

New York, New York, 10032, United States

Location

Strong Health Pharmacy Services

Rochester, New York, 14642, United States

Location

Staten Island University Hospital

Staten Island, New York, 10305, United States

Location

University Hospital at Stony Brook

Stony Brook, New York, 11794, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

MS Center at Carolinas Medical Center

Charlotte, North Carolina, 28232-2861, United States

Location

Raleigh Neurology Associates

Raleigh, North Carolina, 27607, United States

Location

Wake Forest University School of Medicine, Department of Neurology

Winston-Salem, North Carolina, 27157, United States

Location

Riverhills Neurology

Cincinnati, Ohio, 45219, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Providence Saint Vincent Medical Center

Portland, Oregon, 97225, United States

Location

Geisinger Medical Center

Danville, Pennsylvania, 17822, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Greenstein Neurology Associates & MS Institute

Philadelphia, Pennsylvania, 19146, United States

Location

Allegheny Singer Research Institute

Pittsburgh, Pennsylvania, 15212, United States

Location

University of Pittsburgh, Department of Neurology

Pittsburgh, Pennsylvania, 15213, United States

Location

University of Tennessee - Memphis

Memphis, Tennessee, 38163, United States

Location

Vanderbilt Medical Center

Nashville, Tennessee, 37215, United States

Location

Option Care Infusion

Dallas, Texas, 75226, United States

Location

UTSW Medical School

Dallas, Texas, 75235-9036, United States

Location

Baylor Methodist International MS Center

Houston, Texas, 77030, United States

Location

Central Texas Neurology

Round Rock, Texas, 78681, United States

Location

Fletcher Allen Health Care

Burlington, Vermont, 05401, United States

Location

University of Virginia Health Sciences

Charlottesville, Virginia, 22908, United States

Location

Neurological Associates, Inc.

Richmond, Virginia, 23226, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98111, United States

Location

MS Research Center

Seattle, Washington, 98195, United States

Location

St. Francis Hospital, Center for Neurological Disorders

Milwaukee, Wisconsin, 53215, United States

Location

Universitatsklinik fur Neurologie

Graz, 8036, Austria

Location

Universitatsklinik fur Neurologie

Innsbruck, 6020, Austria

Location

Hopital Universitaire U.L.B. Erasme

Brussels, 1780, Belgium

Location

Elisabeth Ziekenhuis

Sijsele, 8340, Belgium

Location

Hopital Pellegrin Tripode, Neurologie

Bordeaux, 33076, France

Location

Hopital neurologique Pierre Werth

Lyon, 69394, France

Location

Judisches Krankenhaus

Berlin, 13347, Germany

Location

Universitaetsklinikum Giessen, Oberarzt Neurologie

Giessen, 35390, Germany

Location

Medizinische Hochschule Hannover, Neurologische Klinik

Hanover, 30625, Germany

Location

Neurologische Abteilung

Henningsdorf, 16761, Germany

Location

Städtische Kliniken Osnabrück

Osnabrück, 49076, Germany

Location

Asklepios Klinik Schildautal

Seesen/Harz, 38723, Germany

Location

Fachbereich Neurologie und Klinische Neurophysiologie

Wiesbaden, 65191, Germany

Location

Hadassah Hebrew Uni Hospital, Department of Neurology

Jerusalem, Israel

Location

Sheba Medical Center, MS Center

Tel Litwinsky, 52621, Israel

Location

Universita di Genova, Clinica Neurologica

Genova, 16132, Italy

Location

Related Publications (2)

  • Rudick RA, Stuart WH, Calabresi PA, Confavreux C, Galetta SL, Radue EW, Lublin FD, Weinstock-Guttman B, Wynn DR, Lynn F, Panzara MA, Sandrock AW; SENTINEL Investigators. Natalizumab plus interferon beta-1a for relapsing multiple sclerosis. N Engl J Med. 2006 Mar 2;354(9):911-23. doi: 10.1056/NEJMoa044396.

  • Strijbis EM, Coerver E, Mostert J, van Kempen ZLE, Killestein J, Comtois J, Repovic P, Bowen JD, Cutter G, Koch M. Association of age and inflammatory disease activity in the pivotal natalizumab clinical trials in relapsing-remitting multiple sclerosis. J Neurol Neurosurg Psychiatry. 2023 Oct;94(10):792-799. doi: 10.1136/jnnp-2022-330887. Epub 2023 May 12.

Related Links

MeSH Terms

Conditions

Multiple Sclerosis, Relapsing-RemittingMultiple Sclerosis

Interventions

Natalizumab

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Michael Panzara, MD, MPH

    Biogen

    STUDY DIRECTOR
  • Richard A Rudick, MD

    The Cleveland Clinic

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

February 15, 2002

First Posted

February 18, 2002

Study Start

January 1, 2002

Primary Completion

April 1, 2005

Study Completion

December 1, 2005

Last Updated

June 18, 2009

Record last verified: 2009-06

Locations