NCT00009906

Brief Summary

Randomized phase III trial to compare the effectiveness of two different doses of STI571 in treating patients who have metastatic or unresectable gastrointestinal stromal tumor. STI571 may interfere with the growth of tumor cells and may be an effective treatment for cancer. It is not yet known which dose of STI571 is more effective in treating gastrointestinal stromal tumors.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
748

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Dec 2000

Longer than P75 for phase_3

Geographic Reach
3 countries

144 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2000

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

February 2, 2001

Completed
3 years until next milestone

First Posted

Study publicly available on registry

February 3, 2004

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2007

Completed
7.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2014

Completed
Last Updated

December 23, 2014

Status Verified

June 1, 2014

Enrollment Period

6.4 years

First QC Date

February 2, 2001

Last Update Submit

December 19, 2014

Conditions

Outcome Measures

Primary Outcomes (3)

  • Overall survival (OS)

    Up to 3 years

  • Progression-free survival

    From date of registration to date of first observation of progressive disease or death due to any cause, assessed up to 3 years

  • Toxicity defined as any grade 3 or greater organ toxicity, or any grade 4 or greater hematological toxicity as assessed by CTCAE version 2.0

    Up to 3 year after completion of treatment

Study Arms (2)

Arm I (imatinib mesylate)

EXPERIMENTAL

Patients receive oral imatinib mesylate once daily.

Drug: Imatinib Mesylate

Arm II (imatinib mesylate)

EXPERIMENTAL

Patients receive oral imatinib mesylate twice daily.

Drug: Imatinib Mesylate

Interventions

Given orally

Arm I (imatinib mesylate)Arm II (imatinib mesylate)

Eligibility Criteria

Age15 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patient must have a biopsy proven diagnosis of gastrointestinal stromal tumor (GIST) which is distantly metastatic or unresectable; tumors must meet BOTH of the following criteria:
  • The primary must be of visceral or intra-abdominal origin
  • All patients must have immunohistochemical documentation of KIT (CD117) expression by tumor documented by DAKO antibody staining for suggested methodology) Material must be submitted to the CALGB Pathology Coordinating Center for pathology review; it is strongly recommended that snap-frozen tissue biopsy and sera be stored for future submission whenever possible
  • Patient must have measurable or non-measurable disease by conventional scan imaging (CT or MRI) or physical examination; tests used to assess disease must have been performed within 28 days prior to registration; if a target lesion has been previously embolized or irradiated, there must be objective evidence of progression to be considered for response assessment
  • Patient must have an identified team (including a medical oncologist and a surgeon) to provide care
  • Patient must not have known brain metastasis
  • Patient must have a Zubrod performance status of 0 - 3
  • Patient must have resolution of transient toxicities from any prior therapy to =\< grade 1 (NCI-CTC version 2.0)
  • The patient must not have received chemotherapy, biologic therapy or any other investigational drug for any reason within 28 days prior to registration; patients must not have had a major surgery within 14 days prior to registration
  • If day 14 or 28 falls on a weekend or holiday, the limit may be extended to the next working day
  • In calculating days of tests and measurements, the day a test or measurement is done is considered day 0; therefore, if a test is done on a Monday, the Monday two weeks later would be considered day 14; this allows for efficient patient scheduling without exceeding the guidelines
  • No other prior malignancy is allowed except for the following: adequately treated basal cell or squamous cell skin cancer, in situ cervical cancer, adequately treated stage I or II cancer from which the patient is currently in complete remission, or any other cancer from which the patient has been disease-free for 5 years
  • All patients must be informed of the investigational nature of this study and must sign and give written informed consent in accordance with institutional and federal guidelines
  • At the time of patient registration, the treating institution's name and ID number must be provided to the Data Operations Center in Seattle in order to ensure that the current (within 365 days) date of institutional review board approval for this study has been entered into the data base
  • Patients on lower dose arm (Arm 1) will be allowed to increase the daily dose of STI-571 in the case of disease progression; if there is questionable disease progression, the treating investigator should contact the primary Study Coordinator, Dr. George Demetri at 617/632-3985 to review progression information and discuss treatment options

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (144)

Western Regional CCOP

Phoenix, Arizona, 85006, United States

Location

University of Arizona Health Sciences Center

Tucson, Arizona, 85724, United States

Location

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

Highlands Oncology Group-Rogers

Rogers, Arkansas, 72758, United States

Location

City of Hope Comprehensive Cancer Center

Duarte, California, 91010, United States

Location

Long Beach Community Hospital

Long Beach, California, 90804, United States

Location

University of Southern California/Norris Cancer Center

Los Angeles, California, 90033, United States

Location

University of California at Los Angeles Health System

Los Angeles, California, 90095, United States

Location

Sutter Cancer Research Consortium

Novato, California, 94945, United States

Location

University of California Davis Comprehensive Cancer Center

Sacramento, California, 95817, United States

Location

Kaiser Permanente - Sacramento

Sacramento, California, 95825, United States

Location

University of California San Diego

San Diego, California, 92103, United States

Location

UCSF Medical Center-Mount Zion

San Francisco, California, 94115, United States

Location

Santa Rosa Memorial Hospital

Sana Rosa, California, 95405, United States

Location

Stanford University Hospitals and Clinics

Stanford, California, 94305, United States

Location

Presbyterian - Saint Lukes Medical Center - Health One

Denver, Colorado, 80218, United States

Location

Rose Medical Center

Denver, Colorado, 80220, United States

Location

Swedish Medical Center

Englewood, Colorado, 80113, United States

Location

Poudre Valley Hospital

Fort Collins, Colorado, 80524, United States

Location

Saint Mary Corwin Medical Center

Pueblo, Colorado, 81004, United States

Location

Middlesex Hospital

Middletown, Connecticut, 06457, United States

Location

MedStar Oncology Network

Washington D.C., District of Columbia, 20010, United States

Location

Mayo Clinic in Florida

Jacksonville, Florida, 32224-9980, United States

Location

Hematology Oncology Associates

Lake Worth, Florida, 33461, United States

Location

Florida Hospital Orlando

Orlando, Florida, 32803, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Phoebe Putney Memorial Hospital

Albany, Georgia, 31701, United States

Location

Emory University/Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Atlanta Regional CCOP

Atlanta, Georgia, 30342, United States

Location

Medical Center of Central Georgia

Macon, Georgia, 31208, United States

Location

University of Hawaii Cancer Center

Honolulu, Hawaii, 96813, United States

Location

Hematology and Oncology Associates

Chicago, Illinois, 60611, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Jesse Brown Veterans Affairs Medical Center

Chicago, Illinois, 60612, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

University of Illinois

Chicago, Illinois, 60612, United States

Location

University of Chicago Comprehensive Cancer Center

Chicago, Illinois, 60637, United States

Location

Central Illinois CCOP

Decatur, Illinois, 62526, United States

Location

Alexian Brothers Medical and Cancer Center

Elk Grove Village, Illinois, 60007, United States

Location

NorthShore University HealthSystem-Evanston Hospital

Evanston, Illinois, 60201, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Mid-Illinois Hematology Oncology Associates

Normal, Illinois, 61761, United States

Location

Advocate Lutheran General Hospital.

Park Ridge, Illinois, 60068, United States

Location

Carle Cancer Center

Urbana, Illinois, 61801, United States

Location

Indiana University/Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

IU Health Methodist Hospital

Indianapolis, Indiana, 46202, United States

Location

McFarland Clinic PC-William R Bliss Cancer Center

Ames, Iowa, 50010, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Kansas City CCOP

Prairie Village, Kansas, 66208, United States

Location

Stormont-Vail Regional Health Center

Topeka, Kansas, 66604, United States

Location

Our Lady Bellefonte Hospital

Ashland, Kentucky, 41101, United States

Location

Louisiana State University Health Science Center

New Orleans, Louisiana, 70112, United States

Location

Sinai Hospital of Baltimore

Baltimore, Maryland, 21215, United States

Location

Johns Hopkins University/Sidney Kimmel Comprehensive Cancer Center

Baltimore, Maryland, 21287, United States

Location

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, 02114, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02115, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Michigan Cancer Research Consortium Community Clinical Oncology Program

Ann Arbor, Michigan, 48106, United States

Location

University of Michigan University Hospital

Ann Arbor, Michigan, 48109, United States

Location

Oakwood Hospital and Medical Center

Dearborn, Michigan, 48124, United States

Location

Wayne State University/Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Grand Rapids Clinical Oncology Program

Grand Rapids, Michigan, 49503, United States

Location

West Michigan Cancer Center

Kalamazoo, Michigan, 49007, United States

Location

Marquette General Hospital

Marquette, Michigan, 49855, United States

Location

Unity Hospital

Fridley, Minnesota, 55432, United States

Location

University of Minnesota Medical Center-Fairview

Minneapolis, Minnesota, 55455, United States

Location

North Memorial Medical Health Center

Robbinsdale, Minnesota, 55422, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Park Nicollet Clinic - Saint Louis Park

Saint Louis Park, Minnesota, 55416, United States

Location

Regions Hospital

Saint Paul, Minnesota, 55101, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Saint Joseph's Health Center

Saint Charles, Missouri, 63301, United States

Location

Ozark Health Ventures LLC-Cancer Research for The Ozarks Springfield

Springfield, Missouri, 65804, United States

Location

Saint Louis Cancer and Breast Institute-South City

St Louis, Missouri, 63109, United States

Location

Barnes-Jewish Hospital

St Louis, Missouri, 63110, United States

Location

Missouri Baptist Medical Center

St Louis, Missouri, 63131, United States

Location

Alegent Health Immanuel Medical Center

Omaha, Nebraska, 68122, United States

Location

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Hackensack University Medical CCOP

Hackensack, New Jersey, 07601, United States

Location

Saint Barnabas Medical Center

Livingston, New Jersey, 07039, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08903, United States

Location

University of New Mexico

Albuquerque, New Mexico, 87106, United States

Location

Roswell Park Cancer Institute

Buffalo, New York, 14263, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Beth Israel Medical Center

New York, New York, 10003, United States

Location

New York University Langone Medical Center

New York, New York, 10016, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10065, United States

Location

Albert Einstein College of Medicine

The Bronx, New York, 10461, United States

Location

Montefiore Medical Center - Moses Campus

The Bronx, New York, 10467-2490, United States

Location

University of North Carolina

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Southeast Cancer Control Consortium CCOP

Winston-Salem, North Carolina, 27104, United States

Location

Wake Forest University Health Sciences

Winston-Salem, North Carolina, 27157, United States

Location

Roger Maris Cancer Center

Fargo, North Dakota, 58122, United States

Location

Case Western Reserve University

Cleveland, Ohio, 44106, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210, United States

Location

Columbus CCOP

Columbus, Ohio, 43215, United States

Location

Dayton CCOP

Dayton, Ohio, 45420, United States

Location

Saint Rita's Medical Center

Lima, Ohio, 45801, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Sky Lakes Medical Center - Cancer Treatment Center

Klamath Falls, Oregon, 97601, United States

Location

Western Oncology Research Consortium

Portland, Oregon, 97213, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Salem Hospital

Salem, Oregon, 97301, United States

Location

Geisinger Medical Center

Danville, Pennsylvania, 17822, United States

Location

Mercy Fitzgerald Hospital

Darby, Pennsylvania, 19023-1291, United States

Location

Delaware County Memorial Hospital

Drexel Hill, Pennsylvania, 19026, United States

Location

University of Pennsylvania/Abramson Cancer Center

Philadelphia, Pennsylvania, 19104, United States

Location

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, 19107, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

Aria Health-Torresdale Campus

Philadelphia, Pennsylvania, 19114, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, 19141, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Upstate Carolina CCOP

Spartanburg, South Carolina, 29303, United States

Location

Baptist Memorial Hospital and Cancer Center-Memphis

Memphis, Tennessee, 38120, United States

Location

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

M D Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Huntsman Cancer Institute/University of Utah

Salt Lake City, Utah, 84112, United States

Location

Central Vermont Medical Center

Barre, Vermont, 05641, United States

Location

Central Vermont Medical Center/National Life Cancer Treatment

Berlin Corners, Vermont, 05602, United States

Location

Rutland Regional Medical Center

Rutland, Vermont, 05701, United States

Location

Virginia Oncology Associates-Hampton

Hampton, Virginia, 23666, United States

Location

Virginia Mason CCOP

Seattle, Washington, 98101, United States

Location

Group Health

Seattle, Washington, 98109, United States

Location

Cancer Care Northwest - Spokane South

Spokane, Washington, 99202, United States

Location

Northwest CCOP

Tacoma, Washington, 98405, United States

Location

Saint Vincent Hospital

Green Bay, Wisconsin, 54301, United States

Location

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, 53792, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

BCCA-Vancouver Cancer Centre

Vancouver, British Columbia, V5Z 4E6, Canada

Location

Hamilton and District Urology Association McMaster Institute

Hamilton, Ontario, L8N 4A6, Canada

Location

Juravinski Cancer Centre at Hamilton Health Sciences

Hamilton, Ontario, L8V 5C2, Canada

Location

London Regional Cancer Program

London, Ontario, N6A 4L6, Canada

Location

Ottawa Health Research Institute-General Division

Ottawa, Ontario, K1H 1C4, Canada

Location

Mount Sinai Hospital

Toronto, Ontario, M5G 1X5, Canada

Location

CHUM - Hopital Notre-Dame

Montreal, Quebec, H2L 4M1, Canada

Location

McGill University Department of Oncology

Montreal, Quebec, H2W 1S6, Canada

Location

San Juan Veterans Affairs Medical Center

San Juan, 00921-3201, Puerto Rico

Location

San Juan City Hospital

San Juan, 00936, Puerto Rico

Location

Related Publications (1)

  • Heinrich MC, Rankin C, Blanke CD, Demetri GD, Borden EC, Ryan CW, von Mehren M, Blackstein ME, Priebat DA, Tap WD, Maki RG, Corless CL, Fletcher JA, Owzar K, Crowley JJ, Benjamin RS, Baker LH. Correlation of Long-term Results of Imatinib in Advanced Gastrointestinal Stromal Tumors With Next-Generation Sequencing Results: Analysis of Phase 3 SWOG Intergroup Trial S0033. JAMA Oncol. 2017 Jul 1;3(7):944-952. doi: 10.1001/jamaoncol.2016.6728.

MeSH Terms

Conditions

Gastrointestinal Stromal Tumors

Interventions

Imatinib Mesylate

Condition Hierarchy (Ancestors)

Neoplasms, Connective TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal Diseases

Intervention Hierarchy (Ancestors)

BenzamidesAmidesOrganic ChemicalsBenzoatesAcids, CarbocyclicCarboxylic AcidsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPiperazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidines

Study Officials

  • George Demetri

    SWOG Cancer Research Network

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 2, 2001

First Posted

February 3, 2004

Study Start

December 1, 2000

Primary Completion

May 1, 2007

Study Completion

November 1, 2014

Last Updated

December 23, 2014

Record last verified: 2014-06

Locations