Thalassemia

A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)

A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia

A Long-term Follow-up Study in Participants Who Received CTX001

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

CINC424A2X01B Rollover Protocol

Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders

A Blood Stem Cell Transplant for Sickle Cell Disease

Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)

Atrial Fibrillation in Beta-Thalassemia

Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling

Multicenter Observational Study on Myocardial Iron Overload in 3 Multitransfused Populations

Evaluation of the Quality of Life in Patients With Chronic Iron Overload Due to Hemoglobinopathies in Greece.

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

A Study on the Effect of Etavopivat on Heart Rhythm in Healthy Participants

A Research Study Looking at a Single Dose of Etavopivat in Healthy Chinese Participants

A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia

A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease

Effect of L-Glutamine on Pulmonary Artery Pressure in Patients With Non-Transfusion-Dependent Thalassemia

Impact of Virtual Reality on Pain and Anxiety During Intravenous Cannulation Procedures Among Thalassemia Patients in UAE.