NCT06948955

Brief Summary

The purpose of this expanded access program (EAP) is to provide investigational bezuclastinib so that it can be coadministered with sunitinib to patients with a diagnosis of gastrointestinal stromal tumors (GIST) with no comparable or satisfactory alternative therapy options. The combination of bezuclastinib and sunitinib provides broad inhibition of all primary and secondary KIT mutations that commonly occur in GIST.

Trial Health

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Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Geographic Reach
1 country

17 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 31, 2025

Completed
29 days until next milestone

First Posted

Study publicly available on registry

April 29, 2025

Completed
Last Updated

April 2, 2026

Status Verified

April 1, 2026

First QC Date

March 31, 2025

Last Update Submit

April 1, 2026

Conditions

Keywords

Solid TumorsSunitinibBezuclastinibGastrointestinal Stromal Tumors

Interventions

Drug: Bezuclastinib

Drug: Sunitinib (locally sourced)

Eligibility Criteria

Age18 Years+
Sexall
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Able to provide written informed consent and commit to recommended EAP assessments.
  • ≥18 years of age.
  • Able to swallow tablets.
  • Histologically confirmed locally advanced, metastatic, and/or unresectable GIST.
  • Intolerant to imatinib or received prior imatinib therapy for treatment of advanced, metastatic, and/or unresectable GIST that resulted in disease progression.
  • Meet clinically acceptable local laboratory results.

You may not qualify if:

  • Patients who are eligible for and capable of participating in and/or enrolled in an on-going bezuclastinib clinical trial.
  • Prior or known intolerance to sunitinib.
  • Patients who have previously participated in a bezuclastinib clinical trial.
  • Patients with persistent \> Grade 2 toxicities from prior therapy.
  • Known PDGFR driving mutations or known SDH deficiency.
  • Pregnant or currently breastfeeding.
  • Other protocol-defined criteria apply.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

Mayo Clinic Hospital

Phoenix, Arizona, 85054, United States

AVAILABLE

USC/Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

AVAILABLE

UCLA Department of Medicine- Hematology/Oncology

Los Angeles, California, 90095, United States

AVAILABLE

University of Colorado

Aurora, Colorado, 80045, United States

AVAILABLE

Smillow Cancer Hospital - Yale New Haven Health

New Haven, Connecticut, 06510, United States

AVAILABLE

Mayo Clinic

Jacksonville, Florida, 32224, United States

AVAILABLE

Orlando Health

Orlando, Florida, 32806, United States

AVAILABLE

The University of Chicago Medical Center

Chicago, Illinois, 60637, United States

AVAILABLE

Dana Farber Cancer Institute (DFCI)

Boston, Massachusetts, 02215, United States

AVAILABLE

Mayo Clinic

Rochester, Minnesota, 55905, United States

AVAILABLE

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

AVAILABLE

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

AVAILABLE

The James Cancer Hospital and Solove Research Institute at The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210, United States

AVAILABLE

Taylor Cancer Research Center

Maumee, Ohio, 43537, United States

AVAILABLE

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

AVAILABLE

MD Anderson Cancer Center

Houston, Texas, 77030, United States

AVAILABLE

Huntsman Cancer Institute, University of Utah

Salt Lake City, Utah, 84112, United States

AVAILABLE

MeSH Terms

Conditions

Gastrointestinal NeoplasmsGastrointestinal Stromal Tumors

Interventions

Sunitinib

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesNeoplasms, Connective TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic Type

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Study Officials

  • Rachael Easton, MD, PhD

    Cogent Biosciences, Inc.

    STUDY DIRECTOR

Central Study Contacts

Alexandra Malinowski, PharmD

CONTACT

Study Design

Study Type
expanded access
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 31, 2025

First Posted

April 29, 2025

Last Updated

April 2, 2026

Record last verified: 2026-04

Locations