NCT06931405

Brief Summary

This is a 2-part, proof-of-concept study to be conducted globally, designed to evaluate the safety, tolerability, clinical activity, pharmacokinetics, and pharmacodynamics of BLU-808, a wild type KIT inhibitor, in participants with CIndU (Part A) or CSU (Part B).

Trial Health

83
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
105

participants targeted

Target at P50-P75 for phase_2

Timeline
8mo left

Started May 2025

Geographic Reach
6 countries

47 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress59%
May 2025Dec 2026

First Submitted

Initial submission to the registry

April 9, 2025

Completed
8 days until next milestone

First Posted

Study publicly available on registry

April 17, 2025

Completed
1 month until next milestone

Study Start

First participant enrolled

May 28, 2025

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2026

Last Updated

February 17, 2026

Status Verified

February 1, 2026

Enrollment Period

1.6 years

First QC Date

April 9, 2025

Last Update Submit

February 16, 2026

Conditions

Keywords

Chronic Inducible UrticariaChronic Spontaneous UrticariaBLU-808CIndUCSUChronic UrticariaCUCold UrticariaColdUSymptomatic DermographismSD

Outcome Measures

Primary Outcomes (1)

  • Part A and Part B: Number of Participants with Treatment-emergent Adverse Events (TEAEs)

    Day 1 through Week 16

Secondary Outcomes (12)

  • Part A: Mean Change From Baseline in Critical Temperature Threshold (CTT) at Week 12

    Baseline, Week 12

  • Part A: Mean Change From Baseline in Total Fric Score (TFS) at Week 12

    Baseline, Week 12

  • Part A and Part B: Complete Response Rate

    Week 12

  • Part A and Part B: Absolute Change From Baseline in Serum Tryptase Concentration at Week 12

    Baseline, Week 12

  • Part A and Part B: Percent Change From Baseline in Serum Tryptase Concentration at Week 12

    Baseline, Week 12

  • +7 more secondary outcomes

Study Arms (3)

Arm A1 (Part A): BLU-808

EXPERIMENTAL

BLU-808 will be administered orally.

Drug: BLU-808

Arm A3 (Part A): BLU-808

EXPERIMENTAL

BLU-808 will be administered orally.

Drug: BLU-808

Arm B (Part B): BLU-808/Placebo

EXPERIMENTAL

BLU-808 or matching placebo will be administered orally.

Drug: BLU-808Drug: Placebo

Interventions

Oral administration

Arm A1 (Part A): BLU-808Arm A3 (Part A): BLU-808Arm B (Part B): BLU-808/Placebo

Oral administration

Arm B (Part B): BLU-808/Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Part A: Confirmed diagnosis of CIndU for ≥3 months prior to Day 1 that is inadequately controlled with second generation H1-antihistamines.
  • Part B: Confirmed diagnosis of CSU for ≥3 months prior to Day 1 that is inadequately controlled with second generation H1-antihistamines.

You may not qualify if:

  • Part A: Any active urticaria that may interfere with study assessments.
  • Part B: Participant has a clearly defined predominant cause of chronic urticaria or sole trigger such as symptomatic dermographism and cold-induced urticaria.
  • Part A and Part B: Any other skin disease associated with chronic itching or angioedema that might influence the study evaluations and results, skin diseases associated with only wheals and no itch, or autoinflammatory diseases with urticarial lesions.
  • Part A and Part B: Significant medical, psychiatric, or surgical conditions, or physical findings that may affect participant safety, study drug metabolism, study participation, or assessment of study results.
  • Part A and Part B: Abnormal laboratory values that may pose risks or interfere with study participation.
  • Part A and Part B: Pregnancy or plans for pregnancy; breastfeeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (47)

Allervie Clinical Research

Birmingham, Alabama, 35209, United States

RECRUITING

Acuro Research, Inc.

Little Rock, Arkansas, 72205, United States

RECRUITING

Modena Allergy & Asthma Clinical Research - La Jolla

La Jolla, California, 92037, United States

RECRUITING

Allergy & Asthma Associates of Southern California

Laguna Niguel, California, 92677, United States

RECRUITING

Allergy & Asthma Medical Group and Research Center

San Diego, California, 92123, United States

RECRUITING

Allergy Affiliates Inc.

Bradenton, Florida, 34208, United States

RECRUITING

University of South Florida

Tampa, Florida, 33613, United States

RECRUITING

Treasure Valley Medical Research

Boise, Idaho, 83706, United States

RECRUITING

Endeavor Health

Northbrook, Illinois, 60062, United States

RECRUITING

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, 46250, United States

RECRUITING

Southern Indiana Clinical Trials

New Albany, Indiana, 47150, United States

RECRUITING

The Indiana Clinical Trials Center

Plainfield, Indiana, 46168, United States

RECRUITING

Equity Medical - Bowling Green

Bowling Green, Kentucky, 42104, United States

RECRUITING

Johns Hopkins University

Baltimore, Maryland, 21224, United States

RECRUITING

Institute For Asthma & Allergy

Wheaton, Maryland, 20902, United States

RECRUITING

Chesapeake Clinical Research

White Marsh, Maryland, 21236, United States

RECRUITING

Henry Ford Health

Detroit, Michigan, 48202, United States

RECRUITING

Mayo Clinic

Rochester, Minnesota, 55905, United States

RECRUITING

The Clinical Research Center LLC.

St Louis, Missouri, 63141, United States

RECRUITING

Montana Medical Research, Inc.

Missoula, Montana, 59808, United States

RECRUITING

Equity Medical (at Cameron Dermatology) - New York

New York, New York, 10023, United States

RECRUITING

Bernstein Clinical Research Center

Cincinnati, Ohio, 45236, United States

RECRUITING

Allergy & Clinical Immunology Associates

Pittsburgh, Pennsylvania, 15241, United States

RECRUITING

National Allergy, Asthma & Urticaria Centers of Charleston

Charleston, South Carolina, 29407, United States

RECRUITING

Medical University of South Carolina (MUSC)

Charleston, South Carolina, 29425, United States

RECRUITING

Reveal Research Institute

Dallas, Texas, 75235, United States

RECRUITING

Austin Institute for Clinical Research

Pflugerville, Texas, 78660, United States

RECRUITING

Odense University Hospital - Odense

Odense, 5000, Denmark

RECRUITING

Fraunhofer-Institut fuer Translationale Medizin und Pharmakologie ITMP - Standort Berlin

Berlin, 12203, Germany

RECRUITING

Universitaetsklinikum Carl Gustav Carus Dresden

Dresden, 01307, Germany

RECRUITING

Universitaetsklinikum Frankfurt - Klinikum der Johann Wolfgang Goethe Universitaet

Frankfurt am Main, 60596, Germany

RECRUITING

Medizinische Hochschule Hannover (MHH)

Hanover, 30625, Germany

RECRUITING

Universitaetsmedizin der Johannes Gutenberg - Universitaet Mainz

Mainz, 55131, Germany

RECRUITING

Universitaetsklinikum Tuebingen

Tübingen, 72016, Germany

RECRUITING

Azienda Ospedale - Università Padova

Padua, 35128, Italy

RECRUITING

Azienda Ospedaliero Universitaria Policlinico Umberto

Rome, 00161, Italy

RECRUITING

Centro Ricerche Cliniche di Verona s.r.l.

Verona, 37134, Italy

RECRUITING

Hospital del Mar

Barcelona, 08003, Spain

RECRUITING

Hospital Universitario Vall d'Hebron

Barcelona, 08035, Spain

RECRUITING

Hospital Universitari de Bellvitge

Barcelona, 08907, Spain

RECRUITING

Hospital Regional Universitario de Malaga

Málaga, 29010, Spain

RECRUITING

National Taiwan University Hospital Hsin-Chu Branch

Hsinchu, 300, Taiwan

RECRUITING

Kaohsiung Veterans General Hospital (KSVGH)

Kaohsiung City, 813414, Taiwan

RECRUITING

Taipei Medical University - Shuang Ho Hospital

New Taipei City, 235, Taiwan

RECRUITING

China Medical University Hospital

Taichung, 40402, Taiwan

RECRUITING

National Taiwan University Hospital

Taipei, 100225, Taiwan

RECRUITING

Linkou Chang Gung Memorial Hospital (CGMHLK)

Taoyuan, 105406, Taiwan

RECRUITING

MeSH Terms

Conditions

Chronic Inducible UrticariaChronic UrticariaCold UrticariaFamilial dermographism

Condition Hierarchy (Ancestors)

UrticariaSkin Diseases, VascularSkin DiseasesSkin and Connective Tissue DiseasesHypersensitivity, ImmediateHypersensitivityImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Central Study Contacts

Blueprint Medicines, EU Contact

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Arms A1 and A3 are non-randomized and open label. Arm B is randomized and double blind.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 9, 2025

First Posted

April 17, 2025

Study Start

May 28, 2025

Primary Completion (Estimated)

December 31, 2026

Study Completion (Estimated)

December 31, 2026

Last Updated

February 17, 2026

Record last verified: 2026-02

Locations