NCT06797583

Brief Summary

Participants are being asked to take part in this clinical trial, a type of research study, because investigators want to learn more about oxygen usage in the brain. Patients diagnosed with sickle cell disease are at risk for difficulties with thinking and academic skills. The brain requires a consistent supply of oxygen for normal function, but this supply is reduced among patients with sickle cell disease. The development of new treatments to improve cerebrovascular functioning is needed to limit these difficulties. Transcranial photobiomodulation (i.e., light stimulation to the brain) has the potential to improve cerebrovascular and neurocognitive functioning among patients with sickle cell disease.Participants will be selected randomly (like the flip of a coin) to receive either active light therapy or placebo (no active light treatment). Primary Objectives

  • Measure the participation rate in a study of transcranial photobiomodulation to improve cognitive functioning in a sample of children with sickle cell disease (ages 8- 17 years).
  • Assess self- and caregiver-reported ratings of feasibility and acceptability.
  • Evaluate the frequency and nature of side effects associated with transcranial photobiomodulation. Secondary Objectives
  • To assess the change in cognitive performance associated with transcranial photobiomodulation compared to a sham control condition.
  • To measure changes in cerebrovascular oxygenation (oxygenated and deoxygenated hemoglobin) following transcranial photobiomodulation compared to a sham control condition.

Trial Health

65
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
60

participants targeted

Target at P25-P50 for not_applicable

Timeline
43mo left

Started Apr 2026

Longer than P75 for not_applicable

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress4%
Apr 2026Dec 2029

First Submitted

Initial submission to the registry

December 12, 2024

Completed
2 months until next milestone

First Posted

Study publicly available on registry

January 28, 2025

Completed
1.2 years until next milestone

Study Start

First participant enrolled

April 1, 2026

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2027

Expected
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2029

Last Updated

April 23, 2026

Status Verified

April 1, 2026

Enrollment Period

1.7 years

First QC Date

December 12, 2024

Last Update Submit

April 22, 2026

Conditions

Keywords

Sickle Cell Disease

Outcome Measures

Primary Outcomes (7)

  • Measure the participation rate in a study of transcranial photobiomodulation to improve cognitive functioning in a sample of children with sickle cell disease (ages 8-17 years).

    A binary variable indicating whether a participant engaged in the study (1 = participated, 0 = did not participate). Overall participation rate will be calculated as the proportion of participants who engaged in this study.

    Through study completion of all enrolled participants, estimated to be 3 years

  • Assess self-reported ratings of feasibility.

    Subgroup analysis and logistic regression analysis will be used to describe factors of interest which may impact participation rates.

    Immediately post intervention period

  • Assess self-reported ratings of acceptability.

    Subgroup analysis and logistic regression analysis will be used to describe factors of interest which may impact participation rates.

    Immediately post intervention period

  • Assess caregiver-reported ratings of feasibility.

    Subgroup analysis and logistic regression analysis will be used to describe factors of interest which may impact participation rates. Qualitative metrics will also be used to analyze semi-structured interviews.

    Immediately post intervention period

  • Assess caregiver-reported ratings of acceptability.

    Subgroup analysis and logistic regression analysis will be used to describe factors of interest which may impact participation rates. Qualitative metrics will also be used to analyze semi-structured interviews.

    Immediately post intervention period

  • Evaluate the frequency and nature of side effects associated with transcranial photobiomodulation.

    The frequency and percentage of each type of side effect will be calculated along with summary statistics for the nature and frequency of side effects.

    Immediately before intervention, immediately after intervention and one week post intervention period.

  • Evaluate the frequency and nature of side effects associated with transcranial photobiomodulation.

    Descriptive statistics of self-report ratings on the Visual Analog Pain Scale will be reported.

    Immediately before intervention, immediately after intervention and one week post intervention period

Secondary Outcomes (6)

  • To assess the change in cognitive performance associated with transcranial photobiomodulation

    Assessed immediately before and immediately after intervention.

  • To assess the change in cognitive performance associated with transcranial photobiomodulation.

    Assessed immediately before and immediately after intervention

  • To assess the change in cognitive performance associated with a sham control condition.

    Assessed immediately before and immediately after intervention.

  • To assess the change in cognitive performance associated with a sham control condition.

    Assessed immediately before and immediately after intervention

  • To measure changes in cerebrovascular oxygenation (oxygenated and deoxygenated hemoglobin) following transcranial photobiomodulation.

    Assessed immediately before and immediately after intervention.

  • +1 more secondary outcomes

Study Arms (4)

SCD Genotype SS/SB0; Age 8-12 Years

ACTIVE COMPARATOR

Transcranial photobiomodulation (TPBM), a light-based treatment using a fNIRS headset to capture changes in cerebral hemodynamics in the prefrontal cortex associated with (TPBM).

Device: Active Transcranial Photobiomodulation (TPBM)

SCD Genotype - SS/SB0; Age 13-17 Years

ACTIVE COMPARATOR

Transcranial photobiomodulation (TPBM), a light-based treatment using a fNIRS headset to capture changes in cerebral hemodynamics in the prefrontal cortex associated with (TPBM).

Device: Active Transcranial Photobiomodulation (TPBM)

SCD Genotype - SC/SB+; Age 8-12 Years

SHAM COMPARATOR

Sham condition using a randomized block design involving 2 (TPBM): 1(sham) randomization.

Device: Sham Transcranial photobiomodulation (TPBM)

SCD Genotype - SC/SB+; Age 13-17 Years

SHAM COMPARATOR

Sham condition using a randomized block design involving 2 (TPBM): 1(sham) randomization.

Device: Sham Transcranial photobiomodulation (TPBM)

Interventions

Sham condition using a randomized block design involving 2 (TPBM): 1(sham) randomization.

SCD Genotype - SC/SB+; Age 13-17 YearsSCD Genotype - SC/SB+; Age 8-12 Years

CytonBrite, 1064nm LED

SCD Genotype - SS/SB0; Age 13-17 YearsSCD Genotype SS/SB0; Age 8-12 Years

Eligibility Criteria

Age8 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Patient diagnosed with sickle cell disease of any genotype
  • Enrolled in the Sickle Cell Clinical Research and Intervention Program (SCCRIP)
  • Between the ages of 8 to 17 years
  • Primary language is English
  • Participant and Parent/Legal Guardian is willing to participate and provide consent/assent according to institutional guidelines

You may not qualify if:

  • History of an abnormal transcranial doppler screening
  • History of a documented silent cerebral infarct
  • History of documented central nervous system injury, including a traumatic brain injury, Moya Moya disease, or overt stroke
  • Participant received transfusion treatment within the past three months.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Related Links

MeSH Terms

Conditions

Anemia, Sickle Cell

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Andrew Heitzer, PhD

    St. Jude Children's Research Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Andrew Heitzer, PhD

CONTACT

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Masking Details
Research participants will be told of their assigned group (sham control or intervention) after all study procedures are completed.
Purpose
SUPPORTIVE CARE
Intervention Model
PARALLEL
Model Details: The fNIRS device uses light to measure blood flow and oxygen levels in the brain. Participants will be assigned to receive transcranial photobiomodulation or a sham condition using a randomized block design. Randomized block design involving 2 (TPBM): 1(sham) randomization. One group will wear fNIRS headset which will deliver light therapy; or a headset with placebo (no light therapy) and complete a series of computer tests while wearing the headset for 10 minutes. The groups will be divided by genotype (SS/SB0 and SC/SB+) and age (8-12 and 13-17) such that there will be four subgroups that are randomly assigned.
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 12, 2024

First Posted

January 28, 2025

Study Start

April 1, 2026

Primary Completion (Estimated)

December 1, 2027

Study Completion (Estimated)

December 1, 2029

Last Updated

April 23, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Individual participant de-identified datasets containing the variables analyzed in the published article will be made available (related to the study primary or secondary objectives contained in the publication). Supporting documents such as the protocol, statistical analyses plan, and informed consent are available through the ClinicalTrials.gov (CTG) website for the specific study. Data used to generate the published article will be made available at the time of article publication. Investigators who seek access to individual level de-identified data will contact the computing team in the Department of Biostatistics (ClinTrialDataRequest@stjude.org) who will respond to the data request.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Data will be made available at the time of article publication.
Access Criteria
Data will be provided to researchers following a formal request with the following information: full name of requestor, affiliation, data set requested, and timing of when data is needed. As an informational point, the lead statistician and study principal investigator will be informed that primary results datasets have been requested.