NCT06791824

Brief Summary

This is a randomized, open-label, phase IB/II clinical study to evaluate the safety, tolerability and preliminary efficacy of CM313(SC) injection in patients with relapsed/refractory aplastic anemia

Trial Health

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Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
125

participants targeted

Target at P75+ for phase_1

Timeline
19mo left

Started Mar 2025

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress45%
Mar 2025Dec 2027

First Submitted

Initial submission to the registry

January 15, 2025

Completed
9 days until next milestone

First Posted

Study publicly available on registry

January 24, 2025

Completed
1 month until next milestone

Study Start

First participant enrolled

March 1, 2025

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2027

Last Updated

February 18, 2025

Status Verified

February 1, 2025

Enrollment Period

2.8 years

First QC Date

January 15, 2025

Last Update Submit

February 14, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Adverse events (AE)

    Assess the safety and tolerability

    Up to 52 weeks

Study Arms (3)

CM313(SC)(low dose group)

EXPERIMENTAL
Biological: CM313(SC) injection

CM313(SC)(medium dose group)

EXPERIMENTAL
Biological: CM313(SC) injection

CM313(SC)(high dose group)

EXPERIMENTAL
Biological: CM313(SC) injection

Interventions

Phase IB: CM313(SC) administered at low dose according to the protocol. Phase II: CM313(SC) administered at different doses based on Phase IB's results.

CM313(SC)(low dose group)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of idiopathic aplastic anemia.
  • Patients must meet the requirements of relapsed/refractory aplastic anemia defined in the protocol.
  • Male or female, age≥18 years.
  • The Eastern Cooperative Oncology Group (ECOG) physical status score ≤2.
  • Willing and able to comply with the requirements for this study and written informed consent.

You may not qualify if:

  • The inherited bone marrow failure syndromes.
  • Previously treated with the anti-CD38 monoclonal antibody.
  • Have an allergy to humanized monoclonal antibody or any part of CM313.
  • Pregnant or breastfeeding females, or females planning to become pregnant during the study.
  • Any condition considered to be ineligible for the study by the investigator.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Institute of Hematology & Blood Diseases Hospital

Tianjin, Tianjin Municipality, China

Location

MeSH Terms

Conditions

Anemia, Aplastic

Interventions

Injections

Condition Hierarchy (Ancestors)

AnemiaHematologic DiseasesHemic and Lymphatic DiseasesBone Marrow Failure DisordersBone Marrow Diseases

Intervention Hierarchy (Ancestors)

Drug Administration RoutesDrug TherapyTherapeutics

Study Officials

  • Jun Shi

    Institute of Hematology & Blood Diseases Hospital, China

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 15, 2025

First Posted

January 24, 2025

Study Start

March 1, 2025

Primary Completion (Estimated)

December 1, 2027

Study Completion (Estimated)

December 1, 2027

Last Updated

February 18, 2025

Record last verified: 2025-02

Locations