NCT03055078

Brief Summary

This study is to evaluate the safety and efficacy of Umbilical Cord Derived Mesenchymal Stem Cells transplantation in aplastic anemia.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
10

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Jan 2017

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2017

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

February 4, 2017

Completed
12 days until next milestone

First Posted

Study publicly available on registry

February 16, 2017

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2018

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2019

Completed
Last Updated

April 7, 2017

Status Verified

April 1, 2017

Enrollment Period

1.9 years

First QC Date

February 4, 2017

Last Update Submit

April 6, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Hemoglobin levels in peripheral blood

    The recovery of bone marrow erythrocyte is evaluated by hemoglobin levels (g/L) in peripheral blood.

    Post cell transplantation: 9months

Secondary Outcomes (5)

  • The number of red blood cell in peripheral blood

    Post cell transplantation: 1, 3, 6, 9months

  • The number of granulocyte in peripheral blood

    Post cell transplantation: 1, 3, 6, 9months

  • The number of white blood cell in peripheral blood

    Post cell transplantation: 1, 3, 6, 9months

  • The evaluation of bone marrow megakaryocytic series

    Post cell transplantation: 1, 3, 6, 9months

  • adverse reaction

    Post cell transplantation: 1, 3, 6, 9months

Study Arms (1)

mesenchymal stem cells

EXPERIMENTAL

According to the inclusion and exclusion criteria, selected patients were divided into a cell therapy group and a control group. Umbilical cord derived mesenchymal stem cells at a dose of 100-300 million by intravenous infusion.

Biological: mesenchymal stem cells

Interventions

Patients in the cell treated group were given umbilical cord derived mesenchymal stem cells by intravenous infusion besides conventional therapy. There was only conventional treatment in the control group. All patients after treatment for 1months, 3months, 6months and 9months were evaluated respectively the therapeutic effect.

mesenchymal stem cells

Eligibility Criteria

Age14 Years - 60 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Diagnosis of AA according to established criteria in 2010
  • Age from 14 to 60 years
  • Suffering from AA within six months
  • No serious infection or acute hemorrhage.
  • Left ventricular ejection fraction (LVEF) ≥ 50%
  • No acute infectious diseases.
  • Understanding and willingness to sign a written informed consent document.
  • Eastern Cooperative Oncology Group(ECOG) score of 0-2pionts.

You may not qualify if:

  • \- Patients with AA have to be disqualified from this study if any of the following is applicable.
  • Severe aplastic anemia(SAA) with severe infection.
  • Severe aplastic anemia(SAA) with active hemorrhage.
  • Severe heart attack, liver and kidney disease following serious complications
  • Patients with allergic constitution.
  • Pregnancy and lactation.
  • Accompanied by malignant tumors and other clonal disease.
  • Patients with active tuberculosis, acute sever hepatitis or infectious period of diseases.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

the First Hospital of Hebei Medical University

Shijiazhuang, Hebei, 050031, China

RECRUITING

MeSH Terms

Conditions

Anemia, Aplastic

Condition Hierarchy (Ancestors)

AnemiaHematologic DiseasesHemic and Lymphatic DiseasesBone Marrow Failure DisordersBone Marrow Diseases

Study Officials

  • Baoyong Yan, Doctor

    The First Hospital of Hebei Medical University

    STUDY CHAIR
  • Qingchi Liu, Doctor

    The First Hospital of Hebei Medical University

    STUDY DIRECTOR
  • Quanhai Li, Doctor

    The First Hospital of Hebei Medical University

    STUDY DIRECTOR
  • Xiaohui Jia, Doctor

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Xianyun Wang, Doctor

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Fan Zhang, Bachelor

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Yang Shen, Master

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Bing Ma, Master

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Wanyi Yin, Master

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Dan Zhao, Master

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR
  • Bojian Sun, Master

    The First Hospital of Hebei Medical University

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Jun Zhang, Master

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Director of Cell Thearpy Center, the First Hospital of HeibeiMU

Study Record Dates

First Submitted

February 4, 2017

First Posted

February 16, 2017

Study Start

January 1, 2017

Primary Completion

December 1, 2018

Study Completion

December 1, 2019

Last Updated

April 7, 2017

Record last verified: 2017-04

Data Sharing

IPD Sharing
Will not share

Locations